A Study to Evaluate a Therapeutic Vaccine, ASP0113, in Cytomegalovirus (CMV)-Seropositive Recipients Undergoing Allogeneic, Hematopoietic Cell Transplant (HCT)

NCT ID: NCT01877655

Last Updated: 2024-10-24

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

514 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-09-11

Study Completion Date

2022-03-01

Brief Summary

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The purpose of the study was to evaluate the efficacy of ASP0113 compared with placebo as measured by a primary composite endpoint of overall mortality and CMV end organ disease (EOD) through 1 year post-transplant. Safety of ASP0113 in participants undergoing allogeneic HCT will also be evaluated.

Detailed Description

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Participants will be followed for 5.5 years post-transplant for long-term safety via an annual telephone contact.

Conditions

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Cytomegalovirus (CMV)-Positive Recipients Allogeneic, Hematopoietic Cell Transplant (HCT)

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

PREVENTION

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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ASP0113

Participants received 1 mL of 5 mg/mL of ASP0113 via intramuscular injection in the deltoid muscle alternating sides with each dose on days -14 to -3 pretransplant, 14 to 40, 60, 90 and 180 in relation to the day of transplant (Day 0).

Group Type EXPERIMENTAL

ASP0113

Intervention Type BIOLOGICAL

Intramuscular injection

Placebo

Participants received 1 mL of 5 mg/mL of matching placebo via intramuscular injection in the deltoid muscle alternating sides with each dose on days -14 to -3 pretransplant, 14 to 40, 60, 90 and 180 in relation to the day of transplant (Day 0).

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Intramuscular injection

Interventions

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ASP0113

Intramuscular injection

Intervention Type BIOLOGICAL

Placebo

Intramuscular injection

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Participant is a CMV-seropositive HCT recipient
* Participant is planned to undergo either of the following:

* Sibling Donor Transplant
* Unrelated Donor Transplant
* Participant has one of the following underlying diseases:

* Acute myeloid leukemia (AML)
* Acute lymphoblastic leukemia (ALL)
* Acute undifferentiated leukemia (AUL)
* Acute biphenotypic leukemia
* Chronic myelogenous leukemia (CML)
* Chronic lymphocytic leukemia (CLL).
* A defined myelodysplastic syndrome(s) (MDS)
* Primary or secondary myelofibrosis
* Lymphoma (including Hodgkin's)

Exclusion Criteria

* Participant has active CMV disease or infection or has received treatment for active CMV disease or infection within 3 months (90 days) prior to transplant
* Participant has a modified hematopoietic cell transplant comorbidity index (HCT-CI) score ≥ 4
* Participant has received a prior HCT and has residual Chronic Graft-versus-host Disease (cGVHD)
* Participant who is scheduled to have a cord blood transplant or a haploidentical transplant
* Participant has a platelet count of less than 50,000 mm3 within 3 days prior to randomization (platelet transfusions are allowed)
* Participant has aplastic anemia or multiple myeloma
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Astellas Pharma Global Development, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Medical Director

Role: STUDY_DIRECTOR

Astellas Pharma Global Development, Inc.

Locations

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Site US10028

Birmingham, Alabama, United States

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Site US10044

Tucson, Arizona, United States

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Site US10035

San Francisco, California, United States

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Site US10026

Stanford, California, United States

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Site US10030

Tampa, Florida, United States

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Site US10012

Atlanta, Georgia, United States

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Site US10013

Chicago, Illinois, United States

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Site US10007

Indianapolis, Indiana, United States

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Site US10020

Westwood, Kansas, United States

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Site US10010

Louisville, Kentucky, United States

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Site US10043

Baltimore, Maryland, United States

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Site US10011

Baltimore, Maryland, United States

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Site US10021

Boston, Massachusetts, United States

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Site US10036

Rochester, Minnesota, United States

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Site US10042

St Louis, Missouri, United States

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Site US10023

Hackensack, New Jersey, United States

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Site US10047

New York, New York, United States

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Site US10027

Rochester, New York, United States

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Site US10025

Chapel Hill, North Carolina, United States

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Site US10016

Nashville, Tennessee, United States

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Site US10002

Dallas, Texas, United States

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Site US10045

Houston, Texas, United States

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Site US10046

Salt Lake City, Utah, United States

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Site US10031

Richmond, Virginia, United States

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Site US10039

Seattle, Washington, United States

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Site US10024

Seattle, Washington, United States

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Site US10019

Milwaukee, Wisconsin, United States

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Site AU43001

Herston, Queensland, Australia

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Site AU43004

Adelaide, South Australia, Australia

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Site BE32001

Bruges, , Belgium

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Site BE32005

Leuven, , Belgium

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Site BE32007

Roeselare, , Belgium

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Site CA15001

Vancouver, British Columbia, Canada

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Site CA15002

Toronto, Ontario, Canada

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Site CA15004

Montreal, Quebec, Canada

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Site CA15003

Québec, Quebec, Canada

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Site FR33011

Besançon, , France

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Site FR33005

Créteil, , France

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Site FR33009

Nantes, , France

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Site FR33010

Nice, , France

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Site DE49010

Bonn, , Germany

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Site DE49014

Cologne, , Germany

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Site DE49012

Düsseldorf, , Germany

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Site DE49013

Göttingen, , Germany

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Site DE49002

Leipzig, , Germany

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Site DE49015

Mainz, , Germany

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Site DE49007

Münster, , Germany

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Site DE49005

Stuttgart, , Germany

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Site DE49008

Tübingen, , Germany

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Site DE49006

Ulm, , Germany

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Site DE49001

Würzburg, , Germany

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Site JP81003

Nagoya, Aichi-ken, Japan

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Site JP81011

Maebashi, Gunma, Japan

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Site JP81007

Sapporo, Hokkaido, Japan

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Site JP81010

Bunkyo-ku, Tokyo, Japan

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Site JP81008

Chuo-ku, Tokyo, Japan

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Site JP81009

Minato-ku, Tokyo, Japan

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Site JP81004

Shinjuku-ku, Tokyo, Japan

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Site JP81001

Fukuoka, , Japan

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Site JP81005

Fukuoka, , Japan

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Site JP81006

Osaka, , Japan

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Site KR82004

Seoul, Seoul Teugbyeolsi, South Korea

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Site KR82002

Seoul, , South Korea

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Site KR82003

Seoul, , South Korea

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Site KR82001

Seoul, , South Korea

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Site ES34001

Badalona, , Spain

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Site ES34006

Barcelona, , Spain

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Site ES34004

Barcelona, , Spain

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Site ES34005

Córdoba, , Spain

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Site ES34003

Granada, , Spain

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Site ES34011

Madrid, , Spain

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Site ES34007

Murcia, , Spain

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Site ES34010

Salamanca, , Spain

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Site ES34002

Santander, , Spain

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Site ES34009

Valencia, , Spain

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Site SE46001

Gothenburg, , Sweden

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Site SE46006

Linköping, , Sweden

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Site SE46004

Lund, , Sweden

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Site SE46003

Stockholm, , Sweden

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Site SE46005

Umeå, , Sweden

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Site TW88601

Taipei, , Taiwan

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Site TW88602

Taipei, , Taiwan

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Site TW88603

Taoyuan, , Taiwan

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Countries

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United States Australia Belgium Canada France Germany Japan South Korea Spain Sweden Taiwan

References

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Ljungman P, Bermudez A, Logan AC, Kharfan-Dabaja MA, Chevallier P, Martino R, Wulf G, Selleslag D, Kakihana K, Langston A, Lee DG, Solano C, Okamoto S, Smith LR, Boeckh M, Wingard JR, Cywin B, Fredericks C, Lademacher C, Wang X, Young J, Maertens J. A randomised, placebo-controlled phase 3 study to evaluate the efficacy and safety of ASP0113, a DNA-based CMV vaccine, in seropositive allogeneic haematopoietic cell transplant recipients. EClinicalMedicine. 2021 Mar 19;33:100787. doi: 10.1016/j.eclinm.2021.100787. eCollection 2021 Mar.

Reference Type DERIVED
PMID: 33842870 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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https://www.clinicaltrials.astellas.com/study/0113-CL-1004/

Link to results and other applicable study documents on the Astellas Clinical Trials website

https://ast.trialsummaries.com/Study/StudyDetails?id=14598&tenant=MT_AST_9011

Link to plain language summary of the study on the Trial Results Summaries website

Other Identifiers

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2013-000903-18

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

0113-CL-1004

Identifier Type: -

Identifier Source: org_study_id

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