Study of Milademetan in Japanese Patients With Relapsed or Refractory Acute Myeloid Leukemia (AML)

NCT ID: NCT03671564

Last Updated: 2023-11-07

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

View full results

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE1

Total Enrollment

14 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-08-23

Study Completion Date

2019-09-11

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

This is a Phase 1, multicenter, open-label study to evaluate safety, tolerability and pharmacokinetics of milademetan in Japanese patients with relapsed or refractory acute myeloid leukemia. The milademetan initial dose will be Level 1: 90 mg. No increase in the milademetan dose will be made in the same participant. Dose-limiting toxicity associated with milademetan occurring at each level will be assessed, and the maximum tolerated dose (MTD) will be decided using a modified continuous reassessment method (mCRM).

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Acute Myeloid Leukemia

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

NON_RANDOMIZED

Intervention Model

SEQUENTIAL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Milademetan (90 mg/Day)

Participants who received milademetan 90 mg daily (QD) Day 1 - 14 followed by 14-day rest in a 28-day cycle.

Group Type EXPERIMENTAL

Milademetan

Intervention Type DRUG

Milademetan was administered orally once daily on Days 1 to 14 in a 28-day cycle.

Milademetan (120 mg/Day)

Participants who received milademetan 120 mg daily (QD) Day 1 - 14 followed by 14-day rest in a 28-day cycle.

Group Type EXPERIMENTAL

Milademetan

Intervention Type DRUG

Milademetan was administered orally once daily on Days 1 to 14 in a 28-day cycle.

Milademetan (160 mg/Day)

Participants who received milademetan 160 mg daily (QD) Day 1 - 14 followed by 14-day rest in a 28-day cycle.

Group Type EXPERIMENTAL

Milademetan

Intervention Type DRUG

Milademetan was administered orally once daily on Days 1 to 14 in a 28-day cycle.

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Milademetan

Milademetan was administered orally once daily on Days 1 to 14 in a 28-day cycle.

Intervention Type DRUG

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

DS-3032b

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Relapsed or refractory AML
* AML for which no standard treatment is available
* Eastern Cooperative Oncology Group (ECOG) Performance Status (PS) of 0 to 2

Exclusion Criteria

* Acute Promyelocytic Leukemia
* Chronic myelogenous leukemia in blast crisis (BCR-ABL fusion gene positive)
* Presence of central nervous system involvement of leukemia or a history of primary central nervous system leukemia
Minimum Eligible Age

20 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Daiichi Sankyo Co., Ltd.

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Clinical Study Leader

Role: STUDY_DIRECTOR

Daiichi Sankyo

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Japanese Red Cross Narita Hospital

Chiba, , Japan

Site Status

Kyusyu University Hospital

Fukuoka, , Japan

Site Status

Gifu Municipal Hospital

Gifu, , Japan

Site Status

Chugoku Central Hospital

Hiroshima, , Japan

Site Status

National Hospital Organization Kumamoto Medical Center

Kumamoto, , Japan

Site Status

Tenri Hospital

Nara, , Japan

Site Status

NTT Medical Center Tokyo

Tokyo, , Japan

Site Status

National Hospital Organization Disaster Medical Center

Tokyo, , Japan

Site Status

Countries

Review the countries where the study has at least one active or historical site.

Japan

Provided Documents

Download supplemental materials such as informed consent forms, study protocols, or participant manuals.

Document Type: Study Protocol and Statistical Analysis Plan

View Document

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

184054

Identifier Type: REGISTRY

Identifier Source: secondary_id

DS3032-A-J104

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.

MB-dNPM1-TCR.1 in Relapsed/Refractory AML
NCT06424340 RECRUITING PHASE1/PHASE2