Efficacy and Safety of Idelalisib in Combination With Rituximab in Patients With Previously Untreated Chronic Lymphocytic Leukemia With 17p Deletion

NCT ID: NCT02044822

Last Updated: 2018-11-19

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

102 participants

Study Classification

INTERVENTIONAL

Study Start Date

2014-08-06

Study Completion Date

2016-05-17

Brief Summary

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The primary objective of this study is to evaluate overall response rate (ORR) following treatment with idelalisib plus rituximab in participants with previously untreated chronic lymphocytic leukemia (CLL) with 17p deletion.

An increased rate of deaths and serious adverse events (SAEs) among participants with front-line CLL and early-line indolent non-Hodgkin lymphoma (iNHL) treated with idelalisib in combination with standard therapies was observed by the independent data monitoring committee (DMC) during regular review of 3 Gilead Phase 3 studies. Gilead reviewed the unblinded data and terminated those studies in agreement with the DMC recommendation and in consultation with the US Food and Drug Administration (FDA). All front-line studies of idelalisib, including this study, were also terminated.

Detailed Description

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Conditions

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B-cell Chronic Lymphocytic Leukemia (CLL) With 17p Deletion

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Idelalisib + rituximab

Participants will receive rituximab for 8 weeks and Idelalisib continuously throughout the study (up to 10 years).

Group Type EXPERIMENTAL

Idelalisib

Intervention Type DRUG

150 mg tablets administered orally twice daily

Rituximab

Intervention Type DRUG

375 mg/m\^2 administered intravenously once weekly x 8 weeks

Interventions

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Idelalisib

150 mg tablets administered orally twice daily

Intervention Type DRUG

Rituximab

375 mg/m\^2 administered intravenously once weekly x 8 weeks

Intervention Type DRUG

Other Intervention Names

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GS-1101 CAL-101 Zydelig® Rituxan

Eligibility Criteria

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Inclusion Criteria

* Documented diagnosis of B-cell CLL, according to International Workshop on Chronic Lymphocytic Leukemia 2008
* Presence of 17p deletion in CLL cells as demonstrated by fluorescence in-situ hybridization (FISH) testing
* No prior therapy for CLL other than corticosteroids for disease complications
* CLL that warrants treatment
* Presence of measurable lymphadenopathy
* Eastern Cooperative Oncology Group (ECOG) performance status of ≤ 2

Exclusion Criteria

* Known histological transformation from CLL to an aggressive lymphoma (ie, Richter transformation)
* Known presence of myelodysplastic syndrome
* History of a non-CLL malignancy except for the following:

* the malignancy has been in remission without treatment for ≥ 5 years prior to enrollment, or
* carcinoma in situ of the cervix, or
* adequately treated basal or squamous cell skin cancer or other localized non-melanoma skin cancer, or
* asymptomatic prostate cancer without known metastatic disease and with no current requirement for therapy or requiring only hormonal therapy and with normal prostate specific antigen for ≥ 1 year prior to enrollment, or
* ductal carcinoma in situ (DCIS) of the breast treated with lumpectomy alone, or
* other adequately treated Stage 1 or 2 cancer currently in complete remission
* Evidence of ongoing systemic bacterial, fungal, or viral infection at the time of enrollment
* Ongoing liver injury
* History of noninfectious pneumonitis
* Ongoing inflammatory bowel disease
* History of prior allogeneic bone marrow progenitor cell or solid organ transplantation
* Ongoing immunosuppressive therapy other than corticosteroids
* Received last dose of study drug on another therapeutic clinical trial within 30 days prior to enrollment
* Prior or ongoing clinically significant illness, medical condition, surgical history, physical finding, electrocardiogram (ECG) finding, or laboratory abnormality
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Gilead Sciences

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Gilead Study Director

Role: STUDY_DIRECTOR

Gilead Sciences

Locations

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Arizona Oncology Associates, PC - HOPE

Tucson, Arizona, United States

Site Status

Innovative Clinical Research Institute

Whittier, California, United States

Site Status

Rocky Mountain Cancer Centers

Boulder, Colorado, United States

Site Status

The University of Chicago Medicine

Chicago, Illinois, United States

Site Status

Illinois Cancer Specialists

Niles, Illinois, United States

Site Status

Washington University School of Medicine

St Louis, Missouri, United States

Site Status

Duke University

Durham, North Carolina, United States

Site Status

GHS Cancer Institute

Greenville, North Carolina, United States

Site Status

Compass Oncology

Portland, Oregon, United States

Site Status

Willamette Valley Cancer Center and Research Institute

Springfield, Oregon, United States

Site Status

Hospital of the University of Pennsylvania, Abramson Cancer Center

Philadelphia, Pennsylvania, United States

Site Status

St Vincent's Hospital, Sydney

Darlinghurst, New South Wales, Australia

Site Status

St George Hospital

Kogarah, New South Wales, Australia

Site Status

Icon Cancer Foundation

South Brisbane, Queensland, Australia

Site Status

St Vincent's Hospital, Melbourne

Fitzroy, Victoria, Australia

Site Status

Liverpool Hospital

Liverpool, , Australia

Site Status

Innsbruck University Hospital, Inner Medicine,

Innsbruck, , Austria

Site Status

Univ. Klinik für Innere Medizin III LKH

Salzburg, , Austria

Site Status

Medizinische Universität Wien, Univ. Klinik f. Innere Med. I, Abteilung für Hämatologie und Hämostaseologie

Vienna, , Austria

Site Status

AZ Sint-Jan AV Brugge-Oostende

Bruges, , Belgium

Site Status

University Hospital Leuven

Leuven, , Belgium

Site Status

University Hospital

Brno, , Czechia

Site Status

Faculty Hospital Hradec Kralove

Hradec Králové, , Czechia

Site Status

Hemato-Onkologicka Klinika Fn

Olomuc, , Czechia

Site Status

Faculty hospital Ostrava

Ostrava-Poruba, , Czechia

Site Status

Faculty Hospital Kralovske Vinohrady

Prague, , Czechia

Site Status

Vseobecna Fakultim Nemocnice

Prague, , Czechia

Site Status

Aalborg University Hospital

Aalborg, , Denmark

Site Status

Centre Hospitalier Universitaire Hôpital Avicenne

Bobigny, , France

Site Status

CHRU de Lille, Hopital Claude Huriez

Lille, , France

Site Status

Centre Hospitalier Universitaire Nancy

Nancy, , France

Site Status

Hopital Pitie-Salpetriere

Paris, , France

Site Status

University of Debrecen HSC Institute of internal Medicine, Department of Hematology

Debrecen, , Hungary

Site Status

Institute of Hematology "L. e A. Seràgnoli"

Bologna, , Italy

Site Status

A.O.Spedali Civili Brescia

Brescia, , Italy

Site Status

A.O.Niguarda Ca' Granda

Milan, , Italy

Site Status

Azienda Ospedaliero Universitaria Policlinico di Modena

Modena, , Italy

Site Status

SCDU Medicina II ed Ematologia, A.O.U. San Luigi Gonzaga

Orbassano, , Italy

Site Status

Uniwersyteckie Centrum Kliniczne

Gdansk, Pomeranian Voivodeship, Poland

Site Status

Szpital Specjalistyczny w Brzozowie

Brzozów, , Poland

Site Status

Malopolskie Centrum Medyczne s.c.

Krakow, , Poland

Site Status

Wojewodzki Szpital Specjalistyczny

Lodz, , Poland

Site Status

Centrum Onkologii-Instytut Marii Sklodowskiej -Curie klinika Nowotworow Ukladu Chlonnego

Warsaw, , Poland

Site Status

Samodzielny Publiczny Szpital Kliniczny

Wroclaw, , Poland

Site Status

Centro Hospitalar De Lisboa Norte, E.P.E. - Hospital Santa Maria

Lisbon, , Portugal

Site Status

IPO Porto Francisco Gentil, E.P.E

Porto, , Portugal

Site Status

Emergency County Clinical Hospital Brasov

Brasov, , Romania

Site Status

Spitalul Clinic Colentina

Bucharest, , Romania

Site Status

Institutul Regional de Oncologie Iasi

Iași, , Romania

Site Status

Hospital Universitario Marques de Valdecilla

Santander, Cantabria, Spain

Site Status

Hospital Clinic

Barcelona, Catalonia, Spain

Site Status

Hospital Universitario Puerta De Hierro

Madrid, , Spain

Site Status

Hospital Clinico Universitario De Valencia (Chuv)

Valencia, , Spain

Site Status

Saint James's University Hospital

Leeds, , United Kingdom

Site Status

Royal Liverpool & Broadgreen Univ. Hospitals

Liverpool, , United Kingdom

Site Status

University Hospital Southampton NHS Trust

Southampton, , United Kingdom

Site Status

Countries

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United States Australia Austria Belgium Czechia Denmark France Hungary Italy Poland Portugal Romania Spain United Kingdom

Other Identifiers

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2013-003314-41

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

GS-US-312-0133

Identifier Type: -

Identifier Source: org_study_id

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