Evaluation of Effectiveness of Two Dosing Regimens of Fostamatinib Compared to Placebo in Patients With Rheumatoid Arthritis (RA) Who Are Taking Methotrexate But Not Responding.

NCT ID: NCT01197521

Last Updated: 2014-04-07

Study Results

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

923 participants

Study Classification

INTERVENTIONAL

Study Start Date

2010-09-30

Study Completion Date

2012-11-30

Brief Summary

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The purpose of the study is to evaluate the effectiveness of two dosing regimens of fostamatinib compared to placebo, in patients with rheumatoid arthritis (RA) who are taking methotrexate but not responding. The study will last for 1 year.

Detailed Description

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Sub-study:

Full title: Optional Genetic Research

Date: 18 June 2010

Version: 1

Objectives: To collect and store, with appropriate consent ,DNA samples for future exploratory research into genes/genetic variation that may influence response (ie, absorption, distribution, metabolism and excretion, safety, tolerability and efficacy) to fostamatinib disodium and/or methotrexate; and/or susceptibility to, progression of and prognosis of RA

Conditions

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Rheumatoid Arthritis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Dosing Regimen A

Oral Treatment

Group Type EXPERIMENTAL

fostamatinib

Intervention Type DRUG

fostamatinib 100 mg twice daily

Dosing Regimen B

Oral Treatment

Group Type EXPERIMENTAL

fostamatinib

Intervention Type DRUG

fostamatinib 100 mg twice daily/150 mg once daily

Dosing Regimen C

Oral Treatment

Group Type PLACEBO_COMPARATOR

placebo, fostamatinib

Intervention Type DRUG

Placebo for 24 weeks followed by fostamatinib 100 mg twice daily

Interventions

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fostamatinib

fostamatinib 100 mg twice daily

Intervention Type DRUG

fostamatinib

fostamatinib 100 mg twice daily/150 mg once daily

Intervention Type DRUG

placebo, fostamatinib

Placebo for 24 weeks followed by fostamatinib 100 mg twice daily

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Active rheumatoid arthritis (RA) diagnosed after the age of 16
* Currently taking methotrexate
* 6 or more swollen joints and 6 or more tender/painful joints (from 28 joint count) and either Erythrocyte Sedimentation Rate (ESR) blood result of 28mm/h or more, or C-Reactive Protein (CRP) blood result of 10mg/L or more
* At least one of the following: documented history of positive rheumatoid factor (blood test), current presence of rheumatoid factor (blood test), radiographic erosion within 12 months prior to study enrolment, presence of serum anti-cyclic citrullinated peptide antibodies (blood test)

Exclusion Criteria

* Females who are pregnant or breast feeding
* Poorly controlled hypertension
* Liver disease or significant liver function test abnormalities
* Certain inflammatory conditions (other than rheumatoid arthritis), connective tissue diseases or chronic pain disorders
* Recent or significant cardiovascular disease
* Significant active or recent infection including tuberculosis
* Previous failure to respond to a TNF alpha antagonist, anakinra or previous treatment with other biological agent
* Severe renal impairment
* Neutropenia
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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AstraZeneca

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Neil MacKillop, MD PhD

Role: STUDY_DIRECTOR

AstraZeneca

Locations

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Research Site

Anniston, Alabama, United States

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Huntsville, Alabama, United States

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Tuscaloosa, Alabama, United States

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Tucson, Arizona, United States

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Huntington Beach, California, United States

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Long Beach, California, United States

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Santa Maria, California, United States

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Santa Monica, California, United States

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Colorado Springs, Colorado, United States

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Bridgeport, Connecticut, United States

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Lewes, Delaware, United States

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Daytona Beach, Florida, United States

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Ocala, Florida, United States

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Atlanta, Georgia, United States

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Marietta, Georgia, United States

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Idaho Falls, Idaho, United States

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Springfield, Illinois, United States

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Wichita, Kansas, United States

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Bowling Green, Kentucky, United States

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Flowood, Mississippi, United States

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Florissant, Missouri, United States

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Richmond Heights, Missouri, United States

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St Louis, Missouri, United States

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Kalispell, Montana, United States

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Albuquerque, New Mexico, United States

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Albany, New York, United States

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Brooklyn, New York, United States

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Olean, New York, United States

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Asheville, North Carolina, United States

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Greensboro, North Carolina, United States

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Perrysburg, Ohio, United States

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Lake Oswego, Oregon, United States

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Erie, Pennsylvania, United States

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Waxford, Pennsylvania, United States

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Charleston, South Carolina, United States

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Hixson, Tennessee, United States

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Memphis, Tennessee, United States

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Dallas, Texas, United States

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Houston, Texas, United States

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Mesquite, Texas, United States

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San Antonio, Texas, United States

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Reading, Berkshire, Argentina

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Buenos Aires, Buenos Aires F.D., Argentina

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Ciudad Autonoma Bs As, CBA, Argentina

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Córdoba, CRD, Argentina

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San Juan, San Juan Province, Argentina

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Rosario, Santa Fe Province, Argentina

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San Miguel de Tucumán, TUC, Argentina

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Caba, , Argentina

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Quilmes, , Argentina

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Camperdown, New South Wales, Australia

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Cairns, Queensland, Australia

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Southport, Queensland, Australia

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Brussels, , Belgium

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Yvoir, , Belgium

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Vitória, Espírito Santo, Brazil

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Curitiba, Paraná, Brazil

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Recife, Pernambuco, Brazil

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São Paulo, São Paulo, Brazil

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Rio de Janeiro, , Brazil

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Plovdiv, , Bulgaria

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Sevlievo, , Bulgaria

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Sofia, , Bulgaria

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Veliko Tarnovo, , Bulgaria

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Osorno, Los Lagos Region, Chile

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Santiago, , Chile

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Pärnu, , Estonia

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Tallinn, , Estonia

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Tartu, , Estonia

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Orléans, , France

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Paris, , France

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Balatonfüred, , Hungary

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Békéscsaba, , Hungary

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Budapest, , Hungary

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Debrecen, , Hungary

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Makó, , Hungary

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Sopron, , Hungary

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Szentes, , Hungary

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Zalaegerszeg-pozva, , Hungary

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Secunderabad, Andhra Pradesh, India

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Visakhapatnam, Andhra Pradesh, India

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Ahmedabad, Gujarat, India

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Bangalore, Karnataka, India

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Mangalore, Karnataka, India

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Udupi, Karnataka, India

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Nagpur, Maharshtra, India

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Lucknow, Uttar Pradesh, India

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Hyderabad, , India

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Kolkata, , India

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Chihuahua City, Chihuahua, Mexico

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Saltillo, Coahuila, Mexico

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Guadalajara, Jalisco, Mexico

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Mexico City, Mexico City, Mexico

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San Luis Potosi, Mexico, Mexico

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Monterrey, Nuevo León, Mexico

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Obrergon, Sonora, Mexico

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Mexicali, , Mexico

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Arequipa, Arequipa, Peru

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Lima, Lima Province, Peru

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Pueblo Libre, Lima region, Peru

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Bytom, , Poland

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Chełm Śląski, , Poland

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Grodzisk Mazowiecki, , Poland

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Katowice, , Poland

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Krakow, , Poland

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Warsaw, , Poland

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Wroclaw, , Poland

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Żyrardów, , Poland

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Bratislava, Slovakia, Slovakia

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Žilina, Slovakia, Slovakia

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Poprad, , Slovakia

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Rimavská Sobota, , Slovakia

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Donetsk, , Ukraine

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Ivano-Frankivsk, , Ukraine

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Kharkiv, , Ukraine

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Kiev, , Ukraine

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Kyiv, , Ukraine

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Lviv, , Ukraine

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Odesa, , Ukraine

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Vinnytsia, , Ukraine

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Zaporyzhzhya, , Ukraine

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Warrington, Cheshire, United Kingdom

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Christchurch, , United Kingdom

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Ipswich, , United Kingdom

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London, , United Kingdom

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Metropolitan Borough of Wirral, , United Kingdom

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Westcliff-on-the Sea, , United Kingdom

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Countries

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United States Argentina Australia Belgium Brazil Bulgaria Chile Estonia France Hungary India Mexico Peru Poland Slovakia Ukraine United Kingdom

References

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Kjelgaard-Petersen CF, Platt A, Braddock M, Jenkins MA, Musa K, Graham E, Gantzel T, Slynn G, Weinblatt ME, Karsdal MA, Thudium CS, Bay-Jensen AC. Translational Biomarkers and Ex Vivo Models of Joint Tissues as a Tool for Drug Development in Rheumatoid Arthritis. Arthritis Rheumatol. 2018 Sep;70(9):1419-1428. doi: 10.1002/art.40527. Epub 2018 Jul 24.

Reference Type DERIVED
PMID: 29669391 (View on PubMed)

Other Identifiers

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2010-020743-12

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

D4300C00001

Identifier Type: -

Identifier Source: org_study_id

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