Expanding Liver Transplant Immunosuppression Minimization Via Everolimus

NCT ID: NCT06280950

Last Updated: 2025-05-31

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

340 participants

Study Classification

INTERVENTIONAL

Study Start Date

2024-09-12

Study Completion Date

2029-06-01

Brief Summary

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This is a study to determine the safety, efficacy, and tolerability of taking away the anti-rejection medicine, tacrolimus, in liver transplant recipients in conjunction with everolimus monotherapy to preserve renal function. Two hundred - seventy (270) subjects will be randomized 2:1 into one of two groups between 2-3 months post-transplant. Seventy participants will be placed into an observational group and will remain on their current post-transplant medications. The duration of the study from time of enrollment is 18-20 months.

Detailed Description

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This study is a multicenter 2:1 randomized nonblinded phase II interventional clinical trial in liver transplant recipients. The primary objective is to determine the safety, efficacy, and tolerability of tacrolimus minimization and eventual withdrawal in conjunction with everolimus monotherapy to preserve renal function. Study subjects will undergo first reduction of tacrolimus with the addition of everolimus. If everolimus is tolerated, subjects will be randomized 2:1 into one of two interventional arms. The first interventional arm will undergo a stepwise reduction of tacrolimus and be on everolimus monotherapy for the remainder of the study. The second interventional arm will remain on the initial reduced tacrolimus dose and everolimus. If subjects prior to randomization are unable to tolerate everolimus, these subjects will be placed in the observational group. These subjects will stop taking everolimus and resume their immunosuppression therapy prior to study enrollment.

Conditions

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Liver Transplant

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Interventional Group 1

Participants in this group will slowly reduce their dose of tacrolimus and continue everolimus as their only immunosuppression medication.

Group Type EXPERIMENTAL

Everolimus

Intervention Type DRUG

* The first step is the addition of everolimus to participants in this group pre-randomization.
* Participants on a mycophenolate compound will stop taking it within 7 days of initiating everolimus, either by immediate discontinuation or a 7-day taper.
* Participants taking prednisone will taper off prednisone by 6 months post-transplant.
* The second step is tacrolimus minimization and withdrawal to everolimus monotherapy in this group after randomization.

Tacrolimus (continued reduction)

Intervention Type DRUG

* Participants randomized in this cohort will have their tacrolimus dose reduced by 50% following randomization.
* They will maintain this daily dose for 4 weeks/1 month (28-30 days). Tacrolimus withdrawal will occur in intervals of 30 days or 4 weeks.
* Each subsequent reduction will be based on LFT stability over the prior time interval before the next reduction

Interventional Group 2

Participants in this group will continue to take reduced Tacrolimus and Everolimus IS regimen.

Group Type EXPERIMENTAL

Tacrolimus (maintain 50% reduction)

Intervention Type DRUG

\- Participants randomized in this cohort maintain initial reduced dose of Tacrolimus and everolimus for study duration.

Everolimus

Intervention Type DRUG

* The first step is the addition of everolimus to participants in the interventional group pre-randomization.
* Participants on a mycophenolate compound will stop taking it within 7 days of initiating everolimus, either by immediate discontinuation or a 7-day taper.
* Participants taking prednisone will taper off prednisone by 6 months post-transplant.
* The second step is to continue on the reduced tacrolimus and everolimus regimen.

Observational Group

Participants in this group could not tolerate the addition of everolimus. These participants will not be randomized.

* Participants in this group will stop taking everolimus.
* Participants in this group will resume taking their tacrolimus +/- mycophenolate compound and prednisone immunosuppression regimen.

Group Type NO_INTERVENTION

No interventions assigned to this group

Interventions

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Everolimus

* The first step is the addition of everolimus to participants in this group pre-randomization.
* Participants on a mycophenolate compound will stop taking it within 7 days of initiating everolimus, either by immediate discontinuation or a 7-day taper.
* Participants taking prednisone will taper off prednisone by 6 months post-transplant.
* The second step is tacrolimus minimization and withdrawal to everolimus monotherapy in this group after randomization.

Intervention Type DRUG

Tacrolimus (continued reduction)

* Participants randomized in this cohort will have their tacrolimus dose reduced by 50% following randomization.
* They will maintain this daily dose for 4 weeks/1 month (28-30 days). Tacrolimus withdrawal will occur in intervals of 30 days or 4 weeks.
* Each subsequent reduction will be based on LFT stability over the prior time interval before the next reduction

Intervention Type DRUG

Tacrolimus (maintain 50% reduction)

\- Participants randomized in this cohort maintain initial reduced dose of Tacrolimus and everolimus for study duration.

Intervention Type DRUG

Everolimus

* The first step is the addition of everolimus to participants in the interventional group pre-randomization.
* Participants on a mycophenolate compound will stop taking it within 7 days of initiating everolimus, either by immediate discontinuation or a 7-day taper.
* Participants taking prednisone will taper off prednisone by 6 months post-transplant.
* The second step is to continue on the reduced tacrolimus and everolimus regimen.

Intervention Type DRUG

Other Intervention Names

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Zortress FK-506 FR-900506 Prograf Prograft FK-506 FR-900506 Prograf Prograft Zortress

Eligibility Criteria

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Inclusion Criteria

1. Subject and/or legal guardian must be able to understand and provide informed consent
2. Adult (age greater than or equal to 18 years of age at time of informed consent) recipient of first liver transplant alone (de novo)
3. Estimated glomerular filtration rate \>=30 ml/min/1.73m\^2 at enrollment using the CKD-EPI 2021 equation
4. Treatment with tacrolimus therapy, with or without mycophenolic acid derivatives and/or corticosteroids
5. Female subjects of childbearing potential with negative pregnancy test upon study entry
6. All subjects of reproductive potential agreeing to use contraception for the duration of the study
7. Previous vaccination or documented immunity to varicella, measles, hepatitis B, pneumococcus, influenza, zoster (if \>=19 years old), and 2019-nCoV (COVID-19) as outlined in the DAIT Vaccination Guideline

Exclusion Criteria

1. Inability or unwillingness of a participant to give written informed consent or comply with study protocol
2. Active unresolved systemic viral, bacterial, fungal, or parasitic infection requiring oral or intravenous anti-infective therapy
3. History of autoimmune liver disease including autoimmune hepatitis, primary sclerosing cholangitis, and/or primary biliary cirrhosis, or other contraindications to drug withdrawal
4. History of non-hepatic autoimmune disease requiring current or future systemic immunosuppressive therapy other than per study protocol
5. History post-transplant of Hepatic Artery Thrombosis or Portal Vein Thrombosis.
6. History of recurrent cirrhosis after liver transplantation.
7. Chronic use of systemic glucocorticoids, biological immunomodulatory therapy, or other immunosuppressive agents other than per study protocol
8. History of hepatitis B or C virus infection with detectable viral PCR at enrollment
9. History of prior organ transplantation (liver or other type)
10. History of \>= 2 biopsy-proven acute cellular rejection episodes of any severity, \>=1 moderate to severe rejection episode (histologically defined or requiring lymphodepletion therapy), or \>= 1 antibody- mediated rejection episode
11. Active treatment with any mTOR-inhibitor agent (everolimus, sirolimus)
12. Contraindication to treatment with everolimus (open wound or wound infection; urine protein: creatinine ratio \> 0.5; significant pancytopenia (any of the following: WBC \<1.5 K/uL or ANC \<1000 cells/uL or actively being treated with GCSF; Hb \<8.0; platelet count \<50K); serum triglycerides \> 1000 mg/dL; other per PI)
13. Abnormal liver function tests on study entry: Total Bilirubin (TB)\>1.5 mg/dL and Direct Bilirubin (DB) \>1.0 mg/dL, Alkaline Phosphatase (AP) \>200 U/L, and Alanine Aminotransaminase (ALT)\>60 U/L
14. Pregnant on enrollment or plan to become pregnant during the study period
15. Participation in another clinical trial that would interfere with this study's procedures and intervention:

1. Use of investigational biologic or drug (within 8 weeks of study enrollment)
2. Additional blood collection that would exceed research blood draw limits
3. Any other procedure or intervention, in the investigator's opinion would interfere with this study
16. Received live attenuated vaccine(s) within 2 months of enrollment
17. Current, diagnosed, mental illness or current, diagnosed, or self-reported drug or alcohol abuse that, in the opinion of the investigator, would interfere with the participant's ability to comply with study requirements or that may impact the quality or interpretation of the data obtained from the study
18. Past or current medical problems or findings from physical examination or laboratory testing that are not listed above, which, in the opinion of the investigator, may pose additional risks from participation in the study, may interfere with the participant's ability to comply with study requirements or that may impact the quality or interpretation of the data obtained from the study.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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National Institute of Allergy and Infectious Diseases (NIAID)

NIH

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Justin Boike, MD

Role: PRINCIPAL_INVESTIGATOR

Northwestern University Feinberg School of Medicine: Transplantation

Locations

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Mayo Clinic Hospital Arizona (Site #: 71144)

Phoenix, Arizona, United States

Site Status RECRUITING

University of California, San Francisco (Site #: 71108)

San Francisco, California, United States

Site Status RECRUITING

Northwestern University (Site #: 71110)

Chicago, Illinois, United States

Site Status RECRUITING

Icahn School of Medicine at Mount Sinai (Site #: 71115)

New York, New York, United States

Site Status RECRUITING

Duke University Medical Center (Site #: 71139)

Durham, North Carolina, United States

Site Status RECRUITING

University of Pennsylvania (Site #: 71111)

Philadelphia, Pennsylvania, United States

Site Status RECRUITING

University of Pittsburgh Medical Center (Site #: 71170)

Pittsburgh, Pennsylvania, United States

Site Status RECRUITING

Baylor Medical Center (Site #: 71153)

Dallas, Texas, United States

Site Status RECRUITING

Countries

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United States

Central Contacts

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Tracia Debnam, MS

Role: CONTACT

301-761-7414

Facility Contacts

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Latasha Bunkley

Role: primary

Joanna Kwan

Role: primary

415-476-2574

Laura Adams

Role: primary

312-694-0242

Bharathi Ramesh

Role: primary

212-241-4145

Linda Perry

Role: primary

919-684-4673

Alyssa Sliwa

Role: primary

215-982-0080

Beth Elinoff

Role: primary

Barbara Lilly

Role: primary

Other Identifiers

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DAIT CTOT-43

Identifier Type: -

Identifier Source: org_study_id

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