A Research Study to Advance the CF Therapeutics Pipeline for People Without Modulators

NCT ID: NCT06504589

Last Updated: 2025-10-01

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Total Enrollment

400 participants

Study Classification

OBSERVATIONAL

Study Start Date

2024-09-18

Study Completion Date

2029-08-14

Brief Summary

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The REACH study is for people with CF who do not take cystic fibrosis transmembrane conductance regulator (CFTR) modulators. The goal of the REACH study is to collect research data, including health data and specimens, from people with CF who do not take CFTR modulators. This data may be used to inform CF research, help design CF clinical trials and support the development of new treatments for people with CF who do not take CFTR modulators.

Another goal of this study is to learn about research involvement for people with CF who do not take CFTR modulators, engage them in research, and give them an opportunity to learn about what is involved in participating in a CF research study.

Detailed Description

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People with Cystic Fibrosis (pwCF) who are genetically ineligible and/or not taking cystic fibrosis transmembrane conductance regulator (CFTR) modulators currently face future health that is considerably different from the approximately 90% of pwCF in the United States who benefit from CFTR modulators. New treatments are being advanced for pwCF who are genetically ineligible or not taking CFTR modulators and these therapies will include both nucleic acid-based therapies (NABTs) to address the underlying defect in CFTR and symptomatic therapies aimed at targeting the symptoms of CF. A key concern for this limited and underserved patient population is being able to advance multiple therapeutic programs in parallel. To complete these studies, CF researchers will need to be able to reach this community effectively while also promoting the use of innovative trial designs.

The REACH Study is a prospective, longitudinal, observational research study to obtain research quality (i.e., monitored research) CF outcome data. Primary outcome endpoints of the Core study (collected across all study participants) are aligned with anticipated clinical trial outcome endpoints needed in overall development of therapies for the CF population unable to benefit from CFTR modulators. This study will also include sub-studies to obtain specialized measures which may help inform efficacy and safety evaluations of new therapies by providing CF control data. Finally, this study also seeks to assess research solicitation and research participation for the CF population that is modulator ineligible or not taking modulators. The observational data collected within this study may be used in characterizing this CF population, developing innovative trial designs, for comparison when evaluating new or experimental CF therapies, and/or in CF research.

Conditions

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Cystic Fibrosis

Study Design

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Observational Model Type

COHORT

Study Time Perspective

PROSPECTIVE

Eligibility Criteria

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Inclusion Criteria

B. No use of an investigational drug within 90 days prior to and including Visit 1

C. Not currently participating in an interventional drug or device trial. Participation in long-term safety follow-up studies (without redosing) and/or behavioral intervention trials is allowed.

D. No initiation of new chronic therapy (e.g., ibuprofen, azithromycin, inhaled tobramycin, Cayston®) within 28 days prior to and including Visit 1

E. No acute use of antibiotics (oral, inhaled or IV) or acute use of systemic corticosteroids for respiratory tract symptoms within 28 days prior to and including Visit 1
Minimum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Washington University School of Medicine

OTHER

Sponsor Role collaborator

Florida State University

OTHER

Sponsor Role collaborator

University of North Carolina, Chapel Hill

OTHER

Sponsor Role collaborator

University of Toronto

OTHER

Sponsor Role collaborator

Cystic Fibrosis Foundation

OTHER

Sponsor Role collaborator

Nicole Hamblett

OTHER

Sponsor Role lead

Responsible Party

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Nicole Hamblett

Professor of Pediatrics, Division of Pulmonary and Sleep Medicine, UW School of Medicine Adjunct Professor, Biostatistics, UW School of Medicine Co-Executive Director, CF Therapeutics Development Network

Responsibility Role SPONSOR_INVESTIGATOR

Principal Investigators

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Deepika Polineni, MD, MPH

Role: PRINCIPAL_INVESTIGATOR

Washington University School of Medicine

Nicole Mayer-Hamblett, PhD

Role: PRINCIPAL_INVESTIGATOR

Seattle Children's Hospital

Scott Donaldson, MD

Role: PRINCIPAL_INVESTIGATOR

University of North Carolina, Chapel Hill

Felix Ratjen, MD

Role: PRINCIPAL_INVESTIGATOR

University of Toronto

Locations

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The Children's Hospital Alabama, University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status RECRUITING

Phoenix Children's Hospital

Phoenix, Arizona, United States

Site Status RECRUITING

Tucson Cystic Fibrosis Center

Tucson, Arizona, United States

Site Status RECRUITING

University of Arkansas for Medical Sciences

Little Rock, Arkansas, United States

Site Status RECRUITING

University of California San Diego

La Jolla, California, United States

Site Status NOT_YET_RECRUITING

Childrens Hospital Los Angeles

Los Angeles, California, United States

Site Status RECRUITING

Stanford University Medical Center

Palo Alto, California, United States

Site Status RECRUITING

University of California, San Francisco - Adult Center

San Francisco, California, United States

Site Status RECRUITING

University of California, San Francisco - Peds Center

San Francisco, California, United States

Site Status RECRUITING

Children's Hospital Colorado

Aurora, Colorado, United States

Site Status RECRUITING

National Jewish Health

Denver, Colorado, United States

Site Status RECRUITING

University of Florida

Gainesville, Florida, United States

Site Status RECRUITING

University of Miami

Miami, Florida, United States

Site Status RECRUITING

Central Florida Pulmonary Group

Orlando, Florida, United States

Site Status RECRUITING

Tampa General Hospital

Tampa, Florida, United States

Site Status RECRUITING

Children's Healthcare of Atlanta and Emory University

Atlanta, Georgia, United States

Site Status RECRUITING

Augusta University

Augusta, Georgia, United States

Site Status RECRUITING

Saint Luke's Cystic Fibrosis Center of Idaho

Boise, Idaho, United States

Site Status RECRUITING

Northwestern University

Chicago, Illinois, United States

Site Status RECRUITING

Riley Hospital for Children

Indianapolis, Indiana, United States

Site Status RECRUITING

University of Kansas Medical Center

Kansas City, Kansas, United States

Site Status RECRUITING

University of Kentucky

Lexington, Kentucky, United States

Site Status RECRUITING

Tulane University

Metairie, Louisiana, United States

Site Status RECRUITING

John Hopkins Hospital

Baltimore, Maryland, United States

Site Status NOT_YET_RECRUITING

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status RECRUITING

Boston Children's Hospital

Boston, Massachusetts, United States

Site Status RECRUITING

University of Massachusetts Memorial Health Care

Worcester, Massachusetts, United States

Site Status RECRUITING

University of Michigan, Michigan Medicine

Ann Arbor, Michigan, United States

Site Status RECRUITING

Wayne State University Harper University Hospital

Detroit, Michigan, United States

Site Status RECRUITING

Corewell Health Helen DeVos

Grand Rapids, Michigan, United States

Site Status RECRUITING

The Minnesota Cystic Fibrosis Center

Minneapolis, Minnesota, United States

Site Status RECRUITING

Washington University School of Medicine

St Louis, Missouri, United States

Site Status RECRUITING

Billings Clinic

Billings, Montana, United States

Site Status RECRUITING

University of Nebraska Medical Center

Omaha, Nebraska, United States

Site Status RECRUITING

Morristown Medical Center

Morristown, New Jersey, United States

Site Status RECRUITING

The Cystic Fibrosis Center of Western New York

Buffalo, New York, United States

Site Status NOT_YET_RECRUITING

Cohen Children's Medical Center of New York

New Hyde Park, New York, United States

Site Status RECRUITING

Columbia University Cystic Fibrosis Program

New York, New York, United States

Site Status RECRUITING

University of Rochester Medical Center Strong Memorial

Rochester, New York, United States

Site Status RECRUITING

New York Medical College at Westchester Medical Center

Valhalla, New York, United States

Site Status RECRUITING

University of North Carolina at Chapel Hill

Chapel Hill, North Carolina, United States

Site Status RECRUITING

Atrium Health Wake Forest Baptist

Winston-Salem, North Carolina, United States

Site Status RECRUITING

Cincinnati Children's Hospital Medical Center

Cincinnati, Ohio, United States

Site Status RECRUITING

Rainbow Babies and Children's Hospital/University Hospitals Cleveland Medical Center

Cleveland, Ohio, United States

Site Status RECRUITING

Cleveland Clinic Cystic Fibrosis Program

Cleveland, Ohio, United States

Site Status NOT_YET_RECRUITING

Nationwide Children's Hospital

Columbus, Ohio, United States

Site Status RECRUITING

Dayton Children's Hospital

Dayton, Ohio, United States

Site Status RECRUITING

Oregon Health & Sciences University

Portland, Oregon, United States

Site Status RECRUITING

Hershey Medical Center Pennsylvania State University

Hershey, Pennsylvania, United States

Site Status RECRUITING

Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, United States

Site Status RECRUITING

University of Pennsylvania

Philadelphia, Pennsylvania, United States

Site Status RECRUITING

University of Pittsburgh Medical Center

Pittsburgh, Pennsylvania, United States

Site Status RECRUITING

Medical University of South Carolina

Charleston, South Carolina, United States

Site Status RECRUITING

Prisma Health Children's Hospital - Midlands

Columbia, South Carolina, United States

Site Status RECRUITING

Vanderbilt University Medical Center

Nashville, Tennessee, United States

Site Status RECRUITING

Dell Children's Medical Center of Central Texas

Austin, Texas, United States

Site Status RECRUITING

University of Texas Southwestern / Children's Health

Dallas, Texas, United States

Site Status RECRUITING

University of Texas Southwestern

Dallas, Texas, United States

Site Status RECRUITING

Cook Children's Medical Center

Fort Worth, Texas, United States

Site Status RECRUITING

Baylor College of Medicine

Houston, Texas, United States

Site Status RECRUITING

Adult Cystic Fibrosis Center at the University of Utah

Salt Lake City, Utah, United States

Site Status RECRUITING

Inova L.J. Murphy Pediatric CF Program

Fairfax, Virginia, United States

Site Status RECRUITING

Virginia Commonwealth University

Richmond, Virginia, United States

Site Status RECRUITING

Seattle Children's Hospital

Seattle, Washington, United States

Site Status RECRUITING

University of Washington Medical Center

Seattle, Washington, United States

Site Status RECRUITING

Providence Medical Group, Cystic Fibrosis Clinic

Spokane, Washington, United States

Site Status RECRUITING

West Virginia University - Morgantown

Morgantown, West Virginia, United States

Site Status RECRUITING

University of Wisconsin

Madison, Wisconsin, United States

Site Status RECRUITING

Countries

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United States

Central Contacts

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Olena Boyarska

Role: CONTACT

206-884-1681

Anna Mead

Role: CONTACT

206-884-7531

Facility Contacts

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Kathryn Monroe

Role: primary

205-638-5599

Natalia Argel

Role: primary

602-933-0343

Elizabeth Ryan

Role: primary

520-850-8688

Kathleen Hicks

Role: primary

501-686-5527

Jenna Mielke

Role: primary

619-471-0822

Carmen Reyes

Role: primary

323-361-2662

Jacquelyn Spano

Role: primary

650-721-1132

Courtney Moreno

Role: primary

415-476-2984

Ngoc Ly

Role: primary

415-476-4979

Mary Cross

Role: primary

720-777-4645

Alix Wilson

Role: primary

303-270-2517

Chrystal Bailey

Role: primary

Ylber (Ivan) Whitaker

Role: primary

305-243-5545

Desiree Serr

Role: primary

407-841-1100

Andrew Marino

Role: primary

813-844-4907

Ashleigh Streby

Role: primary

404-727-0305

Heidi Stapp

Role: primary

706-721-7699

Lejla Godusevic

Role: primary

208-381-4717

Rachel Nelson

Role: primary

312-695-0415

Lisa Bendy

Role: primary

317-278-7152

Lawrence Scott

Role: primary

913-588-4020

Chase Whitaker

Role: primary

Role: backup

859-218-4810

Adrienne Savant

Role: primary

504-896-9436

Jeanne Pinto

Role: primary

410-955-9782

Margot Hardcastle

Role: primary

617-726-3719

Robert Fowler

Role: primary

6173551834

Jaclyn Longtine

Role: primary

508-856-5472

Dawn Kruse

Role: primary

734-615-3266

Debra Driscoll

Role: primary

313-745-2221

Alicia Castillo Bahena

Role: primary

6162679304

CF Trials Contact University of Minnesota, Participant Contact

Role: primary

Irma Bauer

Role: primary

314-747-2940

Jerimiah Lysinger

Role: primary

406-238-5137

Michel Veit

Role: primary

402-559-7585

Debra Connolly

Role: primary

973-971-7293

Julianne Hergenroder

Role: primary

Susan Galvin

Role: primary

516-321-8606

Emily DiMango

Role: primary

212-305-0290

Barb Johnson

Role: primary

585-276-4123

Zachary Messer

Role: primary

914-594-2352

Julie Goudy

Role: primary

984-974-2364

Anna Pippins

Role: primary

Kelly Thornton

Role: primary

513-636-0604

Primary RC & Participant Contact General Contact

Role: primary

Dave Weaver

Role: primary

216-445-6671

Diana Gilmore

Role: primary

614-722-4752

Amy Jones

Role: primary

937-641-3693

Jenna Bucher

Role: primary

503-494-7807

Diane M Kitch

Role: primary

717-531-5646

Erin Donnelly

Role: primary

609-781-0307

Melissa Molter

Role: primary

215-662-3116

Adrienne DeRicco

Role: primary

4126928069

Ashley Warden

Role: primary

843-792-4349

Veronica Lipscomb

Role: primary

Brijesh Patel

Role: primary

615-343-4865

Kristina "Tina" Adrean

Role: primary

512-324-9999

Keianna Brown

Role: primary

214-456-5489

Ashley Keller

Role: primary

214-648-6233

Anna Reyes

Role: primary

682-885-6589

Tracy Mosely

Role: primary

832-822-3309

Kristyn Packer

Role: primary

801-520-5106

Colleen Mann

Role: primary

703-776-6485

Akilah Pierre-Louis

Role: primary

Sharon McNamara

Role: primary

206-987-3921

Lauren Bartlett

Role: primary

503-583-2869

Joan Milton

Role: primary

509-474-4323

Tammy Clark

Role: primary

3042935264

Melanie Nelson

Role: primary

608-265-4617

Other Identifiers

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REACH-OB-23

Identifier Type: -

Identifier Source: org_study_id

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