BOTOX® Open-Label Treatment in Pediatric Lower Limb Spasticity

NCT ID: NCT01603641

Last Updated: 2019-08-21

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

370 participants

Study Classification

INTERVENTIONAL

Study Start Date

2012-11-05

Study Completion Date

2018-08-25

Brief Summary

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This study will evaluate the long-term safety of BOTOX® (botulinum toxin Type A) for the treatment of pediatric lower limb spasticity.

Detailed Description

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Conditions

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Pediatrics Muscle Spasticity Cerebral Palsy

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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BOTOX®

Participants received maximum of 5 treatments of intramuscular injections of BOTOX® (botulinum toxin Type A) into a single lower limb muscles or divided between both lower limb muscles or into the lower limb muscles and/or upper limb muscles at a minimum of 12 weeks apart. Treatment dosing was according to investigator judgment not to exceed a maximum of 8 unit per kilogram (U/kg) of body weight (not to exceed 300 U) in treatment Cycle 1. Dose could be increased to a maximum of 10 U/kg (not to exceed 340 U) in treatment Cycles 2-5. Participants received intramuscular injections of BOTOX® (botulinum toxin Type A) 4 or 8 U/kg into the lower limb in the previous study or were de novo participants who were not enrolled in the previous study.

Group Type EXPERIMENTAL

Botulinum Toxin Type A

Intervention Type BIOLOGICAL

Participants received intramuscular injections of botulinum toxin Type A into the lower limb muscles and/or upper limb muscles at a minimum of 12 weeks apart for a maximum of 5 treatments.

Interventions

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Botulinum Toxin Type A

Participants received intramuscular injections of botulinum toxin Type A into the lower limb muscles and/or upper limb muscles at a minimum of 12 weeks apart for a maximum of 5 treatments.

Intervention Type BIOLOGICAL

Other Intervention Names

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BOTOX® OnabotulinumtoxinA

Eligibility Criteria

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Inclusion Criteria

* Minimum weight of 10 kilograms (kg)/22 pounds (lb)
* Cerebral palsy with dynamic muscle contracture of the ankle

Exclusion Criteria

* Muscular dystrophy, myasthenia gravis, Eaton-Lambert syndrome, amyotrophic lateral sclerosis, or mitochondrial disease
* Uncontrolled epilepsy
* Botulinum Toxin therapy of any serotype for any condition within the last 3 months
* History of surgical intervention of the lower study leg within 1 year, or planned surgery of any limb during the study
Minimum Eligible Age

2 Years

Maximum Eligible Age

17 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Allergan

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Emily McCusker

Role: STUDY_DIRECTOR

Allergan

Locations

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ABS Health, LLC

Pasadena, California, United States

Site Status

Harrison Clinical Management

Pomona, California, United States

Site Status

Rady Children's Hospital San Diego

San Diego, California, United States

Site Status

Children's Hospital Colorado

Aurora, Colorado, United States

Site Status

Associated Neurologists of Southern Connecticut, P.C.

Fairfield, Connecticut, United States

Site Status

New England Institute for Clinical Research

Stamford, Connecticut, United States

Site Status

NW FL Clinical Research Group, LLC

Gulf Breeze, Florida, United States

Site Status

Axcess Medical Research, LLC

Loxahatchee Groves, Florida, United States

Site Status

Pediatric Neurology, P.A.

Orlando, Florida, United States

Site Status

Children's Healthcare of Atlanta Children's Rehabilitation Associates

Atlanta, Georgia, United States

Site Status

Shirley Ryan Ability Lab

Chicago, Illinois, United States

Site Status

Beaumont Children's Hospital Pediatric Research

Royal Oak, Michigan, United States

Site Status

The Children's Mercy Hospital

Kansas City, Missouri, United States

Site Status

Washington University School of Medicine

St Louis, Missouri, United States

Site Status

Clinical Research Center of New Jersey

Voorhees Township, New Jersey, United States

Site Status

NYU Hospital for Joint Diseases

New York, New York, United States

Site Status

Columbia University Dept. of Rehab. & Regenerative Medicine

New York, New York, United States

Site Status

OnSite Clinical Solutions, LLC

Charlotte, North Carolina, United States

Site Status

PMG Research of Charlotte, LLC

Charlotte, North Carolina, United States

Site Status

Hasbro Children's Hospital

Providence, Rhode Island, United States

Site Status

Vanderbilt University Medical Center

Nashville, Tennessee, United States

Site Status

University of Texas Southwestern Medical Center

Dallas, Texas, United States

Site Status

Baylor College of Medicine Texas Children's Hospital

Houston, Texas, United States

Site Status

Road Runner Research

San Antonio, Texas, United States

Site Status

Seattle Children's Hospital

Seattle, Washington, United States

Site Status

Marshfield Clinic

Marshfield, Wisconsin, United States

Site Status

Semmelweis Egyetem- Ortopédiai Klinika Karolina út 27

Budapest, , Hungary

Site Status

Debrecen University Clinical Center, Orthopedic Clinic

Debrecen, , Hungary

Site Status

Istituto IRCCS G. Salini

Genoa, , Italy

Site Status

Philippine Orthopedic Center

Quezon City, , Philippines

Site Status

St. Luke's Medical Center

Quezon City, , Philippines

Site Status

Philippine Children's Medical Center

Quezon City, , Philippines

Site Status

Uniwersytecki Dzieciecy Szpita

Bialystok, , Poland

Site Status

Uniwersyteckie Centrum Kliniczne

Gdansk, , Poland

Site Status

Centrum Rehabilitacji Krok po Kroku

Gdansk, , Poland

Site Status

Specjalistyczny Gabinet Neurologiczny

Krakow, , Poland

Site Status

Centrum Medyczne "POMOC"

Lodz, , Poland

Site Status

INTERMED, Lublin

Lublin, , Poland

Site Status

CRH ŻAGIEL MED, Lublin

Lublin, , Poland

Site Status

Szpital Wojewodzki Nr 2

Rzeszów, , Poland

Site Status

Poradnia Rehab - Neurologiczneij dla Dzieci I Mlodziezy Aga

Warsaw, , Poland

Site Status

NZOZ Mazowieckie Centrum

Warsaw, , Poland

Site Status

Childrens Republic Hospital

Kazan', , Russia

Site Status

Smolensk Regional Hospital- Regional Budget State Healthcare institution

Smolensk, , Russia

Site Status

Tyumen Regional Hospital #2 - State Budget Healthcare Institution of Tyumen region

Tyumen, , Russia

Site Status

Daegu Fatima Hospital

Daegu, , South Korea

Site Status

National Health Insurance Service Ilsan Hospital

Gyeonggi-do, , South Korea

Site Status

Seoul National University Hospital

Seoul, , South Korea

Site Status

Severance Hospital, Yonsei University Health System

Seoul, , South Korea

Site Status

Asan Medical Center

Seoul, , South Korea

Site Status

Samsung Medical Center

Seoul, , South Korea

Site Status

Maharaj Nakorn ChiangMai Hospital

Chiang Mai, , Thailand

Site Status

Srinagarind Hospital, Khon Kaen University

Khon Kaen, , Thailand

Site Status

Ankara Diskapi Yildrim Beyazit

Ankara, , Turkey (Türkiye)

Site Status

Kocaeli Üniversitesi

Kocaeli, , Turkey (Türkiye)

Site Status

Selçuk Üniversitesi

Konya, , Turkey (Türkiye)

Site Status

Countries

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United States Hungary Italy Philippines Poland Russia South Korea Thailand Turkey (Türkiye)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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Other Identifiers

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2012-000084-24

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

191622-112

Identifier Type: -

Identifier Source: org_study_id

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