A Phase 1b Study of the NLRP3 Inhibitor VENT-02 in Patients With Mild to Moderate Parkinson's Disease

NCT ID: NCT06822517

Last Updated: 2025-10-29

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

TERMINATED

Clinical Phase

PHASE1/PHASE2

Total Enrollment

29 participants

Study Classification

INTERVENTIONAL

Study Start Date

2025-03-05

Study Completion Date

2025-10-09

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

This trial is a randomized, double-blind, placebo-controlled Phase 1b study evaluating the safety/tolerability, PK, and pharmacodynamics of VENT 02, administered orally at 1 dose level twice daily (BID) over 28 days in patients with mild to moderate Parkinson's disease.

The study includes a screening period, a 28-day double-blind treatment period, and a 7-day follow-up period after last dose.

Approximately 30 patients will be randomized into 1 of the 2 treatment arms.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Parkinson Disease

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

VENT-02 Dose 1

Group Type EXPERIMENTAL

VENT-02

Intervention Type DRUG

Orally administered capsules

Placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Orally administered capsules

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

VENT-02

Orally administered capsules

Intervention Type DRUG

Placebo

Orally administered capsules

Intervention Type DRUG

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* 45 to 90 years of age, inclusive.
* Body weight and body mass index (BMI) within the range of 100 to 265 pounds (45 to 120 kg) and 18 to 34 kg/m2 (inclusive), respectively.
* A diagnosis of idiopathic PD according to United Kingdom (UK) Brain Bank or Movement Disorder Society (MDS) criteria with bradykinesia and ≥ 1 additional cardinal sign of PD (e.g., resting tremor, rigidity).
* A diagnosis of PD for ≤ 7 years at Screening.
* A modified Hoehn \& Yahr stage 1 to 2.5.
* If presently receiving treatment for PD, must be on a stable dose for ≥ 2 weeks prior to dosing, with no expected change in this regimen for the duration of the study.
* If presently taking any non-PD concomitant medications, must be on a stable dose for ≥ 2 weeks prior to dosing.

Exclusion Criteria

* Any clinically significant abnormality at Screening
* A positive serology for hepatitis B surface antigen (HBsAg), hepatitis C virus antibody (anti-HCV), or human immunodeficiency virus antibodies (anti-HIV) 1/2 at Screening.
* A significant neurological disease affecting the central nervous system, other than PD, that may affect cognition or ability to complete the study, including but not limited to dementias, severe and repetitive past (up to 5 years) head trauma, normal pressure hydrocephalus, or epilepsy or recurrent seizures (except febrile childhood seizures), as determined by the investigator.
* Current serious or unstable illnesses, that, in the investigator's opinion, could compromise patient safety and ability to comply with study procedures, or has a life expectancy of \< 24 months.
* A history of suicidal ideation or previous suicide attempt in the 12 months prior to Screening or is clinically judged by the investigator to be at serious risk for suicide as assessed by medical history, examination, or the C-SSRS.
* A contraindication (e.g., current use of anticoagulants) that would prohibit a lumbar puncture (LP).
* Currently enrolled in any other interventional clinical trial involving an investigational product or any other type of medical research judged not to be scientifically or medically compatible with this study, as assessed by the investigator.
* Has participated in a clinical trial involving an investigational product within 30 days or 5 half-lives (whichever is longer) prior to dosing.
* Has levodopa-induced dyskinesias lasting for \> 25% of waking day or dyskinesias interfering with many daily activities.
* Has dysphagia to the extent that it would affect the patient's ability to swallow the investigational medicinal product (IMP).
* Has a parkinsonian syndrome, including atypical parkinsonism.
* Is a known carrier (i.e., confirmed by historical medical documentation) of familial PD genes.
Minimum Eligible Age

45 Years

Maximum Eligible Age

90 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Ventus Therapeutics U.S., Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Investigative Site

Fountain Valley, California, United States

Site Status

Investigative Site

San Jose, California, United States

Site Status

Investigative Site

West Hills, California, United States

Site Status

Investigative Site

Englewood, Colorado, United States

Site Status

Investigative Site

Aventura, Florida, United States

Site Status

Investigative Site

Boca Raton, Florida, United States

Site Status

Investigative Site

Coral Gables, Florida, United States

Site Status

Investigative Site

Coral Springs, Florida, United States

Site Status

Investigative Site

Cutler Bay, Florida, United States

Site Status

Investigative Site

Daytona Beach, Florida, United States

Site Status

Investigative Site

Doral, Florida, United States

Site Status

Investigative Site

Jacksonville, Florida, United States

Site Status

Investigative Site

Maitland, Florida, United States

Site Status

Investigative Site

Miami, Florida, United States

Site Status

Investigative Site

Miami, Florida, United States

Site Status

Investigative Site

Winter Park, Florida, United States

Site Status

Investigative Site

Scarborough, Maine, United States

Site Status

Investigative Site

Farmington Hills, Michigan, United States

Site Status

Investigative Site

Abington, Pennsylvania, United States

Site Status

Investigative Site

Memphis, Tennessee, United States

Site Status

Investigative Site

Cypress, Texas, United States

Site Status

Investigative Site

Round Rock, Texas, United States

Site Status

Investigative Site

Spokane, Washington, United States

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

VENT-02-102

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.

DNS-7801 vs. Placebo in Parkinson's Disease
NCT03306329 TERMINATED PHASE2