A Study of Setmelanotide in Patients With Prader-Willi Syndrome

NCT ID: NCT06772597

Last Updated: 2025-10-15

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

20 participants

Study Classification

INTERVENTIONAL

Study Start Date

2025-03-04

Study Completion Date

2027-10-31

Brief Summary

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This is a Phase 2, open-label study designed to assess the safety and efficacy of setmelanotide in patients with obesity due to Prader-Willi Syndrome (PWS) who are 6 to 65 years of age. Up to 20 patients are planned to be enrolled. Patients will take a daily subcutaneous dose of open-label setmelanotide for up to 52 weeks.

Detailed Description

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Conditions

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Prader-Willi Syndrome Obesity Hyperphagia

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Setmelanotide (Open-label)

Group Type EXPERIMENTAL

Setmelanotide

Intervention Type DRUG

Setmelanotide (daily subcutaneous injection)

Interventions

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Setmelanotide

Setmelanotide (daily subcutaneous injection)

Intervention Type DRUG

Other Intervention Names

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Imcivree

Eligibility Criteria

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Inclusion Criteria

* Confirmed diagnosis of Prader-Willi Syndrome (PWS)
* Age 6 to 65
* BMI ≥30 kg/m2 for patients ≥18 years of age or BMI ≥95th Percentile for age and sex
* Agree to use a highly effective form of contraception and follow the study contraception requirements throughout study duration and for 90 days after.
* Patient and/or guardian is able to communicate well with the Investigator, understand and comply with the requirements of the study, and understand English and sign the written informed consent.

Exclusion Criteria

* Use of weight modulating medications
* Abnormal HbA1c, eGFR, ALT, AST, bilirubin, T4 values
* Current, clinically significant pulmonary, cardiac, metabolic, or oncologic disease considered severe enough to interfere with the trial and/or confound the results.
* Participation in any clinical trial with an investigational drug/device within 3 months or 5 half-lives, whichever is longer, prior to the first trial dose
* Hypersensitivity to setmelanotide
* Diagnosis of severe psychiatric disorders
* Pregnant and/or breastfeeding
Minimum Eligible Age

6 Years

Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Rhythm Pharmaceuticals, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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David Meeker, MD

Role: STUDY_CHAIR

Rhythm Pharmaceuticals, Inc.

Locations

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University of Florida

Gainesville, Florida, United States

Site Status RECRUITING

Countries

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United States

Central Contacts

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Rhythm Clinical Trials

Role: CONTACT

(857) 264-4280

Physician Inquiry Clinical Trials

Role: CONTACT

(857) 264-4280

Other Identifiers

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RM-493-043

Identifier Type: -

Identifier Source: org_study_id

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