Efficacy and Safety Study of Botulinum Toxin Type A Against Placebo to Treat Abnormal Contraction or Twitch of the Eyelid

NCT ID: NCT01896895

Last Updated: 2018-03-01

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

61 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-11-30

Study Completion Date

2016-11-30

Brief Summary

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This phase 3 study will serve to collect efficacy and safety data of two different doses of NT 201 in subjects suffering from Bilateral Blepharospasm (BEB) who are BTX treatment-naïve.

In this study, BTX treatment-naïve subjects are defined as those who have not received BTX treatment within the last 12 months for the treatment of BEB. This definition aims to avoid bias by comparison of treatment effects in the subject's assessments. Furthermore, this study will substantiate the existing efficacy and safety database for the indication BEB.

Detailed Description

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Subjects to receive one injection with NT 201 or placebo at baseline of the placebo-controlled first cycle. Thereafter, all subjects entering the Open-Label Extension Period (OLEX) to receive a second injection of NT 201 (second injection cycle).

Conditions

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Bilateral Blepharospasm (BEB)

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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IncobotulinumtoxinA (Xeomin) 25U per eye

Main Period: one injection session, 25 Units per eye. Open-Label Extension: one injection session, up to 35 Units per eye. Mode of administration: intramuscular injection.

Group Type EXPERIMENTAL

IncobulinumtoxinA (Xeomin), 25 Units

Intervention Type DRUG

IncobotulinumtoxinA (active ingredient: Clostridium Botulinum neurotoxin Type A free from complexing proteins) powder for solution for injection, prepared by reconstitution of powder with 0.9% Sodium Chloride (NaCl). Main Period: 25 Units per eye.

IncobotulinumtoxinA (Xeomin), 35 Units

Intervention Type DRUG

IncobotulinumtoxinA (active ingredient: Clostridium Botulinum neurotoxin Type A free from complexing proteins) powder for solution for injection, prepared by reconstitution of powder with 0.9% Sodium Chloride (NaCl).

Open-Label Extension: up to 35 Units per eye.

IncobotulinumtoxinA (Xeomin) 12.5U per eye

Main Period: one injection session, 12.5 Units per eye. Open-Label Extension Period: one injection session, up to 35 Units per eye. Mode of administration: intramuscular injection.

Group Type EXPERIMENTAL

IncobotulinumtoxinA (Xeomin), 12.5 Units

Intervention Type DRUG

IncobotulinumtoxinA (active ingredient: Clostridium Botulinum neurotoxin Type A free from complexing proteins) powder for solution for injection, prepared by reconstitution of powder with 0.9% Sodium Chloride (NaCl). Main Period: 12.5 Units per eye.

IncobotulinumtoxinA (Xeomin), 35 Units

Intervention Type DRUG

IncobotulinumtoxinA (active ingredient: Clostridium Botulinum neurotoxin Type A free from complexing proteins) powder for solution for injection, prepared by reconstitution of powder with 0.9% Sodium Chloride (NaCl).

Open-Label Extension: up to 35 Units per eye.

Placebo

Main Period: Placebo to IncobotulinumtoxinA (Xeomin)(12.5 or 25U/eye), one injection session.

Open-Label Extension: IncobotulinumtoxinA (Xeomin), one injection session, up to 35 Units per eye. Mode of administration: intramuscular injection.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Main Period: Placebo to IncobotulinumtoxinA (Xeomin), powder for solution for injection, prepared by reconstitution of powder with 0.9% Sodium Chloride (NaCl).

IncobotulinumtoxinA (Xeomin), 35 Units

Intervention Type DRUG

IncobotulinumtoxinA (active ingredient: Clostridium Botulinum neurotoxin Type A free from complexing proteins) powder for solution for injection, prepared by reconstitution of powder with 0.9% Sodium Chloride (NaCl).

Open-Label Extension: up to 35 Units per eye.

Interventions

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IncobulinumtoxinA (Xeomin), 25 Units

IncobotulinumtoxinA (active ingredient: Clostridium Botulinum neurotoxin Type A free from complexing proteins) powder for solution for injection, prepared by reconstitution of powder with 0.9% Sodium Chloride (NaCl). Main Period: 25 Units per eye.

Intervention Type DRUG

IncobotulinumtoxinA (Xeomin), 12.5 Units

IncobotulinumtoxinA (active ingredient: Clostridium Botulinum neurotoxin Type A free from complexing proteins) powder for solution for injection, prepared by reconstitution of powder with 0.9% Sodium Chloride (NaCl). Main Period: 12.5 Units per eye.

Intervention Type DRUG

Placebo

Main Period: Placebo to IncobotulinumtoxinA (Xeomin), powder for solution for injection, prepared by reconstitution of powder with 0.9% Sodium Chloride (NaCl).

Intervention Type DRUG

IncobotulinumtoxinA (Xeomin), 35 Units

IncobotulinumtoxinA (active ingredient: Clostridium Botulinum neurotoxin Type A free from complexing proteins) powder for solution for injection, prepared by reconstitution of powder with 0.9% Sodium Chloride (NaCl).

Open-Label Extension: up to 35 Units per eye.

Intervention Type DRUG

Other Intervention Names

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NT 201 Xeomin Botulinum toxin type A (150 kiloDalton), free from complexing proteins NT 201 Xeomin Botulinum toxin type A (150 kiloDalton), free from complexing proteins NT 201 Xeomin Botulinum toxin type A (150 kiloDalton), free from complexing proteins

Eligibility Criteria

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Inclusion Criteria

* Male or female out-patients age ≥ 18 and ≤ 80 years.
* A clinical diagnosis of bilateral BEB characterized by spontaneous, spasmodic, intermittent or persistent involuntary contractions of orbicular oculi muscles.
* A need for injection of BTX defined as a Jankovic Rating Scale \[JRS\] severity subscore ≥ 2.
* Treatment-naïve subject defined as at least 12 months without BTX of any serotype for the treatment of BEB before administration of IP.

Exclusion Criteria

* Subject with any previous unsuccessful treatment with BTX of any serotype for the treatment of BEB.
* Atypical variant of BEB (e.g., apraxia of the eyelid opening) caused by inhibition of levator palpebrae muscle.
* Neuroleptic-induced blepharospasm.
* Myotomy or denervation surgery in the affected muscles (e.g., peripheral denervation, spinal cord stimulation) and surgery in the upper face.
* Generalized disorders of muscles activity (e.g., myasthenia gravis in particular ocularis, Lambert-Eaton-Syndrome, amyotrophic lateral sclerosis) or any other significant neuromuscular dysfunction which might interfere with the study.
Minimum Eligible Age

18 Years

Maximum Eligible Age

80 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Merz Pharmaceuticals GmbH

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Merz Medical Expert

Role: STUDY_DIRECTOR

Merz Pharmaceuticals GmbH

Locations

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Merz Investigational Site #030002

Athens, , Greece

Site Status

Merz Investigational Site #030001

Athens, , Greece

Site Status

Merz Investigational Site #060007

George Town, Pulau Pinang, Malaysia

Site Status

Merz Investigational Site #060004

Kota Kinabalu, Sabah, Malaysia

Site Status

Merz Investigational Site #060006

Kuala Lumpur, , Malaysia

Site Status

Merz Investigational Site #060002

Kuala Lumpur, , Malaysia

Site Status

Merz Investigational Site #060003

Kuala Selangor, , Malaysia

Site Status

Merz Investigational Site #094001

Colombo, , Sri Lanka

Site Status

Merz Investigational Site #094005

Colombo, , Sri Lanka

Site Status

Merz Investigational Site #094006

Kurunegala, , Sri Lanka

Site Status

Merz Investigational Site #094002

Nugegoda, , Sri Lanka

Site Status

Countries

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Greece Malaysia Sri Lanka

References

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Mitsikostas DD, Dekundy A, Hanschmann A, Althaus M, Scheschonka A, Pagan F, Jankovic J. Duration and onset of effect of incobotulinumtoxinA for the treatment of blepharospasm in botulinum toxin-naive subjects. Curr Med Res Opin. 2021 Oct;37(10):1761-1768. doi: 10.1080/03007995.2021.1965975. Epub 2021 Aug 24.

Reference Type DERIVED
PMID: 34384301 (View on PubMed)

Duarte GS, Rodrigues FB, Marques RE, Castelao M, Ferreira J, Sampaio C, Moore AP, Costa J. Botulinum toxin type A therapy for blepharospasm. Cochrane Database Syst Rev. 2020 Nov 19;11(11):CD004900. doi: 10.1002/14651858.CD004900.pub3.

Reference Type DERIVED
PMID: 33211907 (View on PubMed)

Mitsikostas DD, Dekundy A, Sternberg K, Althaus M, Pagan F. IncobotulinumtoxinA for the Treatment of Blepharospasm in Toxin-Naive Subjects: A Multi-Center, Double-Blind, Randomized, Placebo-Controlled Trial. Adv Ther. 2020 Oct;37(10):4249-4265. doi: 10.1007/s12325-020-01427-6. Epub 2020 Aug 10.

Reference Type DERIVED
PMID: 32779096 (View on PubMed)

Other Identifiers

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2012-004821-26

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

MRZ60201_3074_1

Identifier Type: -

Identifier Source: org_study_id

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