Intermediate Expanded Access Protocol CNMAu8.EAP04

NCT ID: NCT06408727

Last Updated: 2025-01-28

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

AVAILABLE

Study Classification

EXPANDED_ACCESS

Brief Summary

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An Intermediate Expanded Access Protocol (EAP) with CNM-Au8 for Amyotrophic Lateral Sclerosis for NIH Grant RFA-NS-23-012

Detailed Description

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An Intermediate Expanded Access Protocol (EAP) with CNM-Au8 for Amyotrophic Lateral Sclerosis for NIH Grant RFA-NS-23-012. The primary objective of this intermediate EAP is to provide access to the investigational product, CNM-Au8 30mg, for up to 180 people living with ALS.

Conditions

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ALS Amyotrophic Lateral Sclerosis PALS

Interventions

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CNM-Au8

CNM-Au8 (cellular energetic nanocatalyst). Faceted clean-surfaced catalytically-active Au nanocrystals.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Able to understand and give written informed consent.
2. Male or female participants aged 18 years or greater (inclusive) at the time of informed consent completion.
3. Participants with a confirmed diagnosis of ALS per Gold Coast criteria as determined by a neurologist specializing in ALS (e.g., the site principal investigator or sub-investigator for this study).
4. Participant is able to daily consume up to 60 mL of the investigational drug suspension without substantial dysphagia, OR can intake the investigational product through a feeding tube.
5. Participant must have completed standard clinical safety labs within the prior 90 days from the Baseline visit, including a chemistry panel (e.g., CMP) and a hematology panel (e.g., CBC).
6. Participant has a baseline score by the TRICALS risk calculator that is less than -2 (i.e., participant is not at increased risk of early death; https://tricals.shinyapps.io/risk-profile/).
7. Participant meets the following criteria:

1. Baseline Vital Capacity \>15% predicted,
2. Baseline ALSFRS-R Score \>8, and,
3. Baseline BMI \>17.5 kg/m2
8. Participants have established care with a neurologist at the specialized ALS center or remotely enrolling site involved in the study and will maintain this clinical care throughout the duration of the EAP within the United States.

Exclusion Criteria

1. Participant is eligible for participation in any double-blind placebo-controlled study the treatment of ALS at the same research site.
2. Participant has a history of any clinically significant or unstable medical condition (other than ALS) that may interfere with assessment of safety or compromise the study objectives.
3. Based on the investigator's judgment, participants who may have difficulty complying with the protocol and/or any study procedures.
4. Within the prior 90-days the participant has had clinically significant findings on standard hepatic, hematologic, or renal safety assays, including but not limited to: (i) ALT or AST ≥ 3 times upper limits of normal, (ii) direct (conjugated) with bilirubin ≥2 times upper limits of normal, (iii) low platelet counts (\< 150 x 109 per liter) or eosinophilia (absolute eosinophil count of ≥ 500 eosinophils per microliter), (iv) serum creatinine \>1.2 mg/dL, or (v) eGFR \< 45 ml/min per 1.73 m2.
5. Participant is currently involved in another placebo-controlled clinical trial (note: concomitant therapy with other investigational products is permitted with certain restrictions-see concomitant medications below).
6. Females who are pregnant or nursing or who plan to get pregnant during the EAP, or within 6 months of the end of this trial.
7. Females of child-bearing potential, or men, who are unwilling or unable to use accepted methods of birth control.
8. History of gold allergy.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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National Institute of Neurological Disorders and Stroke (NINDS)

NIH

Sponsor Role collaborator

Clene Nanomedicine

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Nova Southeastern University

Fort Lauderdale, Florida, United States

Site Status AVAILABLE

Northwestern University

Chicago, Illinois, United States

Site Status AVAILABLE

Synapticure

Chicago, Illinois, United States

Site Status AVAILABLE

University of Iowa

Iowa City, Iowa, United States

Site Status AVAILABLE

Columbia Unniversity

New York, New York, United States

Site Status AVAILABLE

Duke University

Durham, North Carolina, United States

Site Status AVAILABLE

Pennsylvania State University

Hershey, Pennsylvania, United States

Site Status AVAILABLE

Texas Neurology

Dallas, Texas, United States

Site Status AVAILABLE

Countries

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United States

Central Contacts

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Austin Rynders, BS

Role: CONTACT

(801)676-9695

Jeremy Evan, PA-C

Role: CONTACT

(801)676-9695

Facility Contacts

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Donovan Mott

Role: primary

954-203-2829

Cadace James

Role: primary

312-503-0747

Mercedes Guevara

Role: primary

708-630-1534

Emily Anderson

Role: primary

319-356-8755

Role: primary

212-305-6788

Michelle Ward

Role: primary

919-613-2681

Hailey Zampa

Role: backup

919-613-2681

Wint Nandar

Role: primary

717-531-8257

Mohamad Nasri

Role: primary

214-827-3610 ext. 251

Other Identifiers

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1U01NS136023-01

Identifier Type: NIH

Identifier Source: secondary_id

View Link

CNMAu8.EAP04

Identifier Type: -

Identifier Source: org_study_id

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