A Study to Investigate the Efficacy and Safety of NT 201 (Botulinum Toxin) Compared With Placebo for the Treatment of Adult Participants With Essential Tremor in the Arm

NCT ID: NCT04766723

Last Updated: 2024-04-22

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

78 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-02-24

Study Completion Date

2023-11-20

Brief Summary

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The purpose of this study is to determine whether a single treatment with administration of NT 201 (botulinum toxin) is superior to placebo (no medicine) for one-sided treatment of essential tremor in the arm (Unilateral Period). Participants will be assigned to the treatment groups by chance and neither the participants nor the research staff who interact with them will know the allocation.

The following treatment cycle will investigate the safety and tolerability of two-sided treatment with NT 201 (botulinum toxin) (Open Label Bliaterial Period). All participants will receive NT 201 treatment.

Detailed Description

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Conditions

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Essential Tremor of the Upper Limb

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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NT 201 (IncobotulinumtoxinA, Xeomin)

Unilateral Treatment Period (1 treatment cycle): subjects to receive unilateral intramuscular injection of NT 201 (130-165 units) into muscles of the upper limb.

Open Label Bilateral Treatment Period (1 treatment cycle): subjects to receive bilateral intramuscular injection of NT 201 (130-165 units) into muscles of the upper limbs.

Group Type EXPERIMENTAL

NT 201

Intervention Type DRUG

Active ingredient: Clostridium Botulinum neurotoxin Type A free from complexing proteins. Solution for injection prepared by reconstitution of powder with 0.9% Sodium Chloride (NaCl).

Placebo

Unilateral Treatment Period (1 treatment cycle): subjects to receive unilateral intramuscular placebo injection into muscles of the upper limb.

Open Label Bilateral Treatment Period (1 treatment cycle): subjects to receive bilateral intramuscular injection of NT 201 (130-165 units per arm) into muscles of the upper limbs.

Group Type PLACEBO_COMPARATOR

NT 201

Intervention Type DRUG

Active ingredient: Clostridium Botulinum neurotoxin Type A free from complexing proteins. Solution for injection prepared by reconstitution of powder with 0.9% Sodium Chloride (NaCl).

Placebo

Intervention Type DRUG

Solution for injection prepared by reconstitution of powder with 0.9% Sodium Chloride (NaCl).

Interventions

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NT 201

Active ingredient: Clostridium Botulinum neurotoxin Type A free from complexing proteins. Solution for injection prepared by reconstitution of powder with 0.9% Sodium Chloride (NaCl).

Intervention Type DRUG

Placebo

Solution for injection prepared by reconstitution of powder with 0.9% Sodium Chloride (NaCl).

Intervention Type DRUG

Other Intervention Names

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Incobotulinumtoxin A IncobotulinumtoxinA Xeomin Botulinum toxin type A (150 kiloDalton), free from complexing proteins

Eligibility Criteria

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Inclusion Criteria

\- Score of ≥ 2 (at least 1 cm tremor amplitude) in at least two out of three maneuvers of test item 4 (upper limb tremor) confirmed by an independent TETRAS expert by means of video assessment.

Exclusion Criteria

* History or presence of day-to-day fluctuations in ET which would jeopardize meaningful tremor assessment over time, e.g. severe tremor on one day and minimal or no tremor on another day.
* Other neurological signs, such as dystonia, ataxia, or parkinsonism, which in the judgment of the investigator could interfere with the ET diagnosis and/or assessment of ET in ULs.
* Tremor types other than ET
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Merz Pharmaceuticals GmbH

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Merz Medical Expert

Role: STUDY_DIRECTOR

Merz Pharmaceuticals GmbH

Locations

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USF, Department of Neurology, Merz Investigational Site #0010020

Tampa, Florida, United States

Site Status

University of Nebraska Medical Center, Merz Investigational Site #0010269

Omaha, Nebraska, United States

Site Status

Cleveland Clinic Lou Ruvo Center for Brain Health, Merz Investigational Site #0010457

Las Vegas, Nevada, United States

Site Status

Mount Sinai Medical Center, Merz Investigational Site #0010191

New York, New York, United States

Site Status

Vanderbilt University Medical Center, Neuroscience Institute, Merz Investigational Site #0010206

Nashville, Tennessee, United States

Site Status

Houston Methodist Neurological Institute, Merz Investigational Site #0010226

Houston, Texas, United States

Site Status

Medstar Georgetown Neurology, Merz Investigational Site #0010231

McLean, Virginia, United States

Site Status

UW Medical Center - Montlake, Merz Investigational Site #0010450

Seattle, Washington, United States

Site Status

Selkirk Neurology, Merz Investigational Site #0010456

Spokane, Washington, United States

Site Status

London Health Sciences Centre, Merz Investigational Site #0010087

London, Ontario, Canada

Site Status

Specjalistyczne Gabinety, Merz Investigational Site #0480059

Krakow, , Poland

Site Status

NeuroKlinika Gabinet Lekarski, Merz Investigational Site #0480101

Lodz, , Poland

Site Status

Instytut Zdrowia Dr. Boczarska-Jedynak

Oświęcim, , Poland

Site Status

Mazowiecki Szpital Bródnowski, Merz Investigational Site #0480064

Warsaw, , Poland

Site Status

Countries

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United States Canada Poland

Other Identifiers

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2021-001988-24

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

M602011069

Identifier Type: -

Identifier Source: org_study_id

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