A Study to Assess the Safety and Tolerability of ZX008 in Children and Young Adults With Dravet Syndrome or Lennox Gastaut Syndrome Currently Taking Cannabidiol

NCT ID: NCT03467113

Last Updated: 2023-12-01

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1

Total Enrollment

9 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-01-19

Study Completion Date

2020-06-24

Brief Summary

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This is an open label study to evaluate the safety of ZX008 (fenfluramine) in patients with Dravet syndrome (DS) or Lennox Gastaut syndrome (LGS) who are being administered cannabidiol (CBD).

Detailed Description

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Conditions

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Dravet Syndrome Lennox Gastaut Syndrome

Keywords

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Dravet Syndrome LGS

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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ZX008 0.2 to 0.8 mg/kg/day

ZX008 is supplied as an oral solution in a concentration of 2.5 mg/mL. Subjects will receive open-label ZX008 (flexible dosing 0.2 mg/kg/day to 0.8 mg/kg/day)

Group Type EXPERIMENTAL

ZX008 0.2 to 0.8 mg/kg/day

Intervention Type DRUG

ZX008 drug is an oral aqueous solution of fenfluramine hydrochloride. The product is sugar free.

Cannabidiol

Intervention Type DRUG

Cannabidiol

Interventions

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ZX008 0.2 to 0.8 mg/kg/day

ZX008 drug is an oral aqueous solution of fenfluramine hydrochloride. The product is sugar free.

Intervention Type DRUG

Cannabidiol

Cannabidiol

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Subject has a clinical diagnosis of DS or LGS, where convulsive seizures (generalized tonic clonic seizures, tonic seizures, atonic seizures, tonic/atonic seizures, focal seizures with clear observable motor signs) are not completely controlled by current AEDs.
* All medications or interventions for epilepsy (including ketogenic diet \[KD\] and vagal nerve stimulation \[VNS\]) must be stable for at least 4 weeks prior to first ZX008 dose and are expected to remain stable throughout the study.
* Subjects must be taking a stable dose of CBD for at least 4 weeks prior to first ZX008 dose.
* Subject's source of CBD is expected to be consistent for at least 3 months during study participation.

Exclusion Criteria

* Subject has current or past history of cardiovascular or cerebrovascular disease, myocardial infarction or stroke.
* Subject with current cardiac valvulopathy or pulmonary hypertension that the Investigator, parent/caregiver, Independent Cardiac Advisory Board, Independent Data and Safety Monitoring Committee, or sponsor deems clinically significant.
* Subject has a current or past history of glaucoma.
Minimum Eligible Age

2 Years

Maximum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Zogenix International Limited, Inc., a subsidiary of Zogenix, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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PANDA Neurology/CIRCA

Atlanta, Georgia, United States

Site Status

MultiCare Institute for Research & Innovation

Tacoma, Washington, United States

Site Status

Countries

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United States

Other Identifiers

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ZX008-1602

Identifier Type: -

Identifier Source: org_study_id