A Study of GLB-001 in Patients With Myeloid Malignancies

NCT ID: NCT06378437

Last Updated: 2025-08-19

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE1

Total Enrollment

108 participants

Study Classification

INTERVENTIONAL

Study Start Date

2024-05-24

Study Completion Date

2027-12-31

Brief Summary

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Study GLB-001-02 is a phase 1, open-label clinical study to evaluate the safety, tolerability, pharmacokinetics (PK), pharmacodynamics (PD) and preliminary efficacy of GLB-001 in study participants with relapsed or refractory or intolerant myeloid malignancies including polycythemia vera (PV), essential thrombocythemia (ET), myelofibrosis (MF), lower-risk myelodysplastic syndrome (LR-MDS), higher-risk myelodysplastic syndromes (HR-MDS), and acute myeloid leukemia (AML). This study consists of 3 parts, dose escalation (Phase 1a), dose exploration (Phase 1b) and dose expansion (Phase 1c). Dose escalation (Phase 1a) and dose exploration (Phase 1b) will evaluate the safety, tolerability, PK, PD and preliminary efficacy of GLB-001, administered orally, in study participants with PV/ET, or study participants with MF/LR-MDS/HR-MDS/AML, respectively. Dose expansion (Phase 1c) will be followed to determine the relationships among dose, exposure, toxicity, tolerability and clinical activity, to identify minimally active dose, and to select the recommended dose(s) for phase 2 study. Approximately 108 study participants may be enrolled in the study.

Detailed Description

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Conditions

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Polycythemia Vera Essential Thrombocythemia Myelofibrosis Myelodysplastic Syndromes Acute Myeloid Leukemia Myeloid Malignancy

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SEQUENTIAL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Dose Escalation of GLB-001 in Study Participants with PV and ET-Phase 1a

Phase 1a (Dose Escalation) will evaluate the safety and tolerability of GLB-001 in PV and ET study participants. A standard 3+3 dose-escalation design will be applied to evaluate a set of dose levels to determine and the maximum tolerated dose (MTD) and/or recommended expansion doses (RED) in PV and ET study participants who are eligible for dose limiting toxicity (DLT) evaluation.

Group Type EXPERIMENTAL

GLB-001

Intervention Type DRUG

Administered orally according to the assigned treatment schedule

Dose Exploration of GLB-001 in Study Participants with MF, LR-MDS, AML and HR-MDS-Phase 1b

Phase Ib 1b (Dose Exploration) will utilize a standard 3+3 dose-escalation design to evaluate the safety and tolerability of GLB-001 in MF, LR-MDS, HR-MDS and AML study participants. The starting dose will be selected within the range of tolerated dose levels determined in Phase 1a (Dose escalation).

Group Type EXPERIMENTAL

GLB-001

Intervention Type DRUG

Administered orally according to the assigned treatment schedule

Dose Expansion of GLB-001 in Study Participants with PV, ET, MF, LR-MDS, AML and HR-MDS-Phase 1c

Phase 1c (Dose Expansion) will be conducted to further determine the tolerability, efficacy and the recommended phase 2 dose (RP2D) of GLB-001 in study participants with relapsed or refractory or intolerant myeloid malignancies including PV, ET, MF, LR-MDS, HR-MDS and AML.

Group Type EXPERIMENTAL

GLB-001

Intervention Type DRUG

Administered orally according to the assigned treatment schedule

Interventions

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GLB-001

Administered orally according to the assigned treatment schedule

Intervention Type DRUG

Other Intervention Names

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GLB-C183-A-2

Eligibility Criteria

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Inclusion Criteria

* Study participants must understand and voluntarily sign a written informed consent form (ICF) prior to any study-related assessments/procedures being performed.
* Study participants is ≥18 years of age at the time of signing the ICF.
* Study participants with confirmed diagnosis of relapsed or refractory or intolerant myeloid malignancies including PV, ET, primary myelofibrosis (PMF), MDS and AML according to 2022 World Health Organization (WHO) criteria classification, and post-polycythemia vera myelofibrosis (post-PV MF) and post-essential thrombocythemia myelofibrosis (post-ET MF) according to the 2013 IWG-MRT criteria.
* Eastern Cooperative Oncology Group (ECOG) performance status of 0,1 or 2.
* Life expectancy \> 3 months.
* Good performance of major organs, including hematology, liver and kidney function, and coagulation. etc.
* Study participants are willing and able to adhere to the study visit schedule and other protocol requirements.

Exclusion Criteria

* Study participants with acute promyelocytic leukemia (APL).
* Receipt of following anticancer medications/therapies prior to the first dose of GLB-001: (1) study participants with PV or ET who received treatment with hydroxyurea within 2 days prior to the first dose, or any other treatment for PV or ET within 7 days prior to first dose of GLB-001, (2) study participants with MF who received any type of treatment for MF within 14 days prior to the first dose, such as chemotherapy, immunotherapy, radiotherapy and erythropoietin, androgens, thrombopoietin or granulocyte colony-stimulating factor, (3) study participants with LR-MDS who received any type of treatment for MDS within 14 days prior to the first dose, (4) study participants with HR-MDS or AML who received chimeric antigen receptor T cell therapy (CAR-T) or other biologic therapy within 28 days prior to the first dose of GLB-001, or received any other anticancer therapies within 14 days prior to the first dose of GLB-001.
* Receipt of any other investigational drug study within 28 days or 5 half-lives of that study drug before the first dose of GLB-001.
* Study participants with unresolved clinically significant non-hematologic toxicities that were ≥ Grade 1 or failed to recover to baseline levels following prior anticancer therapies (with the exception of alopecia or skin hyperpigmentation).
* Study participants who are scheduled to receive other anticancer therapies or other investigational drugs during the study period.
* Study participants with active acute or chronic graft versus host disease (GVHD) requiring systemic immunosuppressive therapy.
* Receipt of autologous stem cell transplantation (ASCT) within the last 3 months prior to the first dose of GLB-001, or allogeneic hematopoietic stem cell transplantation (allo-HSCT) within the last 6 months prior to the first dose of GLB-001.
* Study participants with known active involvement in central nervous system (CNS).
* Study participants with peripheral neuropathy ≥ Grade 2 (Graded according to CTCAE version 5.0).
* Study participants have a history of known malignancy other than the inclusion diagnosis for the past 5 years, with the exception of curatively resected cancer in situ, including cervical carcinoma in situ, basal cell carcinoma of the skin, or prostate cancer in situ, etc.
* QT interval interval \> 450 milliseconds (ms) using electrocardiographic (ECG) at screening.
* Study participants have impaired cardiac function or clinically significant cardiac disease at current or within last 6 months.
* Study participants with known active infection of hepatitis B virus (HBV) or hepatitis C virus C (HCV).
* Study participants with known human immunodeficiency virus (HIV) infection.
* Study participants with known life-threatening or clinical significant uncontrolled active systemic infections unrelated to malignant hematologic diseases.
* Study participants with a state condition that may alter affects the absorption, distribution, metabolism and excretion of GLB-001 after judgment of the investigator.
* Medications or supplements that are known to be strong and moderate inhibitors or inducers of cytochrome P-450 isozyme 3A (CYP3A) and/or P-glycoprotein (P-gp), or strong inhibitors or inducers of CYP450 isozyme 2C8 (CYP2C8) within 7 days or 5 half-lives prior to the first dose of GLB-001, whichever is shorter prior to the first dose of GLB-001.
* Study participants who have undergone major surgery within 28 days prior to the first dose of the GLB-001, or unability to recover from effects of surgery.
* Pregnant or lactating women.
* Study participants who have cognitive impairment due to any psychiatric or neurological condition, including epilepsy and dementia, may limit their understanding, performance, and study compliance with the ICF.
* Study participants, in the opinion of the Investigator, who are unsuitable to participate in the study.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Hangzhou GluBio Pharmaceutical Co., Ltd.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Gang Lu, Ph.D.

Role: STUDY_DIRECTOR

Hangzhou GluBio Pharmaceutical Co., Ltd.

Locations

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The First Affiliated Hospital of University of Science and Technology of China (Anhui Provincial Hospital)

Hefei, Anhui, China

Site Status RECRUITING

China-Japan Friendship Hospital

Beijing, Beijing Municipality, China

Site Status RECRUITING

The First Affiliated Hospital of Chongqing Medical University

Chongqing, Chongqing Municipality, China

Site Status RECRUITING

The First Hospital of Hebei Medical Universtiy

Shijiazhuang, Hebei, China

Site Status RECRUITING

Henan Cancer Hospital

Zhengzhou, Henan, China

Site Status RECRUITING

Zhongnan Hospital of Wuhan University

Wuhan, Hubei, China

Site Status RECRUITING

The First Affiliated Hospital of Soochow University

Suzhou, Jiangsu, China

Site Status RECRUITING

The First Affiliated Hospital of Nanchang University

Nanchang, Jiangxi, China

Site Status RECRUITING

Sheng Jing Hospital of China Medical Universtiy

Shenyang, Liaoning, China

Site Status RECRUITING

Huashan Hospital Affiliated to Fudan University

Shanghai, Shanghai Municipality, China

Site Status RECRUITING

Institute of Hematology and Blood Diseases Hospital, Chinese Academy of Medical Sciences

Tianjin, Tianjin Municipality, China

Site Status RECRUITING

The Second Hospital of Tianjin Medical Universtiy

Tianjin, Tianjin Municipality, China

Site Status RECRUITING

The First Affilicated Hospital, Zhejiang University School of Medicine

Hangzhou, Zhejiang, China

Site Status RECRUITING

The First Affiliated Hospital of Wenzhou Medical University

Wenzhou, Zhejiang, China

Site Status RECRUITING

Countries

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China

Central Contacts

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Jing Liu, Ph.D.

Role: CONTACT

86-18616699599

Facility Contacts

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Xiaoyu Zhu, MD

Role: primary

86-0551-62283160

Zhenling Li, MD

Role: primary

86-010-84205566

Li Wang, MD

Role: primary

86-023-68811360

Qingchi Liu, MD

Role: primary

86-0311-85917000

Hu Zhou, MD

Role: primary

86-0371-65587320

Xuelan Zuo, MD

Role: primary

86-027-67812888

Miao Miao, MD

Role: primary

86-0512-65223637

Fei Li, MD

Role: primary

86-0791-88603000

Wei Yang, MD

Role: primary

86-024-96615

Wei Wang, MD

Role: primary

86-021-52889999

Lei Zhang, MD

Role: primary

86-022-23909240

Jie Bai, MD

Role: primary

86-022-88328832

Hongyan Tong, MD

Role: primary

86-0571-87236114

Songfu Jiang, MD

Role: primary

86-0577-55578532

Other Identifiers

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GLB-001-02

Identifier Type: -

Identifier Source: org_study_id

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