Study of Choline Chloride for Injection in Adolescent and Adult Patients With Intestinal Failure Receiving Long Term Parenteral Support

NCT ID: NCT06910943

Last Updated: 2026-01-27

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2/PHASE3

Total Enrollment

129 participants

Study Classification

INTERVENTIONAL

Study Start Date

2025-12-10

Study Completion Date

2028-06-30

Brief Summary

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TARA-001-301 is a Phase 2b/3 randomized Open-Label Dose-Selection study with an Open-Label Extension and randomized Double-Blind, Placebo-Controlled Study with Open-Label Extension to investigate the safety and efficacy of Choline Chloride for Injection (Low Dose and High Dose) versus Placebo in adolescents (ages 12 to \< 18 years of age) and adults (≥ 18 years of age) with intestinal failure receiving long-term PS when oral or enteral nutrition is not possible, insufficient, or contraindicated.

Participants will be enrolled in one of 2 parts, each part will be followed by an open-label extension period of approximately a year.

Part 1: Open-Label Dose-Selection Phase Part 2: Double-Blind, Placebo-Controlled Phase

The purpose of the Open-Label Dose-Selection Phase is to evaluate the safety, tolerability, how Choline Chloride for Injection (study drug) is distributed in the body, and to select 2 of 3 doses for testing in the Double-Blind, Placebo-Controlled Phase.

The purpose of the Double-Blind, Placebo-Controlled Phase is to assess the safety of the study drug and how well the study drug works at the 2 selected dose levels.

Detailed Description

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Conditions

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Choline Deficiency Liver Injury

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Outcome Assessors
The Open-Label Dose Selection Phase will be open label, and the Double-Blind, Placebo-Controlled Phase will be double blind. The Open Label Extension Phase will be open label.

Study Groups

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Open-Label, Dose-Selection: Dose 1

Group Type EXPERIMENTAL

Choline Chloride for Injection

Intervention Type DRUG

Intravenous use

Open-Label, Dose-Selection: Dose 2

Group Type EXPERIMENTAL

Choline Chloride for Injection

Intervention Type DRUG

Intravenous use

Open-Label, Dose-Selection: Dose 3

Group Type EXPERIMENTAL

Choline Chloride for Injection

Intervention Type DRUG

Intravenous use

Double-Blind, Placebo-Controlled: High Dose

Group Type EXPERIMENTAL

Choline Chloride for Injection

Intervention Type DRUG

Intravenous use

Double-Blind, Placebo-Controlled: Low Dose

Group Type EXPERIMENTAL

Choline Chloride for Injection

Intervention Type DRUG

Intravenous use

Double-Blind, Placebo-Controlled: Placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Intravenous use

Open Label Extension: High Dose

Group Type EXPERIMENTAL

Choline Chloride for Injection

Intervention Type DRUG

Intravenous use

Open Label Extension: Low Dose

Group Type EXPERIMENTAL

Choline Chloride for Injection

Intervention Type DRUG

Intravenous use

Interventions

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Choline Chloride for Injection

Intravenous use

Intervention Type DRUG

Placebo

Intravenous use

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Male or female 12 years of age or older at the time of signing the informed consent
* Individuals who have voluntarily given written informed consent after the nature of the study has been explained according to applicable requirements, prior to study entry
* Individuals with intestinal failure receiving long-term PS when oral or enteral nutrition is not possible, insufficient, or contraindicated who are receiving stable PS at time of screening and for the duration of the study; Note: Long-Term PS = Participant must have been receiving PS for at least 6 months prior to screening and requiring PS at least 3 times per week
* Females of childbearing potential must have a negative urine pregnancy test at screening

Exclusion Criteria

* Patients taking steatogenic medications for ≥ 12 weeks in the past 12 months; those taking any medicine that could affect the measurement of hepatic steatosis within 12 weeks prior to study entry
* Evidence of systemic active infection at the time of dosing
* Participants intending to take non-study drug choline supplements or choline-containing multivitamins during the course of the study
* Participants unwilling to limit alcohol intake to no more than 20/g a day for 24 hours prior to their screening visit and for the duration of the study
* Active malignancy (excluding basal cell skin tumor, low or very low risk prostate cancer, cervical carcinoma in situ and local resected cervical cancer)
* Clinically significant renal disease
* Low B12 or low serum folic acid levels that are less than the normal range
* Fulminant liver failure, with active bleeding and/or encephalopathy
Minimum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Protara Therapeutics

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Chief Scientific Operations Officer

Role: STUDY_DIRECTOR

Protara Therapeutics

Locations

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University of Colorado School of Medicine

Aurora, Colorado, United States

Site Status RECRUITING

Columbia University Medical Center/ New York Presbyterian Hospital

New York, New York, United States

Site Status NOT_YET_RECRUITING

Duke Clinic - Abdominal Transplant Research Office

Durham, North Carolina, United States

Site Status RECRUITING

Cleveland Clinic

Cleveland, Ohio, United States

Site Status RECRUITING

University Hospitals Leuven, Campus Gasthuisberg

Leuven, , Belgium

Site Status NOT_YET_RECRUITING

Aalborg University Hospital, Department of Medical Gastroenterology

Aalborg, , Denmark

Site Status NOT_YET_RECRUITING

Rigshospitalet - University Hospital Copenhagen

Copenhagen, , Denmark

Site Status RECRUITING

Beaujon Hospital - APHP

Clichy, , France

Site Status NOT_YET_RECRUITING

Rennes University Hospital Center - Pontchaillou Site

Rennes, , France

Site Status NOT_YET_RECRUITING

CHRU Nancy - Barbois Hospital

Vandœuvre-lès-Nancy, , France

Site Status NOT_YET_RECRUITING

Charite - University Hospital Berlin

Berlin, , Germany

Site Status NOT_YET_RECRUITING

University Duisburg-Essen, University Hospital Essen

Essen, , Germany

Site Status NOT_YET_RECRUITING

M. Pirogow Provincial Specialized Hospital in Lodz, Nutritional Treatment Center

Lodz, , Poland

Site Status NOT_YET_RECRUITING

Czerniakowski Hospital Sp. z o.o. (LCC)

Warsaw, , Poland

Site Status RECRUITING

Countries

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United States Belgium Denmark France Germany Poland

Central Contacts

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Chief Scientific Operations Officer

Role: CONTACT

16468440337

Facility Contacts

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Use Central Contact

Role: primary

Use Central Contact

Role: primary

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Role: primary

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Role: primary

Use Central Contact

Role: primary

Use Central Contact

Role: primary

Use Central Contact

Role: primary

Use Central Contact

Role: primary

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Role: primary

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Role: primary

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Role: primary

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Use Central Contact

Role: primary

Other Identifiers

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TARA-001-301

Identifier Type: -

Identifier Source: org_study_id

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