Double-Blind, Placebo Controlled, Phase 3 Trial of ZGN-440 (Beloranib) in Obese Subjects With Prader-Willi Syndrome

NCT ID: NCT02179151

Last Updated: 2017-01-26

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

108 participants

Study Classification

INTERVENTIONAL

Study Start Date

2014-09-30

Study Completion Date

2016-10-31

Brief Summary

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The purpose of this study is to evaluate efficacy and safety of ZGN-440 (beloranib) in obese adolescent and adult subjects with Prader-Willi Syndrome.

Detailed Description

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Phase 3, Randomized, Double-Blind, Placebo Controlled, Phase 3 Trial of ZGN-440 (Subcutaneous Beloranib in Suspension) in Obese Subjects with Prader-Willi Syndrome to Evaluate Total Body Weight, Food-related Behavior, and Safety Over 6 Months

Conditions

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Prader-Willi Syndrome Obesity

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Placebo

Intervention: ZGN-440 Placebo for Injectable Suspension

Group Type PLACEBO_COMPARATOR

ZGN-440 Placebo for Injectable Suspension

Intervention Type DRUG

Subjects will receive placebo twice weekly subcutaneous injections for up to 28 weeks.

ZGN-440 Injectable Suspension (1.8 mg)

Intervention: ZGN-440 for Injectable Suspension

Group Type EXPERIMENTAL

ZGN-440 for Injectable Suspension

Intervention Type DRUG

Subjects will receive ZGN-440 twice weekly subcutaneous injections for up to 28 weeks.

ZGN-440 Injectable Suspension (2.4 mg)

Intervention: ZGN-440 for Injectable Suspension

Group Type EXPERIMENTAL

ZGN-440 for Injectable Suspension

Intervention Type DRUG

Subjects will receive ZGN-440 twice weekly subcutaneous injections for up to 28 weeks.

Interventions

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ZGN-440 for Injectable Suspension

Subjects will receive ZGN-440 twice weekly subcutaneous injections for up to 28 weeks.

Intervention Type DRUG

ZGN-440 Placebo for Injectable Suspension

Subjects will receive placebo twice weekly subcutaneous injections for up to 28 weeks.

Intervention Type DRUG

Other Intervention Names

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ZGN-440 Beloranib Placebo

Eligibility Criteria

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Inclusion Criteria

* Confirmed genetic diagnosis of Prader-Willi Syndrome
* Age 12-65
* Obesity
* Age 12-17: BMI ≥ 95th percentile for age and gender
* Age 18-65: BMI ≥27 to ≤60 kg/m2

Exclusion Criteria

* Subjects living in a group home ≥ 50% of the time
* Recent use (within 3 months) of weight loss agents including herbal medication
* Poorly controlled severe psychiatric disorders
Minimum Eligible Age

12 Years

Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Zafgen, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Dennis Kim, MD

Role: STUDY_DIRECTOR

Zafgen, Inc.

Locations

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University of California, Davis

Sacramento, California, United States

Site Status

UCSD: Rady Children's Hospital

San Diego, California, United States

Site Status

Children's Hospital of Colorado

Aurora, Colorado, United States

Site Status

University of Florida

Gainesville, Florida, United States

Site Status

Kansas University Medical Center

Kansas City, Kansas, United States

Site Status

National Institute of Child Health

Bethesda, Maryland, United States

Site Status

Children's Hospital Boston

Boston, Massachusetts, United States

Site Status

Children's Hospital and Clinics of Minnesota

Saint Paul, Minnesota, United States

Site Status

Saint Louis University

St Louis, Missouri, United States

Site Status

Winthrop University

Mineola, New York, United States

Site Status

University Hospitals Case Medical Center

Cleveland, Ohio, United States

Site Status

Vanderbilt University

Nashville, Tennessee, United States

Site Status

Texas Children's Hospital

Houston, Texas, United States

Site Status

University of Utah

Salt Lake City, Utah, United States

Site Status

Seattle Children's Research Institute

Seattle, Washington, United States

Site Status

Countries

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United States

References

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McCandless SE, Yanovski JA, Miller J, Fu C, Bird LM, Salehi P, Chan CL, Stafford D, Abuzzahab MJ, Viskochil D, Barlow SE, Angulo M, Myers SE, Whitman BY, Styne D, Roof E, Dykens EM, Scheimann AO, Malloy J, Zhuang D, Taylor K, Hughes TE, Kim DD, Butler MG. Effects of MetAP2 inhibition on hyperphagia and body weight in Prader-Willi syndrome: A randomized, double-blind, placebo-controlled trial. Diabetes Obes Metab. 2017 Dec;19(12):1751-1761. doi: 10.1111/dom.13021. Epub 2017 Jul 13.

Reference Type DERIVED
PMID: 28556449 (View on PubMed)

Other Identifiers

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ZAF-311

Identifier Type: -

Identifier Source: org_study_id

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