A Randomized, Double-Blind, Placebo-Controlled Study of Idelalisib in Combination With Rituximab for Previously Treated Chronic Lymphocytic Leukemia (CLL)

NCT ID: NCT01539512

Last Updated: 2019-05-14

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

220 participants

Study Classification

INTERVENTIONAL

Study Start Date

2012-04-30

Study Completion Date

2014-04-30

Brief Summary

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This Phase 3, randomized, double-blind, placebo-controlled study is to evaluate the effect of idelalisib in combination with rituximab on the onset, magnitude, and duration of tumor control in participants previously treated for chronic lymphocytic leukemia (CLL). Eligible patients will be randomized with a 1:1 ratio into 1 of the 2 treatment arms to receive either idelalisib plus rituximab or placebo plus rituximab. Participants who are tolerating primary study therapy but experience definitive CLL progression are eligible to receive active idelalisib therapy in the extension study, GS-US-312-0117.

Detailed Description

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Conditions

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Chronic Lymphocytic Leukemia

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

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Idelalisib + rituximab

Participants will receive idelalisib plus rituximab

Group Type ACTIVE_COMPARATOR

Idelalisib

Intervention Type DRUG

Idelalisib 150 mg tablet administered orally twice daily

Rituximab

Intervention Type DRUG

Rituximab administered intravenously 8 times through Week 20: Day 1: 375 mg/m\^2, and 500 mg/m\^2 thereafter

Placebo + rituximab

Participants will receive placebo to match idelalisib plus rituximab

Group Type PLACEBO_COMPARATOR

Rituximab

Intervention Type DRUG

Rituximab administered intravenously 8 times through Week 20: Day 1: 375 mg/m\^2, and 500 mg/m\^2 thereafter

Placebo to match idelalisib

Intervention Type DRUG

Placebo to match idelalisib administered orally twice daily

Interventions

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Idelalisib

Idelalisib 150 mg tablet administered orally twice daily

Intervention Type DRUG

Rituximab

Rituximab administered intravenously 8 times through Week 20: Day 1: 375 mg/m\^2, and 500 mg/m\^2 thereafter

Intervention Type DRUG

Placebo to match idelalisib

Placebo to match idelalisib administered orally twice daily

Intervention Type DRUG

Other Intervention Names

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Zydelig® GS-1101 CAL 101 Rituxan®

Eligibility Criteria

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Inclusion Criteria

* Adult subjects with previously treated recurrent CLL who have measurable lymphadenopathy
* Require therapy for CLL
* Have experienced CLL progression \< 24 months since the completion of the last prior therapy
* Currently not sufficiently fit to receive cytotoxic therapy because of chemotherapy-induced bone marrow damage or comorbidities.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Gilead Sciences

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Thomas Jahn, MD

Role: STUDY_DIRECTOR

Gilead Sciences

Locations

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Clearview Cancer Institute

Huntsville, Alabama, United States

Site Status

Arizona Oncology Associates

Tucson, Arizona, United States

Site Status

University of California, San Diego- Moores Cancer Center

La Jolla, California, United States

Site Status

Ventura County Hematology Oncology Specialists

Oxnard, California, United States

Site Status

UCLA

Santa Monica, California, United States

Site Status

Stanford Cancer Center

Stanford, California, United States

Site Status

Rocky Mountain Blood and Marrow Transplant Program

Denver, Colorado, United States

Site Status

Rocky Mountain Cancer Center

Denver, Colorado, United States

Site Status

Georgetown University Medical Center Lombardi Cancer Center

Washington D.C., District of Columbia, United States

Site Status

Collaborative Medical Research Corporation

Boynton Beach, Florida, United States

Site Status

Collaborative Research Group LLC

Boynton Beach, Florida, United States

Site Status

Florida Cancer Specialists

Fort Myers, Florida, United States

Site Status

University of Florida

Gainesville, Florida, United States

Site Status

Florida Cancer Specialists

St. Petersburg, Florida, United States

Site Status

Winship Cancer Institute at Emory University

Atlanta, Georgia, United States

Site Status

Northwestern University

Chicago, Illinois, United States

Site Status

Hackensack University Medical Center

Hackensack, New Jersey, United States

Site Status

Hematology Oncology Associates of Northern New Jersey

Morristown, New Jersey, United States

Site Status

Long Island Jewish Medical Center

New Hyde Park, New York, United States

Site Status

Weill Cornell Medical College

New York, New York, United States

Site Status

Columbia University Medical Center

New York, New York, United States

Site Status

Memorial Sloan Kettering Cancer Center

New York, New York, United States

Site Status

Willamette Valley Cancer Center

Springfield, Oregon, United States

Site Status

Northwest Cancer Specialists, PC

Tualatin, Oregon, United States

Site Status

Cancer Centers of the Carolinas

Greenville, South Carolina, United States

Site Status

Sarah Cannon Cancer Center

Nashville, Tennessee, United States

Site Status

Texas Oncology, P.A.

Fort Worth, Texas, United States

Site Status

M.D. Anderson Cancer Center

Houston, Texas, United States

Site Status

Cancer Care Network of South Texas

San Antonio, Texas, United States

Site Status

Virginia Cancer Specialists, PC

Fairfax, Virginia, United States

Site Status

Oncology and Hematology Associates of Southwest Virginia, Inc

Roanoke, Virginia, United States

Site Status

Seattle Cancer Care Alliance

Seattle, Washington, United States

Site Status

Yakima Valley Memorial Hospital / North Star Lodge

Yakima, Washington, United States

Site Status

Medical College of Wisconsin

Milwaukee, Wisconsin, United States

Site Status

Hôpital Henri Mondor

Créteil, , France

Site Status

Centre Hospitalier Régional Universitaire de Lille (CHRU)

Lille, , France

Site Status

Hôpital Emile Muller

Mulhouse, , France

Site Status

Centre Hospitalier Lyon Sud

Pierre-Bénite, , France

Site Status

Hôpital Pontchaillou

Rennes, , France

Site Status

Centre Henri Becquerel

Rouen, , France

Site Status

Hopital Purpan

Toulouse, , France

Site Status

Universitätsklinikum Köln

Cologne, , Germany

Site Status

Gemeinschaftspraxis Hämatologie-Onkologie

Dresden, , Germany

Site Status

Internistische Gemeinschaftspraxis

Erlangen, , Germany

Site Status

Stauferklinikum Schwäb. Gmünd

Mutlangen, , Germany

Site Status

Hämatologische/Onkologische Gemeinschaftspraxis Dr. Peter Schmidt / Dr. Holger Klaproth

Neunkirchen, , Germany

Site Status

Universitätsklinikum Ulm

Ulm, , Germany

Site Status

Ospedale Oncologico Regionale A. Businco

Cagliari, , Italy

Site Status

Ospedale San Raffaele S.r.l.

Milan, , Italy

Site Status

Azienda Ospedaliera Città della Salute e della Scienza di Torino

Torino, , Italy

Site Status

Royal Bournemouth Hospital

Bournemouth, , United Kingdom

Site Status

Addenbrooke's Hospital

Cambridge, , United Kingdom

Site Status

University Hospital of Wales

Cardiff, , United Kingdom

Site Status

Castle Hill Hospital

Cottingham, , United Kingdom

Site Status

Dorset County Hospital

Dorchester, , United Kingdom

Site Status

Western General Hospital

Edinburgh, , United Kingdom

Site Status

Northwick Park Hospital

Harrow, , United Kingdom

Site Status

St James's University Hospital

Leeds, , United Kingdom

Site Status

Royal Liverpool University Hospital

Liverpool, , United Kingdom

Site Status

King's College Hospital

London, , United Kingdom

Site Status

Hammersmith Hospital

London, , United Kingdom

Site Status

Sarah Cannon Research Institute UK

London, , United Kingdom

Site Status

Freeman Hospital

Newcastle upon Tyne, , United Kingdom

Site Status

Princess Royal University Hospital

Orpington, , United Kingdom

Site Status

Salisbury District Hospital

Salisbury, , United Kingdom

Site Status

Southampton General Hospital

Southampton, , United Kingdom

Site Status

Royal Marsden Hospital

Sutton, , United Kingdom

Site Status

Great Western Hospital

Swindon, , United Kingdom

Site Status

Torbay District General Hospital

Torquay, , United Kingdom

Site Status

Royal Cornwall Hospital

Truro, , United Kingdom

Site Status

New Cross Hospital

Wolverhampton, , United Kingdom

Site Status

Yeovil District Hospital

Yeovil, , United Kingdom

Site Status

Countries

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United States France Germany Italy United Kingdom

References

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Barrientos JC, Hillmen P, Salles G, Sharman J, Stilgenbauer S, Gurtovaya O, Xing G, Ruzicka B, Bhargava P, Ghia P, Pagel JM. No increased bleeding events in patients with relapsed chronic lymphocytic leukemia and indolent non-Hodgkin lymphoma treated with idelalisib. Leuk Lymphoma. 2021 Apr;62(4):837-845. doi: 10.1080/10428194.2020.1845339. Epub 2020 Dec 10.

Reference Type DERIVED
PMID: 33297794 (View on PubMed)

Gordon MJ, Huang J, Chan RJ, Bhargava P, Danilov AV. Medical comorbidities in patients with chronic lymphocytic leukaemia treated with idelalisib: analysis of two large randomised clinical trials. Br J Haematol. 2021 Feb;192(4):720-728. doi: 10.1111/bjh.16879. Epub 2020 Jun 29.

Reference Type DERIVED
PMID: 32599655 (View on PubMed)

Furman RR, Sharman JP, Coutre SE, Cheson BD, Pagel JM, Hillmen P, Barrientos JC, Zelenetz AD, Kipps TJ, Flinn I, Ghia P, Eradat H, Ervin T, Lamanna N, Coiffier B, Pettitt AR, Ma S, Stilgenbauer S, Cramer P, Aiello M, Johnson DM, Miller LL, Li D, Jahn TM, Dansey RD, Hallek M, O'Brien SM. Idelalisib and rituximab in relapsed chronic lymphocytic leukemia. N Engl J Med. 2014 Mar 13;370(11):997-1007. doi: 10.1056/NEJMoa1315226. Epub 2014 Jan 22.

Reference Type DERIVED
PMID: 24450857 (View on PubMed)

Other Identifiers

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2011-005180-24

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

GS-US-312-0116

Identifier Type: -

Identifier Source: org_study_id

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