Efficacy and Safety of Idelalisib (GS-1101) in Combination With Rituximab for Previously Treated Indolent Non-Hodgkin Lymphomas

NCT ID: NCT01732913

Last Updated: 2018-11-16

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

295 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-01-16

Study Completion Date

2016-05-18

Brief Summary

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The primary objective of this study is to evaluate the effect of the addition of idelalisib to rituximab on progression-free survival (PFS) in adults with previously treated indolent non-Hodgkin lymphoma (iNHL).

An increased rate of deaths and serious adverse events (SAEs) among participants with front-line chronic lymphocytic leukemia (CLL) and early-line iNHL treated with idelalisib in combination with standard therapies was observed by the independent data monitoring committee (DMC) during regular review of 3 Gilead Phase 3 studies. Gilead reviewed the unblinded data and terminated this study in agreement with the DMC recommendation and in consultation with the US Food and Drug Administration (FDA).

Detailed Description

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Conditions

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Indolent Non-Hodgkin's Lymphomas

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

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Rituximab + idelalisib

Participants will receive rituximab + idelalisib.

Group Type EXPERIMENTAL

Rituximab

Intervention Type DRUG

375 mg/m\^2 administered intravenously weekly for 4 weeks, then every 8 weeks (up to a total of 8 infusions)

Idelalisib

Intervention Type DRUG

150 mg tablets administered orally twice daily

Rituximab + Placebo

Participants will receive rituximab + placebo. Following confirmation of iNHL disease progression by the independent review committee and unblinding, participants may be eligible to receive open-label idelalisib 150 mg twice daily.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Tablets administered orally twice daily

Rituximab

Intervention Type DRUG

375 mg/m\^2 administered intravenously weekly for 4 weeks, then every 8 weeks (up to a total of 8 infusions)

Idelalisib

Intervention Type DRUG

150 mg tablets administered orally twice daily

Interventions

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Placebo

Tablets administered orally twice daily

Intervention Type DRUG

Rituximab

375 mg/m\^2 administered intravenously weekly for 4 weeks, then every 8 weeks (up to a total of 8 infusions)

Intervention Type DRUG

Idelalisib

150 mg tablets administered orally twice daily

Intervention Type DRUG

Other Intervention Names

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Rituxan® MabThera® GS-1101 CAL-101 Zydelig®

Eligibility Criteria

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Inclusion Criteria

* Histologically confirmed diagnosis of B-cell iNHL, with histological subtype limited to the following:

1. Follicular lymphoma (FL) Grade 1, 2, or 3a
2. Small lymphocytic lymphoma (SLL) with absolute lymphocyte count \< 5 x 10\^9/L at the time of diagnosis
3. Lymphoplasmacytoid lymphoma/Waldenström macroglobulinemia (LPL/WM)
4. Marginal zone lymphoma (MZL) (splenic, nodal, or extra-nodal)

* Ongoing drug-induced liver injury, active hepatitis C, active hepatitis B , alcoholic liver disease, non-alcoholic steatohepatitis, primary biliary cirrhosis, extrahepatic obstruction caused by cholelithiasis, cirrhosis of the liver, or portal hypertension.
* Received previous treatment with rituximab that was not effective.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Gilead Sciences

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Gilead Study Director

Role: STUDY_DIRECTOR

Gilead Sciences

Locations

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Clearview Cancer Institute

Huntsville, Alabama, United States

Site Status

Ironwood Cancer and Research Center

Chandler, Arizona, United States

Site Status

City of Hope Cancer Center

Duarte, California, United States

Site Status

Saint Jude Heritage Healthcare

Fullerton, California, United States

Site Status

Pacific Shores Medical Group

Long Beach, California, United States

Site Status

UCLA Medical Center

Los Angeles, California, United States

Site Status

Cancer Care Associates

Redondo Beach, California, United States

Site Status

Cancer Center of Santa Barbara

Santa Barbara, California, United States

Site Status

Central Coast Medical Oncology Group

Santa Maria, California, United States

Site Status

Middlesex Hospital Cancer Center

Middletown, Connecticut, United States

Site Status

Georgetown University Medical Center

Washington D.C., District of Columbia, United States

Site Status

Florida Cancer Specialists and Research Institute

Fort Myers, Florida, United States

Site Status

Moffitt Cancer Center

Tampa, Florida, United States

Site Status

Cancer Center of Kansas

Wichita, Kansas, United States

Site Status

Wayne State University

Detroit, Michigan, United States

Site Status

Comprehensive Cancer Centers of Nevada

Las Vegas, Nevada, United States

Site Status

Icahn School of Medicine at Mount Sinai

New York, New York, United States

Site Status

Weill Cornell Medical College

New York, New York, United States

Site Status

Montefiore Medical Center

The Bronx, New York, United States

Site Status

MetroHealth Medical Center

Cleveland, Ohio, United States

Site Status

Signal Point Clinical Research Center, LLC

Middletown, Ohio, United States

Site Status

Perelman Center for Advanced Medicine

Philadelphia, Pennsylvania, United States

Site Status

Prairie Lakes Healthcare System

Watertown, South Dakota, United States

Site Status

Tennessee Oncology, PLLC

Chattanooga, Tennessee, United States

Site Status

Sarah Cannon Cancer Center

Nashville, Tennessee, United States

Site Status

Texas Oncology, P.A.

Bedford, Texas, United States

Site Status

Brooke Army Medical Center

Fort Sam Houston, Texas, United States

Site Status

Center for Cancer and Blood Disorders, PC

Fort Worth, Texas, United States

Site Status

Shenandoah Oncology Associates, PC

Winchester, Virginia, United States

Site Status

Virginia Mason Medical Center

Seattle, Washington, United States

Site Status

Northwest Medical Specialties, PLLC

Tacoma, Washington, United States

Site Status

Froedtert Hospital and Medical College of Wisconsin

Milwaukee, Wisconsin, United States

Site Status

Haematology and Oncology Clinics of Australia at Chermside

Milton, Queensland, Australia

Site Status

Box Hill Hospital

Box Hill, Victoria, Australia

Site Status

Monash Medical Centre

Clayton, Victoria, Australia

Site Status

Saint Vincent's Hospital

Fitzroy, Victoria, Australia

Site Status

Western Hospital

Footscray, Victoria, Australia

Site Status

Royal Perth Hospital

Perth, Western Australia, Australia

Site Status

Adelaide Cancer Centre

Kurralta Park, , Australia

Site Status

Fiona Stanley Hospital

Murdoch, , Australia

Site Status

Fakultní nemocnice Hradec Králové

Hradec Králové, , Czechia

Site Status

University Hospital of Bordeaux

Pessac, Aquitaine, France

Site Status

Centre Hospitalier Régional Universitaire de Lille, Hôpital Claude Huriez

Lille, Hauts-de-France, France

Site Status

Centre Hospitalier Universitaire Brest

Brest, , France

Site Status

Centre Hospitalier de Dunkerque

Dunkirk, , France

Site Status

Centre Hospitalier de Versailles

Le Chesnay, , France

Site Status

Centre Léon Bérard

Lyon, , France

Site Status

Hôpital Hôtel-Dieu

Nantes, , France

Site Status

Centre Hospitalier Lyon Sud

Pierre-Bénite, , France

Site Status

Centre Hospitalier Universitaire de Poitiers Hôpital de la Milétrie

Poitiers, , France

Site Status

Hôpital Necker-Enfants Malades

Paris, Île-de-France Region, France

Site Status

Schwarzwald-Baar Klinikum Villingen-Schwenningen GmbH

Villingen-Schwenningen, Baden-Wurttemberg, Germany

Site Status

Gemeinschaftspraxis Dres. Söling Und Siehl

Kassel, Hesse, Germany

Site Status

Debreceni Egyetem Orvos-és Egészségtudományi Centrum

Debrecen, Hajdú-Bihar, Hungary

Site Status

Somogy Megyei Kaposi Mór Oktató Kórház

Kaposvár, Somogy County, Hungary

Site Status

Markusovszky Egyetemi Oktatókórház

Szombathely, Vas County, Hungary

Site Status

Semmelweis Egyetem

Budapest, , Hungary

Site Status

Országos Onkológiai Intézet

Budapest, , Hungary

Site Status

Hadassah Medical Organization, Ein Kerem

Jerusalem, , Israel

Site Status

Rabin Medical Center

Petah Tikva, , Israel

Site Status

Azienda Ospedaliero-Universitaria di Bologna - Policlinico S.Orsola-Malpighi

Bologna, , Italy

Site Status

Azienda Ospedaliero Universitaria (AOU) "Maggiore della Carita" di Novara

Novara, , Italy

Site Status

Azienda Ospedaliera Ospedali Riuniti Marche Nord

Pesaro, , Italy

Site Status

Centro di Riferimento Oncologico di Aviano

Pordenone, , Italy

Site Status

Azienda Ospedaliera Città della Salute e della Scienza di Torino

Torino, , Italy

Site Status

National Hospital Organization Nagoya Medical Center

Nagoya, Aichi-ken, Japan

Site Status

Aichi Cancer Center Hospital

Nagoya, Aichi-ken, Japan

Site Status

Nagoya City University Hospital

Nagoya, Aichi-ken, Japan

Site Status

National Hospital Organization Kyushu Cancer Center

Minamiku, Fukuoka, Japan

Site Status

Kobe City Medical Center General Hospital

Kobe, Hyōgo, Japan

Site Status

Tokai University Hospital

Isehara-shi, Kanagawa, Japan

Site Status

National Hospital Organization Kumamoto Medical Center

Chuo-ku, Kumamoto, Japan

Site Status

Tohoku University Hospital

Sendai, Miyagi, Japan

Site Status

Okayama University Hospital

Okayama, Okayama-ken, Japan

Site Status

Osaka City University Hospital

Osaka, Osaka, Japan

Site Status

National Cancer Center Hospital

Chuo-ku, Tokyo, Japan

Site Status

The Cancer Institute Hospital of JFCR

Koto-ku, Tokyo, Japan

Site Status

Toranomon Hospital

Minato-ku, Tokyo, Japan

Site Status

Malopolskie Centrum Medyczne S.C.

Krakow, , Poland

Site Status

Samodzielny Publiczny Zaklad Opieki Zdrowotnej Ministerstwa Spraw Wewnetrznych z Warminsko-Mazurskim

Olsztyn, , Poland

Site Status

Centrum Onkologii i Hipertermii

Warsaw, , Poland

Site Status

Hospital Geral de Santo António do Centro Hospitalar do Porto

Porto, , Portugal

Site Status

Institutul Clinic Fundeni

Bucharest, , Romania

Site Status

Nizhny Novgorod Regional Clinical Hospital n.a. N.A. Semashko

Nizhny Novgorod, , Russia

Site Status

Ryazan Regional Clinical Hospital

Ryazan, , Russia

Site Status

Saint Petersburg I.P. Pavlov State Medical University

Saint Petersburg, , Russia

Site Status

FSI "V.A. Almazov Federal Centre of Heart, Blood and Endocrinology of Rosmedtechnologies"

Saint Petersburg, , Russia

Site Status

Saratov State Medical University

Saratov, , Russia

Site Status

Sverdlovsk Regional Clinical Hospital #1

Yekaterinburg, , Russia

Site Status

Singapore General Hospital

Singapore, , Singapore

Site Status

National Cancer Centre Singapore

Singapore, , Singapore

Site Status

Gleneagles Medical Centre

Singapore, , Singapore

Site Status

Seoul National University Hospital

Seoul, , South Korea

Site Status

Samsung Medical Center

Seoul, , South Korea

Site Status

Asan Medical Center

Seoul, , South Korea

Site Status

Hospital Universitario Puerta de Hierro

Majadahonda, Madrid, Spain

Site Status

Hospital Universitari Germans Trias i Pujol

Badalona, , Spain

Site Status

Skånes Universitetssjukhus, Malmö

Malmo, , Sweden

Site Status

Chang Gung Memorial Hospital (CGMH)

Kaohsiung City, , Taiwan

Site Status

Tri-Service General Hospital

Taipei, , Taiwan

Site Status

Barts and The London NHS Trust

London, England, United Kingdom

Site Status

Mount Vernon Hospital

Middlesex, , United Kingdom

Site Status

Sunderland Royal Infirmary

Sunderland, , United Kingdom

Site Status

Countries

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United States Australia Czechia France Germany Hungary Israel Italy Japan Poland Portugal Romania Russia Singapore South Korea Spain Sweden Taiwan United Kingdom

Other Identifiers

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GS-US-313-0124

Identifier Type: -

Identifier Source: org_study_id

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