Single-dose Study to Assess Efficacy of Canakinumab (ACZ885) in Patients With Active Juvenile Idiopathic Arthritis (SJIA)

NCT ID: NCT00886769

Last Updated: 2017-03-29

Study Results

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

84 participants

Study Classification

INTERVENTIONAL

Study Start Date

2009-07-31

Study Completion Date

2011-01-31

Brief Summary

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This study assessed the initial efficacy and safety of canakinumab over a 4 week period in patients with systemic juvenile idiopathic arthritis (SJIA) having a flare. Response to treatment will be according to the adapted American College of Rheumatology(ACR)Pediatric 30 criteria at Day 15.

Detailed Description

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Conditions

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Systemic Juvenile Idiopathic Arthritis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Canakinumab

Patients received a single dose of subcutaneous(sc) injection of canakinumab (4 mg/kg) on Day 1. Maximal total single dose of canakinumab allowed was 300 mg. Any patient who required a dose greater than 150 mg (patients\>37.5 kg) received two sc injections.

Group Type EXPERIMENTAL

Canakinumab

Intervention Type DRUG

Canakinumab was supplied in individual 6 mL glass vials each containing 150 mg canakinumab powder as a lyophilized cake. Each reconstituted vial provided 150mg of canakinumab per 1 mL.

Placebo

Patients received a single dose matching placebo of canakinumab on day 1.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo was provided in individual 6 mL glass vials each containing 150 mg placebo powder matching canakinumab as a lyophilized cake. Each reconstitued vial provided 150mg of placebo per 1 mL.

Interventions

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Canakinumab

Canakinumab was supplied in individual 6 mL glass vials each containing 150 mg canakinumab powder as a lyophilized cake. Each reconstituted vial provided 150mg of canakinumab per 1 mL.

Intervention Type DRUG

Placebo

Placebo was provided in individual 6 mL glass vials each containing 150 mg placebo powder matching canakinumab as a lyophilized cake. Each reconstitued vial provided 150mg of placebo per 1 mL.

Intervention Type DRUG

Other Intervention Names

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ACZ885

Eligibility Criteria

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Inclusion Criteria

1. Confirmed diagnosis of systemic juvenile idiopathic arthritis as per ILAR definition that must have occurred at least 2 months prior to enrollment with onset of disease \< 16 years of age:

* Arthritis in one or more joints with or preceded by fever of at least 2 weeks duration that is documented to be daily/quotidian for at least 3 days and accompanied by one or more of the following:
* evanescent nonfixed erythematous rash,
* generalized lymph node enlargement,
* hepatomegaly and/ or splenomegaly,
* serositis
2. Parent's or legal guardian's written informed consent and child's assent, if appropriate, or patient's informed consent for ≥ 18 years of age
3. Male and female patients aged ≥ 2 to \< 20 years of age
4. Active disease at the time of enrollment defined as follows:

* At least 2 joints with active arthritis
* Documented spiking, intermittent fever (body temperature \> 38°C) for at least 1 day during the screening period within 1 week before first canakinumab/placebo dose
* C-reactive protein (CRP) \> 30 mg/L (normal range \< 10 mg/L)
5. Naïve to canakinumab

Exclusion Criteria

Patients who fulfilled one or more of the following criteria were not eligible for inclusion in this study:

1. Pregnant or nursing (lactating) female patients
2. Female patients having reached sexual maturity unless their career, lifestyle, or sexual orientation precluded intercourse with a male partner and/or they were using an acceptable method of contraception
3. History of hypersensitivity to study drug or to biologics.
4. Diagnosis of active macrophage-activation syndrome (MAS) (Ravelli, Magni-Manzoni and Pistorio 2005) within the last 6 months
5. With active or recurrent bacterial, fungal or viral infection, including patients with evidence of human immunodeficiency virus (HIV) infection, hepatitis B or hepatitis C infection
Minimum Eligible Age

2 Years

Maximum Eligible Age

19 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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International Maternal Pediatric Adolescent AIDS Clinical Trials Group

NETWORK

Sponsor Role collaborator

Southwest Pediatric Nephrology Study Group

OTHER

Sponsor Role collaborator

Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Novartis Pharmaceuticals

Role: STUDY_DIRECTOR

Novartis Pharmaceuticals

Locations

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University of Alabama at Birmingham

Birmingham, Alabama, United States

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Arkansas Children's Hospital Research Inst

Little Rock, Arkansas, United States

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Children's Hospital Los Angeles

Los Angeles, California, United States

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Children's National Medical Center

Washington D.C., District of Columbia, United States

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University of Chicago Medical Center

Chicago, Illinois, United States

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University of Louisville

Louisville, Kentucky, United States

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Tufts Medical Center

Boston, Massachusetts, United States

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Tufts New England Medical Center-Dept. of Allergy

Boston, Massachusetts, United States

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St. Barnabas Ambulatory Care Center

Livingston, New Jersey, United States

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Children's Hospital Medical Center

Cincinnati, Ohio, United States

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Children's Hospital/Neurology

Cinncinati, Ohio, United States

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Nationwide Children's Hospital

Columbus, Ohio, United States

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Legacy Emanuel Hospital

Portland, Oregon, United States

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Legacy Emanual Research

Portland, Oregon, United States

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Specially For Children

Austin, Texas, United States

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Novartis Investigative Site

Buenos Aires, , Argentina

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Capital Federal, , Argentina

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La Plata, , Argentina

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Brussels, , Belgium

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Ghent, , Belgium

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Laken, , Belgium

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Leuven, , Belgium

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Curitiba, , Brazil

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Porto Alegre, , Brazil

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Rio de Janeiro, , Brazil

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São Paulo, , Brazil

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Vancouver, British Columbia, Canada

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Halifax, Nova Scotia, Canada

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Toronto, Ontario, Canada

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Montreal, Quebec, Canada

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Calgary, , Canada

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Arhus N, , Denmark

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Le Kremlin-Bicêtre, , France

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Lyon, , France

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Paris, , France

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Strasbourg, , France

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Bad Bamstedt, , Germany

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Berlin, , Germany

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Bremen, , Germany

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Dresden, , Germany

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Freiburg im Breisgau, , Germany

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Garmisch-Partenkirch, , Germany

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Geißen, , Germany

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Hamburg, , Germany

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Hanover, , Germany

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Krefeld, , Germany

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Mainz, , Germany

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Münster, , Germany

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Saint Augustin, , Germany

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Stuttgart, , Germany

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Tübingen, , Germany

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Thessaloniki, , Greece

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Budapest, , Hungary

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Haifa, , Israel

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Kfar Saba, , Israel

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Petah Tikva, , Israel

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Ramat Gan, , Israel

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Rehovot, , Israel

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Bologna, , Italy

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Florence, , Italy

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Genova, , Italy

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Milan, , Italy

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Napoli, , Italy

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Padua, , Italy

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Rome, , Italy

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Scafati, , Italy

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Torino, , Italy

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Utrecht, , Netherlands

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Oslo, , Norway

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Lima, , Peru

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Warsaw, , Poland

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Berea, Durban, South Africa

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Mayville, Durban, South Africa

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Pretoria, , South Africa

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Barcelona, , Spain

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Madrid, , Spain

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Valencia, , Spain

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Stockholm, , Sweden

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Bern, , Switzerland

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Lausanne, , Switzerland

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Zurich, , Switzerland

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Ankara, , Turkey (Türkiye)

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Istanbul, , Turkey (Türkiye)

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Izmir, , Turkey (Türkiye)

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Birmingham, , United Kingdom

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Liverpool, , United Kingdom

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London, , United Kingdom

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Manchester, , United Kingdom

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New Castle Upon Tyne, , United Kingdom

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Norwich, , United Kingdom

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Oxford, , United Kingdom

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Countries

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United States Argentina Belgium Brazil Canada Denmark France Germany Greece Hungary Israel Italy Netherlands Norway Peru Poland South Africa Spain Sweden Switzerland Turkey (Türkiye) United Kingdom

References

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Ruperto N, Brunner HI, Quartier P, Constantin T, Wulffraat NM, Horneff G, Kasapcopur O, Schneider R, Anton J, Barash J, Berner R, Corona F, Cuttica R, Fouillet-Desjonqueres M, Fischbach M, Foster HE, Foell D, Radominski SC, Ramanan AV, Trauzeddel R, Unsal E, Levy J, Vritzali E, Martini A, Lovell DJ; Paediatric Rheumatology International Trials Organisation (PRINTO) and the Pediatric Rheumatology Collaborative Study Group (PRCSG). Canakinumab in patients with systemic juvenile idiopathic arthritis and active systemic features: results from the 5-year long-term extension of the phase III pivotal trials. Ann Rheum Dis. 2018 Dec;77(12):1710-1719. doi: 10.1136/annrheumdis-2018-213150. Epub 2018 Sep 29.

Reference Type DERIVED
PMID: 30269054 (View on PubMed)

Brachat AH, Grom AA, Wulffraat N, Brunner HI, Quartier P, Brik R, McCann L, Ozdogan H, Rutkowska-Sak L, Schneider R, Gerloni V, Harel L, Terreri M, Houghton K, Joos R, Kingsbury D, Lopez-Benitez JM, Bek S, Schumacher M, Valentin MA, Gram H, Abrams K, Martini A, Lovell DJ, Nirmala NR, Ruperto N; Pediatric Rheumatology International Trials Organization (PRINTO) and the Pediatric Rheumatology Collaborative Study Group (PRCSG). Early changes in gene expression and inflammatory proteins in systemic juvenile idiopathic arthritis patients on canakinumab therapy. Arthritis Res Ther. 2017 Jan 23;19(1):13. doi: 10.1186/s13075-016-1212-x.

Reference Type DERIVED
PMID: 28115015 (View on PubMed)

Grom AA, Ilowite NT, Pascual V, Brunner HI, Martini A, Lovell D, Ruperto N; Paediatric Rheumatology International Trials Organisation and the Pediatric Rheumatology Collaborative Study Group; Leon K, Lheritier K, Abrams K. Rate and Clinical Presentation of Macrophage Activation Syndrome in Patients With Systemic Juvenile Idiopathic Arthritis Treated With Canakinumab. Arthritis Rheumatol. 2016 Jan;68(1):218-28. doi: 10.1002/art.39407.

Reference Type DERIVED
PMID: 26314396 (View on PubMed)

Ruperto N, Brunner HI, Quartier P, Constantin T, Wulffraat N, Horneff G, Brik R, McCann L, Kasapcopur O, Rutkowska-Sak L, Schneider R, Berkun Y, Calvo I, Erguven M, Goffin L, Hofer M, Kallinich T, Oliveira SK, Uziel Y, Viola S, Nistala K, Wouters C, Cimaz R, Ferrandiz MA, Flato B, Gamir ML, Kone-Paut I, Grom A, Magnusson B, Ozen S, Sztajnbok F, Lheritier K, Abrams K, Kim D, Martini A, Lovell DJ; PRINTO; PRCSG. Two randomized trials of canakinumab in systemic juvenile idiopathic arthritis. N Engl J Med. 2012 Dec 20;367(25):2396-406. doi: 10.1056/NEJMoa1205099.

Reference Type DERIVED
PMID: 23252526 (View on PubMed)

Related Links

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http://www.NovartisClinicalTrials.com

Click here for more information about this study

Other Identifiers

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EudraCT: 2008-005476-27

Identifier Type: -

Identifier Source: secondary_id

CACZ885G2305

Identifier Type: -

Identifier Source: org_study_id

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