ADVATE/ ADYNOVI Hemophilia A Outcome Database (AHEAD)

NCT ID: NCT02078427

Last Updated: 2024-06-17

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Total Enrollment

951 participants

Study Classification

OBSERVATIONAL

Study Start Date

2011-06-28

Study Completion Date

2024-01-16

Brief Summary

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The purpose of the study is to document the natural history of hemophilia A disease and long-term outcomes in terms of effectiveness, safety and quality of life in participants receiving Antihemophilic Factor (Recombinant) - Plasma/Albumin Free Method (rAHF-PFM) or Antihemophilic Factor (Recombinant) - Pegylated (rAHF-PEG) in routine clinical practice

Detailed Description

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Conditions

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Hemophilia A

Study Design

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Observational Model Type

COHORT

Study Time Perspective

PROSPECTIVE

Study Groups

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rAHF-PFM

Participants treated with rAHF-PFM alone

ADVATE

Intervention Type BIOLOGICAL

Antihemophilic Factor (Recombinant) - Plasma/Albumin Free Method

rAHF-PEG

Participants treated with rAHF-PEG alone

ADYNOVI

Intervention Type BIOLOGICAL

Antihemophilic Factor (Recombinant) Pegylated

rAHF-PFM then rAHF-PEG

Participants treated with rAHF-PFM and subsequently switched to rAHF-PEG

ADVATE

Intervention Type BIOLOGICAL

Antihemophilic Factor (Recombinant) - Plasma/Albumin Free Method

ADYNOVI

Intervention Type BIOLOGICAL

Antihemophilic Factor (Recombinant) Pegylated

Interventions

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ADVATE

Antihemophilic Factor (Recombinant) - Plasma/Albumin Free Method

Intervention Type BIOLOGICAL

ADYNOVI

Antihemophilic Factor (Recombinant) Pegylated

Intervention Type BIOLOGICAL

Other Intervention Names

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octocog alfa rAHF-PFM rurioctocog alfa pegol rAHF-PEG

Eligibility Criteria

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Inclusion Criteria

* Participant has hemophilia A {FVIII lesser than or equal to (\<=)5%}
* Participant is prescribed Antihemophilic Factor (Recombinant) - Plasma/Albumin Free Method (rAHF-PFM) or Antihemophilic Factor (Recombinant) - Pegylated (rAHF-PEG) by the treating physician
* Participant or participant's legally authorized representative provides informed consent

Exclusion Criteria

* Participant has known hypersensitivity to the active substance or any of the excipients
* Participant has known allergic reaction to mouse or hamster proteins
* Participant has participated in another clinical study involving an investigational product (IP) or device within 30 days prior to study enrollment or is scheduled to participate in another clinical study involving another FVIII concentrate or device during the course of this study
Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Baxalta Innovations GmbH, now part of Shire

INDUSTRY

Sponsor Role collaborator

Baxalta now part of Shire

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Study Director

Role: STUDY_DIRECTOR

Takeda

Locations

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Royal Prince Alfred Hospital

Camperdown, New South Wales, Australia

Site Status

South Metropolitan Health Service trading as Fiona Stanley Hospital

Murdoch, Western Australia, Australia

Site Status

Landes Frauen und Kinderklinik Linz (LFKK Linz)

Linz, , Austria

Site Status

Kepler Universitätsklinikum Klinik für Kinder-und Jugendheilkunde

Linz, , Austria

Site Status

Medizinische Universitaet Wien

Vienna, , Austria

Site Status

Cliniques Universitaires Saint-Luc

Brussels, , Belgium

Site Status

Hemoce - Ce

Fortaleza, Ceará, Brazil

Site Status

Hemocentro do Espírito Santo

Vitória, Espírito Santo, Brazil

Site Status

Hemepar - Pr

Curitiba, Paraná, Brazil

Site Status

Hemorgs - Rs

Porto Alegre, Parthenon, Brazil

Site Status

Fundação HEMOPA

Belém, Pará, Brazil

Site Status

Hemocentro da UNICAMP

Campinas, São Paulo, Brazil

Site Status

Hemocentro Ribeirão Preto - SP

Ribeirão Preto, São Paulo, Brazil

Site Status

Hemorio - Rj

Rio de Janeiro, , Brazil

Site Status

Faculdade de Medicina da Universidade de São Paulo

São Paulo, , Brazil

Site Status

Stollery Children's Hospital, University of Alberta

Edmonton, Alberta, Canada

Site Status

The Moncton City Hospital

Moncton, New Brunswick, Canada

Site Status

Children's Hospital of Eastern Ontario

Ottawa, Ontario, Canada

Site Status

St-Michael's Hospital

Toronto, Ontario, Canada

Site Status

Sick Kids Hospital

Toronto, Ontario, Canada

Site Status

Royal University Hospital

Saskatoon, Saskatchewan, Canada

Site Status

Shenzhen Children's Hospital

Shenzhen, Futian, China

Site Status

Nanfang Hospital Affiliated to Nanfang Medical University

Guangzhou, Guangdong, China

Site Status

Institute of Hematology, Blood Disease Hospital, PUMC&CAMS

Tianjin, Heping, China

Site Status

Tongji Hospital, Tongji Medical College of Huazhong University of Science & Technology

Wuhan, Hubei, China

Site Status

The Affiliated Hospital of Xuzhou Medical University

Xuzhou, Jiangsu, China

Site Status

The Blood Center of Shandong Province

Jinan, Shandong, China

Site Status

Beijing Children's Hospital Affiliated to Capital University of Medical Sciences

Beijing, , China

Site Status

Nanjing Drum Tower Hospital The Affiliated Hospital of Nanjing University Medical School

Nanjing, , China

Site Status

Shenzhen Second People's Hospital

Shenzhen, , China

Site Status

IPS FUSA SAS Centro Integral de Coagulacion

Atlántico, , Colombia

Site Status

Integral Solutions SD SAS

Bogotá, , Colombia

Site Status

Fundación Oftalmológica de Santander FOSCAL

Floridablanca, , Colombia

Site Status

Fakultní nemocnice Brno

Brno, , Czechia

Site Status

Fakultní nemocnice Ostrava, Oddělení dětské hematologie a hematoonkologie

Ostrava, , Czechia

Site Status

Fakultní nemocnice Ostrava

Ostrava, , Czechia

Site Status

Fakultní nemocnice v Motole

Prague, , Czechia

Site Status

Rigshospitalet

Copenhagen, , Denmark

Site Status

"Hôpital Morvan CHRU de Brest"

Brest, , France

Site Status

CHU Côte de Nacre - CRTH

Caen, , France

Site Status

Centre Hospitalier Générale - CTH

Chambéry, , France

Site Status

CTRH - CHU Bocage

Dijon, , France

Site Status

Hôpital André Mignot

Le Chesnay, , France

Site Status

Hôpital de la Mère et de l'Enfant - CHU de LIMOGES

Limoges, , France

Site Status

CHRU Hôtel Dieu - CRTH

Nantes, , France

Site Status

Hôpital Cochin

Paris, , France

Site Status

CHU de Reims Hôpital Maison Blanche - CRTH

Reims, , France

Site Status

Centre Régional de Traitement de l'Hémophilie et des Maladies hémorragiques. CHU de Rennes - Hôpital Pontchaillou

Rennes, , France

Site Status

CHRU Charles Nicolle

Rouen, , France

Site Status

CIC

Saint-Priest-en-Jarez, , France

Site Status

CHRU Purpan CRTH - Pavillon Sénac

Toulouse, , France

Site Status

Aghia Sofia Children's Hospital

Goudi, Athens, Greece

Site Status

Laikon General Hospital

Goudi, Athens, Greece

Site Status

General Hospital of Thessaloniki "Ippokratio"

Thessaloniki, , Greece

Site Status

Heim Pál Gyermekkórház

Budapest, , Hungary

Site Status

Debreceni Egyetem Klinikai Kozpont

Debrecen, , Hungary

Site Status

Mohács City Hospital

Mohács, , Hungary

Site Status

Jósa András County Hospital

Nyíregyháza, , Hungary

Site Status

Markusovszky Hospital

Szombathely, , Hungary

Site Status

Azienda Ospedaliera Policlinico Consorziale Di Bari

Bari, , Italy

Site Status

Policlinico S Orsola Malpighi

Bologna, , Italy

Site Status

Azienda Ospedaliera Universitaria Vittorio Emanuele, Ferrarotto, S. Bambino

Catania, , Italy

Site Status

Ospedale Pugliese -Ciaccio

Catanzaro, , Italy

Site Status

Az. Osp. Univ. Careggi

Florence, , Italy

Site Status

Ospedale di Macerata

Macerata, , Italy

Site Status

Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico

Milan, , Italy

Site Status

Azienda Ospedaliera Universitaria Federico II

Napoli, , Italy

Site Status

Azienda Ospedaliera di Padova Clinica Medica II

Padua, , Italy

Site Status

AOUP P. Giaccone

Palermo, , Italy

Site Status

Azienda Ospedaliera Bianchi Melacrino Morelli

Reggio Calabria, , Italy

Site Status

Università degli studi di Roma "La Sapienza"

Roma, , Italy

Site Status

Ospedale Pediatrico Bambino Gesù

Roma, , Italy

Site Status

Policlinico Universitario Gemelli

Roma, , Italy

Site Status

Centro Emofilia e Coagulopatie Rare

Scorrano, , Italy

Site Status

Ospedale Molinette

Torino, , Italy

Site Status

Rikshospitalet

Oslo, , Norway

Site Status

Rikshospitalet, Oslo University Hospital

Oslo, , Norway

Site Status

Szpital Uniwersytecki nr 1 im. dr Andrzeja Jurasza

Bydgoszcz, , Poland

Site Status

Samodzielny Publiczny Szpital Kliniczny nr 1

Gdansk, , Poland

Site Status

Samodzielny Publiczny Dzieciecy Szpital Kliniczny

Warsaw, , Poland

Site Status

Uniwersytecki Szpital Kliniczny we Wrocławiu

Wroclaw, , Poland

Site Status

Hospital do Divino Espírito Santo

Ponta Delgada, Azores, Portugal

Site Status

Centro Hospitalar e Universitade de Coimbra

Coimbra, , Portugal

Site Status

Centro Hospitalar Lisboa Norte Hospital de Sta. Maria

Lisbon, , Portugal

Site Status

Centro Hospitalar de São João, E.P.E.

Porto, , Portugal

Site Status

SBHI Chelyabinsk Regional Children's Clinical Hospital

Chelyabinsk, , Russia

Site Status

Federal State Budget Institution "Hematology Research Center" of Ministry of Healthcare of Russian Federation

Moscow, , Russia

Site Status

SBHI of the Republic of Kareliya Republican Hospital n.a. V.A. Baranov

Petrozavodsk, , Russia

Site Status

State Budget Healthcare Institution of Saint-Petersburg "City polyclinic #37"

Saint Petersburg, , Russia

Site Status

Clinics of FSBEI High Education Samara SMU of MoH of Russia

Samara, , Russia

Site Status

University Medical Centre Ljubljana

Ljubljana, , Slovenia

Site Status

Hospital Teresa Herrera-Materno Infantil

A Coruña, , Spain

Site Status

Hospital Hospital Sant Joan de Déu

Barcelona, , Spain

Site Status

Hospital Universitari Vall d'Hebron (HUVH)

Barcelona, , Spain

Site Status

Hospital Universitario Son Espases

Palma de Mallorca, , Spain

Site Status

Sahlgrenska University Hospital

Gothenburg, , Sweden

Site Status

Kliniska studier i Sverige - Forum Söder

Malmo, , Sweden

Site Status

Karolinska Universitetssjukhuset Solna

Stockholm, , Sweden

Site Status

Universitätsspital Basel

Basel, , Switzerland

Site Status

Inselspital Bern

Bern, , Switzerland

Site Status

Centre Hospitalier Universitaire Vaudois

Lausanne, , Switzerland

Site Status

Luzerner Kantonsspital

Lucerne, , Switzerland

Site Status

Kantonsspital St. Gallen

Sankt Gallen, , Switzerland

Site Status

FMH Kinder und Jugendmedizin, im Wabern-Zentrum

Wabern, , Switzerland

Site Status

Kinderspital Zürich

Zurich, , Switzerland

Site Status

Universitätsspital Zürich

Zurich, , Switzerland

Site Status

Hampshire Hospitals NHS Foundation Trust, Basingstoke and North Hampshire Hospital

Basingstoke, Hampshire, United Kingdom

Site Status

Cambridge University Hospital NHS Foundation Trust, Addenbrooke's Hospital

Cambridge, , United Kingdom

Site Status

East Kent Hospitals University Foundation Trust, Kent & Canterbury Hospital

Canterbury, , United Kingdom

Site Status

Great Ormond Street Hospital for Children NHS Trust

London, , United Kingdom

Site Status

Countries

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Australia Austria Belgium Brazil Canada China Colombia Czechia Denmark France Greece Hungary Italy Norway Poland Portugal Russia Slovenia Spain Sweden Switzerland United Kingdom

References

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Ozelo MC, Hermans C, Carcao M, Guillet B, Gu J, Guerra R, Tang L, Khair K. The effectiveness and safety of octocog alfa in patients with hemophilia A: up to 7-year follow-up of the real-world AHEAD international study. Ther Adv Hematol. 2024 Feb 15;15:20406207231218624. doi: 10.1177/20406207231218624. eCollection 2024.

Reference Type DERIVED
PMID: 38371314 (View on PubMed)

Related Links

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https://clinicaltrials.takeda.com/study-detail/5f6b5fc24db2bf003ab45765

To obtain more information on the study, click here/on this link

Other Identifiers

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061001

Identifier Type: -

Identifier Source: org_study_id

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