A Randomized Controlled Trial of Aliskiren in the Prevention of Major Cardiovascular Events in Elderly People

NCT ID: NCT01259297

Last Updated: 2014-04-08

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

2336 participants

Study Classification

INTERVENTIONAL

Study Start Date

2011-01-31

Study Completion Date

2012-11-30

Brief Summary

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This study was planned to provide new information regarding the role of aliskiren (with or without additional therapy with a diuretic or a Calcium channel blockers (CCB)) in elderly individuals (≥ 65 years) with systolic blood pressure (SBP) 130 to 159 mmHg, in preventing major cardiovascular (CV) events and on global measures of physical, executive and cognitive function.

Detailed Description

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This was 2x2 factorial design study with 2 strata. As per protocol, the first co- Primary analysis as well as secondary analysis were aliskiren based regimen vs non-aliskiren based regimen. All aliskiren based arm were combined into the aliskiren based regimen and all non-aliskiren based arms were combined into non-aliskiren based regimen.

Conditions

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Cardiovascular Events

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

FACTORIAL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Aliskiren + Amlodipine

In run-in period (4-5 weeks) , patients on thiazide background therapy and approximately 50% of patients on neither CCB nor thiazide background therapy received Amlodipine 5 mg and Aliskiren 150/300 mg daily in a titrated manner as per protocol.

In double blind period, patients who successfully completed run-in with Amlodipine plus Aliskiren were randomized equally to the 4 arms of the Amlodipine add-on stratum.

Patients randomized to this arm received Aliskiren 300 mg + Amlodipine 5 mg once daily during the double blind period.

Group Type EXPERIMENTAL

Aliskiren

Intervention Type DRUG

Aliskiren 150/300 mg once daily

Amlodipine

Intervention Type DRUG

Amlodipine 5 mg

Aliskiren + Hydrochlorothiazide (HCTZ)

In run-in period (4-5 weeks) , patients on CCB background therapy and approximately 50% of patients on neither thiazide nor CCB background therapy: received Hydrochlorothiazide 12.5/25 mg and Aliskiren 150/300 mg daily in a titrated manner as per protocol.

In double blind period, all patients who successfully completed run-in with HCTZ plus Aliskiren were randomized equally to the 4 arms of the HCTZ add-on stratum.

Patients randomized to this arm received Aliskiren 300 mg + HCTZ 25 mg once daily.

Group Type EXPERIMENTAL

Aliskiren

Intervention Type DRUG

Aliskiren 150/300 mg once daily

Hydrochlorothiazide (HCTZ)

Intervention Type DRUG

HCTZ 12.5/25 mg

Aliskiren + Placebo for Amlodipine

In double blind period, all patients who successfully completed run-in with Amlodipine plus Aliskiren were randomized equally to the 4 arms of the Amlodipine add-on stratum.

In double blind period, randomized patients to this arm received Aliskiren 300 mg + Placebo for Amlodipine 5 mg

Group Type EXPERIMENTAL

Aliskiren

Intervention Type DRUG

Aliskiren 150/300 mg once daily

Placebo for Amlodipine

Intervention Type DRUG

Placebo for Amlodipine

Aliskiren + Placebo for HCTZ

In double blind period, all patients who successfully completed run-in with HCTZ plus Aliskiren were randomized equally to the 4 arms of the HCTZ add-on stratum.

In double blind period, randomized patients to this arm received Aliskiren 300 mg + Placebo for HCTZ 25 mg once daily

Group Type EXPERIMENTAL

Aliskiren

Intervention Type DRUG

Aliskiren 150/300 mg once daily

Placebo for Hydrochlorothiazide (HCTZ)

Intervention Type DRUG

Placebo for HCTZ 12.5/25 mg

Amlodipine + Placebo for Aliskiren

In double blind period, all patients who successfully completed run-in with Amlodipine plus Aliskiren were randomized equally to the 4 arms of the Amlodipine add-on stratum.

In double blind period, randomized patients to this arm received Amlodipine 5 mg + placebo for Aliskiren 300 mg once daily

Group Type EXPERIMENTAL

Amlodipine

Intervention Type DRUG

Amlodipine 5 mg

Placebo for Aliskiren

Intervention Type DRUG

Placebo for Aliskiren 300 mg

HCTZ + Placebo for Aliskiren

In double blind period, all patients who successfully completed run-in with HCTZ plus Aliskiren were randomized equally to the 4 arms of the HCTZ add-on stratum.

In double blind period, randomized patients to this arm received HCTZ 25 mg + placebo for Aliskiren 300 mg once daily

Group Type EXPERIMENTAL

Hydrochlorothiazide (HCTZ)

Intervention Type DRUG

HCTZ 12.5/25 mg

Placebo for Aliskiren

Intervention Type DRUG

Placebo for Aliskiren 300 mg

Placebo for Aliskiren + Placebo for Amlodipine

In double blind period, all patients who successfully completed run-in with Amlodipine plus Aliskiren were randomized equally to the 4 arms of the Amlodipine add-on stratum.

In double blind period, randomized patients to this arm received placebo for Aliskiren 300 mg + placebo for Amlodipine 5 mg once daily

Group Type PLACEBO_COMPARATOR

Placebo for Aliskiren

Intervention Type DRUG

Placebo for Aliskiren 300 mg

Placebo for Amlodipine

Intervention Type DRUG

Placebo for Amlodipine

Placebo for Aliskiren + Placebo for HCTZ

In double blind period, all patients who successfully completed run-in with HCTZ plus Aliskiren were randomized equally to the 4 arms of the HCTZ add-on stratum.

In double blind period, randomized patients to this arm received placebo for Aliskiren 300 mg + placebo for HCTZ 25 mg once daily

Group Type PLACEBO_COMPARATOR

Placebo for Aliskiren

Intervention Type DRUG

Placebo for Aliskiren 300 mg

Placebo for Hydrochlorothiazide (HCTZ)

Intervention Type DRUG

Placebo for HCTZ 12.5/25 mg

Interventions

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Aliskiren

Aliskiren 150/300 mg once daily

Intervention Type DRUG

Amlodipine

Amlodipine 5 mg

Intervention Type DRUG

Hydrochlorothiazide (HCTZ)

HCTZ 12.5/25 mg

Intervention Type DRUG

Placebo for Aliskiren

Placebo for Aliskiren 300 mg

Intervention Type DRUG

Placebo for Amlodipine

Placebo for Amlodipine

Intervention Type DRUG

Placebo for Hydrochlorothiazide (HCTZ)

Placebo for HCTZ 12.5/25 mg

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

Systolic blood pressure 130 - 159 mmHg with any one of the following (1, 2 or 3):

1. Men and women aged ≥ 65 years if they have at least one of the following: (secondary prevention) Coronary heart disease

* Previous myocardial infarction or
* Stable angina or unstable angina with documented multi-vessel coronary artery disease, \> 50% stenosis in at least 2 major coronary arteries on coronary angiography, or positive stress test (ECG or nuclear perfusion scintogram), or
* Multi-vessel PCI, or
* Multi-vessel CABG surgery \> 4 years prior to informed consent, or with recurrent angina or ischemia following surgery Stroke/TIA Previous documented stroke or documented TIA \< 1 year before informed consent Peripheral artery disease
* Previous limb bypass surgery or percutaneous transluminal angioplasty, or
* Previous limb or foot amputation, or
* History of intermittent claudication, with an ankle:arm BP ratio ≤ 0.80 on at least one side, or significant peripheral artery stenosis (\> 50%) documented by angiography or non-invasive testing
* Diabetes mellitus: High-risk diabetics with evidence of end-organ damage
2. Men and women aged ≥ 65 years with no history of CVD, and with at least 1 CV risk factor (primary prevention):

* History of dyslipidemia, defined as LDL cholesterol \> 3.5 mmol/L (135 mg/dL) or HDL\< 1.3 mmol/L (50 mg/dL) in women or \< 1.0 mmol/L (39 mg/dL) in men or total cholesterol/HDL ratio \> 5
* History of current or recent smoking (regular tobacco use within 5 years)
* Abdominal adiposity defined as waist/hip ratio ≥ 0.90 in women and ≥ 0.95 in men
* History of dysglycemia defined as impaired fasting glucose (IFG - fasting plasma glucose 5.6 to 6.9 mmol/L \[101 to 124 mg/dL\]), or impaired glucose tolerance (IGT - fasting plasma glucose \< 7 mmol/L \[126 mg/dL\] but 2 hour glucose 7.8 to 11.0 mmol/L \[140 to 198 mg/dL\]) or type 2 diabetes
* Renal dysfunction: eGFR\< 60 ml/min/1.73m2 but \> 30 ml/min/1.73m2 (MDRD formula) and/or microalbuminurea/macroalbuminurea
* Clinical evidence of left ventricular hypertrophy
3. Men and women aged ≥ 70 years if they do not have any of the above (primary prevention)

Exclusion Criteria

1. Current treatment with aliskiren, an ACE-inhibitor, an ARB or an aldosterone antagonist and unable to discontinue this therapy in those without clinical vascular disease. Individuals with CVD or type 2 diabetes and/or renal dysfunction may receive an ACE-inhibitor or an ARB, but not both, contraindications to Aliskiren, Amlodipine or Hydrochlorothiazide.
2. Use of both thiazide diuretic and amlodipine or another calcium channel blocker. Patients on only one of these two classes of drugs are eligible
3. Uncontrolled hypertension (systolic blood pressure ≥ 160 mmHg and/or diastolic blood pressure ≥ 100 mmHg)
4. Symptomatic heart failure, requiring the use of loop diuretics
5. Hemodynamically significant primary valvular or outflow tract obstruction (e.g. aortic or mitral valve stenosis, asymmetric septal hypertrophy, malfunctioning prosthetic valve). Constrictive pericarditis. Complex congenital heart disease.
6. Acute stroke \< 3 months or TIA ≤ 7 days before informed consent, acute coronary syndrome \< 1 months before informed consent
7. Planned cardiac surgery or angioplasty \< 3 months after informed consent or having had the procedure \< 3 months before informed consent
8. Severe renal impairment eGFR ≤ 30 ml/min/1.73m2 (MDRD formula); known renal artery stenosis ; serum potassium ≥ 5.3 mmol/L
9. Chronic liver disease (i.e. cirrhosis, esophageal varices, portocaval shunt or persistent hepatitis) or abnormal liver function, i.e., alanine transaminase (ALT) or AST \> 3x upper limit of normal (ULN)
10. Concurrent treatment with cyclosporine or quinidine; chronic use of non-steroidal anti-inflammatory drug (NSAIDs) or cyclooxygenase-2 (COX 2) inhibitors in patients with eGFR \< 60 ml/min/1.73m2 (MDRD formula)
11. History of malignancy of any organ system (other than localized basal cell carcinoma of the skin), treated or untreated, within the past 5 years regardless of whether there is evidence of local recurrence or metastases
12. Other serious condition(s) likely to interfere with study participation or with the ability to complete the study. Significant psychiatric illness, senility, dementia, alcohol or substance abuse, which could impair the ability to provide informed consent and to adhere to the study procedures
Minimum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Novartis Pharmaceuticals

Role: STUDY_DIRECTOR

Novartis Pharmaceuticals

Locations

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Birmingham, Alabama, United States

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Los Angeles, California, United States

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Northridge, California, United States

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Sylmar, California, United States

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Tucker, Georgia, United States

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Pocatello, Idaho, United States

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Haverhill, Massachusetts, United States

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St Louis, Missouri, United States

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Westfiled, New York, United States

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Winston-Salem, North Carolina, United States

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Portland, Oregon, United States

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Falls Church, Virginia, United States

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Marshfield, Wisconsin, United States

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Milwaukee, Wisconsin, United States

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Buenos Aires, Buenos Aires, Argentina

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Buenos Aires, Buenos Aires, Argentina

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Buenos Aires, Buenos Aires, Argentina

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Buenos Aires, Buenos Aires, Argentina

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Ciudad Autonoma de Bs As, Buenos Aires, Argentina

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Coronel Suárez, Buenos Aires, Argentina

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Jenin, Buenos Aires, Argentina

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Mar del Plata, Buenos Aires, Argentina

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Merlo, Buenos Aires, Argentina

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Quilmes, Buenos Aires, Argentina

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San Nicolás de los Arroyos, Buenos Aires, Argentina

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Córdoba, Córdoba Province, Argentina

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Cipolletti, Río Negro Province, Argentina

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Salta, Salta Province, Argentina

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San Miguel de Tucumán, San Miguel de Tucuman, Argentina

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Rosario, Santa Fe Province, Argentina

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Santa Fe, Santa Fe Province, Argentina

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Venado Tuerto, Santa Fe Province, Argentina

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Belo Horizonte, Minas Gerais, Brazil

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Uberaba, Minas Gerais, Brazil

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Campina Grande do Sul, Paraná, Brazil

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Porto Alegre, Rio Grande do Sul, Brazil

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Campinas, São Paulo, Brazil

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Marília, São Paulo, Brazil

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São José do Rio Preto, São Paulo, Brazil

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São Paulo, São Paulo, Brazil

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Votuporanga, São Paulo, Brazil

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Calgary, Alberta, Canada

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Edmonton, Alberta, Canada

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Coquitlam, British Columbia, Canada

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Winnipeg, Manitoba, Canada

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St. John's, Newfoundland and Labrador, Canada

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Brampton, Ontario, Canada

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Hamilton, Ontario, Canada

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Hamilton, Ontario, Canada

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Hamilton, Ontario, Canada

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London, Ontario, Canada

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Markham, Ontario, Canada

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Missisauga, Ontario, Canada

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Newmarket, Ontario, Canada

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Niagara Falls, Ontario, Canada

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North York, Ontario, Canada

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Ottawa, Ontario, Canada

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Ottawa, Ontario, Canada

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Saint Catherines, Ontario, Canada

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Toronto, Ontario, Canada

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Toronto, Ontario, Canada

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Toronto, Ontario, Canada

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Lévis, Quebec, Canada

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Montreal, Quebec, Canada

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Québec, Quebec, Canada

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Sainte-Foy, Quebec, Canada

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Sainte-Foy, Quebec, Canada

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St.Gorges de Beauce, Quebec, Canada

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Terrebonne, Quebec, Canada

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Saskatoon, Saskatchewan, Canada

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Temuco, Cautin, Chile

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Osorno, Osorno, Chile

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Vista Del Mar, Tarapacá, Chile

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Temuca, TX, Chile

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Santiago, , Chile

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Barranquilla, Atlántico, Colombia

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Manizoles, Caldas Department, Colombia

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Barranquilla, Colombia, Colombia

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Cali, Colombia, Colombia

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Cartegena, Colombia, Colombia

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Pasto, Colombia, Colombia

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Bogota, Cundinamarca, Colombia

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Cartagena, Departamento de Bolívar, Colombia

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Pereira, Risaralda Department, Colombia

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Floridablanca, Santander Department, Colombia

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Armenia, , Colombia

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Baranquilla, , Colombia

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Barranquilla, , Colombia

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Bogotá, , Colombia

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Bogotá, , Colombia

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Espinal, , Colombia

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Montería, , Colombia

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Beroun, Czech Republic, Czechia

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Brandýs nad Labem, Czech Republic, Czechia

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Prague, Czech Republic, Czechia

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Prague, Czech Republic, Czechia

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Ústí nad Orlicí, Czech Republic, Czechia

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Nový Jičín, , Czechia

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Prague, , Czechia

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Uherské Hradiště, , Czechia

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Wiesbaden, Germany, Germany

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Berlin, , Germany

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Frankfurt, , Germany

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Melsungen, , Germany

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Nuremberg, , Germany

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Witten, , Germany

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Komárom, Hungary, Hungary

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Budapest, , Hungary

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Budapest, , Hungary

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Gyöngyös, , Hungary

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Kaposvár, , Hungary

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Mosonmagyaróvár, , Hungary

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Pécs, , Hungary

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Sopron, , Hungary

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Szentes, , Hungary

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Veszprém, , Hungary

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Adoni, Andhra Pradesh, India

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Adoni, Andhra Pradesh, India

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Hyderabad, Andhra Pradesh, India

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Visakhapatnam, Andhra Pradesh, India

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Ahmedabad, Gujarat, India

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Ahmedabad, Gujarat, India

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Bangalore, Karnataka, India

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Bangalore, Karnataka, India

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Belagavi, Karnataka, India

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Bengaluru, Karnataka, India

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Nagpur, Maharashtra, India

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Nagpur, Maharashtra, India

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Nagpur, Maharashtra, India

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Pune, Maharashtra, India

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Wardha, Maharashtra, India

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Jalandhar, Punjab, India

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Ludhiana, Punjab, India

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Bikaner, Rajasthan, India

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Tiruvannamalai, Tamil Nadu, India

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Trichy, Tamil Nadu, India

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Lucknow, Uttar Pradesh, India

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Chennai, , India

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Hyderabad, , India

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Mumbai, , India

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Nagpur, , India

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Trichy, , India

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Gorey, Co. Wexford, Ireland

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Ballinsloe, Galway, Ireland

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Galway, Ireland, Ireland

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Safed, Israel, Israel

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Giv‘atayim, , Israel

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Haifa, , Israel

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Alor Star, Kedah, Malaysia

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Kota Bharu, Kelantan, Malaysia

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Kota Bharu, Kelantan, Malaysia

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Kuala Lumpur, Kuala Lumpur, Malaysia

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Kuantan, Pahang, Malaysia

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Batu Caves, Selangor, Malaysia

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Kuala Lumpur, , Malaysia

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Breda, , Netherlands

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Eindhoven, , Netherlands

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Groningen, , Netherlands

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Leiderdorp, , Netherlands

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Rotterdam, , Netherlands

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Velp, , Netherlands

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Zoetermeer, , Netherlands

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Dasmariñas, Cavite, Philippines

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Laoag, Ilocos Norte, Philippines

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Quezon City, National Capital Region, Philippines

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Biñan, , Philippines

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Manila, , Philippines

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Manila, , Philippines

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Pasig, , Philippines

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Quezon City, , Philippines

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Paarl, Western Province, South Africa

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Bloemfontein, , South Africa

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Durban, , South Africa

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Pretoria, , South Africa

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Ferrol, Galicia, Spain

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Madrid, Madrid, Spain

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Valencia, Valencia, Spain

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Port de Sagunt, , Spain

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Dalby, , Sweden

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Gothenburg, , Sweden

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Gothenburg, , Sweden

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Malmo, , Sweden

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Rättvik, , Sweden

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Stockholm, , Sweden

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Countries

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United States Argentina Brazil Canada Chile Colombia Czechia Germany Hungary India Ireland Israel Malaysia Netherlands Philippines South Africa Spain Sweden

References

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Teo KK, Pfeffer M, Mancia G, O'Donnell M, Dagenais G, Diaz R, Dans A, Liu L, Bosch J, Joseph P, Copland I, Jung H, Pogue J, Yusuf S; Aliskiren Prevention of Later Life Outcomes trial Investigators. Aliskiren alone or with other antihypertensives in the elderly with borderline and stage 1 hypertension: the APOLLO trial. Eur Heart J. 2014 Jul;35(26):1743-51. doi: 10.1093/eurheartj/ehu079. Epub 2014 Mar 9.

Reference Type DERIVED
PMID: 24616335 (View on PubMed)

Other Identifiers

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2009-010170-38

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CSPP100G2301

Identifier Type: -

Identifier Source: org_study_id

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