Study of Magrolimab in Combination With Azacitidine Versus Physician's Choice of Venetoclax in Combination With Azacitidine or Intensive Chemotherapy in Patients With TP53 Mutant Acute Myeloid Leukemia That Have Not Been Treated

NCT ID: NCT04778397

Last Updated: 2025-02-05

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

258 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-07-01

Study Completion Date

2024-03-25

Brief Summary

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The goal of this clinical study is to compare the effectiveness of the study drugs, magrolimab in combination with azacitidine, versus venetoclax in combination with azacitidine in participants with previously untreated TP53 mutant acute myeloid leukemia (AML).

Detailed Description

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Conditions

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Acute Myeloid Leukemia

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Magrolimab + Azacitidine

Participants will receive an escalating dose of magrolimab and a fixed dose of azacitidine.

Group Type EXPERIMENTAL

Magrolimab

Intervention Type DRUG

Administered intravenously (IV).

Azacitidine

Intervention Type DRUG

Administered either subcutaneously (SC) or IV, 75 milligrams per square meter (mg/m\^2) on Days 1-7 or Days 1-5, 8 and 9 during every cycle (Cycle=28 days).

Control Arm: Venetoclax + Azacitidine

Participants who are appropriate for non-intensive therapy will receive an escalating dose of venetoclax and a fixed dose of azacitidine.

Group Type ACTIVE_COMPARATOR

Venetoclax

Intervention Type DRUG

Administered orally at a dose of 100 milligrams (mg) on Day 1, 200 mg on Day 2, 400 mg on Days 3-28 during Cycle 1, followed by 400 mg on Days 1-28 during every cycle (Cycle=28 days).

Azacitidine

Intervention Type DRUG

Administered either subcutaneously (SC) or IV, 75 milligrams per square meter (mg/m\^2) on Days 1-7 or Days 1-5, 8 and 9 during every cycle (Cycle=28 days).

Control Arm: 7+3 Chemotherapy

Participants who are appropriate for intensive therapy will receive 7+3 chemotherapy: 7 day treatment with cytarabine and 3 day treatment with daunorubicin or idarubicin during induction and high-dose cytarabine and steroidal eye drops during consolidation.

Group Type ACTIVE_COMPARATOR

Cytarabine

Intervention Type DRUG

Induction: administered continuous infusion, 100 or 200 mg/m\^2 on Days 1-7 (7+3 induction) and if needed Days 1-5 (5+2 induction) during a cycle (Cycle=Up to 42 Days).

Consolidation: administered IV, 1500 or 3000 mg/m\^2 on Days 1, 3, and 5 once every 12 hours for up to 4 cycles.

Daunorubicin

Intervention Type DRUG

Administered IV peripherally (IVP), 60 mg/m\^2 on Days 1-3 (7+3 induction) and if needed Days 1-2 (5+2 induction) during a cycle (Cycle=Up to 42 days).

Idarubicin

Intervention Type DRUG

Administered IV, 12 mg/m\^2 on Days 1-3 (7+3 induction) and if needed Days 1-2 (5+2 induction) during a cycle (Cycle=Up to 42 days).

Steroidal Eye Drops

Intervention Type DRUG

Administered per institutional standard during consolidation.

Interventions

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Magrolimab

Administered intravenously (IV).

Intervention Type DRUG

Venetoclax

Administered orally at a dose of 100 milligrams (mg) on Day 1, 200 mg on Day 2, 400 mg on Days 3-28 during Cycle 1, followed by 400 mg on Days 1-28 during every cycle (Cycle=28 days).

Intervention Type DRUG

Azacitidine

Administered either subcutaneously (SC) or IV, 75 milligrams per square meter (mg/m\^2) on Days 1-7 or Days 1-5, 8 and 9 during every cycle (Cycle=28 days).

Intervention Type DRUG

Cytarabine

Induction: administered continuous infusion, 100 or 200 mg/m\^2 on Days 1-7 (7+3 induction) and if needed Days 1-5 (5+2 induction) during a cycle (Cycle=Up to 42 Days).

Consolidation: administered IV, 1500 or 3000 mg/m\^2 on Days 1, 3, and 5 once every 12 hours for up to 4 cycles.

Intervention Type DRUG

Daunorubicin

Administered IV peripherally (IVP), 60 mg/m\^2 on Days 1-3 (7+3 induction) and if needed Days 1-2 (5+2 induction) during a cycle (Cycle=Up to 42 days).

Intervention Type DRUG

Idarubicin

Administered IV, 12 mg/m\^2 on Days 1-3 (7+3 induction) and if needed Days 1-2 (5+2 induction) during a cycle (Cycle=Up to 42 days).

Intervention Type DRUG

Steroidal Eye Drops

Administered per institutional standard during consolidation.

Intervention Type DRUG

Other Intervention Names

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GS-4721

Eligibility Criteria

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Inclusion Criteria

* Individuals with confirmation of acute myeloid leukemia (AML) by World Health Organization criteria, previously untreated for AML, and who have presence of at least 1 TP53 gene mutation that is not benign or likely benign based on evaluation by either central laboratory or an approved local laboratory (after central review of the bone marrow TP53 mitigation next-generation sequencing test results) (individuals with biallelic 17p deletions, loss of both 17p alleles, are eligible based on locally evaluated cytogenetics/karyotype/fluorescence in situ hybridization (FISH) report).
* Individuals with white blood cell (WBC) count ≤ 20×10\^3/microliter (μL) prior to randomization. If the individual's WBC is \> 20×10\^3/μL prior to randomization, the individual can be enrolled, assuming all other eligibility criteria are met. However, the WBC should be ≤ 20×10\^3/μL prior to the first dose of study treatment and prior to each magrolimab dose the first 4 weeks (if the individual is randomized to the experimental arm) Note: Individuals can be treated with hydroxyurea and/or leukapheresis throughout the study or prior to randomization to reduce the WBC to ≤ 20×10\^3/μL to enable eligibility for study drug dosing.
* The hemoglobin must be ≥ 9 grams per deciliter (g/dL) prior to initial dose of study treatment.

Notes: Transfusions are allowed to meet hemoglobin eligibility.

* Individual has provided informed consent.
* Individual is willing and able to comply with clinic visits and procedure outlined in the study protocol.
* Individuals must have an Eastern Cooperative Oncology Group (ECOG) performance status of 0 to 2, except for individuals less than 75 years of age and appropriate for non-intensive treatment. For these individuals, the ECOG performance status score may be 0 to 3.
* Individuals must have adequate renal function as demonstrated by a creatinine clearance ≥ 30 milliliters per minute calculated by the Cockcroft Gault formula.
* Adequate cardiac function as demonstrated by:

* Lack of symptomatic congestive heart failure and clinically significant cardiac arrhythmias and ischemic heart disease.
* Left ventricular ejection fraction (LVEF) \> 50% for individuals appropriate for intensive therapy.
* Adequate liver function as demonstrated by:

* Aspartate aminotransferase ≤ 3.0 × upper limit of normal (ULN).
* Alanine aminotransferase ≤ 3.0 × ULN.
* Total bilirubin ≤ 1.5 × ULN, or primary unconjugated bilirubin ≤ 3.0 × ULN if individual has a documented history of Gilbert's syndrome or genetic equivalent.
* Pretreatment blood cross-match completed.
* Males and females of childbearing potential who engage in heterosexual intercourse must agree to use protocol-specified method(s) of contraception.
* Individuals must be willing to consent to mandatory pretreatment and on-treatment bone marrow biopsies (aspirate and trephines).

Exclusion Criteria

* Positive serum pregnancy test.
* Breastfeeding female.
* Known hypersensitivity to any of the study drugs, the metabolites, or formulation excipient.
* Prior treatment with any of the following:

* Cluster of differentiation 47 (CD47) or signal regulatory protein alpha (SIRPα)-targeting agents
* Antileukemic therapy for the treatment of AML (excluding hydroxyurea), hypomethylating agent (HMA), low dose cytarabine and/or venetoclax.

Note: Individuals with prior myelodysplastic syndrome (MDS) who have not received prior HMAs or chemotherapeutic agents for MDS are allowed on study. Other prior MDS therapies including, but not limited to, lenalidomide, erythroid stimulating agents, or similar red blood cell (RBC)-direct therapies, were allowed. Localized non-central nervous system (CNS) radiotherapy, erythroid and/or myeloid growth factors, hormonal therapy with luteinizing hormone-releasing hormone agonists for prostate cancer, hormonal therapy or maintenance for breast cancer, and treatment with bisphosphonates and receptor activator of nuclear factor kappa-B ligand inhibitors are also not criteria for exclusion.

* Individuals who are appropriate for intensive treatment but who have been previously treated with maximum cumulative doses of idarubicin and/or other anthracyclines and anthracenediones will be excluded.
* Individuals receiving any live vaccine within 4 weeks prior to initiation of study treatments.
* For individuals appropriate for intensive therapy, individuals treated with trastuzumab within 7 months prior to initiation of study treatments.
* Current participation in another interventional clinical study.
* Known inherited or acquired bleeding disorders.
* Individuals appropriate for non-intensive therapy, who have received treatment with strong and/or moderate cytochrome P450 enzyme 3A (CYP3A) inducers within 7 days prior to the initiation of study treatments.
* Individuals appropriate for non-intensive therapy who have consumed grapefruit, grapefruit products, Seville oranges (including marmalade containing Seville oranges) or starfruit within 3 days prior to the initiation of study treatment.
* Individuals appropriate for non-intensive therapy who have malabsorption syndrome or other conditions that preclude enteral route of administration.
* Clinical suspicion of active CNS involvement with AML.
* Individuals who have acute promyelocytic leukemia.
* Significant disease or medical conditions, as assessed by the investigator and sponsor, that would substantially increase the risk-benefit ratio of participating in the study. This includes, but is not limited to, acute myocardial infarction within the last 6 months, unstable angina, uncontrolled diabetes mellitus, significant active infections, and congestive heart failure New York Heart Association Class III-IV.
* Second malignancy, except MDS, treated basal cell or localized squamous skin carcinomas, localized prostate cancer, or other malignancies for which individuals are not on active anti-cancer therapies and have had no evidence of active malignancy for at least ≥ 1 year Note: Individuals on maintenance therapy alone who have no evidence of active malignancy for at least ≥ 1 year are eligible.
* Known active or chronic hepatitis B virus (HBV) or hepatitis C virus (HCV) infection or human immunodeficiency virus (HIV) infection in medical history.
* Active HBV, and/or active HCV, and/or HIV following testing at screening:

* Individuals who test positive for hepatitis B surface antigen (HBsAg). Individuals who test positive for hepatitis B core antibody (anti-HBc) will require HBV deoxyribose nucleic acid (DNA) by quantitative polymerase chain reaction (PCR) for confirmation of active disease.
* Individuals who test positive for HCV antibody. These individuals will require HCV ribose nucleic acid (RNA) quantitative PCR for confirmation of active disease.
* Individuals who test positive for HIV antibody.
* Individuals not currently receiving antiviral therapy and who have an undetectable viral load in the prior 3 months may be eligible for the study.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Gilead Sciences

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Gilead Study Director

Role: STUDY_DIRECTOR

Gilead Sciences

Locations

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Nagasaki University Hospital

Nagasaki, , Japan

Site Status

University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

City of Hope (City of Hope National Medical Center, City of Hope Medical Center)

Duarte, California, United States

Site Status

USC/ Norris Comprehensive Cancer Center

Los Angeles, California, United States

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Ronald Reagan UCLA Medical Center

Los Angeles, California, United States

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UC Irvine Health

Orange, California, United States

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Colorado Blood Cancer Institute

Denver, Colorado, United States

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Mayo Clinic Florida

Jacksonville, Florida, United States

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Miami Cancer Institute

Miami, Florida, United States

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AdventHealth Orlando

Orlando, Florida, United States

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Memorial Cancer Institute

Pembroke Pines, Florida, United States

Site Status

Moffitt Cancer Center

Tampa, Florida, United States

Site Status

Winship Cancer Institute

Atlanta, Georgia, United States

Site Status

Northwestern Memorial Hospital/Main Lab

Chicago, Illinois, United States

Site Status

The University of Chicago Medical Centre

Chicago, Illinois, United States

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University of Kansas Hospital

Fairway, Kansas, United States

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University of Kentucky Medical Center

Lexington, Kentucky, United States

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Tulane Medical center

New Orleans, Louisiana, United States

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Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins

Baltimore, Maryland, United States

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Massachusetts General Hospital

Boston, Massachusetts, United States

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Dana-Farber Cancer Institute

Boston, Massachusetts, United States

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Mayo Clinic Cancer Center Outpatient Pharmacy

Rochester, Minnesota, United States

Site Status

MidAmerica Division, Inc., c/o Research Medical Center

Kansas City, Missouri, United States

Site Status

SSM Health Saint Louis University Hospital

St Louis, Missouri, United States

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Roswell Park Cancer Institute

Buffalo, New York, United States

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Columbia University Medical Center - Herbert Irving Pavilion

New York, New York, United States

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UNC Hospitals, The University of North Carolina at Chapel Hill

Chapel Hill, North Carolina, United States

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Duke Blood Cancer Center

Durham, North Carolina, United States

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The Ohio State University Wexner Medical Center/ James Cancer Hospital

Columbus, Ohio, United States

Site Status

University of Oklahoma Health Sciences Center - OU Health Stephenson Cancer Center

Oklahoma City, Oklahoma, United States

Site Status

Thomas Jefferson University, Sidney Kimmel Cancer Center, Clinical Research Organization

Philadelphia, Pennsylvania, United States

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St. Francis Cancer Center

Greenville, South Carolina, United States

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Prisma Health Cancer Institute

Greenville, South Carolina, United States

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Baylor College of Medicine Medical Center

Houston, Texas, United States

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The University of Texas MD Anderson Cancer Center

Houston, Texas, United States

Site Status

Huntsman Cancer Institute ,The University of Utah

Salt Lake City, Utah, United States

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Froedtert Hospital / Medical College of Wisconsin

Milwaukee, Wisconsin, United States

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Canberra Hospital

Garran, Australian Capital Territory, Australia

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Calvary Master Newcastle

Waratah, New South Wales, Australia

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Westmead Hospital / Department of Haematology and Bone Marrow Transplantation

Westmead, New South Wales, Australia

Site Status

Princess Alexandra Hospital

Woolloongabba, Queensland, Australia

Site Status

Royal Adelaide Hospital

Adelaide, South Australia, Australia

Site Status

Andrew Love Cancer Centre, University Hospital Geelong

Geelong, Victoria, Australia

Site Status

The Alfred

Melbourne, Victoria, Australia

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St Vincents Hospital Melbourne

Melbourne, Victoria, Australia

Site Status

Fiona Stanley Hospital

Murdoch, Western Australia, Australia

Site Status

Royal Perth Hospital

Perth, Western Australia, Australia

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Univ. -Klinik für Hämatologie und Internistische Onkologie, Kepler Universitätskilkun GmbHMed

Linz, , Austria

Site Status

Uniklinikum Salzburg, Universitatsklinik f. Innere Medizin III der PMU

Salzburg, , Austria

Site Status

Algemeen Ziekenhuis Sint-Jan Brugge-Oostende AV

Bruges, , Belgium

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Universitair Ziekenhuis Brussel

Brussels, , Belgium

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Grand Hôpital De Charleroi - Notre Dame

Charleroi, , Belgium

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Universitaire Ziekenhuis Antwerpen

Edegem, , Belgium

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Universitair Ziekenhuis Gent

Ghent, , Belgium

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AZ Delta vzw

Roeselare, , Belgium

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Tom Baker Cancer Center

Calgary, , Canada

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Queen Elizabeth II Health Sciences Centre

Halifax, , Canada

Site Status

CIUSSS de L'Est-de-L'Ile-de- Montreal - Hopital Maisonneuve-Rosemont

Montreal, , Canada

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McGill University Health Centre

Montreal, , Canada

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Sunnybrook Research Institute

Toronto, , Canada

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Princess Margaret Cancer Centre

Toronto, , Canada

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Aalborg University Hospital

Aalborg, , Denmark

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Odense University Hospital

Odense C, , Denmark

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CHU d'Angers

Angers, , France

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CHU de Caen

Caen, , France

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CHRU Lille - Hospital Claude Huriez

Lille, , France

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CHU Limoges

Limoges, , France

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Central Hospital Lyon Sud

Lyon, , France

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Institut Paoli Calmettes

Marseille, , France

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CHU de Nantes, Hotel Dieu

Nantes, , France

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CHU Nice - Hopital Archet 1

Nice, , France

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Gustave Roussy

Paris, , France

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Hopital Haut-Leveque

Pessac, , France

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IUCT Oncopole

Toulouse, , France

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Hopitaux de Brabois

Vandœuvre-lès-Nancy, , France

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Uniklinik RWTH Aachen, Medizinische Klunuk IV - Klinik fur Hamatologie, Onkologie, Hamastaseologie und Srammzelltransplantation

Aachen, , Germany

Site Status

Dept. of Hematology, Oncology and Tumor Immunology, Charite- University Medicine Berlin, Campus Virchow Klinikum

Berlin, , Germany

Site Status

Department of Hematology and Oncology, Braunschweig Community Hospital

Braunschweig, , Germany

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Universitatsklinikum Koln

Cologne, , Germany

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Universitatsklinikum Carl Gustav Carus Dresden an der Technische Universitat Dresden, Medizinische Klinik und Poliklinik 1, Bereich Hamatologie

Dresden, , Germany

Site Status

Universitätsklinikum Düsseldorf -Klinik für Hämatologie, Onkologie und Klinische Immunologie

Düsseldorf, , Germany

Site Status

Dept. of Medicine II, University Hospital Hamburg-Eppendorf

Hamburg, , Germany

Site Status

Universitatsklinikum Heidelberg, Innere Medizin V, Hamatologie, Onkologie und Rheumatologie

Heidelberg, , Germany

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Universitatsklinikum Schleswig-Holstein

Kiel, , Germany

Site Status

Klinikum Ludwigshafen Medizinische Klinik A

Ludwigshafen, , Germany

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LMU - Klinikum der Universitat Munchen, Medizinische Klinik und Poliklinik III, Campus Grosshadern

München, , Germany

Site Status

Klinikum rechts der Isar der Technischen Universitat Munchen, Klinik und Poliklinik fur Innere Medizin III

München, , Germany

Site Status

Universitatsklinikum Ulm, Zentrum fur Innere Medizin, Innere Medizin III

Ulm, , Germany

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Prince of Wales Hospital, The Chinese University of Hong Kong

Hong Kong, , Hong Kong

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Queen Mary Hospital

Hong Kong, , Hong Kong

Site Status

Azienda Ospedaliero Universitaria delle Marche

Ancona, , Italy

Site Status

AOU Consorziale Policlinico Bari

Bari, , Italy

Site Status

Azienda Ospedaliero-Universitaria di Bologna Policlinico Sant'Orsola-Malphigi U.O Ematologia

Bologna, , Italy

Site Status

Istituto Romagnolo per lo Studio dei Tumori "Dino Amadori" - IRS - Oncologia Medica

Meldola, , Italy

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Azienda Ospedaliera di Rilievo Nazionale Antonio Cardarelli U.O.S.C. di Ematologia con Trapianto di Midollo Osseo

Napoli, , Italy

Site Status

SC Ematologia, Azienda Ospedaliera di Perugia - Santa Maria della Misericordia

Perugia, , Italy

Site Status

AORM - AO Riuniti Marche Norde - Pesaro Presidio "San Salvatore" - Muraglia

Pesaro, , Italy

Site Status

Fondazione PTV Policinico Tor Vergata

Roma, , Italy

Site Status

SCDU Ematologia e Terrapie cellulari AO O Ordine Mauriziano Torino

Torino, , Italy

Site Status

ASST Sette Laghi - Ospedale di Circolo e Fondazione Macchi

Varese, , Italy

Site Status

Hyogo Prefectural Amagasaki General Medical Center

Amagasaki, , Japan

Site Status

Chiba Aoba Municipal Hospital

Chiba, , Japan

Site Status

University of Yamanashi Hospital

Chūō, , Japan

Site Status

Kyushu University Hospital

Fukuoka, , Japan

Site Status

Fukushima Medical University Hospital

Fukushima, , Japan

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Aiiku Hospital

Hokkaido, , Japan

Site Status

Tokai University School of Medicine

Isehara, , Japan

Site Status

Kanazawa University Hospital

Kanazawa, , Japan

Site Status

National Cancer Center Hospital East

Kashiwa, , Japan

Site Status

Hospital of the University of Occupational and Environmental Health, Japan

Kitakyushu-shi, , Japan

Site Status

Kobe City Medical Center General Hospital

Kobe, , Japan

Site Status

Gunmaken Saiseikai Maebashi Hospital

Maebashi, , Japan

Site Status

Ehime Prefectural Center Hospital

Matsuyama, , Japan

Site Status

Japanese Red Cross Aichi Medical Center Nagoya Daiichi Hospital

Nagoya, , Japan

Site Status

Japanese Red Cross Aichi Medical Center Nagoya Daini Hospital

Nagoya, , Japan

Site Status

Okayama University Hospital

Okayama, , Japan

Site Status

Osaka Metropolitan University Hospital

Osaka, , Japan

Site Status

Kindai University Hospital

Sayama, , Japan

Site Status

National University Corporation Tohoku University Tohoku University Hospital

Sendai, , Japan

Site Status

NTT Medical Center Tokyo

Shinagawa-Ku, , Japan

Site Status

Yamagata University Hospital

Yamagata, , Japan

Site Status

University of Fukui Hospital

Yoshida-gun, , Japan

Site Status

Hospital General Universitario de Alicante

Alicante, , Spain

Site Status

Hospital del la Santa Creu i Sant Pau

Barcelona, , Spain

Site Status

Hospital Universitari Vall d'Hebron

Barcelona, , Spain

Site Status

Hospital Clinic de Barcelona

Barcelona, , Spain

Site Status

Institut Catala d'Oncologia

Barcelona, , Spain

Site Status

Complejo Asistencial Universitario de Burgos/H.U. de Burgos

Burgos, , Spain

Site Status

Complejo Hospitalario San Pedro de Alcantara

Cáceres, , Spain

Site Status

Hospital Universitario Reina Sofia

Córdoba, , Spain

Site Status

Hospital Universitario de Gran Canaria Doctor Negrin

Las Palmas de Gran Canaria, , Spain

Site Status

Hospital Universitario de La Princesa

Madrid, , Spain

Site Status

Hospital General Universitario Gregorio Maranon

Madrid, , Spain

Site Status

MD Anderson Cancer Center Madrid

Madrid, , Spain

Site Status

Hospital Regional Universitario de Malaga

Málaga, , Spain

Site Status

Hospital Universitario Central de Asturias

Oviedo, , Spain

Site Status

Clinica Universidad de Navarra - Pamplona (Main Site)

Pamplona, , Spain

Site Status

Complejo Asistencial Universitario de Salamanca - Hsopital Clinico

Salamanca, , Spain

Site Status

Hospital U. Marques de Valdecilla

Santander, , Spain

Site Status

Hospital Clinico Universitario de Valencia

Valencia, , Spain

Site Status

Hospital Universitari I Politècnic La Fe

Valencia, , Spain

Site Status

Universitetssjukhus, Hematologimottagnungen

Lund, , Sweden

Site Status

Universitatsspital Basel - Klinik fur Hamatrologie, Bereich Innere Medizin

Basel, , Switzerland

Site Status

Inselspital, Universitatsspital Bern - Universitatsklinik fur Medizinisch Onkologie

Bern, , Switzerland

Site Status

University Hospitals Birmingham NHS Foundation Trust

Birmingham, , United Kingdom

Site Status

United Lincolnshire Hospitals NHS Trust, Pilgrim Hospital, Sibsey Road

Boston, , United Kingdom

Site Status

Cambridge University Hospital NHS Foundation Trust

Cambridge, , United Kingdom

Site Status

Cardiff and Vale University Health Board

Cardiff Wales, , United Kingdom

Site Status

Barts Health NHS Trust

City of London, , United Kingdom

Site Status

NHS Tayside

Dundee, , United Kingdom

Site Status

Beatson West of Scotland Cancer Centre

Glasgow, , United Kingdom

Site Status

University College London Hospitals NHS Foundation Trust

London, , United Kingdom

Site Status

King's College NHS Foundation Trust

London, , United Kingdom

Site Status

Oxford University Hospital NHS Foundation Trust

Oxford, , United Kingdom

Site Status

The Royal Marsden NHS Foundation Trust

Sutton, , United Kingdom

Site Status

The Christie NHS Foundation Trust

Withington, , United Kingdom

Site Status

Countries

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United States Australia Austria Belgium Canada Denmark France Germany Hong Kong Italy Japan Spain Sweden Switzerland United Kingdom

References

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Zeidner JF, Sallman DA, Recher C, Daver NG, Leung AYH, Hiwase DK, Subklewe M, Pabst T, Montesinos P, Larson RA, Wilde L, Enjeti AK, Kawashima I, Papayannidis C, O'Nions J, Johnson L, Dong M, Huang J, Bagheri T, Hacohen Kleiman G, Lee C, Vyas P. Magrolimab plus azacitidine vs physician's choice for untreated TP53-mutated acute myeloid leukemia: the ENHANCE-2 study. Blood. 2025 Jul 31;146(5):590-600. doi: 10.1182/blood.2024027408.

Reference Type DERIVED
PMID: 40009500 (View on PubMed)

Daver NG, Vyas P, Kambhampati S, Al Malki MM, Larson RA, Asch AS, Mannis G, Chai-Ho W, Tanaka TN, Bradley TJ, Jeyakumar D, Wang ES, Sweet K, Kantarjian HM, Garcia-Manero G, Komrokji R, Xing G, Ramsingh G, Renard C, Zeidner JF, Sallman DA. Tolerability and Efficacy of the Anticluster of Differentiation 47 Antibody Magrolimab Combined With Azacitidine in Patients With Previously Untreated AML: Phase Ib Results. J Clin Oncol. 2023 Nov 1;41(31):4893-4904. doi: 10.1200/JCO.22.02604. Epub 2023 Sep 13.

Reference Type DERIVED
PMID: 37703506 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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Other Identifiers

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2020-003949-11

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

jRCT2071220076

Identifier Type: OTHER

Identifier Source: secondary_id

GS-US-546-5857

Identifier Type: -

Identifier Source: org_study_id

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