Metabolic Screening in Patients With Donnai-Barrow Syndrome

NCT ID: NCT01509287

Last Updated: 2022-11-22

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Total Enrollment

78 participants

Study Classification

OBSERVATIONAL

Study Start Date

2010-03-31

Study Completion Date

2022-06-30

Brief Summary

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This study focuses on the genetics and metabolism of Donnai-Barrow Syndrome (DBS).

Detailed Description

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The purpose of this study is to better understand the role of certain nutrients and vitamins in promoting the healthy development of individuals with Donnai-Barrow Syndrome. The investigators hope that the information gained by studying the metabolism of children with Donnai-Barrow Syndrome and their family members will lead to significant advances in the treatment of this disease.

Conditions

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Donnai-Barrow Syndrome

Study Design

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Observational Model Type

CASE_ONLY

Study Time Perspective

CROSS_SECTIONAL

Study Groups

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Donnai-Barrow Syndrome (DBS)

Individuals affected with Donnai-Barrow Syndrome (DBS)

No interventions assigned to this group

Unaffected

Healthy family members of individuals affected with Donnai-Barrow Syndrome (DBS)

No interventions assigned to this group

Eligibility Criteria

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Inclusion Criteria

All individuals affected with Donnai-Barrow Syndrome
Eligible Sex

ALL

Accepts Healthy Volunteers

Yes

Sponsors

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Massachusetts General Hospital

OTHER

Sponsor Role lead

Responsible Party

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Barbara R. Pober

Principal Investigator and Clinical Geneticist

Responsibility Role PRINCIPAL_INVESTIGATOR

Principal Investigators

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Barbara Pober, MD

Role: PRINCIPAL_INVESTIGATOR

Massachusetts General Hospital

Locations

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Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status

Countries

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United States

Other Identifiers

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2009p001589

Identifier Type: -

Identifier Source: org_study_id

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