UCAN CAN-DU: Canada-Netherlands Personalized Medicine Network in Childhood Arthritis and Rheumatic Disease

NCT ID: NCT06560606

Last Updated: 2024-08-19

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Total Enrollment

4100 participants

Study Classification

OBSERVATIONAL

Study Start Date

2018-08-24

Study Completion Date

2027-03-30

Brief Summary

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Childhood arthritis is a chronic disabling disease. New medications called biologic therapies are now available to treat arthritis that target key biologic molecules that cause inflammation. Biologic therapies, while very effective in treating arthritis in children, may have serious side effects including infections and potentially cancers, and are very expensive and doctors don't know, which one to choose for which child. The investigators will develop tests that enable them to learn about the biology of each child's arthritis and be able to predict when and which biologic therapy to start and when to stop.

Detailed Description

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UCAN CAN-DU is a multicenter observational cohort study that will collect prospective data from children with arthritis. Biologic samples, clinical data and patient reported outcomes will be collected.

In addition, the study will also include a health economics component which will include a number of complementary approaches for quantifying and comparing benefits and risks that promote evidence-based, patient centered health care. This will address both the personal and societal economic burden of disease and include qualitative methods to inform the measurement of preferences, economic and simulation modelling to assess the value of biomarker testing. The socioeconomic impact of biomarker based treatment will be evaluated.

All clinical, biological and patient-derived data will be collected at an aggregation point housed and managed by High Performance Computing 4 Health (HPC4Health), a private hospital-only secure cloud-computing service within Compute Canada and physically located at SickKids/UHN. These databases and apps include biospecimen data and data collected through the eHealth platform. This will enable the study team to share and integrate data in near real-time into analytic models throughout the study course; hence providing a near real-time feedback from bench to bedside and vice versa.

The analysis of the cohorts will help define and confirm the biologic pathways predictive of disease course, treatment response and disease remission. This knowledge will then be used to develop a comprehensive clinical predictive tool to guide effective and safe treatment of childhood arthritis.

Conditions

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Juvenile Idiopathic Arthritis

Study Design

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Observational Model Type

COHORT

Study Time Perspective

PROSPECTIVE

Study Groups

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Cohort 1 - Biologic Basis of JIA

The objectives for this group are to help researchers look at childhood arthritis and determine which management approach is best for each individual child.

To be eligible for this group:

Participant must be ≤ 18 years of age at time of study enrollment. Participant is suspected to have JIA. Participant has not received any treatment other than non-steroidal anti-inflammatory drugs, such as acetaminophen.

No interventions assigned to this group

Cohort 2 - Start Biologics

The objectives for this group are to help researchers develop a tool to predict response to therapy.

To be eligible for this group:

Participant ≤ 18 years of age at time of study enrollment. Participant has been diagnosed with JIA and arthritis is active. Participant will be starting, re-starting or switching to a new biologic therapy.

No interventions assigned to this group

Cohort 3 - Stop Biologics

The objectives for this group are to help researchers develop a tool to predict who will remain in remission after discontinuing therapy.

To be eligible for this group:

Participant ≤ 18 years of age at time of study enrollment. Participant has been diagnosed with JIA and arthritis is inactive. Participant will be stopping or tapering biologic therapy.

No interventions assigned to this group

Cohort 4: Extreme Phenotypes

The objective for this group is new gene discovery and drug target identification.

To be eligible for this group:

There is high suspicion of genetic contribution. Participants are severely affected with difficult to control arthritis or systemic disease.

There is unexplained systemic inflammation with arthritis/arthralgia as a part of manifestations

No interventions assigned to this group

Eligibility Criteria

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Inclusion Criteria

Cohort 1: - Biologic Basis of JIA

* ≤18 years\*
* Active objective arthritis suspected to be JIA or diagnosed with JIA within 6 months of enrolment
* Treatment naïve except for NSAIDs, allowed to have received NSAIDS within 6 months of diagnosis

Cohort 2 - Start Biologics

* JIA diagnosis as per ILAR criteria (all subtypes)
* ≤18 years\*
* Active arthritis
* For sJIA, active disease not necessarily with arthritis.
* Time of start, restart or switch biologic therapy: e.g. failure, insufficient/partial response or intolerance

Cohort 3 - Stop Biologics

* JIA diagnosis as per ILAR criteria (all subtypes)
* ≤18 years\*
* Inactive disease
* Discontinuing/tapering biologics for inactive disease

Cohort 4: Extreme Phenotypes

* Unexplained systemic inflammation with arthritis/arthralgia as a part of manifestations
* High suspicion of genetic contribution
* Severely affected patients with difficult to control disease (ie failure of multiple biologics)

Exclusion Criteria

Cohort 1 :

* Arthritis explained by another diagnosis
* Joint injections as previous treatment less than 4 weeks prior to enrollment

Cohort 2:

* Arthritis explained by any other cause
* Start on biologics as an indication for uveitis only

Cohort 3:

\- Tapering scheme \> 12 months to complete biologics stop

Cohort 4:

\- Arthritis explained by another diagnosis
Maximum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Canadian Institutes of Health Research (CIHR)

OTHER_GOV

Sponsor Role collaborator

Genome Canada

OTHER

Sponsor Role collaborator

Genome Alberta

OTHER

Sponsor Role collaborator

The Arthritis Society, Canada

OTHER

Sponsor Role collaborator

ReumaNederland

UNKNOWN

Sponsor Role collaborator

ZonMw: The Netherlands Organisation for Health Research and Development

OTHER

Sponsor Role collaborator

Alberta Children's Hospital

OTHER

Sponsor Role collaborator

Ontario Genomics

UNKNOWN

Sponsor Role collaborator

The Hospital for Sick Children

OTHER

Sponsor Role lead

Responsible Party

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Rae Yeung

Professor, Staff Physician and Senior Scientist

Responsibility Role PRINCIPAL_INVESTIGATOR

Principal Investigators

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Rae SM Yeung, MD, PhD, FRCPC

Role: PRINCIPAL_INVESTIGATOR

The Hospital for Sick Children (SickKids), University of Toronto

Nico Wulffraat, MD, PhD

Role: PRINCIPAL_INVESTIGATOR

Wilhelmina Children's Hospital, University Medical Center Utrecht

Susa Benseler, MD, PhD

Role: PRINCIPAL_INVESTIGATOR

Alberta Children's Hospital and Cumming School of Medicine, University of Calgary

Joost Swart, MD, PhD

Role: PRINCIPAL_INVESTIGATOR

Wilhelmina Children's Hospital, University Medical Center Utrecht

Bas Vastert, MD, PhD

Role: PRINCIPAL_INVESTIGATOR

Wilhelmina Children's Hospital, University Medical Center Utrecht

Locations

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Alberta Children's Hospital - University of Calgary

Calgary, Alberta, Canada

Site Status RECRUITING

Stollery Children's Hospital

Edmonton, Alberta, Canada

Site Status RECRUITING

BC Children's Hospital

Vancouver, British Columbia, Canada

Site Status RECRUITING

Children's Hospital Health Science Centre Winnipeg

Winnipeg, Manitoba, Canada

Site Status RECRUITING

Janeway Children's Hospital and Rehabilitation Centre

St. John's, Newfoundland and Labrador, Canada

Site Status RECRUITING

IWK Health Centre

Halifax, Nova Scotia, Canada

Site Status RECRUITING

McMaster Children's Hospital

Hamilton, Ontario, Canada

Site Status RECRUITING

Children's Hospital, London Health Sciences Centre

London, Ontario, Canada

Site Status RECRUITING

Children's Hospital of Eastern Ontario

Ottawa, Ontario, Canada

Site Status RECRUITING

The Hospital for Sick Children

Toronto, Ontario, Canada

Site Status RECRUITING

Montréal Children's Hospital

Montreal, Quebec, Canada

Site Status RECRUITING

University of Saskatchewan

Saskatoon, Saskatchewan, Canada

Site Status RECRUITING

Amalia Children's Hospital, Radboudumc

Nijmegen, Gelderland, Netherlands

Site Status RECRUITING

Sint Maartenskinderkliniek

Boxmeer, North Brabant, Netherlands

Site Status RECRUITING

Emma Children's Hospital, Amsterdam UMC

Amsterdam, North Holland, Netherlands

Site Status RECRUITING

Willem-Alexander Children's Hospital, LUMC

Leiden, South Holland, Netherlands

Site Status RECRUITING

Sophia Children's Hospital, EMC

Rotterdam, South Holland, Netherlands

Site Status RECRUITING

Beatrix Children's Hospital, UMCG

Groningen, , Netherlands

Site Status RECRUITING

Wilhelmina Children's Hospital, UMCU

Utrecht, , Netherlands

Site Status RECRUITING

Countries

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Canada Netherlands

Central Contacts

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Alexander Mosoiu

Role: CONTACT

416-813-7654 ext. 302495

Amy Xu

Role: CONTACT

416-813-7654 ext. 302495

Facility Contacts

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Michele Gibbon

Role: primary

Regina de Geus

Role: primary

Other Identifiers

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1771

Identifier Type: -

Identifier Source: org_study_id

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