HLA-haploidentical Hematopoietic Stem Cell Transplantation for Children and Adolescents With Acute Leukemia, Myelodysplastic Syndrome and Solid Tumors

NCT ID: NCT01509300

Last Updated: 2012-01-13

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Clinical Phase

PHASE1/PHASE2

Total Enrollment

10 participants

Study Classification

INTERVENTIONAL

Study Start Date

2012-01-31

Study Completion Date

2014-03-31

Brief Summary

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RATIONALE: Conditioning with total body irradiation (TBI) and fludarabine, cyclophosphamide and anti-thymocyte globulin may induce the engraftment cross the immunologic barrier in the setting of HLA-haploidentical allogeneic hematopoietic cell transplantation. In addition, T-cell depletion may contribute to prevent developing severe acute graft versus host disease (GVHD) in haploidentical transplantation.

PURPOSE: This phase I/II trial is to evaluate the safety and efficacy of TBI, fludarabine, cyclophosphamide and antithymocyte globulin with T-cell depleted graft from haploidentical donors in treating patients with acute leukemia and myelodysplastic syndrome.

Detailed Description

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Conditions

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Acute Leukemia Myelodysplastic Syndrome Solid Tumors

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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HAPLO

Group Type EXPERIMENTAL

anti-thymocyte globulin

Intervention Type BIOLOGICAL

On days -10 to -9

filgrastim

Intervention Type BIOLOGICAL

Beginning on day 4 and continuing until blood counts recover

Total body irradiation

Intervention Type RADIATION

2Gy D-6 to D-4

Fludarabine

Intervention Type DRUG

30mg/M2 once daily IV on days -8 to -4

cyclophosphamide

Intervention Type DRUG

60 mg/kg IV on day-3 and -2

Tacrolimus

Intervention Type DRUG

begin on 0

Mycophenolate mofetil

Intervention Type DRUG

begin on 0

Rituximab

Intervention Type DRUG

375mg/m2 on day +21

Interventions

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anti-thymocyte globulin

On days -10 to -9

Intervention Type BIOLOGICAL

filgrastim

Beginning on day 4 and continuing until blood counts recover

Intervention Type BIOLOGICAL

Total body irradiation

2Gy D-6 to D-4

Intervention Type RADIATION

Fludarabine

30mg/M2 once daily IV on days -8 to -4

Intervention Type DRUG

cyclophosphamide

60 mg/kg IV on day-3 and -2

Intervention Type DRUG

Tacrolimus

begin on 0

Intervention Type DRUG

Mycophenolate mofetil

begin on 0

Intervention Type DRUG

Rituximab

375mg/m2 on day +21

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Disease characteristics

* Acute lymphoblastic leukemia (first remission, high risk; beyond first remission; refractory)
* Acute myeloblastic leukemia (first remission, high risk; beyond first remission; refractory)
* Myelodysplastic syndrome
* Solid tumors (Refractory/relapse)
2. No HLA-identical family member or closely matched (8 or 7 of 8 HLA-locus match) unrelated marrow donor available
3. HLA-haploidentical related donor available

Exclusion Criteria

1. Active fungal infections
2. HIV positive
3. Pregnant or nursing
Maximum Eligible Age

21 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Asan Medical Center

OTHER

Sponsor Role lead

Responsible Party

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Ho Joon Im

Principal investigator

Responsibility Role PRINCIPAL_INVESTIGATOR

Principal Investigators

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Ho Joon Im, MD & PhD

Role: PRINCIPAL_INVESTIGATOR

Asan Medical Center

Locations

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Asan Medical Center

Seoul, , South Korea

Site Status RECRUITING

Countries

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South Korea

Central Contacts

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Ho Joon Im, MD & PhD

Role: CONTACT

82-2-3010-3371

Facility Contacts

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Ho Joon Im, MD & PhD

Role: primary

82-2-3010-3371

References

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Koh KN, Im HJ, Kim BE, Choi ES, Jang S, Kwon SW, Park CJ, Seo JJ. Haploidentical haematopoietic stem cell transplantation using CD3 or CD3/CD19 depletion and conditioning with fludarabine, cyclophosphamide and antithymocyte globulin for acquired severe aplastic anaemia. Br J Haematol. 2012 Apr;157(1):139-42. doi: 10.1111/j.1365-2141.2011.08924.x. Epub 2011 Nov 5. No abstract available.

Reference Type BACKGROUND
PMID: 22055111 (View on PubMed)

Lang P, Handgretinger R. Haploidentical SCT in children: an update and future perspectives. Bone Marrow Transplant. 2008 Oct;42 Suppl 2:S54-9. doi: 10.1038/bmt.2008.285.

Reference Type BACKGROUND
PMID: 18978746 (View on PubMed)

Im HJ, Koh KN, Suh JK, Lee SW, Choi ES, Jang S, Kwon SW, Park CJ, Seo JJ. Refinement of treatment strategies in ex vivo T-cell-depleted haploidentical SCT for pediatric patients. Bone Marrow Transplant. 2015 Feb;50(2):225-31. doi: 10.1038/bmt.2014.232. Epub 2014 Oct 13.

Reference Type DERIVED
PMID: 25310303 (View on PubMed)

Other Identifiers

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AMCPHO-SCT0902

Identifier Type: -

Identifier Source: org_study_id

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