ARD-101 for Treatment of PWS: The Hunger Elimination or Reduction Objective Trial

NCT ID: NCT06828861

Last Updated: 2026-02-12

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE3

Total Enrollment

90 participants

Study Classification

INTERVENTIONAL

Study Start Date

2024-12-20

Study Completion Date

2026-04-30

Brief Summary

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The goal of this clinical trial is to learn if ARD-101 works to treat hyperphagia-related behavior in patients with Prader-Willi syndrome (PWS). It will also teach us about the safety of ARD-101.

The main questions it aims to answer are:

* Does ARD-101 improve the total score of the HQCT-9 (hyperphagia questionnaire for clinical trials, 9 questions)?
* What medical problems do participants have when taking ARD-101?

Researchers will compare ARD-101 to a placebo (a look-alike substance that contains no drug) to see if ARD-101 works to treat hyperphagia in PWS subjects.

Eligible participants will:

* Take ARD-101 or a placebo every day for 12 weeks.
* Visit the clinic or have a tele-visit once every 2 to 4 weeks during dosing and then have a tele-visit 4 weeks after stopping the ARD-101 or placebo.
* Patients/Caregivers will keep a daily diary.

Participants who complete the study may be eligible to enter an open-label extension study where everyone will receive ARD-101.

Detailed Description

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Conditions

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Hyperphagia Prader-Willi Syndrome

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Treatment Arm A

ARD-101

Group Type EXPERIMENTAL

ARD-101

Intervention Type DRUG

200 mg BID (twice per day) for 1 week, 400 mg BID for 1 week, 800 mg BID for 10 weeks

Treatment Arm B

Placebo for ARD-101

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

200 mg BID (twice per day) for 1 week, 400 mg BID for 1 week, 800 mg BID for 10 weeks

Interventions

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Placebo

200 mg BID (twice per day) for 1 week, 400 mg BID for 1 week, 800 mg BID for 10 weeks

Intervention Type DRUG

ARD-101

200 mg BID (twice per day) for 1 week, 400 mg BID for 1 week, 800 mg BID for 10 weeks

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Documented confirmation of Prader-Willi Syndrome (PWS)
* Stable care setting with same, single designated caregiver for at least 6 months prior to Visit 1
* At least 7 years of age or older in the US at the time of consent
* At least 10 years of age or older in Australia
* At least 13 years of age or older in countries outside of the US and Australia

Exclusion Criteria

* Diagnosis of schizophrenia, bipolar disorder, personality disorder or other severe mood, anxiety or eating disorder (other than hyperphagia).
* Presence of any malignancy within 5 years with the exception of basal or squamous cell carcinoma of the skin, in situ carcinoma of the service, or in situations prostate cancer.
* Presence of clinically relevant renal, hepatic, pancreatic, cardiovascular, neurological, psychiatric, hematological, pulmonary, or GI abnormality that, in the opinion of the investigator, may preclude the patient from safe completion of the study
* Adults: systolic blood pressure \>=160 mmHg and/or diastolic blood pressure \>=100 mmHg
* Children and Adolescents: systolic blood pressure \>=140 mmHg and/or diastolic blood pressure \>=90 mmHg.
* Type 1 diabetes mellitus; HbA1c \>8.5%
* Use of agents to promote weight gain or loss, alter hunger or appetite within 30 days of Visit 1 and throughout the study.
* Use of any commercially available medication for the treatment of hyperphagia (i.e., Vykat) within 60 days of randomization and throughout the study.
* Very high doses of glucocorticoids in the previous 3 months of Visit 1 and throughout the study.
Minimum Eligible Age

7 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Aardvark Therapeutics, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Children's of Alabama

Birmingham, Alabama, United States

Site Status RECRUITING

Rady Children's Hospital

Encinitas, California, United States

Site Status RECRUITING

Children's Hospital of Orange Country

Orange, California, United States

Site Status NOT_YET_RECRUITING

Stanford Children's Health Specialty Services

Palo Alto, California, United States

Site Status RECRUITING

Children's Hospital Colorado

Denver, Colorado, United States

Site Status RECRUITING

Nemours Children Clinic Wilmington

Wilmington, Delaware, United States

Site Status RECRUITING

UF Shands Children's Hospital

Gainesville, Florida, United States

Site Status RECRUITING

Emory University School of Medicine

Atlanta, Georgia, United States

Site Status RECRUITING

Ann and Robert H. Lurie Children's Hospital of Chicago

Chicago, Illinois, United States

Site Status RECRUITING

The Johns Hopkins Hospital

Baltimore, Maryland, United States

Site Status NOT_YET_RECRUITING

University of Minnesota Masonic Children's Hospital

Minneapolis, Minnesota, United States

Site Status RECRUITING

Maimonides Medical Center

Brooklyn, New York, United States

Site Status RECRUITING

NYU Langone Children's Ambulatory Care Center

Mineola, New York, United States

Site Status RECRUITING

Vanderbilt University Medical Center

Nashville, Tennessee, United States

Site Status RECRUITING

Cook Children's Medical Center

Fort Worth, Texas, United States

Site Status RECRUITING

Texas Valley Clinical Research, LLC

Weslaco, Texas, United States

Site Status WITHDRAWN

Seattle Children's Hospital

Seattle, Washington, United States

Site Status RECRUITING

Royal Prince Alfred Hospital

Camperdown, New South Wales, Australia

Site Status RECRUITING

The Children's Hospital at Westmead

Westmead, New South Wales, Australia

Site Status RECRUITING

Queensland Children's Hospital

South Brisbane, Queensland, Australia

Site Status RECRUITING

Alberta Children's Hospital Research Institute

Calgary, Alberta, Canada

Site Status NOT_YET_RECRUITING

Stollery Children's Hospital

Edmonton, Alberta, Canada

Site Status RECRUITING

Children's Hospital at London Health Sciences Centre

London, Ontario, Canada

Site Status NOT_YET_RECRUITING

Centre Hospitalier Universitaire Sainte-Justine

Montreal, Quebec, Canada

Site Status RECRUITING

Samsung Medical Center

Seoul, South Korea, South Korea

Site Status RECRUITING

Inha University Hospital

Incheon, , South Korea

Site Status RECRUITING

Ajou University Hospital

Suwon, , South Korea

Site Status RECRUITING

Leicester Royal Infirmary

Leicester, Leicestershire, United Kingdom

Site Status RECRUITING

Fulborn Hospital

Cambridge, , United Kingdom

Site Status NOT_YET_RECRUITING

Royal Hospital for Children (Glasgow) - PPDS - PIN

Glasgow, , United Kingdom

Site Status RECRUITING

The Royal London Hospital

London, , United Kingdom

Site Status RECRUITING

Countries

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United States Australia Canada South Korea United Kingdom

Central Contacts

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Robin Schmidt, MS

Role: CONTACT

(858) 225-7696

Facility Contacts

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Hussein Abdul-Latif, MD

Role: primary

Tushima Reeves

Role: backup

205-638-9173

Lynne Bird, MD

Role: primary

Katherine Bunda

Role: backup

858-236-5145

Virginia Kimonis, MD

Role: primary

Diane Stafford, MD

Role: primary

Alondra Loyola

Role: backup

650-725-0641

Shawn McCandless, MD

Role: primary

Lukas Jacyniuk Moskalis

Role: backup

720-777-5693

Aaron Chidekel, MD

Role: primary

Kerry Smallacombe, DO

Role: backup

302-559-0247

Jennifer Miller, MD

Role: primary

352-294-8229

Michael Gambello, MD

Role: primary

Gwendolyn Gunn

Role: backup

Priya Khanna, MD

Role: primary

Madeleine Muller

Role: backup

312-227-8290

Ann Scheimann, MD

Role: primary

410-955-8769

Bradley Miller, MD

Role: primary

612-624-5409

Edward Yi, MD

Role: primary

Hasan Mustafić

Role: backup

718-283-8170

Jorge Mejia-Corletto, MD

Role: primary

516-663-4600

Ashley Shoemaker, MD

Role: primary

Robert Manning, RN

Role: backup

615-421-6118

Sani Roy, MD

Role: primary

Amy Morell

Role: backup

Isabella Niu, MD

Role: primary

Stephanie Purdy

Role: backup

206-987-2640

Tania Markovic, MD

Role: primary

Tegan Picone

Role: backup

Yoon Hi Cho, MD

Role: primary

Rochelle Burgess

Role: backup

Helen Heussler, MD

Role: primary

Michael Duhig

Role: backup

Josephine Ho, MD

Role: primary

Heidi Virtanen

Role: backup

Andrea Haqq, MD

Role: primary

Olena Zaliavska

Role: backup

780-492-0346

Marina Ybarra, MD

Role: primary

Nathalie Alos, MD

Role: primary

Teresa Bouramia

Role: backup

Sung Yoon Cho, MD

Role: primary

Ji Eun Lee, MD

Role: primary

Young Bae Sohn, MD

Role: primary

James Greening, MD

Role: primary

Shahid Zaman, MD

Role: primary

Mohamad Guftar Shaikh, MBBS

Role: primary

Evelien Gevers, MD

Role: primary

Other Identifiers

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AVK-101-301

Identifier Type: -

Identifier Source: org_study_id

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