A Study to Assess the Safety, Tolerability, and Efficacy of NDI-219216 in Patients With Advanced Solid Tumors.

NCT ID: NCT06898450

Last Updated: 2026-02-03

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE1/PHASE2

Total Enrollment

134 participants

Study Classification

INTERVENTIONAL

Study Start Date

2025-03-31

Study Completion Date

2031-12-31

Brief Summary

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The goal of this clinical trial is to learn if NDI-219216 is safe for patients, and if NDI-219216 might be a possible treatment for advanced solid tumors in the later phases of the study.

The main questions it aims to answer are:

Is NDI-219216 safe and what kinds of side effects might it cause? What kind of effects does NDI-219216 have on the body? Does NDI-219216 have any impact on tumor size?

Participants will:

Take NDI-219216 every day by mouth. Visit the clinic 6 times during Cycle 1, 2 times during Cycle 2, once a month thereafter for checkups and tests while on the study, then one time for an end of treatment visit. After the End of Study, a follow up will occur but can be done on the phone.

Keep a diary of their tablet consumption and symptoms experienced.

Detailed Description

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Study 9216-101 is a first-in-human (FIH), Phase 1/2, open-label, dose escalation, dose optimization, and dose expansion study to evaluate the safety, tolerability, pharmacokinetics (PK), pharmacodynamics, and preliminary antitumor activity of NDI-219216 in patients with advanced solid tumors.

Conditions

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Advanced Solid Tumors Cancer MSI-H Cancer

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SEQUENTIAL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Part A dose escalation

Part A Dose Escalation will involve enrolling sequential cohorts with increasing doses of NDI-219216 administered daily in repeating 28-day treatment cycles. The Dose Limiting Toxicity review period for each cohort will be 21 days for each patient enrolled, with review by a Safety Review Committee prior to escalation to the next dose level.

Group Type EXPERIMENTAL

NDI-219216

Intervention Type DRUG

NDI-219216 is a highly selective small molecule inhibitor of WRN helicase activity.

Part B Project Optimus

Part B will enroll up to 3 cohorts of patients randomized between up to 3 dose levels determined from Part A Dose Escalation. NDI-219216 will be administered daily in repeating 28-day treatment cycles.

Group Type EXPERIMENTAL

NDI-219216

Intervention Type DRUG

NDI-219216 is a highly selective small molecule inhibitor of WRN helicase activity.

Part C Dose Expansion

Part C will enroll 2 groups of patients with dMMR/MSI-h status and other select criteria, utilizing the optimal dose identified from Part B. NDI-219216 will be administered daily in 28-day repeating cycles.

Group Type EXPERIMENTAL

NDI-219216

Intervention Type DRUG

NDI-219216 is a highly selective small molecule inhibitor of WRN helicase activity.

Interventions

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NDI-219216

NDI-219216 is a highly selective small molecule inhibitor of WRN helicase activity.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Eastern Cooperative Oncology Group (ECOG) performance status score of 0 or 1
* Have unresectable and/or metastatic solid tumors (with or without MSI-H/dMMR) refractory to or intolerant to previous SoC therapy or for which no SoC therapy exists
* Presence of measurable disease according to RECIST version 1.1 except for Part A (Dose Escalation)
* Adequate bone marrow / hematologic, end-organ, and cardiovascular function
* Resolution of all acute (or toxic) adverse effects of prior therapies, radiation therapy, or surgical procedures to Grade ≤ 1 (except fatigue, alopecia, and peripheral neuropathy).

Exclusion Criteria

* Clinically significant cardiovascular disease.
* Patients with known WRN syndrome.
* Pregnancy, breastfeeding, or intention of becoming pregnant during the study.
Minimum Eligible Age

18 Years

Maximum Eligible Age

99 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Worldwide Clinical Trials

OTHER

Sponsor Role collaborator

Nimbus Wadjet, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Anita Scheuber, MD, PhD

Role: STUDY_DIRECTOR

Nimbus Therapeutics, Inc.

Locations

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USC Norris Comprehensive Cancer Center

Los Angeles, California, United States

Site Status RECRUITING

University of Chicago Medicine

Chicago, Illinois, United States

Site Status NOT_YET_RECRUITING

University of Louisville James Graham Brown Cancer Center

Louisville, Kentucky, United States

Site Status RECRUITING

Cayuga Cancer Center

Ithaca, New York, United States

Site Status TERMINATED

Atrium Health Levine Cancer Institute

Charlotte, North Carolina, United States

Site Status NOT_YET_RECRUITING

Taylor Cancer Research Center

Maumee, Ohio, United States

Site Status RECRUITING

Brown University Health

Providence, Rhode Island, United States

Site Status RECRUITING

Prisma Health Cancer Institute - Multidisciplinary Center

Greenville, South Carolina, United States

Site Status RECRUITING

University of Virginia Emily Couric Clinical Cancer Center

Charlottesville, Virginia, United States

Site Status RECRUITING

Virginia Cancer Specialists, P.C. - Fairfax

Fairfax, Virginia, United States

Site Status RECRUITING

Liverpool Hospital

Liverpool, New South Wales, Australia

Site Status RECRUITING

Southern Oncology Clinical Research Unit

Bedford Park, South Australia, Australia

Site Status RECRUITING

BC Cancer Center

Kelowna, British Columbia, Canada

Site Status NOT_YET_RECRUITING

Princess Margaret Cancer Center

Toronto, Ontario, Canada

Site Status NOT_YET_RECRUITING

McGill University Health Centre (MUHC)

Montreal, Quebec, Canada

Site Status NOT_YET_RECRUITING

Hôpital Saint-Antoine - Assistance Publique-Hopitaux de Paris (AP-HP)

Paris, , France

Site Status RECRUITING

Centre Hospitalier Universitaire (CHU) de Poitiers

Poitiers, , France

Site Status RECRUITING

START Dublin

Dublin, , Ireland

Site Status RECRUITING

START Lisbon

Lisbon, , Portugal

Site Status RECRUITING

START Barcelona

Barcelona, , Spain

Site Status RECRUITING

Hospital Clinico San Carlos

Madrid, , Spain

Site Status RECRUITING

Beatson Clinical Research Facility

Glasgow, , United Kingdom

Site Status NOT_YET_RECRUITING

Sarah Cannon Research Institute UK

London, , United Kingdom

Site Status RECRUITING

The Christie NHS Foundation Trust UK

Manchester, , United Kingdom

Site Status RECRUITING

Countries

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United States Australia Canada France Ireland Portugal Spain United Kingdom

Central Contacts

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Sean Rossi

Role: CONTACT

857-600-8779

Katie Ard, MSN

Role: CONTACT

303-646-7297

Other Identifiers

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9216-101

Identifier Type: -

Identifier Source: org_study_id

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