Human Cell Line-derived Recombinant Factor VIII (Human-cl-rhFVIII) in Previously Untreated Patients

NCT ID: NCT01712438

Last Updated: 2021-01-19

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

110 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-02-28

Study Completion Date

2019-12-20

Brief Summary

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Investigate the inhibitor development rate of Human cl rhFVIII in previously untreated patients with severe Hemophilia A.

Detailed Description

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Conditions

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Severe Hemophilia A

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Human cl rhFVIII

Group Type EXPERIMENTAL

Human cl rhFVIII

Intervention Type BIOLOGICAL

Interventions

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Human cl rhFVIII

Intervention Type BIOLOGICAL

Eligibility Criteria

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Inclusion Criteria

* Male patients
* Severe Hemophilia A (FVIII:C \<1%)
* No previous treatment with FVIII concentrates or other blood products containing FVIII

Exclusion Criteria

* Diagnosis with a coagulation disorder other than Hemophilia A
* Severe liver or kidney disease
* Concomitant treatment with any systemic immunosuppressive drug
Eligible Sex

MALE

Accepts Healthy Volunteers

No

Sponsors

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Octapharma

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Sigurd Knaub

Role: STUDY_DIRECTOR

Octapharma

Locations

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UC Davis

Sacramento, California, United States

Site Status

All Children's Hospital

St. Petersburg, Florida, United States

Site Status

Harvard Children's Hospital Boston

Boston, Massachusetts, United States

Site Status

Republican Scientific Practical Center for Pediatric Oncology and Hematology

Minsk, , Belarus

Site Status

University of Alberta

Edmonton, Alberta, Canada

Site Status

BC Children's Hospital

Vancouver, British Columbia, Canada

Site Status

Mc Master Children's Hospital

Hamilton, Ontario, Canada

Site Status

Hospital for Sick Children

Toronto, Ontario, Canada

Site Status

Hopital Ste-Justine

Montreal, Quebec, Canada

Site Status

L'hôpital Côte de Nacre - CHU de Caen

Caen, , France

Site Status

Centre de traitement de l'hemophilie, Hôpital Bicêtre

Le Kremlin-Bicêtre, , France

Site Status

Hopital de la Timone

Marseille, , France

Site Status

Hôtel-Dieu de Nantes, Centre Regional de Traitement de l'hemophilie

Nantes, , France

Site Status

Hôpital Necker

Paris, , France

Site Status

CHU de Rennes - Hôpital Pontchaillou

Rennes, , France

Site Status

Hopital Trousseau - CHU Tours

Tours, , France

Site Status

Institute of Haematology and Transfusiology

Tbilisi, , Georgia

Site Status

Institut für Experimentelle Hämatologie und Transfusionsmedizin (IHT)

Bonn, , Germany

Site Status

University Hospital Frankfurt/M

Frankfurt, , Germany

Site Status

Universitätsmedizin der Johannes-Gutenberg-Universität Mainz

Mainz, , Germany

Site Status

Kasturba Medical College, Dr. TMA Pai Hospital

Manipal, Karnataka, India

Site Status

Sahyadri Speciality Hospital, Haematology & BMT Unit

Pune, , India

Site Status

Christian Medical College & Hospital, Dept of Haematology

Vellore, , India

Site Status

Univ. Di Perugia

Perugia, , Italy

Site Status

Centro di Referimento per le Malattie Emorragiche e Trombotiche

Torino, , Italy

Site Status

Scientific Research Institute of Mother and Child Health Care

Chisinau, , Moldova

Site Status

Centre Hospitalier Ibn Sina

Rabat, , Morocco

Site Status

University Medical School Warsaw

Warsaw, , Poland

Site Status

HSJ - Hospital de São João, EPE

Porto, , Portugal

Site Status

Morozovsky Children's Hospital

Moscow, , Russia

Site Status

Haemophilia Centre, University Clinical Centre

Ljubljana, , Slovenia

Site Status

Unitat d'hemofilia, Hospital Universitari Vall d'Hebron

Barcelona, , Spain

Site Status

Hospital Universitario La Paz

Madrid, , Spain

Site Status

National Children's Specialized Hospital "OHMATDET"

Kiev, , Ukraine

Site Status

Institute of Blood Pathology and Transfusion Medicine

Lviv, , Ukraine

Site Status

Cambridge University Hospital

Cambridge, , United Kingdom

Site Status

Great Ormond Street Hospital for Children

London, , United Kingdom

Site Status

Countries

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United States Belarus Canada France Georgia Germany India Italy Moldova Morocco Poland Portugal Russia Slovenia Spain Ukraine United Kingdom

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2012-002554-23

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

GENA-05

Identifier Type: -

Identifier Source: org_study_id

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