Safety and Efficacy Study of a Recombinant and Protein-Free Factor VIII (rAHF-PFM) in Hemophilia A Patients Undergoing Surgery

NCT ID: NCT00157105

Last Updated: 2021-08-24

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2/PHASE3

Total Enrollment

59 participants

Study Classification

INTERVENTIONAL

Study Start Date

2001-02-12

Study Completion Date

2004-08-03

Brief Summary

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The purpose of this study is to evaluate whether rAHF-PFM is safe and effective in the treatment of hemophilia A patients undergoing surgery.

Detailed Description

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Conditions

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Hemophilia A

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Interventions

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Antihemophilic factor, recombinant, manufactured protein-free

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Age \>= 5 years
* The subject has severe or moderately severe hemophilia A defined by a baseline factor VIII level \<= 2% of normal documented at screening or historically (e.g., at hemophilia diagnosis)
* Subjects may enroll regardless of their serologic status for human immunodeficiency virus (HIV-1) and hepatitis C virus (HCV)
* The subject requires a surgical, dental or other invasive procedure--either elective or emergency
* The subject has a history of at least 150 exposure days for all other factor VIII products (as estimated by the study site investigator) prior to study entry
* The subject has a life expectancy of at least 28 days from the day of surgery
* The subject has been informed of the nature of the study, agreed to its provisions, and signed and dated the informed consent form approved by the appropriate IRB/IEC and Baxter BioScience

Exclusion Criteria

* The subject has a detectable inhibitor to factor VIII in the local hemostasis laboratory at the investigative site at the time of enrollment
* The subject has a history of inhibitor to factor VIII \> 1.0 BU. Note: If the subject has a history of an inhibitor titer \> 1.0 BU at any time prior to enrollment but demonstrated expected clinical responses to conventional doses of factor VIII therapy, the subject may enroll
* The subject has known hypersensitivity to Recombinate
* The subject is currently participating in another investigational drug study, or has participated in any clinical trial involving an investigational drug within 30 days of study entry
* The subject has clinical and/or laboratory evidence of abnormal hemostasis from causes other than hemophilia A (e.g., late-stage chronic liver disease, immune thrombocytopenic purpura, disseminated intravascular coagulation)
* The subject is identified by the investigator as being unable or unwilling to cooperate with study procedures.
Minimum Eligible Age

5 Years

Eligible Sex

MALE

Accepts Healthy Volunteers

No

Sponsors

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Baxalta now part of Shire

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Study Director

Role: STUDY_DIRECTOR

Takeda

Locations

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Children´s Hospital Los Angeles, Hemophilia Comprehensive Care Center, Division of Pediatric Hematology/Oncology

Los Angeles, California, United States

Site Status

Children´s Healthcare of Atlanta Blood Bank

Atlanta, Georgia, United States

Site Status

Indiana Hemophilia & Thrombosis Center

Indianapolis, Indiana, United States

Site Status

University of Iowa Hospitals and Clinics, Iowa Regional Hemophilia Center, Department of Pediatrics

Iowa City, Iowa, United States

Site Status

Brigham and Women´s Hospital, Hematology Division

Boston, Massachusetts, United States

Site Status

Michigan State University

East Lansing, Michigan, United States

Site Status

Mt. Sinai Medical School, Hemophilia Comprehensive Care Center

New York, New York, United States

Site Status

Children´s Hospital Medical Center Pharmacy, Hemophilia Treatment Center

Cincinnati, Ohio, United States

Site Status

Hemophilia Center of Western Pennsylvania

Pittsburgh, Pennsylvania, United States

Site Status

Puget Sound Blood Center

Seattle, Washington, United States

Site Status

Countries

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United States

References

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Shapiro A, Gruppo R, Pabinger I, Collins PW, Hay CR, Schroth P, Casey K, Patrone L, Ehrlich H, Ewenstein BM. Integrated analysis of safety and efficacy of a plasma- and albumin-free recombinant factor VIII (rAHF-PFM) from six clinical studies in patients with hemophilia A. Expert Opin Biol Ther. 2009 Mar;9(3):273-83. doi: 10.1517/14712590902729392.

Reference Type DERIVED
PMID: 19216617 (View on PubMed)

Other Identifiers

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069902

Identifier Type: -

Identifier Source: org_study_id

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