Evaluation of Effectiveness of Two Dosing Regimens of Fostamatinib Compared to Placebo in Patients With Rheumatoid Arthritis (RA) Who Are Taking Disease Modifying Anti-rheumatic Drug (DMARD) But Not Responding.

NCT ID: NCT01197534

Last Updated: 2014-04-17

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

913 participants

Study Classification

INTERVENTIONAL

Study Start Date

2010-09-30

Study Completion Date

2013-03-31

Brief Summary

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The purpose of the study is to evaluate the effectiveness of two dosing regimens of fostamatinib compared to placebo, in patients with rheumatoid arthritis (RA) who are taking disease modifying anti-rheumatic drug (DMARD) but not responding. The study will last for 1 year.

Detailed Description

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Sub-study:

Full title: Optional Genetic Research

Date: 18 June 2010

Version: 1

Objectives: To collect and store, with appropriate consent ,DNA samples for future exploratory research into genes/genetic variation that may influence response (ie, absorption, distribution, metabolism and excretion, safety, tolerability and efficacy) to fostamatinib disodium and/or methotrexate; and/or susceptibility to, progression of and prognosis of RA

Conditions

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Rheumatoid Arthritis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Dosing Regimen A

Oral Treatment

Group Type EXPERIMENTAL

fostamatinib

Intervention Type DRUG

fostamatinib 100 mg twice daily

Dosing Regimen B

Oral Treatment

Group Type EXPERIMENTAL

fostamatinib

Intervention Type DRUG

fostamatinib 100 mg twice daily/ 150 mg once daily

Dosing Regimen C

Oral Treatment

Group Type PLACEBO_COMPARATOR

placebo, fostamatinib

Intervention Type DRUG

Placebo for 24 weeks followed by fostamatinib 100 mg twice daily.

Interventions

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fostamatinib

fostamatinib 100 mg twice daily

Intervention Type DRUG

fostamatinib

fostamatinib 100 mg twice daily/ 150 mg once daily

Intervention Type DRUG

placebo, fostamatinib

Placebo for 24 weeks followed by fostamatinib 100 mg twice daily.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Active rheumatoid arthritis (RA) diagnosed after the age of 16
* Treatment with one the following disease modifying anti-rheumatic drug: methotrexate, sulfasalazine, hydroxychloroquine or chloroquine
* 4 or more swollen joints and 4 or more tender/painful joints (from 28 joint count)and either Erythrocyte Sedimentation Rate (ESR) blood result of 28mm/h or more, or C-Reactive Protein (CRP) blood result of 10mg/L or more
* At least one of the following: documented history of positive rheumatoid factor (blood test), current presence of rheumatoid factor (blood test), radiographic erosion within 12 months prior to study enrolment, presence of serum anti-cyclic citrullinated peptide antibodies (blood test)

Exclusion Criteria

* Females who are pregnant or breast feeding
* Poorly controlled hypertension
* Liver disease or significant liver function test abnormalities
* Certain inflammatory conditions (other than rheumatoid arthritis), connective tissue diseases or chronic pain disorders
* Recent or significant cardiovascular disease
* Significant active or recent infection including tuberculosis
* Previous failure to respond to a TNF alpha antagonist, anakinra or previous treatment with other biological agent
* Severe renal impairment
* Neutropenia
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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AstraZeneca

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Neil MacKillop, MD PhD

Role: STUDY_DIRECTOR

AstraZeneca

Locations

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Birmingham, Alabama, United States

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Glendale, Arizona, United States

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Mesa, Arizona, United States

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Phoenix, Arizona, United States

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Scottsdale, Arizona, United States

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Tucson, Arizona, United States

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Hot Springs, Arkansas, United States

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Huntington Beach, California, United States

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Torrance, California, United States

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Trumbull, Connecticut, United States

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Washington D.C., District of Columbia, United States

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Boca Raton, Florida, United States

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Brandon, Florida, United States

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Jacksonville, Florida, United States

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Miami, Florida, United States

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Orlando, Florida, United States

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Tampa, Florida, United States

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Venice, Florida, United States

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Zephyrhills, Florida, United States

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Canton, Georgia, United States

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Decatur, Georgia, United States

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Macon, Georgia, United States

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Boise, Idaho, United States

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South Bend, Indiana, United States

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Elizabethtown, Kentucky, United States

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Crofton, Maryland, United States

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Cumberland, Maryland, United States

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Hagerstown, Maryland, United States

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Kalamazoo, Michigan, United States

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Flowood, Mississippi, United States

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St Louis, Missouri, United States

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Kalispell, Montana, United States

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Omaha, Nebraska, United States

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Manalapan, New Jersey, United States

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Las Cruces, New Mexico, United States

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Brooklyn, New York, United States

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Rochester, New York, United States

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Roslyn, New York, United States

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Syracuse, New York, United States

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Charlotte, North Carolina, United States

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Durham, North Carolina, United States

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Dayton, Ohio, United States

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Duncansville, Pennsylvania, United States

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Philadelphia, Pennsylvania, United States

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West Reading, Pennsylvania, United States

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Greenville, South Carolina, United States

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Orangeburg, South Carolina, United States

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Memphis, Tennessee, United States

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Amarillo, Texas, United States

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Austin, Texas, United States

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Dallas, Texas, United States

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Houston, Texas, United States

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Lubbock, Texas, United States

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Mesquite, Texas, United States

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San Antonio, Texas, United States

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Chesapeake, Virginia, United States

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Tacoma, Washington, United States

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Edmonton, Alberta, Canada

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Winnipeg, Manitoba, Canada

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Bowmanville, Ontario, Canada

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Hamilton, Ontario, Canada

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Mississauga, Ontario, Canada

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Ottawa, Ontario, Canada

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Toronto, Ontario, Canada

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Montreal, Quebec, Canada

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Québec, Quebec, Canada

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Trois-Rivières, Quebec, Canada

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Reading, , Canada

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Brno, , Czechia

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Bruntál, , Czechia

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Česká Lípa, , Czechia

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České Budějovice, , Czechia

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Hlučín, , Czechia

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Liberec, , Czechia

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Ostrava - Trebovice, , Czechia

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Prague, , Czechia

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Sokolov, , Czechia

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Terezín, , Czechia

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Zlín, , Czechia

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Erlangen, , Germany

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Hamburg, , Germany

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München, , Germany

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Hyderabad, Andhra Pradesh, India

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Ahmedabad, Gujarat, India

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Gandhinagar, Gujarat, India

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Vadodara, Gujarat, India

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Bangalore, Karnataka, India

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Mangalore, Karnataka, India

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Mumbai, Maharashtra, India

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Pune, Maharashtra, India

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Coimbatore, Tamil Nadu, India

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Madurai, Tamil Nadu, India

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Lucknow, , India

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Ashkelon, , Israel

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Beer Yaakov, , Israel

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Haifa, , Israel

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Kfar Saba, , Israel

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Petah Tikva, , Israel

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Ramat Gan, , Israel

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Rehovot, , Israel

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Tel Aviv, , Israel

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Iesi, AN, Italy

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Legnano, MI, Italy

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Udine, UD, Italy

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Varese, VA, Italy

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Liepāja, , Latvia

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Riga, , Latvia

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Valmiera, , Latvia

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Kaunas, , Lithuania

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Klaipėda, , Lithuania

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Šiauliai, , Lithuania

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Aveiro, , Portugal

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Lisbon, , Portugal

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Porto, , Portugal

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Baia Mare, , Romania

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Brailari, , Romania

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Bucharest, , Romania

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Ploieşti, , Romania

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Belgrade, , Serbia

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Kragujevac, , Serbia

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Niška Banja, , Serbia

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Novi Sad, , Serbia

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Kempron Park, Gauteng, South Africa

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Pretoria, Gauteng, South Africa

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Durban, Kz-natal, South Africa

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Cape Town, W Cape, South Africa

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Port Elizabeth, , South Africa

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Stellenbosch, , South Africa

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La Laguna (tenerife), Canary Islands, Spain

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Mérida, Extremadura, Spain

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Barcelona, , Spain

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Getafe, , Spain

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Kharkiv, , Ukraine

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Kyiv, , Ukraine

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Lutsk, , Ukraine

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Lviv, , Ukraine

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Simferopol, , Ukraine

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Vinnytsia, , Ukraine

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Zaporizhzhya, , Ukraine

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Zaporyzhzhya, , Ukraine

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Maidstone, Kent, United Kingdom

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Eastbourne, Sussex, United Kingdom

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Solihull, West Midlands, United Kingdom

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Basingstoke, , United Kingdom

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Cambridge, , United Kingdom

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London, , United Kingdom

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Newcastle upon Tyne, , United Kingdom

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Stoke-on-Trent, , United Kingdom

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Swindon, , United Kingdom

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Countries

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United States Canada Czechia Germany India Israel Italy Latvia Lithuania Portugal Romania Serbia South Africa Spain Ukraine United Kingdom

Other Identifiers

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2010-020744-35

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

D4300C00002

Identifier Type: -

Identifier Source: org_study_id

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