Safety and Effectiveness of Botulinum Toxin in Elderly Patients With Dementia and Muscle Stiffness

NCT ID: NCT02212119

Last Updated: 2014-08-08

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

10 participants

Study Classification

INTERVENTIONAL

Study Start Date

2010-12-31

Study Completion Date

2014-01-31

Brief Summary

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Aim of the study is to perform a pilot study to assess the impact of Botulinum toxin on muscle tone, and caregiver burden in individuals who are cognitively impaired and who are fully dependent.

The primary objective is to confirm proof of principle that paratonic rigidity and the consequences associated with it can be reduced with injection of Botulinum toxin injections resulting in reduced care-giver burden.

The secondary objectives are to determine optimal time points for evaluation of efficacy in this patient population and whether the time period is sufficient for washout of Botulinum toxin effect; determine most salient and sensitive outcome measures; identify obstacles in data gathering; and lastly, to determine feasibility of battery of assessments in this pilot study.

Detailed Description

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Conditions

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Dementia Paratonia

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

CROSSOVER

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Saline

Saline injection up to 5 cc in arm with paratonia (one time injection)

Group Type PLACEBO_COMPARATOR

Saline

Intervention Type DRUG

Botulinum Toxin

Up to 300 U (5 cc) of Botulinum toxin diluted 2:1 (2 cc per 100 U of Botulinum toxin) (one time injection)

Group Type ACTIVE_COMPARATOR

Botulinum Toxin

Intervention Type DRUG

Interventions

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Botulinum Toxin

Intervention Type DRUG

Saline

Intervention Type DRUG

Other Intervention Names

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Xeomin

Eligibility Criteria

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Inclusion Criteria

* Severe cognitive impairment (complete dependency in all activities of daily living (ADLs)
* Diagnosis of Alzheimer's disease, vascular dementia,or frontotemporal dementia
* Score\> 3 on the paratonic assessment instrument, with paratonic rigidity in an arm(s) interfering in the provision of care

Exclusion Criteria

* Alternate etiologies for increased tone
* Botulinum toxin 6 months preceding the study
Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Merz Pharmaceuticals GmbH

INDUSTRY

Sponsor Role collaborator

Baycrest

OTHER

Sponsor Role collaborator

Assistive Technology Clinic, Canada

OTHER

Sponsor Role lead

Responsible Party

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Dr. Galit Kleiner-Fisman

Medical Director, Assistive Technology Clinic, Assistant Professor Department of Medicine, University of Toronto

Responsibility Role PRINCIPAL_INVESTIGATOR

Principal Investigators

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Galit Kleiner-Fisman, MD

Role: PRINCIPAL_INVESTIGATOR

University of Toronto, Baycrest

Locations

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Assistive Technology Clinic at Baycrest

Toronto, Ontario, Canada

Site Status

Countries

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Canada

References

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Hobbelen JS, Koopmans RT, Verhey FR, Habraken KM, de Bie RA. Diagnosing paratonia in the demented elderly: reliability and validity of the Paratonia Assessment Instrument (PAI). Int Psychogeriatr. 2008 Aug;20(4):840-52. doi: 10.1017/S1041610207006424. Epub 2008 Jan 7.

Reference Type BACKGROUND
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Reference Type BACKGROUND
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Brashear A, Gordon MF, Elovic E, Kassicieh VD, Marciniak C, Do M, Lee CH, Jenkins S, Turkel C; Botox Post-Stroke Spasticity Study Group. Intramuscular injection of botulinum toxin for the treatment of wrist and finger spasticity after a stroke. N Engl J Med. 2002 Aug 8;347(6):395-400. doi: 10.1056/NEJMoa011892.

Reference Type BACKGROUND
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Reference Type BACKGROUND
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Giovannelli M, Borriello G, Castri P, Prosperini L, Pozzilli C. Early physiotherapy after injection of botulinum toxin increases the beneficial effects on spasticity in patients with multiple sclerosis. Clin Rehabil. 2007 Apr;21(4):331-7. doi: 10.1177/0269215507072772.

Reference Type BACKGROUND
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Reference Type BACKGROUND
PMID: 18977811 (View on PubMed)

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Reference Type BACKGROUND
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Reference Type BACKGROUND
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Reference Type BACKGROUND
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Reference Type BACKGROUND
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Naumann M, Yakovleff A, Durif F; BOTOX Cervical Dystonia Prospective Study Group. A randomized, double-masked, crossover comparison of the efficacy and safety of botulinum toxin type A produced from the original bulk toxin source and current bulk toxin source for the treatment of cervical dystonia. J Neurol. 2002 Jan;249(1):57-63. doi: 10.1007/pl00007848.

Reference Type BACKGROUND
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Albright AL, Barron WB, Fasick MP, Polinko P, Janosky J. Continuous intrathecal baclofen infusion for spasticity of cerebral origin. JAMA. 1993 Nov 24;270(20):2475-7.

Reference Type BACKGROUND
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Reference Type BACKGROUND

Knapp M, Comas-Herrera, Somani A, Banerjee S. Dementia: Summary report for the National Audit Office international comparisons. London: Personal Social Services Research Unit London School of Economics and Political Science and Section of Mental Health and Ageing The Institute of Psychiatry, King's College London; 2007.

Reference Type BACKGROUND

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Reference Type BACKGROUND

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Reference Type BACKGROUND

Bhakta BB, Tennant A, Cozens JA, et al. Application of item response theory to measure the disabling effects of severe upper limb spasticity in stroke and the consequent carer burden. Cerebrovascular Dis 1999;9:124.

Reference Type BACKGROUND

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Waardenburg H, Elvers W, Van Vechgel F, Oostendorp R. Can paratonia be measured reliably? Evaluation of the reliability of a visual analogue scale and the modified tonus sclae of Ashworth for measuring paratonia. Nederlands Tijdschrift voor Fysiotherapie (in dutch) 1999;102:30-35.

Reference Type BACKGROUND

Kleiner-Fisman G, Khoo E, Moncrieffe N, Forbell T, Gryfe P, Fisman D. A randomized, placebo controlled pilot trial of botulinum toxin for paratonic rigidity in people with advanced cognitive impairment. PLoS One. 2014 Dec 23;9(12):e114733. doi: 10.1371/journal.pone.0114733. eCollection 2014.

Reference Type DERIVED
PMID: 25536218 (View on PubMed)

Other Identifiers

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NT-036

Identifier Type: -

Identifier Source: org_study_id

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