Neulasta in Type 1 Diabetes

NCT ID: NCT00662519

Last Updated: 2015-04-09

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE1

Total Enrollment

21 participants

Study Classification

INTERVENTIONAL

Study Start Date

2008-04-30

Study Completion Date

2014-03-31

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

The primary purpose of this study is to find out if giving a 12 week course of Neulasta (Pegylated granulocyte colony stimulating factor (GCSF)) to people with type 1 diabetes (T1D) is safe. The secondary purpose of this research study is to determin if giving GCSF to patients with T1D changes the immune system or preserves insulin production.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

As a participant in this study the following will happen:

Blood test, Mixed meal Tolerance Test (MMT) to find out how much C-peptide is being produced, Human Leukocyte Antigen (HLA) test, Hemoglobin A1C (HbA1c) test for overall blood sugar control, and randomized to either receive the 12 week course of Neulasta (Pegylated granulocyte colony stimulating factor (GCSF)) or a placebo (no medication).

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Type 1 Diabetes

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Neulasta

Subjects will receive Neulasta subcutaneously every 2 weeks for 12 weeks (6 doses). In addition, the following test will be done: Mixed Meal Tolerance Test (MMTT), Hemoglobin A1C (HbA1c) blood test, and Human Leukocyte Antigen (HLA) DNA Test.

Group Type EXPERIMENTAL

Neulasta (Pegylated)

Intervention Type DRUG

Subjects will receive 6mg/dose given every 2 weeks for 12 weeks. Subjects less than 45kg will receive 100mcg/kg/dose every 2 weeks for 12 weeks.

Mixed Meal Tolerance Test (MMTT)

Intervention Type DIETARY_SUPPLEMENT

This is a 2 hour test to find out how much C-peptide is being produced. C-peptide is used to measure the insulin being made by the cells of the pancreas. Both groups will have this test performed.

Blood test

Intervention Type OTHER

HbA1c is a blood test that measures the average blood sugar control and will be performed in both groups.

DNA Test

Intervention Type OTHER

The HLA test looks at the different chromosomes (DNA) for diabetes and will be performed in both groups.

Placebo

Placebo injections will be given in identical volumes in identical syringes in the identical subcutaneous manner. In addition, the following test will be done: Mixed Meal Tolerance Test (MMTT), Hemoglobin A1C (HbA1c) blood test, and Human Leukocyte Antigen (HLA) DNA Test.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo injections will be given in identical volumes in identical syringes in the identical subcutaneous manner. 6mg/dose given every 2 weeks for 12 weeks. Subjects less than 45kg will receive 100mcg/kg/dose every 2 weeks for 12 weeks.

Mixed Meal Tolerance Test (MMTT)

Intervention Type DIETARY_SUPPLEMENT

This is a 2 hour test to find out how much C-peptide is being produced. C-peptide is used to measure the insulin being made by the cells of the pancreas. Both groups will have this test performed.

Blood test

Intervention Type OTHER

HbA1c is a blood test that measures the average blood sugar control and will be performed in both groups.

DNA Test

Intervention Type OTHER

The HLA test looks at the different chromosomes (DNA) for diabetes and will be performed in both groups.

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Neulasta (Pegylated)

Subjects will receive 6mg/dose given every 2 weeks for 12 weeks. Subjects less than 45kg will receive 100mcg/kg/dose every 2 weeks for 12 weeks.

Intervention Type DRUG

Placebo

Placebo injections will be given in identical volumes in identical syringes in the identical subcutaneous manner. 6mg/dose given every 2 weeks for 12 weeks. Subjects less than 45kg will receive 100mcg/kg/dose every 2 weeks for 12 weeks.

Intervention Type DRUG

Mixed Meal Tolerance Test (MMTT)

This is a 2 hour test to find out how much C-peptide is being produced. C-peptide is used to measure the insulin being made by the cells of the pancreas. Both groups will have this test performed.

Intervention Type DIETARY_SUPPLEMENT

Blood test

HbA1c is a blood test that measures the average blood sugar control and will be performed in both groups.

Intervention Type OTHER

DNA Test

The HLA test looks at the different chromosomes (DNA) for diabetes and will be performed in both groups.

Intervention Type OTHER

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

Pegylated granulocyte colony stimulating factor (GCSF) Saline Hemoglobin A1C (HbA1c) Human Leukocyte Antigen (HLA)

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Must be \> 12 years old and have a confirmed diagnosis of "recent onset T1D" as defined by:
* T1D for \< 6 months,
* Stimulated C-peptide ≥ 0.2 pmol/ml
* Presence of at least one diabetes-related autoantibody (e.g., GAD, IA-2, IAA, ICA)
* Normal screening values for CBC
* Willing to comply with intensive diabetes management
* No history of allergy to GCSF
* Females having reproductive potential must be willing to avoid pregnancy and have a negative pregnancy test

Exclusion Criteria

* Known hypersensitivity to E.Coli-derived proteins, pegfilgrastim, Filgrastim, or any other component of the product
* Chronic use of steroids or other immunosuppressive agents
* Active infection
* Inability to maintain intensive diabetes management
* Pregnancy
* History of malignancy
* Currently participating in another type 1 diabetes treatment study.
* Use of non-insulin pharmaceuticals that affect glycemic control
Minimum Eligible Age

12 Years

Maximum Eligible Age

45 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

Yes

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Juvenile Diabetes Research Foundation

OTHER

Sponsor Role collaborator

National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)

NIH

Sponsor Role collaborator

University of Florida

OTHER

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Michael J Haller, MD

Role: PRINCIPAL_INVESTIGATOR

University of Florida

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

University of Florida

Gainesville, Florida, United States

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

JDRF 11-2007-825

Identifier Type: OTHER_GRANT

Identifier Source: secondary_id

1R21DK078863-01A1

Identifier Type: NIH

Identifier Source: secondary_id

View Link

GCRC 683

Identifier Type: OTHER_GRANT

Identifier Source: secondary_id

UF IRB 280-2006

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.

Teplizumab in Pediatric Stage 2 Type 1 Diabetes
NCT05757713 ACTIVE_NOT_RECRUITING PHASE4