Phase 2B Efficacy/Safety of Ornithine Phenylacetate in Hospitalized Cirrhotic Patients With Hepatic Encephalopathy (STOP-HE)

NCT ID: NCT01966419

Last Updated: 2021-09-16

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

231 participants

Study Classification

INTERVENTIONAL

Study Start Date

2014-01-07

Study Completion Date

2016-12-29

Brief Summary

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The purpose of this study is to determine whether ornithine phenylacetate can speed recovery from an acute hepatic encephalopathy episode requiring hospitalization in cirrhotic patients.

Detailed Description

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The primary objectives of the study were to evaluate the efficacy of OCR-002 for treatment of an acute hepatic encephalopathy (HE) episode in cirrhotic patients requiring hospitalization and the safety and tolerability of OCR-002 in hospitalized cirrhotic patients with an acute episode of HE.

Conditions

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Acute Episode of Overt Hepatic Encephalopathy Hepatic Encephalopathy

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators
While the study was double-blind (participant and investigator blinded), the care provider and outcomes assessor were also blinded.

Study Groups

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Ornithine phenylacetate

Participants receive ornithine phenylacetate for up to 5 days via continuous IV infusion in addition to standard of care (SOC)

Group Type ACTIVE_COMPARATOR

ornithine phenylacetate

Intervention Type DRUG

Ornithine phenylacetate for continuous IV infusion at dose levels predicated on level of hepatic decompensation

Placebo

Participants receive matching placebo up to 5 days via continuous IV infusion in addition to SOC

Group Type PLACEBO_COMPARATOR

placebo intravenous infusion

Intervention Type DRUG

Placebo for continuous IV infusion that is visually identical to the experimental product

Interventions

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ornithine phenylacetate

Ornithine phenylacetate for continuous IV infusion at dose levels predicated on level of hepatic decompensation

Intervention Type DRUG

placebo intravenous infusion

Placebo for continuous IV infusion that is visually identical to the experimental product

Intervention Type DRUG

Other Intervention Names

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OCR-002 Matching Placebo

Eligibility Criteria

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Inclusion Criteria

* Hospitalized with an acute episode of hepatic encephalopathy as complication of cirrhosis
* Elevated venous ammonia

Exclusion Criteria

* Renal failure with serum creatinine \> 3 mg/dL or need for dialysis
* Molecular Adsorbent Recirculation System utilized
* Pregnancy or breastfeeding
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Ocera Therapeutics, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Team Leader

Role: STUDY_CHAIR

Ocera Therapeutics, Inc.

Locations

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Phoenix, Arizona, United States

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Phoenix, Arizona, United States

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Little Rock, Arkansas, United States

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Coronado, California, United States

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Los Angeles, California, United States

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Los Angeles, California, United States

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San Francisco, California, United States

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San Francisco, California, United States

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New Haven, Connecticut, United States

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Miami, Florida, United States

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Atlanta, Georgia, United States

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Atlanta, Georgia, United States

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Chicago, Illinois, United States

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Chicago, Illinois, United States

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Chicago, Illinois, United States

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Glenview, Illinois, United States

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Iowa City, Iowa, United States

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Iowa City, Iowa, United States

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New Orleans, Louisiana, United States

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New Orleans, Louisiana, United States

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Baltimore, Maryland, United States

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Baltimore, Maryland, United States

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Bethesda, Maryland, United States

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Boston, Massachusetts, United States

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Boston, Massachusetts, United States

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Minneapolis, Minnesota, United States

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Jackson, Mississippi, United States

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Columbia, Missouri, United States

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Newark, New Jersey, United States

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Buffalo, New York, United States

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New York, New York, United States

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New York, New York, United States

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Chapel Hill, North Carolina, United States

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Columbus, Ohio, United States

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Philadelphia, Pennsylvania, United States

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Philadelphia, Pennsylvania, United States

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Philadelphia, Pennsylvania, United States

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Pittsburgh, Pennsylvania, United States

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Charleston, South Carolina, United States

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Nashville, Tennessee, United States

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Dallas, Texas, United States

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Dallas, Texas, United States

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Dallas, Texas, United States

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Dallas, Texas, United States

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Houston, Texas, United States

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Richmond, Virginia, United States

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Seattle, Washington, United States

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Seattle, Washington, United States

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Milwaukee, Wisconsin, United States

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Kingswood, New South Wales, Australia

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Adelaide, South Australia, Australia

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Bedford Park, South Australia, Australia

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Melbourne, Victoria, Australia

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Melbourne, , Australia

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Parkville, , Australia

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Graz, , Austria

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Vienna, , Austria

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Vienna, , Austria

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Brussels, , Belgium

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Brussels, , Belgium

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Brussels, , Belgium

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Ghent, , Belgium

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Leuven, , Belgium

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Brno, , Czechia

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Prague, , Czechia

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Ústí nad Labem, , Czechia

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Aarhus, , Denmark

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Copenhagen, , Denmark

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Esbjerg, , Denmark

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Hvidovre, , Denmark

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Tartu, , Estonia

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Bordeaux, , France

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Grenoble, , France

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La Roche, , France

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Lille, , France

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Lyon, , France

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Nice, , France

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Paris, , France

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Pessac, , France

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Toulouse, , France

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Villejuif, , France

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Hanover, Niedersachesen, Germany

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Bonn, , Germany

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Freiburg im Breisgau, , Germany

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Halle, , Germany

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Hamburg, , Germany

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Heidelberg, , Germany

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Leipzig, , Germany

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Mainz, , Germany

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Debrecen, , Hungary

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Gyula, , Hungary

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Kaposvár, , Hungary

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Pécs, , Hungary

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Haifa, , Israel

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Haifa, , Israel

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Jerusalem, , Israel

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Petah Tikva, , Israel

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Ramat Gan, , Israel

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Safed, , Israel

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Tel Aviv, , Israel

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Bergamo, , Italy

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Bologna, , Italy

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Florence, , Italy

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Milan, , Italy

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Palermo, , Italy

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Roma, , Italy

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Rozzano, , Italy

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San Giovanni Rotondo, , Italy

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Leiden, , Netherlands

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Maastricht, , Netherlands

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Auckland, , New Zealand

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Moscow, , Russia

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Moscow, , Russia

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Moscow, , Russia

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Moscow, , Russia

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Samara, , Russia

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A Coruña, , Spain

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Barcelona, , Spain

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Barcelona, , Spain

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Barcelona, , Spain

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Girona, , Spain

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Madrid, , Spain

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Madrid, , Spain

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Madrid, , Spain

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Málaga, , Spain

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Pontevedra, , Spain

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Santander, , Spain

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Seville, , Spain

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Valencia, , Spain

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Countries

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United States Australia Austria Belgium Bulgaria Czechia Denmark Estonia France Germany Hungary Israel Italy Netherlands New Zealand Russia Spain

References

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Safadi R, Rahimi RS, Thabut D, Bajaj JS, Ram Bhamidimarri K, Pyrsopoulos N, Potthoff A, Bukofzer S, Wang L, Jamil K, Devarakonda KR. Pharmacokinetics/pharmacodynamics of L-ornithine phenylacetate in overt hepatic encephalopathy and the effect of plasma ammonia concentration reduction on clinical outcomes. Clin Transl Sci. 2022 Jun;15(6):1449-1459. doi: 10.1111/cts.13257. Epub 2022 Mar 3.

Reference Type DERIVED
PMID: 35238476 (View on PubMed)

Wang X, Vilchez RA. Population Pharmacokinetic Analysis to Assist Dose Selection of the L-Ornithine Salt of Phenylacetic Acid. Clin Pharmacokinet. 2022 Apr;61(4):515-526. doi: 10.1007/s40262-021-01075-1. Epub 2021 Nov 17.

Reference Type DERIVED
PMID: 34786649 (View on PubMed)

Rahimi RS, Safadi R, Thabut D, Bhamidimarri KR, Pyrsopoulos N, Potthoff A, Bukofzer S, Bajaj JS. Efficacy and Safety of Ornithine Phenylacetate for Treating Overt Hepatic Encephalopathy in a Randomized Trial. Clin Gastroenterol Hepatol. 2021 Dec;19(12):2626-2635.e7. doi: 10.1016/j.cgh.2020.10.019. Epub 2020 Oct 16.

Reference Type DERIVED
PMID: 33069881 (View on PubMed)

Other Identifiers

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2013-005412-10

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

OCR002-HE209

Identifier Type: -

Identifier Source: org_study_id

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