VTP-1000 in Adults With Celiac Disease

NCT ID: NCT06310291

Last Updated: 2026-01-09

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

EARLY_PHASE1

Total Enrollment

45 participants

Study Classification

INTERVENTIONAL

Study Start Date

2024-08-01

Study Completion Date

2026-06-30

Brief Summary

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GLU001 is a first-in-human clinical trial to assess the safety and tolerability of VTP-1000 for adults with celiac disease. This trial will assess VTP-1000 at various dose levels compared to placebo in a single ascending dose (SAD) and multiple ascending dose (MAD) format. Participants will be followed for a short period of time to assess the impact of VTP-1000 on their immune system (Adverse events, reactions in the blood, and physical exam differences). Participants enrolled in the MAD portion of the trial will undergo a gluten challenge to assess the impact exposure to gluten has on participants after administration of VTP-1000.

Detailed Description

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VTP-1000 is a gluten-derived (GLU) peptide immunotherapy that is designed to induce antigen-specific immune tolerance against gluten in patients with celiac disease. The technology underlying VTP-1000 consists of the sponsor's proprietary self-assembling nanoparticles based on amphiphilic peptides tolerance immunotherapy (SNAP-TI) platform which has been configured to package 12 GLU peptide antigens and rapamycin into nanoparticles of \~20 nm diameter.

The goal of treatment with VTP-1000 is to induce tolerance to gluten in patients with coeliac disease by activating antigen-specific regulatory T (Treg) cells that promote tolerance and reducing pre-existing, pathogenic antigen-specific effector T (Teff) cells that underly disease pathogenesis. In turn, this may allow for better management of the condition.

GLU001 is a multi-center phase I first in human study to assess the safety and tolerability of VTP-1000 in adults with celiac disease. The trial also aims to demonstrate proof-of-principle of induction of immune tolerance and early proof-of-concept for VTP-1000 as a potential treatment for coeliac disease based on assessment of pharmacodynamics and preliminary efficacy determined by means of a controlled gluten challenge.

GLU001 will be conducted as a randomized double-blind placebo-controlled study in two parts - Part A and Part B. Part A will be a single ascending dose (SAD) followed by Part B a multiple ascending dose (MAD) which incorporates a gluten challenge.

Part A (Single Ascending Dose)

A stepwise single dose escalation of 3 dose levels of VTP-1000 is planned. A total of 6 participants will be treated at each dose level (4 will receive VTP-1000 and 2 will receive matched placebo). A sentinel dosing approach will be followed, with the first 2 participants randomized to receive VTP1000 or placebo in a 1:1 ratio. Subsequent participants will be randomized in a 3:1 ratio at least 7 days after the second sentinel participant has received trial intervention. Participants will be screened for eligibility up to 28 days prior treatment. Participants will be followed for 21 days after dosing including a 3-day domicile period following administration of VTP-1000.

Part B (Multiple Ascending Dose)

A stepwise multiple dose escalation of up to 3 dose levels of VTP-1000 is planned. A total of 8 participants will be treated at each dose level (6 will receive VTP-1000 and 2 will receive matched placebo). A sentinel dosing approach will be followed, with the first 2 participants randomized to receive VTP1000 or placebo in a 1:1 ratio. Subsequent participants will be randomized in a 3:1 ratio at least 7 days after the second sentinel participant has received trial intervention. Participants will be screened for eligibility up to 28 days prior to the start of treatment. Eligible participants will receive 3 doses of trial intervention every 2 weeks at a given dose level with and followed for 57 days. After completion of the third dose of trial intervention, participants will undergo a gluten challenge.

Conditions

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Celiac Disease

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

SEQUENTIAL

The Single Ascending Dose part of the trial contains a placebo controlled randomized 4+2 design, where four participants will receive active IMP and two placebo. The Multiple Ascending Dose is a standard sequential design
Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Matched Placebo (SAD)

2 placebo comparators; 1 for each part of the study

Group Type PLACEBO_COMPARATOR

Matched Placebo

Intervention Type OTHER

Intramuscular (IM) injection comprised of saline solution

VTP-1000 Dose 1 (SAD)

3 dose levels in SAD and MAD parts of trial

Group Type EXPERIMENTAL

VTP-1000

Intervention Type BIOLOGICAL

Intramuscular (IM) injection comprised of self-assembling nanoparticles of gluten peptides and a rapamycin component

VTP-1000 Dose 2 (SAD)

3 dose levels in SAD and MAD parts of trial

Group Type EXPERIMENTAL

VTP-1000

Intervention Type BIOLOGICAL

Intramuscular (IM) injection comprised of self-assembling nanoparticles of gluten peptides and a rapamycin component

VTP-1000 Dose 3 (SAD)

3 dose levels in SAD and MAD parts of trial

Group Type EXPERIMENTAL

VTP-1000

Intervention Type BIOLOGICAL

Intramuscular (IM) injection comprised of self-assembling nanoparticles of gluten peptides and a rapamycin component

Matched Placebo (MAD)

2 placebo comparators; 1 for each part of the study

Group Type PLACEBO_COMPARATOR

Matched Placebo

Intervention Type OTHER

Intramuscular (IM) injection comprised of saline solution

VTP-1000 Dose 1 (MAD)

3 dose levels in SAD and MAD parts of trial

Group Type EXPERIMENTAL

VTP-1000

Intervention Type BIOLOGICAL

Intramuscular (IM) injection comprised of self-assembling nanoparticles of gluten peptides and a rapamycin component

VTP-1000 Dose 2 (MAD)

3 dose levels in SAD and MAD parts of trial

Group Type EXPERIMENTAL

VTP-1000

Intervention Type BIOLOGICAL

Intramuscular (IM) injection comprised of self-assembling nanoparticles of gluten peptides and a rapamycin component

VTP-1000 Dose 3 (MAD)

3 dose levels in SAD and MAD parts of trial

Group Type EXPERIMENTAL

VTP-1000

Intervention Type BIOLOGICAL

Intramuscular (IM) injection comprised of self-assembling nanoparticles of gluten peptides and a rapamycin component

Interventions

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VTP-1000

Intramuscular (IM) injection comprised of self-assembling nanoparticles of gluten peptides and a rapamycin component

Intervention Type BIOLOGICAL

Matched Placebo

Intramuscular (IM) injection comprised of saline solution

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

* Diagnosis of celiac disease as confirmed by positive serology and intestinal histology
* Presence of Human Leukocyte Antigen (HLA)-DQ2.5 genotype
* Participants who are on a well controlled gluten restricted diet
* Negative or weak positive anti-tissue transglutaminase (tTG) IgA antibodies and negative or weak positive anti-deamidated gliadin peptide IgG (anti-DGP)-IgA/IgA antibodies
* Non-pregnant or breast feeding females
* No other clinical significant findings at screening

Exclusion Criteria

* Refractory celiac disease
* Selective IgA deficiency
* Positive for HLA-DQ8
* Known wheat allergy or that is Type I hypersensitivity
* Active inflammatory bowel disease or other condition with symptoms that will be similar to celiac disease
Minimum Eligible Age

18 Years

Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Barinthus Biotherapeutics

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Parexel EPCU LA

Los Angeles, California, United States

Site Status RECRUITING

Peak Gastroenterology Associates

Colorado Springs, Colorado, United States

Site Status RECRUITING

Jacksonville Center for Clinical Research

Jacksonville, Florida, United States

Site Status RECRUITING

GCP Research

St. Petersburg, Florida, United States

Site Status RECRUITING

Parexel EPCU Baltimore

Baltimore, Maryland, United States

Site Status RECRUITING

Clinical Research Institute of Michigan

Clinton Township, Michigan, United States

Site Status RECRUITING

West Michigan Clinical Research Center

Wyoming, Michigan, United States

Site Status RECRUITING

Mayo Clinic

Rochester, Minnesota, United States

Site Status RECRUITING

NYU Langone - Gastroenterology Associates

New York, New York, United States

Site Status RECRUITING

North Carolina Clinical Research

Raleigh, North Carolina, United States

Site Status RECRUITING

Centricity Research

Columbus, Ohio, United States

Site Status RECRUITING

Vanderbilt University Medical Center

Nashville, Tennessee, United States

Site Status RECRUITING

PPD Research Unit

Austin, Texas, United States

Site Status RECRUITING

Velocity Clinical Research, Salt Lake City

West Jordan, Utah, United States

Site Status RECRUITING

Clinical Research Partners

Richmond, Virginia, United States

Site Status RECRUITING

Velocity Clinical Research, Seattle

Seattle, Washington, United States

Site Status RECRUITING

Countries

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United States

Facility Contacts

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Jess Mehrasaz

Role: primary

(626)298 2756

Rutva Nakarani

Role: primary

719-636-1201

Sara Villotti

Role: primary

(904) 730-0101

Jessica Cruz

Role: primary

(727) 520-1427

Jess Mehrsaz

Role: primary

(626) 298-2756

Molly Wythe

Role: primary

586-598-3329

Rochelle Copeland

Role: primary

616-328-5344

Chadrick Hinson

Role: primary

(507) 266-0237

Valeria Pasuizaca-Yanez

Role: primary

212-263-3095

Daunita Audesuyi

Role: primary

(919) 881-0309

Stephanie Scarberry

Role: primary

(614) 501-6164

Mary Vozar

Role: primary

615-936-1288

Al Gonzalez

Role: primary

(512) 747-4656

Srinivas Mulamalla

Role: primary

801-542-8190

Aundraya Bray

Role: primary

804-477-3045

Luis Casanova

Role: primary

206-710-1574

Other Identifiers

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GLU001

Identifier Type: -

Identifier Source: org_study_id

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