Clinical Trial to Evaluate Safety and Efficacy of CCX168 in ANCA-Associated Vasculitis

NCT ID: NCT02222155

Last Updated: 2025-03-13

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

View full results

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

42 participants

Study Classification

INTERVENTIONAL

Study Start Date

2015-02-04

Study Completion Date

2016-07-19

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

The aim of this trial is to test the safety and efficacy of two dose regimens of the complement C5a receptor CCX168 in patients with anti-neutrophil cytoplasmic antibody (ANCA)-associated vasculitis (AAV).

Funding Source - FDA OOPD

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Complement 5a and its receptor C5aR (CD88) is involved in the pathogenesis of anti-neutrophil cytoplasmic antibody (ANCA)-associated vasculitis. This is a randomized, double-blind, placebo-controlled Phase 2 study to evaluate the safety and efficacy of the C5aR inhibitor CCX168 in subjects with ANCA-associated vasculitis. The aim of this trial is to test the safety and efficacy of two dose regimens of the complement C5a receptor CCX168 in patients with anti-neutrophil cytoplasmic antibody (ANCA)-associated vasculitis (AAV).

Study acquired by Amgen and all disclosures were done by previous sponsor ChemoCentryx.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

ANCA-associated Vasculitis

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

CCX168 low dose plus standard of care

Capsule, 10 mg, twice daily + standard of care for 12 weeks

Group Type ACTIVE_COMPARATOR

CCX168 10 mg, twice daily, plus cyclophosphamide/rituximab plus glucocorticoids

Intervention Type DRUG

CCX168 high dose plus standard of care

Capsule, 30 mg, twice daily + standard of care for 12 weeks

Group Type ACTIVE_COMPARATOR

CCX168 30 mg, twice daily, cyclophosphamide/rituximab plus glucocorticoids

Intervention Type DRUG

Placebo, twice daily + standard of care

Capsule, placebo, twice daily + standard of care for 12 weeks

Group Type PLACEBO_COMPARATOR

Placebo, twice daily, plus cyclophosphamide/rituximab plus glucocorticoids

Intervention Type OTHER

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

CCX168 10 mg, twice daily, plus cyclophosphamide/rituximab plus glucocorticoids

Intervention Type DRUG

CCX168 30 mg, twice daily, cyclophosphamide/rituximab plus glucocorticoids

Intervention Type DRUG

Placebo, twice daily, plus cyclophosphamide/rituximab plus glucocorticoids

Intervention Type OTHER

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Clinical diagnosis of granulomatosis with polyangiitis (Wegener's), microscopic polyangiitis or renal limited vasculitis
* Male and female subjects, aged at least 18 years, with new or relapsed AAV where treatment with cyclophosphamide or rituximab would be required
* Use of adequate contraception during, and for at least the three months after, any administration of study medication is required
* Positive indirect immunofluorescence (IIF) test for P-ANCA or C-ANCA, or positive ELISA test for anti-proteinase-3 (PR3) or anti-myeloperoxidase (MPO) at screening
* Have at least one "major" item, or at least 3 other items, or at least 2 renal items on the Birmingham Vasculitis Activity Score (BVAS) version 3
* Estimated glomerular filtration rate (eGFR) ≥ 20 mL per minute

Exclusion Criteria

* Severe disease as determined by rapidly progressive glomerulonephritis, alveolar hemorrhage, hemoptysis, rapid-onset mononeuritis multiplex or central nervous system involvement
* Any other multi-system autoimmune disease
* Medical history of coagulopathy or bleeding disorder
* Received cyclophosphamide within 12 weeks prior to screening; if on azathioprine, mycophenolate mofetil, or methotrexate at the time of screening, these drugs must be withdrawn prior to receiving the cyclophosphamide or rituximab dose on Day 1
* Received intravenous corticosteroids, \>3000 mg methylprednisolone equivalent, within 12 weeks prior to screening
* Received an oral daily dose of a corticosteroid of more than 10 mg prednisone-equivalent for more than 6 weeks continuously prior to the screening visit
* Received rituximab or other B-cell antibody within 52 weeks of screening or 26 weeks provided B cell reconstitution has occurred; received anti-tumor necrosis factor (TNF) treatment, abatacept, alemtuzumab, intravenous immunoglobulin (IVIg), belimumab, tocilizumab, or plasma exchange within 12 weeks prior to screening
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Amgen

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

MD

Role: STUDY_DIRECTOR

Amgen

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Huntsville, Alabama, United States

Site Status

Phoenix, Arizona, United States

Site Status

Tucson, Arizona, United States

Site Status

Long Beach, California, United States

Site Status

Los Angeles, California, United States

Site Status

San Francisco, California, United States

Site Status

Aurora, Colorado, United States

Site Status

Washington D.C., District of Columbia, United States

Site Status

Miami Springs, Florida, United States

Site Status

Tampa, Florida, United States

Site Status

Chicago, Illinois, United States

Site Status

Kansas City, Kansas, United States

Site Status

Lexington, Kentucky, United States

Site Status

Louisville, Kentucky, United States

Site Status

Shreveport, Louisiana, United States

Site Status

Charlestown, Massachusetts, United States

Site Status

Duluth, Minnesota, United States

Site Status

Tupelo, Mississippi, United States

Site Status

St Louis, Missouri, United States

Site Status

Reno, Nevada, United States

Site Status

Lebanon, New Hampshire, United States

Site Status

Albuquerque, New Mexico, United States

Site Status

Great Neck, New York, United States

Site Status

Mineola, New York, United States

Site Status

New York, New York, United States

Site Status

Syracuse, New York, United States

Site Status

Chapel Hill, North Carolina, United States

Site Status

New Bern, North Carolina, United States

Site Status

Columbus, Ohio, United States

Site Status

Duncansville, Pennsylvania, United States

Site Status

Philadelphia, Pennsylvania, United States

Site Status

Providence, Rhode Island, United States

Site Status

Charleston, South Carolina, United States

Site Status

Chattanooga, Tennessee, United States

Site Status

Amarillo, Texas, United States

Site Status

Austin, Texas, United States

Site Status

Houston, Texas, United States

Site Status

Salt Lake City, Utah, United States

Site Status

Seattle, Washington, United States

Site Status

Calgary, Alberta, Canada

Site Status

Toronto, Ontario, Canada

Site Status

Greenfield Park, Quebec, Canada

Site Status

Lévis, Quebec, Canada

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Canada

References

Explore related publications, articles, or registry entries linked to this study.

Merkel PA, Niles J, Jimenez R, Spiera RF, Rovin BH, Bomback A, Pagnoux C, Potarca A, Schall TJ, Bekker P; CLASSIC Investigators. Adjunctive Treatment With Avacopan, an Oral C5a Receptor Inhibitor, in Patients With Antineutrophil Cytoplasmic Antibody-Associated Vasculitis. ACR Open Rheumatol. 2020 Nov;2(11):662-671. doi: 10.1002/acr2.11185. Epub 2020 Oct 31.

Reference Type DERIVED
PMID: 33128347 (View on PubMed)

Provided Documents

Download supplemental materials such as informed consent forms, study protocols, or participant manuals.

Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

#FD-R-5414

Identifier Type: OTHER

Identifier Source: secondary_id

CL003_168

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.

Belimumab in Remission of VASculitis
NCT01663623 COMPLETED PHASE3
Iptacopan in Patients With ANCA Associated Vasculitis
NCT06388941 ACTIVE_NOT_RECRUITING PHASE2