A Study of Tagraxofusp in Combination With Venetoclax and Azacitidine in Adults With Untreated CD123+ Acute Myeloid Leukemia Who Cannot Undergo Intensive Chemotherapy

NCT ID: NCT06456463

Last Updated: 2026-01-12

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

83 participants

Study Classification

INTERVENTIONAL

Study Start Date

2025-01-14

Study Completion Date

2030-02-11

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

This study will be divided into 2 parts (Part 1 and Part 2). Part 1 will evaluate 2 doses of tagraxofusp (9 and 12 micrograms/kilogram/day \[μg/kg/day\]), used in combination with venetoclax and azacitidine, to determine the dose for Part 2. This determined dose, in combination with venetoclax and azacitidine, will then be further evaluated in Part 2 in 2 cohorts (TP53 mutated and TP53 wild type). Both parts will be conducted in participants with previously untreated CD123+ AML who are ineligible for intensive chemotherapy.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Acute Myeloid Leukemia

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

SEQUENTIAL

Part 1 (randomized) will evaluate 2 dose levels of tagraxofusp in parallel. The decision to proceed to Part 2 (non-randomized) will be based upon review of cumulative data from Part 1.
Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Part 1 - Tagraxofusp (9 μg/kg/day)

Participants will receive tagraxofusp in combination with venetoclax and azacitidine.

Group Type EXPERIMENTAL

Tagraxofusp

Intervention Type DRUG

Tagraxofusp will be administered by intravenous infusion for 3 consecutive days during each 28-day cycle.

Venetoclax

Intervention Type DRUG

Venetoclax will be administered as an oral tablet (400 milligrams \[mg\]) daily, with ramp up in Cycle 1, and should be continued at target dose (400 mg) for the remainder of Cycle 1 and subsequent cycles of 28 days each.

Azacitidine

Intervention Type DRUG

Azacitidine will be administered subcutaneously or by intravenous infusion (75 milligrams/square meter) over 7 days of each 28-day cycle, per institutional guidelines/physician choice.

Part 1 - Tagraxofusp (12 μg/kg/day)

Participants will receive tagraxofusp in combination with venetoclax and azacitidine.

Group Type EXPERIMENTAL

Tagraxofusp

Intervention Type DRUG

Tagraxofusp will be administered by intravenous infusion for 3 consecutive days during each 28-day cycle.

Venetoclax

Intervention Type DRUG

Venetoclax will be administered as an oral tablet (400 milligrams \[mg\]) daily, with ramp up in Cycle 1, and should be continued at target dose (400 mg) for the remainder of Cycle 1 and subsequent cycles of 28 days each.

Azacitidine

Intervention Type DRUG

Azacitidine will be administered subcutaneously or by intravenous infusion (75 milligrams/square meter) over 7 days of each 28-day cycle, per institutional guidelines/physician choice.

Part 2 - Tagraxofusp (Selected Dose) and TP53 Wild Type

Participants (TP53 wild type) will receive tagraxofusp in combination with venetoclax and azacitidine.

Group Type EXPERIMENTAL

Tagraxofusp

Intervention Type DRUG

Tagraxofusp will be administered by intravenous infusion for 3 consecutive days during each 28-day cycle.

Venetoclax

Intervention Type DRUG

Venetoclax will be administered as an oral tablet (400 milligrams \[mg\]) daily, with ramp up in Cycle 1, and should be continued at target dose (400 mg) for the remainder of Cycle 1 and subsequent cycles of 28 days each.

Azacitidine

Intervention Type DRUG

Azacitidine will be administered subcutaneously or by intravenous infusion (75 milligrams/square meter) over 7 days of each 28-day cycle, per institutional guidelines/physician choice.

Part 2 - Tagraxofusp (Selected Dose) and TP53 Mutated

Participants (TP53 mutated) will receive tagraxofusp in combination with venetoclax and azacitidine.

Group Type EXPERIMENTAL

Tagraxofusp

Intervention Type DRUG

Tagraxofusp will be administered by intravenous infusion for 3 consecutive days during each 28-day cycle.

Venetoclax

Intervention Type DRUG

Venetoclax will be administered as an oral tablet (400 milligrams \[mg\]) daily, with ramp up in Cycle 1, and should be continued at target dose (400 mg) for the remainder of Cycle 1 and subsequent cycles of 28 days each.

Azacitidine

Intervention Type DRUG

Azacitidine will be administered subcutaneously or by intravenous infusion (75 milligrams/square meter) over 7 days of each 28-day cycle, per institutional guidelines/physician choice.

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Tagraxofusp

Tagraxofusp will be administered by intravenous infusion for 3 consecutive days during each 28-day cycle.

Intervention Type DRUG

Venetoclax

Venetoclax will be administered as an oral tablet (400 milligrams \[mg\]) daily, with ramp up in Cycle 1, and should be continued at target dose (400 mg) for the remainder of Cycle 1 and subsequent cycles of 28 days each.

Intervention Type DRUG

Azacitidine

Azacitidine will be administered subcutaneously or by intravenous infusion (75 milligrams/square meter) over 7 days of each 28-day cycle, per institutional guidelines/physician choice.

Intervention Type DRUG

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

Tag Elzonris Ven Venclexta Aza Vidaza

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Previously untreated with histological confirmation of AML by World Health Organization 2022 criteria and are ineligible for treatment with a standard cytarabine and anthracycline induction regimen due to age, or comorbidity.
* Participant has any level of CD123 expression on blasts.
* Participants must be considered ineligible for intensive chemotherapy, defined by the following:

* ≥75 years of age; or
* ≥18 to 74 years of age with at least 1 of the following:

* Eastern Cooperative Oncology Group (ECOG) performance status of 2 or 3.
* Diffusing capacity of the lung for carbon monoxide of ≤65% or forced expiratory volume in 1 second ≤65%.
* Baseline creatinine clearance ≥30 to \<45 milliliters/minute calculated by the Cockcroft Gault formula or measured by 24-hour urine collection.
* Hepatic disorder with total bilirubin \>1.5 x upper limit of normal.
* Any other condition for which the physician judges the participant to be unsuitable for intensive chemotherapy.
* ECOG performance status:

* 0 to 2 for participants ≥75 years of age, or
* 0 to 3 for participants ≥18 to 74 years of age.

Exclusion Criteria

* Participant has received prior therapy for AML.
* Participant is willing and able to receive standard induction therapy.
* Participant has received treatment for an antecedent hematologic disease with a hypomethylating agent, venetoclax, tagraxofusp, purine analogue, cytarabine, intensive chemotherapy, SCT, chimeric antigen receptor-T therapy, or other experimental therapies.
* Participant has AML with central nervous system involvement.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Stemline Therapeutics, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

University of California, Los Angeles

Los Angeles, California, United States

Site Status RECRUITING

Stanford Health Care

Stanford, California, United States

Site Status RECRUITING

University of Miami

Miami, Florida, United States

Site Status RECRUITING

AdventHealth Cancer Institute

Orlando, Florida, United States

Site Status RECRUITING

University of Chicago

Chicago, Illinois, United States

Site Status NOT_YET_RECRUITING

Dana Farber Cancer Institute (DFCI)

Boston, Massachusetts, United States

Site Status RECRUITING

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status RECRUITING

Beth Israel Deaconess Medical Center

Boston, Massachusetts, United States

Site Status RECRUITING

Henry Ford Health System Brigitte Harris Cancer Pavillion

Detroit, Michigan, United States

Site Status RECRUITING

Washington University - Siteman Cancer Center

St Louis, Missouri, United States

Site Status RECRUITING

John Theurer Cancer Center - Hackensack Meridian Health

Hackensack, New Jersey, United States

Site Status RECRUITING

Rutgers Cancer Institute

New Brunswick, New Jersey, United States

Site Status RECRUITING

Roswell Park Cancer Institute

Buffalo, New York, United States

Site Status RECRUITING

North Shore University Hospital

Manhasset, New York, United States

Site Status NOT_YET_RECRUITING

NYU Langone Health

New York, New York, United States

Site Status RECRUITING

Columbia University Irving Medical Center

New York, New York, United States

Site Status RECRUITING

Novant Health Presbyterian Medical Center

Charlotte, North Carolina, United States

Site Status RECRUITING

Novant Health Derrick L Davis Cancer Center

Winston-Salem, North Carolina, United States

Site Status RECRUITING

Cleveland Clinic Foundation

Cleveland, Ohio, United States

Site Status RECRUITING

Sydney Kimmel (Thomas Jefferson University)

Philadelphia, Pennsylvania, United States

Site Status NOT_YET_RECRUITING

Sarah Cannon, the Cancer Institute of HCA Healthcare

Nashville, Tennessee, United States

Site Status RECRUITING

Tennessee Oncology

Nashville, Tennessee, United States

Site Status RECRUITING

Baylor Scott & White Health

Dallas, Texas, United States

Site Status RECRUITING

University of Texas MD Anderson Cancer Center

Houston, Texas, United States

Site Status RECRUITING

Huntsman Cancer Institute

Salt Lake City, Utah, United States

Site Status NOT_YET_RECRUITING

Concord Repatriation General Hospital

Concord, New South Wales, Australia

Site Status RECRUITING

Townsville Hospital

Douglas, Queensland, Australia

Site Status RECRUITING

Royal Adelaide Hospital

Adelaide, South Australia, Australia

Site Status RECRUITING

Box Hill Hospital

Box Hill, Victoria, Australia

Site Status RECRUITING

Monash Medical Centre

Clayton, Victoria, Australia

Site Status RECRUITING

St. Vincents Hospital

Fitzroy, Victoria, Australia

Site Status RECRUITING

Austin Hospital

Heidelberg, Victoria, Australia

Site Status RECRUITING

Royal Perth Hospital

Perth, Western Australia, Australia

Site Status NOT_YET_RECRUITING

Countries

Review the countries where the study has at least one active or historical site.

United States Australia

Central Contacts

Reach out to these primary contacts for questions about participation or study logistics.

Stemline Trials

Role: CONTACT

1-877-332-7961

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

U1111-1290-9087

Identifier Type: OTHER

Identifier Source: secondary_id

2024-514660-48

Identifier Type: OTHER

Identifier Source: secondary_id

STML-401-0423

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.