Teplizumab in Pediatric Stage 2 Type 1 Diabetes

NCT ID: NCT05757713

Last Updated: 2024-09-19

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE4

Total Enrollment

20 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-07-25

Study Completion Date

2026-08-27

Brief Summary

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The purpose of this study is to assess the safety and pharmacokinetics (PK) of teplizumab in participants with Stage 2 type 1 diabetes who are \<8 years of age.

Detailed Description

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This is a single-arm, non-randomized, open-label, multicenter study in the U.S. to assess the safety and pharmacokinetics of teplizumab in pediatric participants with Stage 2 type 1 diabetes (T1D) (two T1D-related autoantibodies and dysglycemia) who are 0 to \<8 years of age. Anti-drug antibodies/neutralizing antibodies (ADA/NAb) will also be assessed.

Approximately 20 participants will be enrolled. The regimen consists of an intravenous infusion of teplizumab once daily for 14 consecutive days. The study duration for each individual may last up to approximately 26 months.

The safety, tolerability, PK, ADA, and T1D clinical feature data will be summarized using descriptive statistics.

Conditions

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Diabetes Mellitus, Type 1

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Single arm, non-randomized, open-label, multi-center study
Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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teplizumab injection

teplizumab injection, sterile solution for intravenous use

Group Type EXPERIMENTAL

teplizumab

Intervention Type BIOLOGICAL

CD3-directed humanized monoclonal antibody

Interventions

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teplizumab

CD3-directed humanized monoclonal antibody

Intervention Type BIOLOGICAL

Eligibility Criteria

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Inclusion Criteria

1. Participant is a male or female 0 to \< 8 years of age, inclusive, at Day 1
2. Participant has Stage 2 T1D (two T1D-related autoantibodies and dysglycemia)

Exclusion Criteria

1. Participant has any autoimmune disease other than T1D with the exception of stable thyroid or celiac disease
2. Has an active infection and/or fever
3. Has a history of or serologic evidence at screening of current or past infection with human immunodeficiency virus (HIV), hepatitis B virus (HBV), or hepatitis C virus (HCV).
4. Has any condition that, in the opinion of the Investigator, would interfere with the study conduct or the safety of the participant.
Minimum Eligible Age

0 Years

Maximum Eligible Age

7 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Provention Bio, a Sanofi Company

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Sciences & Operations

Role: STUDY_DIRECTOR

Sanofi

Locations

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UCSF Medical Center Site Number : 107

San Francisco, California, United States

Site Status

Barbara Davis Center for Diabetes Site Number : 102

Aurora, Colorado, United States

Site Status

Yale University School of Medicine Site Number : 101

New Haven, Connecticut, United States

Site Status

Centricity Research Site Number : 104

Columbus, Georgia, United States

Site Status

Indianapolis University Health Riley Hospital for Children Site Number : 110

Indianapolis, Indiana, United States

Site Status

UBMD Pediactrics Site Number : 105

Buffalo, New York, United States

Site Status

Children's Hospital of Philadelphia Site Number : 108

Philadelphia, Pennsylvania, United States

Site Status

Sanford Diabetes and Thyroid Clinic Site Number : 106

Sioux Falls, South Dakota, United States

Site Status

Vanderbilt Univerity Medical Center Site Number : 109

Nashville, Tennessee, United States

Site Status

MulitCare Institute for Research & Innovation Site Number : 103

Tacoma, Washington, United States

Site Status

Countries

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United States

References

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Novograd J, Frishman WH. Teplizumab Therapy to Delay the Onset of Type 1 Diabetes. Cardiol Rev. 2024 Nov-Dec 01;32(6):572-576. doi: 10.1097/CRD.0000000000000563. Epub 2023 May 9.

Reference Type DERIVED
PMID: 37158990 (View on PubMed)

Other Identifiers

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SFY18116

Identifier Type: OTHER

Identifier Source: secondary_id

PRV-031-005

Identifier Type: -

Identifier Source: org_study_id

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