Study of Efficacy and Safety of LEE011 in Postmenopausal Women With Advanced Breast Cancer

NCT ID: NCT01958021

Last Updated: 2025-03-07

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

668 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-12-17

Study Completion Date

2023-03-16

Brief Summary

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The primary purpose of this study was to assess the efficacy of ribociclib, as measured by progression free survival (PFS), in postmenopausal women with hormone receptor positive (HR+), human epidermal growth factor receptor 2 negative (HER2-) advanced breast cancer who received no prior treatment for advanced disease.

Detailed Description

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This was an international, multi-center, randomized, double-blinded, placebo controlled Phase III trial to determine the efficacy and safety of treatment with ribociclib plus letrozole versus placebo plus letrozole in postmenopausal women with HR+, HER2-negative advanced breast cancer who received no prior therapy for advanced disease.

Eligible patients were randomized in 1:1 ratio to either ribociclib group or placebo group. Study treatment continued until disease progression, unacceptable toxicity, death, or discontinuation from the study treatment for any other reason.

Participants who discontinued treatment due to reasons other than disease progression or withdrawal of consent for efficacy follow-up continued to be monitored until disease progression, death, withdrawal of consent, loss to follow-up, or subject/guardian decision (post-treatment efficacy follow-up).

All participants who discontinued treatment were followed for survival until the predetermined number of overall survival (OS) events was reached.

Following the final OS analysis (performed when approximately 400 deaths were recorded) and with protocol amendment 10 (dated 30-Apr-2021), participants and investigators were unblinded and those participants in the placebo arm had the opportunity to cross-over to the ribociclib arm to receive ribociclib plus letrozole. Cross-over was optional and was conducted at the investigator's discretion and upon participant consent.

Conditions

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Advanced, Metastatic Breast Cancer

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Ribociclib+ letrozole

Ribociclib 600 mg daily oral (3 weeks on/ 1 week off) in combination with letrozole 2.5 mg daily oral

Group Type EXPERIMENTAL

Ribociclib

Intervention Type DRUG

Ribociclib (600 mg, in three 200 mg hard gelatin capsules or tablets) was administered orally once daily on Days 1-21 of each 28-day cycle.

Letrozole

Intervention Type DRUG

Letrozole (2.5 mg, tablets) was administered orally once daily on a continuous daily schedule (days 1-28 of each 28-day cycle)

Placebo + letrozole

Placebo daily oral (3 weeks on/ 1 week off) in combination with letrozole 2.5 mg daily oral.

Participants were unblinded once the final OS analysis was completed and after the implementation of protocol amendment 10 (30-Apr-21) and were given the option to crossover to treatment with ribociclib + letrozole

Group Type PLACEBO_COMPARATOR

Letrozole

Intervention Type DRUG

Letrozole (2.5 mg, tablets) was administered orally once daily on a continuous daily schedule (days 1-28 of each 28-day cycle)

Placebo

Intervention Type DRUG

Placebo (hard gelatin capsules or tablets) was administered orally once daily on Days 1-21 of each 28-day cycle.

Interventions

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Ribociclib

Ribociclib (600 mg, in three 200 mg hard gelatin capsules or tablets) was administered orally once daily on Days 1-21 of each 28-day cycle.

Intervention Type DRUG

Letrozole

Letrozole (2.5 mg, tablets) was administered orally once daily on a continuous daily schedule (days 1-28 of each 28-day cycle)

Intervention Type DRUG

Placebo

Placebo (hard gelatin capsules or tablets) was administered orally once daily on Days 1-21 of each 28-day cycle.

Intervention Type DRUG

Other Intervention Names

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LEE011

Eligibility Criteria

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Inclusion Criteria

1. Women with advanced (locoregionally recurrent or metastatic) breast cancer that was not amenable to curative therapy.
2. The patient was postmenopausal. Postmenopausal status was defined either by:

* Prior bilateral oophorectomy
* Age ≥60
* Age \<60 and amenorrhea for 12 or more months (in the absence of chemotherapy, tamoxifen, toremifen, or ovarian suppression) and FSH and estradiol in the postmenopausal range per local normal range.
3. There was no prior systemic anti-cancer therapy for advanced disease.
4. The patient had a histologically and/or cytologically confirmed diagnosis of estrogen-receptor positive and/or progesterone receptor positive breast cancer by the local laboratory.
5. The patient had HER2-negative breast cancer defined as a negative in situ hybridization test or an IHC status of 0, 1+ or 2+. If IHC was 2+, a negative in situ hybridization (FISH, CISH, or SISH) test was required by local laboratory testing.
6. The patient must have had either:

Measurable disease, i.e., at least one measurable lesion as per RECIST 1.1 criteria (Tumor lesions previously irradiated or subjected to other locoregional therapy were considered measurable if disease progression at the treated site after completion of therapy was clearly documented). OR If no measurable disease was present, then at least one predominantly lytic bone lesion must have been present (Patients with no measurable disease and only one predominantly lytic bone lesion previously irradiated were eligible if there was documented evidence of disease progression of the bone lesion after irradiation).
7. The patient had an Eastern Cooperative Oncology Group (ECOG) performance status of 0 or 1.

Exclusion Criteria

1. The patient had received any CDK4/6 inhibitor.
2. The patient had received any prior systemic anti-cancer therapy (including hormonal therapy and chemotherapy) for advanced breast cancer.

Note:
* Patients who had received (neo) adjuvant therapy for breast cancer were eligible. If the prior neo (adjuvant) therapy included letrozole or anastrozole, the disease-free interval had to be greater than 12 months from the completion of treatment until randomization.
* Patients who had received ≤ 14 days of letrozole or anastrozole for advanced disease prior to randomization were eligible.
* Any prior (neo) adjuvant anti-cancer therapy had to be stopped at least 5 half-lives or 7 days, whichever was longer, before randomization.
3. The patient was concurrently using other anti-cancer therapy.
4. The patient had a concurrent malignancy or malignancy within 3 years of randomization, with the exception of adequately treated, basal or squamous cell carcinoma, non-melanomatous skin cancer, or curatively resected cervical cancer.
5. The patient had active cardiac disease or a history of cardiac dysfunction, including any of the following:

* History of angina pectoris, symptomatic pericarditis, or myocardial infarction within 12 months prior to study entry.
* History of documented congestive heart failure (New York Heart Association functional classification III-IV).
* Documented cardiomyopathy.
* The patient had a Left Ventricular Ejection Fraction (LVEF) \< 50% as determined by Multiple Gated acquisition (MUGA) scan or echocardiogram (ECHO).
* History of any cardiac arrhythmias, e.g., ventricular, supraventricular, nodal arrhythmias, or conduction abnormality in the previous 12 months.
* On screening, any of the following cardiac parameters: bradycardia (heart rate \< 50 at rest), tachycardia (heart rate \> 90 at rest), PR interval \> 220 msec, QRS interval \>109 msec, or QTcF \>450 msec.
* Systolic blood pressure \>160 or \<90 mmHg.
6. The patient was currently receiving any of the following medications and could not be discontinued 7 days prior to the start of treatment:

* Medications known to be strong inducers or inhibitors of CYP3A4.
* Medications known to have a risk of prolonging the QT interval or inducing Torsades de Pointes.
* Medications with a narrow therapeutic window and predominantly metabolized through CYP3A4.
* Herbal preparations/medications.
Minimum Eligible Age

18 Years

Maximum Eligible Age

100 Years

Eligible Sex

FEMALE

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Novartis Pharmaceuticals

Role: STUDY_DIRECTOR

Novartis Pharmaceuticals

Locations

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Ironwood Cancer and Research Centers

Chandler, Arizona, United States

Site Status

Arizona Oncology Associates PC HAL

Sedona, Arizona, United States

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Highlands Oncology Group

Fayetteville, Arkansas, United States

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NEA Baptist Cancer Center

Jonesboro, Arkansas, United States

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Alta Bates Cancer Center

Berkeley, California, United States

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City of Hope National Medical Center

Duarte, California, United States

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Glendale Adventist Medical Center

Glendale, California, United States

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The Angeles Clinic and Research Institute

Los Angeles, California, United States

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Cedars Sinai Medical Center SC-5

Los Angeles, California, United States

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Comprehensive Cancer Center

Sacramento, California, United States

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Univ of Colorado School of Medicine

Aurora, Colorado, United States

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Rocky Mountain Cancer Centers

Longmont, Colorado, United States

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University Cancer Institute

Boynton Beach, Florida, United States

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Florida Cancer Research Institute

Davie, Florida, United States

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Florida Cancer Specialists

Fort Myers, Florida, United States

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Memorial Hospital

Hollywood, Florida, United States

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University Of Miami

Miami, Florida, United States

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Florida Retina Institute

Orlando, Florida, United States

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Sacred Heart Medical Oncology

Pensacola, Florida, United States

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Florida Cancer Specialists-North

St. Petersburg, Florida, United States

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Georgia Cancer Specialists

Decatur, Georgia, United States

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Lewis Hall Singletary Onc Ctr at John D. Archbold Mem Hosp.

Thomasville, Georgia, United States

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Moanalua Medical Center Attn Oncology Dept

Honolulu, Hawaii, United States

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University of Illinois Cancer Center at Chicago

Chicago, Illinois, United States

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University of Chicago

Chicago, Illinois, United States

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NorthShore University Health System

Evanston, Illinois, United States

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Ingalls Memorial Hospital

Harvey, Illinois, United States

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Edward Hospital

Naperville, Illinois, United States

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IU Simon Cancer Center

Indianapolis, Indiana, United States

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Sidney Kimmel CCC At JH

Baltimore, Maryland, United States

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Frederick Memorial Hospital

Frederick, Maryland, United States

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Dana Farber Cancer Institute

Boston, Massachusetts, United States

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Allina Hlth Cancer Inst Minneapolis

Minneapolis, Minnesota, United States

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Jackson Oncology Associates

Jackson, Mississippi, United States

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St Lukes Hos Marion Bloch Neur Inst

Kansas City, Missouri, United States

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Mercy Medical Research Institute

Manchester, Missouri, United States

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Foundation Medical Partners

Nashua, New Hampshire, United States

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Cooper Cancer Center

Camden, New Jersey, United States

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Hackensack Meridian Health

Edison, New Jersey, United States

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Cancer Institute of New Jersey

New Brunswick, New Jersey, United States

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C R Wood Cancer Center at Glens Falls Hospital

Glens Falls, New York, United States

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Winthrop University Hospital

Mineola, New York, United States

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NYU Langone Med Center CV Research

New York, New York, United States

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Mount Sinai School Of Medicine

New York, New York, United States

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Montefiore Medical Center

The Bronx, New York, United States

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Duke Univ Medical Center

Durham, North Carolina, United States

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Oncology Hematology Care Inc

Cincinnati, Ohio, United States

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The Ohio State University Comprehensive Cancer Center

Columbus, Ohio, United States

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Mercy Clinic Oklahoma Communities Mercy Oncology

Oklahoma City, Oklahoma, United States

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Lehigh Valley Hospital

Allentown, Pennsylvania, United States

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Penn State Hershey Cancer Institute

Hershey, Pennsylvania, United States

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Avera Cancer

Sioux Falls, South Dakota, United States

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Chattanooga Onc And Hem Assoc PC

Chattanooga, Tennessee, United States

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Sarah Cannon Research Institute

Nashville, Tennessee, United States

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Vanderbilt University Medical Ctr

Nashville, Tennessee, United States

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Texas Oncology P A

Bedford, Texas, United States

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Texas Oncology

Dallas, Texas, United States

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University of Texas Southwestern Medical Center

Dallas, Texas, United States

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Ctr For Cancer And Blood Disorders

Fort Worth, Texas, United States

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Texas Oncology P A

Fort Worth, Texas, United States

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Texas Oncology Houston Memorial City

Houston, Texas, United States

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Uni Of TX MD Anderson Cancer Cntr

Houston, Texas, United States

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Millennium Research Clin Develop

Houston, Texas, United States

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Texas Oncology

McAllen, Texas, United States

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Richardson Hematology Oncology Associates

Richardson, Texas, United States

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Texas Oncology P A

San Antonio, Texas, United States

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Texas Oncology Northeast Texas

Tyler, Texas, United States

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Utah Cancer Specialists

Salt Lake City, Utah, United States

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Virginia Cancer Specialists

Fairfax, Virginia, United States

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Oncology and Hematology Associates of Southwest Virginia Inc

Salem, Virginia, United States

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Providence Regional Cancer Partnership

Everett, Washington, United States

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Northwest Medical Specialties

Tacoma, Washington, United States

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Dean Health System

Madison, Wisconsin, United States

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Novartis Investigative Site

San Miguel de Tucumán, Tucumán Province, Argentina

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Córdoba, , Argentina

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La Rioja, , Argentina

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Kurralta Park, South Australia, Australia

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East Melbourne, Victoria, Australia

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Nedlands, Western Australia, Australia

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Salzburg, , Austria

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Vienna, , Austria

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Vienna, , Austria

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Sint-Niklaas, Oost Vlaanderen, Belgium

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Hasselt, , Belgium

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Leuven, , Belgium

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Namur, , Belgium

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Wilrijk, , Belgium

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Ribeirão Preto, São Paulo, Brazil

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São Paulo, São Paulo, Brazil

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São Paulo, São Paulo, Brazil

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Burnaby, British Columbia, Canada

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Halifax, Nova Scotia, Canada

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Hamilton, Ontario, Canada

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Kitchener, Ontario, Canada

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Ottawa, Ontario, Canada

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Toronto, Ontario, Canada

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Montreal, Quebec, Canada

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Québec, Quebec, Canada

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Brno, Czech Republic, Czechia

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Brno Bohunice, , Czechia

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Liberec, , Czechia

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Olomouc, , Czechia

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Aarhus, , Denmark

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Copenhagen, , Denmark

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Odense C, , Denmark

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Vejle, , Denmark

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Helsinki, , Finland

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Turku, , Finland

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Nice, Alpes Maritimes, France

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Angers, , France

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Avignon, , France

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Besançon, , France

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Bordeaux, , France

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Créteil, , France

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Le Mans, , France

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Lyon, , France

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Pierre-Bénite, , France

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Rouen, , France

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Saint-Herblain, , France

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Villejuif, , France

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Bielefeld, North Rhine-Westphalia, Germany

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Aschaffenburg, , Germany

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Berlin, , Germany

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Berlin, , Germany

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Bonn, , Germany

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Bottrop, , Germany

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Düsseldorf, , Germany

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Erlangen, , Germany

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Essen, , Germany

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Freiburg im Breisgau, , Germany

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Fürth, , Germany

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Goslar, , Germany

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Heidelberg, , Germany

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München, , Germany

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Offenbach, , Germany

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Ravensburg, , Germany

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Recklinghausen, , Germany

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Tübingen, , Germany

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Ulm, , Germany

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Velbert, , Germany

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Budapest, Pest County, Hungary

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Debrecen, , Hungary

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Győr, , Hungary

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Gyula, , Hungary

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Cork, , Ireland

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Dublin, , Ireland

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Petah Tikva, , Israel

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Ramat Gan, , Israel

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Tel Aviv, , Israel

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Brescia, BS, Italy

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Genova, GE, Italy

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Lecco, LC, Italy

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Messina, ME, Italy

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Milan, MI, Italy

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Padua, PD, Italy

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Perugia, PG, Italy

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Pisa, PI, Italy

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Aviano, PN, Italy

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Reggio Calabria, RC, Italy

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Roma, RM, Italy

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Candiolo, TO, Italy

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Terni, TR, Italy

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Viterbo, VT, Italy

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Napoli, , Italy

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Beirut, , Lebanon

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Beirut, , Lebanon

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El Achrafiyé, , Lebanon

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Saida, , Lebanon

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Sittard-Geleen, BG, Netherlands

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Leiden, South Holland, Netherlands

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Alkmaar, , Netherlands

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Deventer, , Netherlands

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Groningen, , Netherlands

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Groningen, , Netherlands

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Maastricht, , Netherlands

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Tilburg, , Netherlands

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Zoetermeer, , Netherlands

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Zwolle, , Netherlands

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Bergen, , Norway

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Oslo, , Norway

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Arkhangelsk, , Russia

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Nizhny Novgorod, , Russia

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Ryazan, , Russia

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Singapore, , Singapore

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Pretoria, Gauteng, South Africa

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Bundang Gu, Gyeonggi-do, South Korea

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Gyeonggi-do, Korea, South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Málaga, Andalusia, Spain

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Seville, Andalusia, Spain

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Barcelona, Catalonia, Spain

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Barcelona, Catalonia, Spain

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L'Hospitalet de Llobregat, Catalonia, Spain

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Santiago de Compostela, Galicia, Spain

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San Cristóbal de La Laguna, Santa Cruz De Tenerife, Spain

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Valencia, Valencia, Spain

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Madrid, , Spain

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Madrid, , Spain

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Madrid, , Spain

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Madrid, , Spain

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Eskilstuna, , Sweden

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Gothenburg, , Sweden

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Jönköping, , Sweden

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Lund, , Sweden

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Uppsala, , Sweden

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Vaxjo, , Sweden

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Kaohsiung City, , Taiwan

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New Taipei City, , Taiwan

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Taipei, , Taiwan

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Taipei, , Taiwan

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Taoyuan District, , Taiwan

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Bangkok, , Thailand

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Ankara, , Turkey (Türkiye)

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Ankara, , Turkey (Türkiye)

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Diyarbakır, , Turkey (Türkiye)

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Istanbul, , Turkey (Türkiye)

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Izmir, , Turkey (Türkiye)

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Truro, Cornwall, United Kingdom

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Newcastle upon Tyne, , United Kingdom

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Countries

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United States Argentina Australia Austria Belgium Brazil Canada Czechia Denmark Finland France Germany Hungary Ireland Israel Italy Lebanon Netherlands Norway Russia Singapore South Africa South Korea Spain Sweden Taiwan Thailand Turkey (Türkiye) United Kingdom

References

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Jhaveri K, O'Shaughnessy J, Fasching PA, Tolaney SM, Yardley DA, Sharma VK, Biswas C, Thuerigen A, Pathak P, Rugo HS. Matching-adjusted indirect comparison of PFS and OS comparing ribociclib plus letrozole versus palbociclib plus letrozole as first-line treatment of HR+/HER2- advanced breast cancer. Ther Adv Med Oncol. 2023 Dec 14;15:17588359231216095. doi: 10.1177/17588359231216095. eCollection 2023.

Reference Type DERIVED
PMID: 38107828 (View on PubMed)

Andre F, Su F, Solovieff N, Hortobagyi G, Chia S, Neven P, Bardia A, Tripathy D, Lu YS, Lteif A, Taran T, Babbar N, Slamon D, Arteaga CL. Pooled ctDNA analysis of MONALEESA phase III advanced breast cancer trials. Ann Oncol. 2023 Nov;34(11):1003-1014. doi: 10.1016/j.annonc.2023.08.011. Epub 2023 Sep 5.

Reference Type DERIVED
PMID: 37673211 (View on PubMed)

Rugo HS, Harmer V, O'Shaughnessy J, Jhaveri K, Tolaney SM, Cardoso F, Bardia A, Maheshwari VK, Tripathi S, Haftchenary S, Pathak P, Fasching PA. Quality of life with ribociclib versus abemaciclib as first-line treatment of HR+/HER2- advanced breast cancer: a matching-adjusted indirect comparison. Ther Adv Med Oncol. 2023 Feb 24;15:17588359231152843. doi: 10.1177/17588359231152843. eCollection 2023.

Reference Type DERIVED
PMID: 36861085 (View on PubMed)

Ji Y, Yartsev V, Quinlan M, Serra P, Wang Y, Chakraborty A, Miller M. Justifying Ribociclib Dose in Patients with Advanced Breast Cancer with Renal Impairment Based on PK, Safety, and Efficacy Data: An Innovative Approach Integrating Data from a Dedicated Renal Impairment Study and Oncology Clinical Trials. Clin Pharmacokinet. 2023 Mar;62(3):493-504. doi: 10.1007/s40262-022-01206-2. Epub 2023 Feb 17.

Reference Type DERIVED
PMID: 36800111 (View on PubMed)

Hortobagyi GN, Stemmer SM, Burris HA, Yap YS, Sonke GS, Hart L, Campone M, Petrakova K, Winer EP, Janni W, Conte P, Cameron DA, Andre F, Arteaga CL, Zarate JP, Chakravartty A, Taran T, Le Gac F, Serra P, O'Shaughnessy J. Overall Survival with Ribociclib plus Letrozole in Advanced Breast Cancer. N Engl J Med. 2022 Mar 10;386(10):942-950. doi: 10.1056/NEJMoa2114663.

Reference Type DERIVED
PMID: 35263519 (View on PubMed)

Burris HA, Chan A, Bardia A, Thaddeus Beck J, Sohn J, Neven P, Tripathy D, Im SA, Chia S, Esteva FJ, Hart L, Zarate JP, Ridolfi A, Lorenc KR, Yardley DA. Safety and impact of dose reductions on efficacy in the randomised MONALEESA-2, -3 and -7 trials in hormone receptor-positive, HER2-negative advanced breast cancer. Br J Cancer. 2021 Aug;125(5):679-686. doi: 10.1038/s41416-021-01415-9. Epub 2021 Jun 22.

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Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

2013-003084-61

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CLEE011A2301

Identifier Type: -

Identifier Source: org_study_id

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