Study of Pharmacokinetics, Efficacy and Safety of a Recombinant and Protein-Free Factor VIII (rAHF-PFM) in Hemophilia A Patients - A Continuation of Clinical Study 069901

NCT ID: NCT00157053

Last Updated: 2021-08-24

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2/PHASE3

Total Enrollment

82 participants

Study Classification

INTERVENTIONAL

Study Start Date

2001-11-22

Study Completion Date

2004-08-03

Brief Summary

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The purpose of this study is to evaluate whether rAHF-PFM is safe and effective in the treatment of hemophilia A subjects. The study consists of 2 parts: Part 1 is a pharmacokinetic and safety study, and Part 2 is an evaluation of efficacy and safety. The study is open to patients who completed Baxter Study 069901.

Detailed Description

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Conditions

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Hemophilia A

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Interventions

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Antihemophilic factor, recombinant, manufactured protein-free

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Subject has completed Baxter protocol 069901
* Subject is HIV-1 seronegative or, if HIV-1 seropositive, has a CD4+ lymphocyte count \>= 400/mm3 documented within three months of the screening visit
* Subject (and his legally acceptable representative, in the case of study participants \>= 10 and \< 18 years of age) has been informed of the nature of the study, agreed to its provisions, and signed and dated the informed consent form approved by the appropriate IRB/IEC and Baxter

Exclusion Criteria

* The subject received factor VIII products other than rAHF-PFM upon completion of Baxter protocol 069901
* The subject developed an inhibitor to factor VIII, measured in the central laboratory, during Baxter protocol 069901. An inhibitor is defined as a Bethesda titer \> 1.0 or, if Bethesda titer \< 1.0, confirmation using the Nijmegen modification of the Bethesda assay with a titer \> 0.6
* The subject is scheduled to receive an immunomodulating drug other than anti-retroviral chemotherapy (e.g., a-interferon, steroids) during the course of the study
* The subject is identified by the investigator as being unable or unwilling to cooperate with study procedures
Minimum Eligible Age

10 Years

Eligible Sex

MALE

Accepts Healthy Volunteers

No

Sponsors

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Baxalta now part of Shire

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Study Director

Role: STUDY_DIRECTOR

Takeda

Locations

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Mountain States Regional Hemophilia and Thrombosis Center

Aurora, Colorado, United States

Site Status

Childrens Healthcare of Atlanta Blood Bank

Atlanta, Georgia, United States

Site Status

Comprehensive Bleeding Disorders Center

Peoria, Illinois, United States

Site Status

Indiana Hemophilia & Thrombosis Center

Indianapolis, Indiana, United States

Site Status

Michigan State University

East Lansing, Michigan, United States

Site Status

University of Medicine & Dentistry of New Jersey

New Brunswick, New Jersey, United States

Site Status

Cornell Medical Center

New York, New York, United States

Site Status

Mt. Sinai Medical School

New York, New York, United States

Site Status

Children's Hospital Medical Center Pharmacy

Cincinnati, Ohio, United States

Site Status

Hemophilia Center of Western Pennsylvania

Pittsburgh, Pennsylvania, United States

Site Status

Puget Sound Blood Center

Seattle, Washington, United States

Site Status

Allgemeines Krankenhaus der Stadt Wien

Vienna, , Austria

Site Status

KU Leuven Universitaire Ziekenhuizen

Leuven, , Belgium

Site Status

University of Alberta

Calgary, Alberta, Canada

Site Status

Hôpital Edouard Herriot

Lyon, , France

Site Status

Klinikum der J. W. Goethe - Universität

Frankfurt am Main, , Germany

Site Status

Medizinische Hochschule Hannover

Hanover, , Germany

Site Status

Klinikum Innenstadt der Universität München

Munich, , Germany

Site Status

Ospedale Maggiore di Milano

Milan, , Italy

Site Status

University Hospital MAS

Malmo, , Sweden

Site Status

The Royal Free Hospital

London, England, United Kingdom

Site Status

Central Manchester Healthcare NHS Trust

Manchester, England, United Kingdom

Site Status

The Churchill Hospital

Oxford, England, United Kingdom

Site Status

University Hospital of Wales

Cardiff, Wales, United Kingdom

Site Status

Countries

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United States Austria Belgium Canada France Germany Italy Sweden United Kingdom

References

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Shapiro A, Gruppo R, Pabinger I, Collins PW, Hay CR, Schroth P, Casey K, Patrone L, Ehrlich H, Ewenstein BM. Integrated analysis of safety and efficacy of a plasma- and albumin-free recombinant factor VIII (rAHF-PFM) from six clinical studies in patients with hemophilia A. Expert Opin Biol Ther. 2009 Mar;9(3):273-83. doi: 10.1517/14712590902729392.

Reference Type DERIVED
PMID: 19216617 (View on PubMed)

Other Identifiers

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060102

Identifier Type: -

Identifier Source: org_study_id

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