A Study Of PF-04449913 In Japanese Patients With Select Hematologic Malignancies

NCT ID: NCT02038777

Last Updated: 2025-02-26

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1

Total Enrollment

48 participants

Study Classification

INTERVENTIONAL

Study Start Date

2014-03-25

Study Completion Date

2023-12-28

Brief Summary

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This is an open-label, multi-center, Phase 1 study of PF-04449913 in Japanese patients. PF-04449913 will be administered orally as a single agent in patients with select advanced hematologic malignancies, or in combination with LDAC \[Low-Dose Ara-C\] or cytarabine and daunorubicin in previously untreated patients with AML \[Acute Myeloid Leukemia\] or high-risk MDS \[Myelodysplastic Syndrome\], or in combination with azacitidine in previously untreated patients with AML.

Detailed Description

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Conditions

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Acute Myeloid Leukemia

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SEQUENTIAL

MTD was determined in monotherapy cohort. Then two combination cohorts (Combination Cohorts 1 and 2) were added to evaluate the safety of glasdegib administered with chemotherapies. Another combination cohort (Combination Cohort 3) was added to evaluate the safety of glasdegib administered with Azacitidine. Then, Continuation Cohort which allows one Japanese patient enrolled from another trial in the same project was added. Afther that, Expansion Cohort of LDAC Combination for efficacy was added.
Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Monotherapy Cohort

PF-04449913 Monotherapy

Group Type EXPERIMENTAL

PF-04449913

Intervention Type DRUG

PF-04449913 administered orally and continuously in 28 day cycles.

Combination Cohort 1

PF-04449913 in combination with low dose ARA-C (LDAC)

Group Type EXPERIMENTAL

PF-04449913

Intervention Type DRUG

PF-04449913 administered orally and continuously in 28 day cycles.

Low dose ARA-C (LDAC)

Intervention Type DRUG

Low dose ARA-C (LDAC) administered at 20 mg SQ, BID on Days 1 through 10.

Combination Cohort 2

PF-04449913 in combination with intensive chemotherapy: PF-04449913 administered continuously for 28 days. Daunorubicin given using 60 mg/m2 for 3-days together with cytarabine 100 mg/m2 on days 1 through 7 followed by cytarabine 1g/m2 on days 1, 3, and 5 during 2-4 cycles of consolidation therapy.

Group Type EXPERIMENTAL

PF-04449913

Intervention Type DRUG

PF-04449913 administered orally and continuously in 28 day cycles.

Daunorubicin

Intervention Type DRUG

Daunorubicin given using 60 mg/m2 for 3-days.

Cytarabine

Intervention Type DRUG

Cytarabine 100 mg/m2 on days 1 through 7.

Azacitidine Combination Cohort

PF-04449913 in combination with azacitidine

Group Type EXPERIMENTAL

PF-04449913

Intervention Type DRUG

PF-04449913 administered orally and continuously in 28 day cycles.

Azacitidine

Intervention Type DRUG

Azacitidine Combination Cohort; Azacitidine 75 mg/m2 for 7 days.

Continuation Cohort

PF-04449913 Monotherapy for one patient rolled-over from another trial in the same project.

Group Type EXPERIMENTAL

PF-04449913

Intervention Type DRUG

PF-04449913 administered orally and continuously in 28 day cycles.

Expansion Cohort of LDAC Combination for Efficacy

PF-04449913 in combination with LDAC to evaluate efficacy

Group Type EXPERIMENTAL

PF-04449913

Intervention Type DRUG

PF-04449913 administered orally and continuously in 28 day cycles.

LDAC

Intervention Type DRUG

Low dose ARA-C (LDAC) administered at 20 mg SQ, BID on Days 1 through 10.

Interventions

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PF-04449913

PF-04449913 administered orally and continuously in 28 day cycles.

Intervention Type DRUG

PF-04449913

PF-04449913 administered orally and continuously in 28 day cycles.

Intervention Type DRUG

Low dose ARA-C (LDAC)

Low dose ARA-C (LDAC) administered at 20 mg SQ, BID on Days 1 through 10.

Intervention Type DRUG

PF-04449913

PF-04449913 administered orally and continuously in 28 day cycles.

Intervention Type DRUG

Daunorubicin

Daunorubicin given using 60 mg/m2 for 3-days.

Intervention Type DRUG

Cytarabine

Cytarabine 100 mg/m2 on days 1 through 7.

Intervention Type DRUG

PF-04449913

PF-04449913 administered orally and continuously in 28 day cycles.

Intervention Type DRUG

Azacitidine

Azacitidine Combination Cohort; Azacitidine 75 mg/m2 for 7 days.

Intervention Type DRUG

PF-04449913

PF-04449913 administered orally and continuously in 28 day cycles.

Intervention Type DRUG

LDAC

Low dose ARA-C (LDAC) administered at 20 mg SQ, BID on Days 1 through 10.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Patients with select advanced hematologic malignancies who are refractory, resistant or intolerant to prior therapies for monotherapy cohort.
* Patients with AML or High-Risk MDS who are newly diagnosed and previously untreated for combination cohort.
* Patients with AML who are newly diagnosed and previously untreated for azacitidine combination cohort.
* ECOG \[Eastern Cooperative Oncology Group\] performance status 0 to 2
* Adequate organ function

Exclusion Criteria

* Patients with active CNS disease
* Patient with active malignancy with the exception of basal cell carcinoma, non melanoma skin cancer, carcinoma in situ cervical
* Patient has an active, life threatening or clinically significant uncontrolled systemic infection
Minimum Eligible Age

20 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Pfizer

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Pfizer CT.gov Call Center

Role: STUDY_DIRECTOR

Pfizer

Locations

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Japanese Red Cross Nagoya First Hospital

Nagoya, Aichi-ken, Japan

Site Status

Kobe University Hospital

Kobe, Hyōgo, Japan

Site Status

Tohoku University Hospital

Sendai, Miyagi, Japan

Site Status

Tokyo Metropolitan Cancer and Infectious diseases Center Komagome Hospital

Bunkyo-ku, Tokyo, Japan

Site Status

National Cancer Center Hospital

Chuo-ku, Tokyo, Japan

Site Status

Yamagata University Hospital

Yamagata, Yamagata, Japan

Site Status

Akita University Hospital

Akita, , Japan

Site Status

Kyushu University Hospital

Fukuoka, , Japan

Site Status

Tokyo Medical University Hospital

Tokyo, , Japan

Site Status

Countries

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Japan

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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Other Identifiers

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NCT02038777

Identifier Type: REGISTRY

Identifier Source: secondary_id

B1371005

Identifier Type: -

Identifier Source: org_study_id

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