Combined Haploidentical-Cord Blood Transplantation for Adults and Children

NCT ID: NCT00943800

Last Updated: 2021-01-27

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

NA

Total Enrollment

87 participants

Study Classification

INTERVENTIONAL

Study Start Date

2006-10-09

Study Completion Date

2018-09-30

Brief Summary

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The primary objective is to assess the rate of engraftment with combined haploidentical-cord blood transplantation. The secondary objective is to evaluate the incidence and severity of acute and chronic graft-versus-host disease (GVHD).

Detailed Description

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Conditions

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Leukemia Myelodysplastic Syndrome Multiple Myeloma Lymphoma

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Good Risks patients

For patients transplanted in remission.

Group Type EXPERIMENTAL

Fludarabine-Melphalan & Rabbit antithymocyte globulin (r-ATG)

Intervention Type DRUG

Fludarabine is given through the vein daily for 5 days. Melphalan is given through the vein daily for 2 days. ATG is given every day in the vein for four days.

Stem Cell Transplant

Intervention Type PROCEDURE

Infusion of haploidentical donor, umbilical cord blood

Stem Cells Collections

Intervention Type PROCEDURE

Haploidentical cells will be T-cell depleted using the Miltenyi Clinimax device.

High Risk Patients eligible for radiation

Group Type EXPERIMENTAL

Stem Cell Transplant

Intervention Type PROCEDURE

Infusion of haploidentical donor, umbilical cord blood

Stem Cells Collections

Intervention Type PROCEDURE

Haploidentical cells will be T-cell depleted using the Miltenyi Clinimax device.

Fludarabine, Thiotepa, Antithymocyte globulin (ATG), and Total Body Irradiation (TBI)

Intervention Type DRUG

Fludarabine is given through the vein daily for 5 days. Thiotepa is given through the vein daily for 2 days. ATG is given through the vein every other day for 4 days. TBI is given twice a day for 3 days.

High Risk Patients not eligible for radiation

Group Type EXPERIMENTAL

Stem Cell Transplant

Intervention Type PROCEDURE

Infusion of haploidentical donor, umbilical cord blood

Stem Cells Collections

Intervention Type PROCEDURE

Haploidentical cells will be T-cell depleted using the Miltenyi Clinimax device.

Fludarabine, Busulfan, and ATG

Intervention Type DRUG

Fludarabine is given through the vein daily for 5 days. Busulfan is given through the vein daily for 4 days. ATG is given through the vein every other day for 4 days.

Interventions

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Fludarabine-Melphalan & Rabbit antithymocyte globulin (r-ATG)

Fludarabine is given through the vein daily for 5 days. Melphalan is given through the vein daily for 2 days. ATG is given every day in the vein for four days.

Intervention Type DRUG

Stem Cell Transplant

Infusion of haploidentical donor, umbilical cord blood

Intervention Type PROCEDURE

Stem Cells Collections

Haploidentical cells will be T-cell depleted using the Miltenyi Clinimax device.

Intervention Type PROCEDURE

Fludarabine, Thiotepa, Antithymocyte globulin (ATG), and Total Body Irradiation (TBI)

Fludarabine is given through the vein daily for 5 days. Thiotepa is given through the vein daily for 2 days. ATG is given through the vein every other day for 4 days. TBI is given twice a day for 3 days.

Intervention Type DRUG

Fludarabine, Busulfan, and ATG

Fludarabine is given through the vein daily for 5 days. Busulfan is given through the vein daily for 4 days. ATG is given through the vein every other day for 4 days.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

Patients will be eligible for this study if they have any one of the diseases that are known to be cured after allogeneic stem cell transplantation.

1. Relapsed or refractory acute leukemia (myeloid or lymphoid)
2. Acute leukemia in first remission at high-risk for recurrence
3. Chronic myelogenous leukemia in accelerated phase or blast-crisis
4. Chronic myelogenous leukemia in chronic phase
5. Recurrent or refractory malignant lymphoma or Hodgkin lymphoma
6. Chronic lymphocytic leukemia, relapsed or with poor prognostic features
7. Multiple myeloma
8. Myelodysplastic syndrome
9. Chronic myeloproliferative disease
10. Hemoglobinopathies
11. Aplastic anemia

Exclusion Criteria

1. Zubrod performance status \> 2
2. Life expectancy is severely limited by concomitant illness
3. Patients with severely decreased LVEF or impaired pulmonary function tests(PFT's)
4. Estimated Creatinine Clearance \<50 ml/min
5. Serum bilirubin\> 2.0 mg/dl or SGPT \>3 x upper limit of normal
6. Evidence of chronic active hepatitis or cirrhosis
7. HIV-positive
8. Patient is pregnant
9. Patient or guardian not able to sign informed consent
Minimum Eligible Age

1 Year

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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University of Chicago

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Hongtao Liu, M.D.

Role: PRINCIPAL_INVESTIGATOR

University of Chicago

Locations

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The University of Chicago

Chicago, Illinois, United States

Site Status

Countries

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United States

References

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Liu H, Rich ES, Godley L, Odenike O, Joseph L, Marino S, Kline J, Nguyen V, Cunningham J, Larson RA, del Cerro P, Schroeder L, Pape L, Stock W, Wickrema A, Artz AS, van Besien K. Reduced-intensity conditioning with combined haploidentical and cord blood transplantation results in rapid engraftment, low GVHD, and durable remissions. Blood. 2011 Dec 8;118(24):6438-45. doi: 10.1182/blood-2011-08-372508. Epub 2011 Oct 5.

Reference Type RESULT
PMID: 21976674 (View on PubMed)

van Besien K, Hari P, Zhang MJ, Liu HT, Stock W, Godley L, Odenike O, Larson R, Bishop M, Wickrema A, Gergis U, Mayer S, Shore T, Tsai S, Rhodes J, Cushing MM, Korman S, Artz A. Reduced intensity haplo plus single cord transplant compared to double cord transplant: improved engraftment and graft-versus-host disease-free, relapse-free survival. Haematologica. 2016 May;101(5):634-43. doi: 10.3324/haematol.2015.138594. Epub 2016 Feb 11.

Reference Type DERIVED
PMID: 26869630 (View on PubMed)

Provided Documents

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Document Type: Study Protocol and Statistical Analysis Plan

View Document

Other Identifiers

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14736B

Identifier Type: -

Identifier Source: org_study_id

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