A Study of Enlicitide Decanoate (MK-0616, an Oral PCSK9 Inhibitor) in Children and Adolescents With Heterozygous Familial Hypercholesterolemia (MK-0616-029)

NCT ID: NCT07058077

Last Updated: 2025-11-12

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2/PHASE3

Total Enrollment

153 participants

Study Classification

INTERVENTIONAL

Study Start Date

2025-08-21

Study Completion Date

2037-01-24

Brief Summary

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This study is designed to learn if enlicitide decanoate is safe and effective to treat children and adolescents with heterozygous familial hypercholesterolemia (HeFH) and high amounts of low-density lipoprotein cholesterol (LDL-C) in the blood.

The goals of this study are to learn about the safety of enlicitide and if children tolerate it, what happens to enlicitide in a child's body over time, and if enlicitide works to lower cholesterol levels in children more than a placebo.

Detailed Description

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Conditions

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Heterozygous Familial Hypercholesterolemia (HeFH)

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

There are two parts of the study. Part A is a non randomized single treatment group. Part B is randomized parallel treatment groups. Participants who complete either part are then eligible to enroll in an open label extension (single group).
Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors
Part A and the extension period are open-label. Part B is double-blinded.

Study Groups

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Part A: Enlicitide Decanoate

Participants receive enlicitide decanoate orally once daily (QD) at a dosage determined by age for up to 2 weeks.

Group Type EXPERIMENTAL

Enlicitide Decanoate

Intervention Type DRUG

Enlicitide decanoate taken by mouth

Part B: Enlicitide Decanoate

Participants receive enlicitide decanoate QD at a dosage determined by age for up to 24 weeks.

Group Type EXPERIMENTAL

Enlicitide Decanoate

Intervention Type DRUG

Enlicitide decanoate taken by mouth

Part B: Placebo

Participants receive placebo orally QD for up to 24 weeks.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo tablet matched to enlicitide decanoate taken by mouth

Open-Label Extension: Enlicitide Decanoate

Participants who complete either Part A or Part B may enroll in this open-label extension arm. Participants in the extension arm receive enlicitide decanoate QD at a dosage determined by age for up to 3 years.

Group Type EXPERIMENTAL

Enlicitide Decanoate

Intervention Type DRUG

Enlicitide decanoate taken by mouth

Interventions

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Enlicitide Decanoate

Enlicitide decanoate taken by mouth

Intervention Type DRUG

Placebo

Placebo tablet matched to enlicitide decanoate taken by mouth

Intervention Type DRUG

Other Intervention Names

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MK-0616 Enlicitide

Eligibility Criteria

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Inclusion Criteria

* Has possible or definite diagnosis of HeFH based on a locally accepted diagnostic algorithm or diagnosis by genetic testing results
* Has a fasted LDL-C value (evaluated by the central laboratory) that is ≥130 mg/dL
* Is receiving either an optimized daily dose of statin (± nonstatin LLT); or a nonstatin LLT with documented intolerance to at least 2 different statins or refusal of statin therapy by the participant or legally acceptable representative
* Is on a stable dose of all background LLTs for at least 30 days prior to screening, with no medication or dose changes planned during participation in Part A or Part B

Exclusion Criteria

* Has a history of homozygous FH based on genetic or clinical criteria, or history of known compound heterozygous FH, or double heterozygous FH
* Has a history of nephrotic syndrome
* Has any clinically significant malabsorption condition based on principal investigator assessment
* Was previously treated/is being treated with certain other cholesterol lowering medications, including proprotein convertase subtilisin/kexin type 9 (PCSK9) inhibitors without adequate washout
Minimum Eligible Age

6 Years

Maximum Eligible Age

17 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Merck Sharp & Dohme LLC

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Medical Director

Role: STUDY_DIRECTOR

Merck Sharp & Dohme LLC

Locations

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Nemours/Alfred I. duPont Hospital for Children ( Site 0001)

Wilmington, Delaware, United States

Site Status RECRUITING

Children's National Medical Center ( Site 0015)

Washington D.C., District of Columbia, United States

Site Status RECRUITING

Excel Medical Clinical Trials ( Site 0008)

Boca Raton, Florida, United States

Site Status RECRUITING

Children's Healthcare of Atlanta Cardiology ( Site 0026)

Atlanta, Georgia, United States

Site Status RECRUITING

New Zealand Clinical Research (Christchurch) ( Site 1700)

Christchurch, Canterbury, New Zealand

Site Status RECRUITING

Countries

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United States New Zealand

Central Contacts

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Toll Free Number

Role: CONTACT

Phone: 1-888-577-8839

Email: [email protected]

Facility Contacts

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Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Related Links

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http://www.merckclinicaltrials.com

Merck Clinical Trials Information

Other Identifiers

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U1111-1314-5796

Identifier Type: REGISTRY

Identifier Source: secondary_id

2024-519068-42-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

0616-029

Identifier Type: -

Identifier Source: org_study_id