Effectiveness and Safety of Dysport® (abobotulinumtoxinA) in Paediatric Lower Limb Spasticity

NCT ID: NCT03017729

Last Updated: 2020-12-19

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Total Enrollment

242 participants

Study Classification

OBSERVATIONAL

Study Start Date

2017-02-10

Study Completion Date

2020-11-30

Brief Summary

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The purpose of this study is to assess the longitudinal attainment of subject centred and functional related goals (cumulated Goal Attainment Scale Total (GAS T) score) after abobotulinumtoxinA injection (including following repeated injection cycles where they occur) alongside spasticity management used in real life settings over a period of 18 months (and a maximum of six injection cycles).

Detailed Description

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Conditions

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Lower Limb Spasticity

Study Design

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Observational Model Type

COHORT

Study Time Perspective

PROSPECTIVE

Interventions

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Botulinum toxin type A

This is an observational study designed to reflect real world clinical practice in the use of abobotulinumtoxinA. AbobotulinumtoxinA injected doses, frequency of injections, number of injection sites and volume injected per site are in accordance with the current USPI and physician's clinical practice.

Intervention Type BIOLOGICAL

Other Intervention Names

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AbobotulinumtoxinA (Dysport®)

Eligibility Criteria

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Inclusion Criteria

* Female or male subjects aged 2 to 17 years inclusive
* Decision to prescribe abobotulinumtoxinA, to be made prior to and independently from the decision to enroll in the study
* Primary diagnosis of paediatric lower limb (PLL) spasticity and either: Previously untreated with BoNT (naïve to BoNT), or previously treated with a BoNT (i.e. non naïve to BoNT), and for those who were previously treated with BoNT-A, they should have responded to BoNT-A treatment according to the investigator's criteria
* For non naïve BoNT subjects, a minimum interval of 12 weeks since the last BoNT injection and in the presence of spasticity

Exclusion Criteria

* Known resistance to any BoNT or experienced serious safety issues with previous use of BoNT
* Concomitant treatment with other BoNT
* Known hypersensitivity to abobotulinumtoxinA or related compounds, or any component in the study drug formulation
* Subjects with any clinical (or subclinical) evidence of marked defective neuromuscular transmission (e.g. Lambert Eaton syndrome or myasthenia gravis) or persistent clinically significant neuromuscular disorders
Minimum Eligible Age

2 Years

Maximum Eligible Age

17 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Ipsen

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Ipsen Medical Director

Role: STUDY_DIRECTOR

Ipsen

Locations

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Children's National Medical Center

Washington D.C., District of Columbia, United States

Site Status

Nicklaus Children's Hospital

Miami, Florida, United States

Site Status

Laszlo J. Mate, M.D.

North Palm Beach, Florida, United States

Site Status

Clinical Integrative Research Central Atlanta

Atlanta, Georgia, United States

Site Status

Mt. Washington Pediatric Hospital

Baltimore, Maryland, United States

Site Status

William Beaumont Hospital Pediatric Research

Royal Oak, Michigan, United States

Site Status

Gillette Children's Specialty Healthcare

Saint Paul, Minnesota, United States

Site Status

University of Missouri

Columbia, Missouri, United States

Site Status

Washington University School Of Medicine

St Louis, Missouri, United States

Site Status

Valley Health System

Ridgewood, New Jersey, United States

Site Status

Montefiore Medical Center

The Bronx, New York, United States

Site Status

Akron Children's Hospital

Akron, Ohio, United States

Site Status

Cleveland Clinic

Cleveland, Ohio, United States

Site Status

Dayton Children's Hospital

Dayton, Ohio, United States

Site Status

The Children's Center

Bethany, Oklahoma, United States

Site Status

Shriners Hospitals for Children

Portland, Oregon, United States

Site Status

Good Shepherd Rehabilitation Network

Allentown, Pennsylvania, United States

Site Status

Shriners Hospitals for Children

Philadelphia, Pennsylvania, United States

Site Status

Shriners Hospitals for Children

Greenville, South Carolina, United States

Site Status

Children's Hospital at Erlanger

Chattanooga, Tennessee, United States

Site Status

Scottish Rite Hospital for Children

Dallas, Texas, United States

Site Status

Shriners Hospitals for Children

Houston, Texas, United States

Site Status

Texas Children's Hospital

Houston, Texas, United States

Site Status

Texas Children's

Plano, Texas, United States

Site Status

The Children's Hospital of San Antonio

San Antonio, Texas, United States

Site Status

Utah Neuro Rehabilitation

Murray, Utah, United States

Site Status

Children's Hospital of Wisconsin

Milwaukee, Wisconsin, United States

Site Status

Countries

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United States

Other Identifiers

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A-US-52120-330

Identifier Type: -

Identifier Source: org_study_id