Dose Range Finding, Efficacy, and Safety Study of Nebulized CSL787 in Adults With Non-cystic Fibrosis Bronchiectasis (NCFB)

NCT ID: NCT07048262

Last Updated: 2025-11-10

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

450 participants

Study Classification

INTERVENTIONAL

Study Start Date

2025-09-03

Study Completion Date

2028-03-28

Brief Summary

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This study is a phase 2b, multicenter, randomized, double-blind, placebo-controlled, parallel-group, dose range finding study designed to explore the efficacy, safety, and tolerability of 2 active treatment regimens of CSL787 (immunoglobulin G \[IgG\] inhalation solution) compared with placebo over a period of 6 to 12 months independent of the occurrence of pulmonary exacerbations.

The primary aim of the study is to characterize the overall effect of CSL787 as well as the dose response of 2 active treatment regimens of inhaled CSL787 administered to participants with NCFB toward prolonging the TTF exacerbation.

Detailed Description

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Conditions

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Non-cystic Fibrosis Bronchiectasis

Keywords

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Chronic respiratory disease Inflammation Chronic bacterial infection

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

This is a randomized, double-blind, parallel-group, placebo-controlled study.
Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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CSL787 High Dose

Participants in this arm will receive a high dose of CSL787.

Group Type EXPERIMENTAL

CSL787

Intervention Type BIOLOGICAL

CSL787 high or low doses once daily (QD) will be administered via inhalation over a period of 6 to 12 months.

Nebulizer

Intervention Type DEVICE

The nebulizer is a CE-marked device.

CSL787 Low Dose

Participants in this arm will receive a low dose of CSL787.

Group Type EXPERIMENTAL

CSL787

Intervention Type BIOLOGICAL

CSL787 high or low doses once daily (QD) will be administered via inhalation over a period of 6 to 12 months.

Nebulizer

Intervention Type DEVICE

The nebulizer is a CE-marked device.

Placebo

Participants in this arm will receive placebo.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Participants will receive a matching volume of placebo QD over a period of 6 to 12 months.

Nebulizer

Intervention Type DEVICE

The nebulizer is a CE-marked device.

Interventions

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CSL787

CSL787 high or low doses once daily (QD) will be administered via inhalation over a period of 6 to 12 months.

Intervention Type BIOLOGICAL

Placebo

Participants will receive a matching volume of placebo QD over a period of 6 to 12 months.

Intervention Type DRUG

Nebulizer

The nebulizer is a CE-marked device.

Intervention Type DEVICE

Eligibility Criteria

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Inclusion Criteria

* Adult between the ages of 18 to 85 years
* Primary diagnosis of NCFB confirmed by chest computed tomography (CT) scan, where bronchiectasis has been documented by a radiologist. Diagnosis in the medical records based on historical scans is acceptable if the chest CT scan confirming the participant's NCFB diagnosis was performed within 12 months before enrollment. Participants for whom no chest CT scan results are available within the previous 12 months will undergo a chest CT scan during the Screening Period
* Exacerbation history within the previous 1 year defined as either 1 of the following:
* \>= 2 documented exacerbations requiring oral and/or intravenous (IV) antibiotic therapy to treat a pulmonary infection.

OR

* 1 documented exacerbation requiring oral and/or IV antibiotic therapy to treat a pulmonary infection and a St. George's Respiratory Questionnaire (SGRQ) Symptoms score of \> 40 at Screening.
* Note: Other medications to treat NCFB such as: oral macrolides, or dipeptidyl peptidase-1 (DPP-1) inhibitors are allowed, provided \>= 1 historical exacerbation occurred while on the medication for \>= 3 months at a stable dose.
* Postbronchodilator percentage of the predicted normal forced expiratory volume in 1 second of expiration \[FEV1% predicted\] \> 35% and forced expiratory volume in 1 second (FEV1) \>= 1 liter (L) obtained in accordance with American Thoracic Society (ATS) / European Respiratory Society (ERS) standards for spirometry during Screening and at Baseline.

Exclusion Criteria

* History of bronchospasm in response to inhaled therapies including inhaled antibiotics
* Known or suspected hypersensitivity, or other severe reactions, to the investigational product (IP), to any excipients of the IP, or to other immunoglobulin.
* Primary diagnosis of other pulmonary disorders, including chronic obstructive pulmonary disease (COPD) asthma or, diffuse panbronchiolitis (DPB), as determined by the investigator.
* Pulmonary exacerbation requiring antibiotic therapy within the 4 weeks before Baseline.
Minimum Eligible Age

18 Years

Maximum Eligible Age

85 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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CSL Behring

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Study Director

Role: STUDY_DIRECTOR

CSL Behring

Locations

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The Prince Charles Hospital

Queensland, , Australia

Site Status RECRUITING

Westmead Hospital

Westmead, , Australia

Site Status RECRUITING

Fukuoka University Chikushi Hopsital

Chikushino-shi, , Japan

Site Status RECRUITING

Kyusho Central Hospital of the Mutual Aid Association of Public School Teachers

Fukuoka, , Japan

Site Status RECRUITING

Ibaraki Prefectural Central Hospital

Ibaraki, , Japan

Site Status RECRUITING

Kazunori Tobino Iizuka Hospital

Iizuka-shi, , Japan

Site Status RECRUITING

National Hospital Organization Minami Kyoto Hospital

Kyoto, , Japan

Site Status RECRUITING

Matsusaka Municipal Hospital

Mie, , Japan

Site Status RECRUITING

National Hospital Organization Kinki Chuo Chest Medical Center

Osaka, , Japan

Site Status RECRUITING

Shimonoseki City Hospital

Shimonoseki-shi, , Japan

Site Status RECRUITING

Japan Anti-Tuberculosis Association, Fukujuji Hospital

Tokyo, , Japan

Site Status RECRUITING

Keio University Hospital

Tokyo, , Japan

Site Status RECRUITING

National Hospital Organization Mie Chuo Medical Center

Tsu, , Japan

Site Status RECRUITING

Countries

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Australia Japan

Central Contacts

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Trial Registration Coordinator

Role: CONTACT

Phone: +1 610-878-4697

Email: [email protected]

Other Identifiers

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2024-518821-13-00

Identifier Type: CTIS

Identifier Source: secondary_id

CSL787_2001

Identifier Type: -

Identifier Source: org_study_id