Dose-response Study of Efficacy and Safety of Botulinum Toxin Type A to Treat Spasticity of the Leg(s) in Cerebral Palsy

NCT ID: NCT01893411

Last Updated: 2021-08-05

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

311 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-06-30

Study Completion Date

2016-05-31

Brief Summary

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The purpose of this study is to determine whether injections of Botulinum toxin type A into muscles of the leg(s) are effective in treating children/adolescents (age 2-17 years) with increased muscle tension/uncontrollable muscle stiffness (spasticity) due to cerebral palsy.

Detailed Description

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Conditions

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Lower Limb Spasticity Due to Cerebral Palsy

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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16 Units per kg body weight incobotulinumtoxinA (Xeomin)

Group Type EXPERIMENTAL

IncobotulinumtoxinA (16 Units per kg body weight)

Intervention Type DRUG

Active ingredient: Clostridium Botulinum neurotoxin Type A free from complexing proteins. Solution for injection prepared by reconstitution of powder with 0.9% Sodium Chloride (NaCl); Total volume 8.0 mL; 400 units; Mode of administration: intramuscular injection into spastic muscles.

12 Units per kg body weight incobotulinumtoxinA (Xeomin)

Group Type EXPERIMENTAL

IncobotulinumtoxinA (12 Units per kg body weight)

Intervention Type DRUG

Active ingredient: Clostridium Botulinum neurotoxin Type A free from complexing proteins. Solution for injection prepared by reconstitution of powder with 0.9% Sodium Chloride (NaCl); Total volume 8.0 mL; 300 units; Mode of administration: intramuscular injection into spastic muscles.

4 Units per kg body weight incobotulinumtoxinA (Xeomin)

Group Type EXPERIMENTAL

IncobotulinumtoxinA (4 Units per kg body weight)

Intervention Type DRUG

Active ingredient: Clostridium Botulinum neurotoxin Type A free from complexing proteins. Solution for injection prepared by reconstitution of powder with 0.9% Sodium Chloride (NaCl); Total volume 8.0 mL; 100 units; Mode of administration: intramuscular injection into spastic muscles.

Interventions

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IncobotulinumtoxinA (16 Units per kg body weight)

Active ingredient: Clostridium Botulinum neurotoxin Type A free from complexing proteins. Solution for injection prepared by reconstitution of powder with 0.9% Sodium Chloride (NaCl); Total volume 8.0 mL; 400 units; Mode of administration: intramuscular injection into spastic muscles.

Intervention Type DRUG

IncobotulinumtoxinA (12 Units per kg body weight)

Active ingredient: Clostridium Botulinum neurotoxin Type A free from complexing proteins. Solution for injection prepared by reconstitution of powder with 0.9% Sodium Chloride (NaCl); Total volume 8.0 mL; 300 units; Mode of administration: intramuscular injection into spastic muscles.

Intervention Type DRUG

IncobotulinumtoxinA (4 Units per kg body weight)

Active ingredient: Clostridium Botulinum neurotoxin Type A free from complexing proteins. Solution for injection prepared by reconstitution of powder with 0.9% Sodium Chloride (NaCl); Total volume 8.0 mL; 100 units; Mode of administration: intramuscular injection into spastic muscles.

Intervention Type DRUG

Other Intervention Names

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Xeomin NT 201 Botulinum toxin type A (150 kiloDalton), free from complexing proteins Xeomin NT 201 Botulinum toxin type A (150 kiloDalton), free from complexing proteins Xeomin NT 201 Botulinum toxin type A (150 kiloDalton), free from complexing proteins

Eligibility Criteria

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Inclusion Criteria

* Female or male subject of 2 to 17 years of age (inclusive).
* Uni- or bilateral cerebral palsy with clinical need for uni- or bilateral LL injections with BoNT for the treatment of spasticity.
* Ashworth Scale \[AS\] score ≥2 in plantar flexors (at least unilaterally).
* Clinical need for a total dose of 16 U/kg BW NT 201 (maximum of 400 U) for the treatment of LL spasticity according to the clinical judgment of the investigator.

Exclusion Criteria

* Fixed contracture defined as severe restriction of the range of joint movement on passive stretch or predominant forms of muscle hypertonia other than spasticity (e.g., dystonia) in the target limb(s).
* Surgery on pes equinus on side(s) intended to be treated with BoNT injections in this study within 12 months prior to Screening Visit (V1), in the screening period or planned for the time of participation in this study.
* Hip flexion requiring BoNT injection.
Minimum Eligible Age

2 Years

Maximum Eligible Age

17 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Merz Pharmaceuticals GmbH

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Merz Medical Expert

Role: STUDY_DIRECTOR

Merz Pharmaceuticals GmbH

Locations

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Merz Investigational Site #043037

Graz, , Austria

Site Status

Merz Investigational Site #043036

Vienna, , Austria

Site Status

Merz Investigational Site #420029

Brno, , Czechia

Site Status

Merz Investigational Site #420028

Olomouc, , Czechia

Site Status

Merz Investigational Site #372001

Tallinn, , Estonia

Site Status

Merz Investigational Site #372002

Tartu, , Estonia

Site Status

Merz Investigational Site #033056

Amiens, , France

Site Status

Merz Investigational Site #033052

Bron, , France

Site Status

Merz Investigational Site #033054

La Tronche, , France

Site Status

Merz Investigational Site #033055

Palavas-les-Flots, , France

Site Status

Merz Investigational Site #049328

Bochum, , Germany

Site Status

Merz Investigational Site #049330

Marburg, , Germany

Site Status

Merz Investigational Site #049327

Munich, , Germany

Site Status

Merz Investigational Site #049329

Münster, , Germany

Site Status

Merz Investigational Site #049326

Vogtareuth, , Germany

Site Status

Merz Investigational Site #972003

Jerusalem, , Israel

Site Status

Merz Investigational Site #972001

Tel Aviv, , Israel

Site Status

Merz Investigational Site #972002

Tel Aviv, , Israel

Site Status

Merz Investigational Site #048089

Bialystok, , Poland

Site Status

Merz Investigational Site #048063

Gdansk, , Poland

Site Status

Merz Investigational Site #048059

Krakow, , Poland

Site Status

Merz Investigational Site #048084

Lublin, , Poland

Site Status

Merz Investigational Site #048072

Luboń, , Poland

Site Status

Merz Investigational Site #048075

Sandomierz, , Poland

Site Status

Merz Investigational Site #048061

Warsaw, , Poland

Site Status

Merz Investigational Site #040003

Bucharest, , Romania

Site Status

Merz Investigational Site #040001

Bucharest, , Romania

Site Status

Merz Investigational Site #040002

Iași, , Romania

Site Status

Merz Investigational Site #007014

Kazan', , Russia

Site Status

Merz Investigational Site #007015

Khabarovsk, , Russia

Site Status

Merz Investigational Site #007018

Novosibirsk, , Russia

Site Status

Merz Investigational Site #007017

Saint Petersburg, , Russia

Site Status

Merz Investigational Site #007013

Smolensk, , Russia

Site Status

Merz Investigational Site #007019

Stavropol, , Russia

Site Status

Merz Investigational Site #421003

Banská Bystrica, , Slovakia

Site Status

Merz Investigational Site #421008

Bratislava, , Slovakia

Site Status

Merz Investigational Site #421006

Krompachy, , Slovakia

Site Status

Merz Investigational Site #421004

Levoča, , Slovakia

Site Status

Merz Investigational Site #082019

Goyang, , South Korea

Site Status

Merz Investigational Site #082021

Incheon, , South Korea

Site Status

Merz Investigational Site #082018

Seongnam-si, , South Korea

Site Status

Merz Investigational Site #082020

Seoul, , South Korea

Site Status

Merz Investigational Site #034031

Granada, , Spain

Site Status

Merz Investigational Site #034032

Manresa, , Spain

Site Status

Merz Investigational Site #034030

Seville, , Spain

Site Status

Merz Investigational Site #034026

Seville, , Spain

Site Status

Merz Investigational Site #090005

Elâzığ, , Turkey (Türkiye)

Site Status

Merz Investigational Site #090003

Izmir, , Turkey (Türkiye)

Site Status

Merz Investigational Site #090002

İzmit, , Turkey (Türkiye)

Site Status

Merz Investigational Site #380001

Dnipropetrovsk, , Ukraine

Site Status

Merz Investigational Site #380005

Kharkiv, , Ukraine

Site Status

Merz Investigational Site #380002

Kiev, , Ukraine

Site Status

Merz Investigational Site #380003

Odesa, , Ukraine

Site Status

Countries

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Austria Czechia Estonia France Germany Israel Poland Romania Russia Slovakia South Korea Spain Turkey (Türkiye) Ukraine

References

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Heinen F, Kanovsky P, Schroeder AS, Chambers HG, Dabrowski E, Geister TL, Hanschmann A, Martinez-Torres FJ, Pulte I, Banach M, Gaebler-Spira D. IncobotulinumtoxinA for the treatment of lower-limb spasticity in children and adolescents with cerebral palsy: A phase 3 study. J Pediatr Rehabil Med. 2021;14(2):183-197. doi: 10.3233/PRM-210040.

Reference Type RESULT
PMID: 34092664 (View on PubMed)

Berweck S, Banach M, Gaebler-Spira D, Chambers HG, Schroeder AS, Geister TL, Althaus M, Hanschmann A, Vacchelli M, Bonfert MV, Heinen F, Dabrowski E. Safety Profile and Lack of Immunogenicity of IncobotulinumtoxinA in Pediatric Spasticity and Sialorrhea: A Pooled Analysis. Toxins (Basel). 2022 Aug 25;14(9):585. doi: 10.3390/toxins14090585.

Reference Type DERIVED
PMID: 36136523 (View on PubMed)

Other Identifiers

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2012-005054-30

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

MRZ60201_3070_1

Identifier Type: -

Identifier Source: org_study_id

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