Study of FF-10101-01 in Patients With Relapsed or Refractory Acute Myeloid Leukemia

NCT ID: NCT03194685

Last Updated: 2024-12-24

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1

Total Enrollment

97 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-05-05

Study Completion Date

2021-07-31

Brief Summary

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A Phase 1 dose escalation and dose ranging study of FF-10101-01 in subjects with relapsed or refractory acute myeloid leukemia to determine the safety, tolerability, PK and preliminary efficacy. A total of 9 cohorts will be enrolled in Phase 1 to establish the Maximum Tolerated Dose (MTD).

Detailed Description

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Subjects will receive FF-10101-01 orally once a day repeated every 28 days =1 cycle Frequent blood draws will be collected to measure pharmacodynamic parameters and pharmacodynamic activity.

Disease assessments, including bone marrow aspirates, will be performed at the beginning of cycles 1-3, and every 3 months thereafter. Subjects who demonstrate objective response or stable disease will be allowed to continue therapy with FF-10101-01 until , observation of unacceptable adverse events, or until the subject is no longer deriving benefit based on the opinion of the investigator.

Conditions

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AML, Adult

Keywords

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Acute Myeloid Leukemia

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SEQUENTIAL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Open Label

Study Groups

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Cohort 1: 10 mg

Orally once a day (QD) on Days 1-28 of a 28-day cycle. Drug: FF-10101-01

Group Type EXPERIMENTAL

FF-10101-01

Intervention Type DRUG

FF-10101-01 will be administered orally once a day on Days 1-28 of a 28-day cycle. In Phase 1, the dose escalation will proceed until MTD is reached.

Cohort 2: 20 mg

Orally once a day (QD) on Days 1-28 of a 28-day cycle. Drug: FF-10101-01

Group Type EXPERIMENTAL

FF-10101-01

Intervention Type DRUG

FF-10101-01 will be administered orally once a day on Days 1-28 of a 28-day cycle. In Phase 1, the dose escalation will proceed until MTD is reached.

Cohort 3: 35 mg

Orally once a day (QD) on Days 1-28 of a 28-day cycle. Drug: FF-10101-01

Group Type EXPERIMENTAL

FF-10101-01

Intervention Type DRUG

FF-10101-01 will be administered orally once a day on Days 1-28 of a 28-day cycle. In Phase 1, the dose escalation will proceed until MTD is reached.

Cohort 4: 50 mg

Orally once a day (QD) on Days 1-28 of a 28-day cycle. Drug: FF-10101-01

Group Type EXPERIMENTAL

FF-10101-01

Intervention Type DRUG

FF-10101-01 will be administered orally once a day on Days 1-28 of a 28-day cycle. In Phase 1, the dose escalation will proceed until MTD is reached.

Cohort 5: 75 mg

Orally once a day (QD) on Days 1-28 of a 28-day cycle. Drug: FF-10101-01

Group Type EXPERIMENTAL

FF-10101-01

Intervention Type DRUG

FF-10101-01 will be administered orally once a day on Days 1-28 of a 28-day cycle. In Phase 1, the dose escalation will proceed until MTD is reached.

Cohort 6: 100 mg

Orally once a day (QD) on Days 1-28 of a 28-day cycle. Drug: FF-10101-01

Group Type EXPERIMENTAL

FF-10101-01

Intervention Type DRUG

FF-10101-01 will be administered orally once a day on Days 1-28 of a 28-day cycle. In Phase 1, the dose escalation will proceed until MTD is reached.

Cohort 7: 150 mg

Orally once a day (QD) on Days 1-28 of a 28-day cycle. Drug: FF-10101-01

Group Type EXPERIMENTAL

FF-10101-01

Intervention Type DRUG

FF-10101-01 will be administered orally once a day on Days 1-28 of a 28-day cycle. In Phase 1, the dose escalation will proceed until MTD is reached.

Cohort 8: 225 mg

Orally once a day (QD) on Days 1-28 of a 28-day cycle. Drug: FF-10101-01

Group Type EXPERIMENTAL

FF-10101-01

Intervention Type DRUG

FF-10101-01 will be administered orally once a day on Days 1-28 of a 28-day cycle. In Phase 1, the dose escalation will proceed until MTD is reached.

Interventions

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FF-10101-01

FF-10101-01 will be administered orally once a day on Days 1-28 of a 28-day cycle. In Phase 1, the dose escalation will proceed until MTD is reached.

Intervention Type DRUG

Other Intervention Names

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FF-10101 succinate

Eligibility Criteria

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Exclusion Criteria

* Subjects diagnosed with acute promyelocytic leukemia
* Subjects with Bcr-Abl positive leukemia (chronic myelogenous leukemia in blast crisis)
* Subjects with clinically active CNS leukemia
* Subjects with major surgery within 28 days prior to the first administration of FF-10101-01
* Subjects with radiation therapy within 28 days prior to the first administration of FF-10101-01
* Subjects with active malignant disease requiring therapy other than AML or myelodysplastic syndrome with transformation into AML
* Subjects with an active uncontrolled infection
* Subjects with a medical condition, serious intercurrent illness, or other circumstance that, in the Investigator's judgment, could jeopardize the subject's safety as a study subject, or that could interfere with the study objectives
* Subjects known to have human immunodeficiency virus infection, or who have active hepatitis B or C infection as determined by serological testing
* Subjects with congestive heart failure, New York Heart Association (NYHA) Class 3 or 4, or subjects with a past history of congestive heart failure NYHA Class 3 or 4 and in whom echocardiogram or multiple gate acquisition (MUGA) scan performed within 3 months prior to screening or at screening showed a LVEF \<40%
* Female subjects who are pregnant or breast feeding
* Subjects on 3-hydroxy-3-methylglutaryl-coenzyme A reductase inhibitors (statins) or other drugs known to have muscle toxicity
* Subjects taking strong inhibitors of CYP3A4 will be excluded from the study unless therapeutic substitution is possible
* Subjects taking strong inducers of CYP3A4 will be excluded from the study unless therapeutic substitution is possible
* Use of systemic immunosuppressive agents within 14 days prior to first dose of FF-10101
* Subjects taking drugs known to cause Torsades de Pointes will be excluded from the study unless therapeutic substitution is possible
* Subjects known to have long QT syndrome
* Subjects with mean QTcF values following 3 ECGs conducted 5 minutes apart of \>470 msec
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Fujifilm Pharmaceuticals U.S.A., Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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University of California Los Angeles, David Geffen School of Medicine

Los Angeles, California, United States

Site Status

University Of California, San Francisco School of Medicine

San Francisco, California, United States

Site Status

Northwestern University

Chicago, Illinois, United States

Site Status

Johns Hopkins Hospital - Sidney Kimmel Cancer Center

Baltimore, Maryland, United States

Site Status

Massachusetts General Hospital Cancer Center

Boston, Massachusetts, United States

Site Status

Roswell Park Comprehensive Cancer Center

Buffalo, New York, United States

Site Status

University of Pennsylvania

Philadelphia, Pennsylvania, United States

Site Status

Countries

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United States

References

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Levis M, Perl A, Schiller G, Fathi AT, Roboz G, Wang ES, Altman J, Rajkhowa T, Ando M, Suzuki T, Subach RA, Maier G, Madden T, Johansen M, Cheung K, Kurman M, Smith C. A phase 1 study of the irreversible FLT3 inhibitor FF-10101 in relapsed or refractory acute myeloid leukemia. Blood Adv. 2024 May 28;8(10):2527-2535. doi: 10.1182/bloodadvances.2023010619.

Reference Type DERIVED
PMID: 38502195 (View on PubMed)

Other Identifiers

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FF-10101-US101

Identifier Type: -

Identifier Source: org_study_id