Safety, Tolerability, and Pharmacokinetics of Exidavnemab in Patients With Parkinson's Disease and Patients With Multiple System Atrophy

NCT ID: NCT06671938

Last Updated: 2025-10-21

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

36 participants

Study Classification

INTERVENTIONAL

Study Start Date

2024-10-24

Study Completion Date

2026-03-16

Brief Summary

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The primary objective of this study is to assess the safety and tolerability of exidavnemab after multiple dosing versus placebo.

Detailed Description

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This Phase 2a, randomized, double-blind, placebo-controlled, multicenter, multinational, multiple ascending dose (MAD) trial is designed to investigate the safety, tolerability, and pharmacokinetics (PK) of exidavnemab in participants with mild to moderate Parkinson's Disease (PD) on stable symptomatic PD medication and Patients With Multiple System Atrophy.

The trial will evaluate two dose cohorts versus placebo. Participants in each cohort will be randomly allocated in a 2:1 ratio to receive either exidavnemab or placebo. There will be approximately 12 evaluable participants with PD in Cohort 1 and approximately 24 evaluable participants in Cohort 2 (approximately 12 participants in each of Cohorts 2a and 2b), resulting in approximately 36 participants, 24 with PD and 12 with MSA, randomized in total.

Conditions

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Parkinson Disease Multiple System Atrophy

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

SEQUENTIAL

The trial will evaluate 2 dose cohorts, dose 1 exidavnemab versus placebo (Cohort 1) and dose 2 exidavnemab versus placebo (Cohort 2). Cohort 2 will consist of a PD cohort (Cohort 2a) and an MSA cohort (Cohort 2b).
Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors
Participants in each cohort will be randomly allocated in a 2:1 ratio to receive either exidavnemab or placebo.

Study Groups

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exidavnemab

exidavnemab (cohort 1 - dose 1; cohort 2 - dose 2)

Group Type EXPERIMENTAL

exidavnemab

Intervention Type DRUG

The trial medication will be administered as an intravenous (IV) infusion (dose 1; dose 2)

Placebo

Group Type PLACEBO_COMPARATOR

Placebo Comparator

Intervention Type DRUG

The trial medication will be administered as an intravenous (IV) infusion

Interventions

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exidavnemab

The trial medication will be administered as an intravenous (IV) infusion (dose 1; dose 2)

Intervention Type DRUG

Placebo Comparator

The trial medication will be administered as an intravenous (IV) infusion

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Male and female participants 40 to 85 years of age.
2. Body weight more than or equal to 50 kg and less than or equal to 120 kg.
3. Have idiopathic PD (i.e., not induced by drugs or other diseases) as defined by bradykinesia combined with at least 1 of resting tremor and rigidity, as per the Movement Disorder Society Criteria for PD (Postuma, et al. 2015).
4. Classified as Stage 1 to 2.5 on the modified Hoehn and Yahr scale for the staging of PD severity.
5. Participants must have cognition inconsistent with dementia as confirmed by a score of more than or equal to 22 on the MoCA.
6. Stable and optimized symptomatic PD medication, defined as the same list of medications for at least 3 months prior to the Screening Visit with no change in the dose for at least 1 month prior to the Baseline Visit, and no planned changes in dose-regimen during trial participation.
7. Prior (any time; i.e., no time limit) or current DaT-SPECT or DaT-PET consistent with dopamine transporter deficit, as per the Movement Disorder Society Criteria for PD(Postuma, et al. 2015). For participants who have not undergone DaT-SPECT or DaT-PET prior to Screening, or who have previously undergone DaT-SPECT or DaT-PET scan(s) but without results consistent with dopamine transporter deficit, DaT-SPECT or DaT-PET should be performed and read locally as part of the Screening procedures.
8. Positive smell test showing hyposmia, as defined by UPSIT scores of around or below the 15% percentile for their relevant sex and age group. Cut-off scores are provided below for reference (Table 5.1; based on Brumm, et al. 2023) Ability to use a tablet device to measure cognitive function, as per Investigator judgment.


1. Male and female participants 40 to 85 years of age.
2. Body weight more than or equal to 50 kg and less than or equal to 120 kg.
3. Have clinically established or clinically probable MSA (either MSA-P or MSA-C), as per the Movement Disorder Society criteria for the diagnosis of MSA (Wenning, et al. 2022).
4. Classified as Stage 1 to 3 on the modified Hoehn and Yahr scale for the staging of MSA severity.
5. Participants must have cognition inconsistent with dementia as confirmed by a score of more than or equal to 22 on the MoCA.
6. Negative urine or serum pregnancy test at the Screening Visit and Baseline for premenopausal women, and for women who have experienced menopause onset less than 12 months prior to the first planned dose of trial medication.
7. Males and POCBP must agree to practice an effective means of birth control during their participation in the trial and until 3 months after their last dose of the trial medication. See specific guidelines regarding contraceptive methods in Section 14.1.
8. Willingness and ability to comply with scheduled visits, treatment plan, laboratory tests, and trial procedures.

Exclusion Criteria

1. Known hypersensitivity to trial medication, the infusion solution, or excipients.
2. More than 5 years of symptomatic treatment for PD.
3. History of neurosurgical intervention for PD including implantation of brain stimulation.
4. Diagnosis of PD dementia or another dementia.
5. Any psychiatric diagnosis or symptoms (e.g., hallucinations, major depression, or delusions) that could interfere with trial procedures.
6. Freezing episodes occurring on a weekly basis or more frequently.
7. Motor fluctuations occurring on a weekly basis or more frequently.
8. Levodopa-induced troublesome dyskinesia of a severity that would significantly interfere with the participant's ability to participate or perform trial procedures as determined by the Movement Disorder Society-Sponsored Revision of the Unified Parkinson's Disease Rating Scale (MDS-UPDRS) Subscale IV.


1. Known hypersensitivity to the trial medication, the infusion solution, or excipients.
2. Any psychiatric diagnosis or symptoms (e.g., hallucinations, major depression, or delusions) that could interfere with trial procedures.
3. History of significant cardiovascular disease or arrhythmia within 6 months of Screening.
4. Abnormal ECG that is or may be clinically significant in the Investigator's opinion and after consultation with the Medical Monitor, including left bundle branch block, atrial fibrillation, QTcF more than 450 msec for males and more than 470 msec for females at the Screening Visit or Baseline.
5. History of transient ischemic attacks, stroke, or seizures within 12 months of Screening.
6. Abnormal liver function tests: GGT, TBil, ALP, ALT, and AST higher than the ULN and regarded as potentially clinically significant by the Investigator.

Note: Gilbert's syndrome is not exclusionary.
7. Poorly controlled diabetes as defined by hemoglobin A1C of more than 8%.
8. Contraindication, condition, or concomitant medication incompatible with lumbar puncture (e.g., lumbar scoliosis, coagulopathy, and infected skin at needle puncture site), 1.5T or 3T MRI (e.g., aneurysm clip, metal fragments \[e.g., in-skull and cardiac devices other than those approved as safe for use in MRI scanners\], and internal electrical devices such as a cochlear implant, spinal cord stimulator, or cardiac pacemaker/defibrillator).
Minimum Eligible Age

40 Years

Maximum Eligible Age

85 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Worldwide Clinical Trials

OTHER

Sponsor Role collaborator

BioArctic AB

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Centrum Medyczyne Neuromed Sp. z o.o.

Bydgoszcz, , Poland

Site Status RECRUITING

Specjalistyczne Gabinety Sp. z o.o.

Krakow, , Poland

Site Status WITHDRAWN

Krakowska Akademia Neurologii Sp. Z o.o

Krakow, , Poland

Site Status RECRUITING

Hospital Universitario Virgen del Rocío

Seville, Andalusia, Spain

Site Status RECRUITING

Hospital Universitari Vall d'Hebron

Barcelona, Barcelona, Spain

Site Status RECRUITING

Hospital Universitari General de Catalunya

Sant Cugat del Vallès, Barcelona, Spain

Site Status RECRUITING

Hospital Universitario Ramón y Cajal

Madrid, Madrid, Spain

Site Status RECRUITING

Policlínica Gipuzkoa

San Sebastián, , Spain

Site Status RECRUITING

Countries

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Poland Spain

Central Contacts

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BioArtic AB

Role: CONTACT

+46 8 695 6930

Facility Contacts

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Pawel Lisewski

Role: primary

+48 692 298 835

Karolina Tomala

Role: primary

+48 663 506 016

Pablo Mir Rivera

Role: primary

+34 955923039

Jorge Hernández Vara

Role: primary

+34 93 489 30 00

Ernest Balaguer Martínez

Role: primary

+34 931751575

Jose Luis López Sendón Moreno

Role: primary

+34 913368821

Nadege Van Blercom

Role: primary

+34 943 00 28 12

Other Identifiers

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2024-511222-30-00

Identifier Type: CTIS

Identifier Source: secondary_id

BAN0805-201

Identifier Type: -

Identifier Source: org_study_id

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