Study to Evaluate the Long-term Safety and Tolerability of USL261 in Patients With Seizure Clusters

NCT ID: NCT01529034

Last Updated: 2023-01-20

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

175 participants

Study Classification

INTERVENTIONAL

Study Start Date

2012-07-31

Brief Summary

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The purpose of this study is to examine the long-term safety and tolerability of USL261 in the treatment of seizure clusters.

Detailed Description

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Participants who completed study P261-401 (NCT01390220), a randomized double-blind study of USL261 (intranasal midazolam) versus placebo to acutely treat a seizure cluster episode, were eligible to to enroll in this open-label extension study (P261-402). The participant's caregiver administered a USL261 5 milligram (mg) dose for a seizure episode meeting study criteria. A second USL261 5 mg dose could be administered after 10 minutes and up to 6 hours after the first dose for persistent or recurrent seizures, unless the participant met exclusions to administration of the second dose. A participant could have more than 1 seizure cluster episode treated during his/her study participation.

Conditions

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Epilepsy

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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USL261

Intranasal midazolam 5 mg

Group Type EXPERIMENTAL

USL261

Intervention Type DRUG

Interventions

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USL261

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Has a competent, adult caregiver who can recognize and observe the subject's seizure cluster episodes
* Has successfully completed study P261-401, and the subject and caregiver have demonstrated adequate compliance with P261-401 study procedures as determined by the investigator

Exclusion Criteria

* Has experienced status epilepticus during or since the P261-401 study
* In the opinion of the investigator, is experiencing an ongoing, uncontrolled, clinically significant adverse event(s) from P261-401 at Visit 1 or did experience a clinically significant adverse event in study P261-401 that might prevent the subject from safely participating in the study
* Has a neurological disorder that is likely to progress in the next year
* Has a history of acute narrow-angle glaucoma
* Has a medical condition including uncontrolled cardiac, pulmonary, renal, hepatic, or gastrointestinal disease that could interfere with the study, subject safety/safety monitoring, or is not stable despite current therapy
* Subject has severe chronic cardio-respiratory disease or the need for ambulatory oxygen
* Has had psychogenic, non-epileptic seizure(s) during or since the P261-401 study
* Has active suicidal plan or intent as determined by the C-SSRS at Visit 1 or medical history
* Subject has had vagus nerve stimulator (VNS) implanted since the completion of study P261-401
Minimum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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UCB Biopharma S.P.R.L.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Israel

Ramat Gan, , Israel

Site Status

United States, Arizona

Phoenix, Arizona, United States

Site Status

United States, Arizona

Scottsdale, Arizona, United States

Site Status

United States, Arizona

Tucson, Arizona, United States

Site Status

United States, Arkansas

Little Rock, Arkansas, United States

Site Status

United States, California

Fresno, California, United States

Site Status

United States, California

Sacramento, California, United States

Site Status

United States, California

Ventura, California, United States

Site Status

United States, Colorado

Aurora, Colorado, United States

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United States, Connecticut

New Haven, Connecticut, United States

Site Status

United States, Florida

Port Charlotte, Florida, United States

Site Status

United States, Florida

Wellington, Florida, United States

Site Status

United States, Idaho

Boise, Idaho, United States

Site Status

United States, Illinois

Chicago, Illinois, United States

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United States, Kentucky

Lexington, Kentucky, United States

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United States, Maryland

Baltimore, Maryland, United States

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United States, Michigan

Detroit, Michigan, United States

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United States, Minnesota

Saint Paul, Minnesota, United States

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United States, Missouri

St Louis, Missouri, United States

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United States, New Hampshire

Lebanon, New Hampshire, United States

Site Status

United States, New Jersey

Hackensack, New Jersey, United States

Site Status

United States, New York

New York, New York, United States

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United States, New York

Stony Brook, New York, United States

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United States, New York

The Bronx, New York, United States

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United States, North Carolina

Durham, North Carolina, United States

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United States, North Carolina

Winston-Salem, North Carolina, United States

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United States, Oklahoma

Oklahoma City, Oklahoma, United States

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United States, Pennsylvania

Philadelphia, Pennsylvania, United States

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United States, Tennessee

Memphis, Tennessee, United States

Site Status

United States, Tennessee

Nashville, Tennessee, United States

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United States, Texas

Dallas, Texas, United States

Site Status

United States, Texas

Greenville, Texas, United States

Site Status

Australia, New South Wales

Randwick, New South Wales, Australia

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Australia, Victoria

Heidelberg West, Victoria, Australia

Site Status

Australia, Victoria

Parkville, Victoria, Australia

Site Status

Canada

Montreal, Ontario, Canada

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Canada, Toronto

Toronto, Ontario, Canada

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Canada

Toronto, Quebec, Canada

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Germany

München, Bavaria, Germany

Site Status

Germany

Marberg, Hesse, Germany

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Germany

Bonn, North Rhine-Westphalia, Germany

Site Status

Germany

Bielefeld, Westfalen-Lippe, Germany

Site Status

Hungary

Budapest, , Hungary

Site Status

Israel

Haifa, , Israel

Site Status

Israel

Petah Tikvah, , Israel

Site Status

New Zealand

Christchurch, Canterbury, New Zealand

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Poland

Gdansk, , Poland

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Poland

Katowice, , Poland

Site Status

Poland

Lublin, , Poland

Site Status

Spain

Seville, Andalusia, Spain

Site Status

Spain

Girona, Cataluyna, Spain

Site Status

Spain

Madrid, , Spain

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Ukraine

Ivano-Frankivsk, , Ukraine

Site Status

Ukraine

Kharkiv, , Ukraine

Site Status

Ukraine

Odesa, , Ukraine

Site Status

Ukraine

Poltava, , Ukraine

Site Status

Ukraine

Ternopil, , Ukraine

Site Status

Ukraine

Vinnytsa, , Ukraine

Site Status

Countries

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United States Australia Canada Germany Hungary Israel New Zealand Poland Spain Ukraine

References

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Meng TC, Szaflarski JP, Chen L, Brunnert M, Campos R, Van Ess P, Pullman WE, Fakhoury T. Psychosocial outcomes of repeated treatment of seizure clusters with midazolam nasal spray: Results of a phase 3, open-label extension trial. Epilepsy Behav. 2023 Jan;138:108989. doi: 10.1016/j.yebeh.2022.108989. Epub 2022 Nov 18.

Reference Type RESULT
PMID: 36410152 (View on PubMed)

Wheless JW, Meng TC, Van Ess PJ, Detyniecki K, Sequeira DJ, Pullman WE. Safety and efficacy of midazolam nasal spray in the outpatient treatment of patients with seizure clusters: An open-label extension trial. Epilepsia. 2019 Sep;60(9):1809-1819. doi: 10.1111/epi.16300. Epub 2019 Jul 29.

Reference Type DERIVED
PMID: 31353457 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2011-004109-25

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

P261-402

Identifier Type: -

Identifier Source: org_study_id

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