Study to Assess Darbepoetin Alfa Dosing for the Correction of Anemia in Pediatric Patients With Chronic Kidney Disease

NCT ID: NCT00436748

Last Updated: 2022-11-29

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

View full results

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

116 participants

Study Classification

INTERVENTIONAL

Study Start Date

2008-09-16

Study Completion Date

2014-03-03

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

The primary objectives of this study are the following:

1. To test if the proportion of participants achieving a hemoglobin value greater than or equal to 10.0 g/dL at any time point after the first dose during the study is greater than 0.8 when administered de novo darbepoetin alfa once a week (QW) for treatment of anemia in pediatric patients with chronic kidney disease receiving and not receiving dialysis, and
2. To test if the proportion of participants achieving a hemoglobin value greater than or equal to 10.0 g/dL at any time point after the first dose during the study is greater than 0.8 when administered de novo darbepoetin alfa every 2 weeks (Q2W) for treatment of anemia in pediatric patients with chronic kidney disease receiving and not receiving dialysis.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Anemia Chronic Kidney Disease Kidney Disease

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Darbepoetin Alfa QW

Participants received darbepoetin alfa once a week (QW) for 24 weeks. The initial dose was 0.45 μg/kg; thereafter, active doses were administered to achieve and then maintain hemoglobin levels within a target range of 10.0 to 12.0 g/dL. Participants not on dialysis or who were receiving peritoneal dialysis were administered darbepoetin alfa subcutaneously; participants receiving hemodialysis were administered darbepoetin alfa intravenously.

Group Type EXPERIMENTAL

Darbepoetin Alfa

Intervention Type DRUG

Administered by subcutaneous or intravenous injection

Darbepoetin Alfa Q2W

Participants received darbepoetin alfa every 2 weeks (Q2W) and a placebo every other 2 weeks to maintain the blind for 24 weeks. The initial dose was 0.75 μg/kg; thereafter, active doses were administered to achieve and then maintain hemoglobin levels within a target range of 10.0 to 12.0 g/dL. Participants not on dialysis or who were receiving peritoneal dialysis were administered darbepoetin alfa subcutaneously; participants receiving hemodialysis were administered darbepoetin alfa intravenously.

Group Type EXPERIMENTAL

Darbepoetin Alfa

Intervention Type DRUG

Administered by subcutaneous or intravenous injection

Placebo

Intervention Type DRUG

Matching placebo solution for subcutaneous or intravenous injection to maintain the blind in the Q2W arm.

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Darbepoetin Alfa

Administered by subcutaneous or intravenous injection

Intervention Type DRUG

Placebo

Matching placebo solution for subcutaneous or intravenous injection to maintain the blind in the Q2W arm.

Intervention Type DRUG

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

Aranesp®

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Current diagnosis of Chronic Kidney Disease, either receiving or not receiving dialysis
* Anemic, with two consecutive screening hemoglobin values drawn at least 7 days apart \< 11.0 g/dL
* Transferrin saturation (Tsat) greater than or equal to 20%

Exclusion Criteria

* Any erythropoiesis stimulating agent (ESA) use within 12 weeks prior to randomization
* other hematologic disorders
* upper or lower gastrointenstinal bleeding within 6 months prior to randomization
* uncontrolled hypertension
* prior history (within 12 weeks prior to randomization) of acute myocardial ischemia, hospitalization for congestive heart failure, myocardial infarction, stroke or transient ischemic attack
* prior history (within 6 months prior to randomization) of thromboembolism
Minimum Eligible Age

1 Year

Maximum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Amgen

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

MD

Role: STUDY_DIRECTOR

Amgen

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Research Site

Birmingham, Alabama, United States

Site Status

Research Site

Los Angeles, California, United States

Site Status

Research Site

Los Angeles, California, United States

Site Status

Research Site

San Diego, California, United States

Site Status

Research Site

San Francisco, California, United States

Site Status

Research Site

Stanford, California, United States

Site Status

Research Site

Washington D.C., District of Columbia, United States

Site Status

Research Site

Gainesville, Florida, United States

Site Status

Research Site

Miami, Florida, United States

Site Status

Research Site

Orlando, Florida, United States

Site Status

Research Site

Boise, Idaho, United States

Site Status

Research Site

Chicago, Illinois, United States

Site Status

Research Site

Iowa City, Iowa, United States

Site Status

Research Site

Louisville, Kentucky, United States

Site Status

Research Site

New Orleans, Louisiana, United States

Site Status

Research Site

Baltimore, Maryland, United States

Site Status

Research Site

Boston, Massachusetts, United States

Site Status

Research Site

Kansas City, Missouri, United States

Site Status

Research Site

Livingston, New Jersey, United States

Site Status

Research Site

New Brunswick, New Jersey, United States

Site Status

Research Site

Albuquerque, New Mexico, United States

Site Status

Research Site

Buffalo, New York, United States

Site Status

Research Site

New Hyde Park, New York, United States

Site Status

Research Site

New York, New York, United States

Site Status

Research Site

The Bronx, New York, United States

Site Status

Research Site

Valhalla, New York, United States

Site Status

Research Site

Charlotte, North Carolina, United States

Site Status

Research Site

Akron, Ohio, United States

Site Status

Research Site

Cincinnati, Ohio, United States

Site Status

Research Site

Cleveland, Ohio, United States

Site Status

Research Site

Cleveland, Ohio, United States

Site Status

Research Site

Columbus, Ohio, United States

Site Status

Research Site

Portland, Oregon, United States

Site Status

Research Site

Portland, Oregon, United States

Site Status

Research Site

Philadelphia, Pennsylvania, United States

Site Status

Research Site

Dallas, Texas, United States

Site Status

Research Site

Houston, Texas, United States

Site Status

Research Site

San Antonio, Texas, United States

Site Status

Research Site

Charlottesville, Virginia, United States

Site Status

Research Site

Norfolk, Virginia, United States

Site Status

Research Site

Richmond, Virginia, United States

Site Status

Research Site

Seattle, Washington, United States

Site Status

Research Site

Edegem, , Belgium

Site Status

Research Site

Ghent, , Belgium

Site Status

Research Site

Leuven, , Belgium

Site Status

Research Site

Jūrmala, , Latvia

Site Status

Research Site

Vilnius, , Lithuania

Site Status

Research Site

Mexico City, Mexico City, Mexico

Site Status

Research Site

Aguascalientes, , Mexico

Site Status

Research Site

Chihuahua City, , Mexico

Site Status

Research Site

Puebla City, , Mexico

Site Status

Research Site

Gdansk, , Poland

Site Status

Research Site

Lodz, , Poland

Site Status

Research Site

Szczecin, , Poland

Site Status

Research Site

San Juan, , Puerto Rico

Site Status

Research Site

Krasnodar, , Russia

Site Status

Research Site

Moscow, , Russia

Site Status

Research Site

Moscow, , Russia

Site Status

Research Site

Orenburg, , Russia

Site Status

Research Site

Saint Petersburg, , Russia

Site Status

Research Site

Samara, , Russia

Site Status

Research Site

Banská Bystrica, , Slovakia

Site Status

Research Site

Bratislava, , Slovakia

Site Status

Research Site

Košice, , Slovakia

Site Status

Research Site

Birmingham, , United Kingdom

Site Status

Research Site

Leeds, , United Kingdom

Site Status

Research Site

London, , United Kingdom

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Belgium Latvia Lithuania Mexico Poland Puerto Rico Russia Slovakia United Kingdom

References

Explore related publications, articles, or registry entries linked to this study.

Warady BA, Barcia J, Benador N, Jankauskiene A, Olson K, Podracka L, Shavkin A, Srivaths P, Wong CJ, Petersen J. De novo weekly and biweekly darbepoetin alfa dosing in pediatric patients with chronic kidney disease. Pediatr Nephrol. 2018 Jan;33(1):125-137. doi: 10.1007/s00467-017-3758-5. Epub 2017 Aug 17.

Reference Type BACKGROUND
PMID: 28815341 (View on PubMed)

Chung EY, Palmer SC, Saglimbene VM, Craig JC, Tonelli M, Strippoli GF. Erythropoiesis-stimulating agents for anaemia in adults with chronic kidney disease: a network meta-analysis. Cochrane Database Syst Rev. 2023 Feb 13;2(2):CD010590. doi: 10.1002/14651858.CD010590.pub3.

Reference Type DERIVED
PMID: 36791280 (View on PubMed)

Related Links

Access external resources that provide additional context or updates about the study.

http://www.amgentrials.com

AmgenTrials clinical trials website

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

20050256

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.