A Study to Assess Efficacy and Safety of KarXT for the Treatment of Psychosis Associated With Alzheimer's Disease (ADEPT-2)

NCT ID: NCT06126224

Last Updated: 2025-03-25

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

400 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-08-28

Study Completion Date

2025-07-31

Brief Summary

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This is a Phase 3, randomized, double-blind, placebo-controlled, parallel group study to evaluate the safety and efficacy of KarXT in male and female subjects who are aged 55 to 90 years and have mild to severe Alzheimer's Disease (AD) with moderate to severe psychosis related to AD.

The primary objective of the study is to evaluate the efficacy of KarXT compared with placebo in the treatment of subjects with psychosis associated with AD as measured by the Neuropsychiatric Inventory-Clinician (NPI-C): Hallucinations and Delusions (H+D) score.

Detailed Description

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Conditions

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Psychosis Associated With Alzheimer's Disease

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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KarXT

Xanomeline and Trospium Chloride Capsules

Group Type EXPERIMENTAL

KarXT

Intervention Type DRUG

KarXT 20/2 mg (total daily dose \[TDD\] 60/6 mg) KarXT 30/3 mg (TDD 90/9 mg) KarXT 40/4 mg (TDD 120/12 mg) KarXT 50/5 mg (TDD 150/15 mg) KarXT 66.7/6.67 mg (TDD 200/20 mg)

Placebo

Placebo Capsules

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo Capsules

Interventions

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KarXT

KarXT 20/2 mg (total daily dose \[TDD\] 60/6 mg) KarXT 30/3 mg (TDD 90/9 mg) KarXT 40/4 mg (TDD 120/12 mg) KarXT 50/5 mg (TDD 150/15 mg) KarXT 66.7/6.67 mg (TDD 200/20 mg)

Intervention Type DRUG

Placebo

Placebo Capsules

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Is a male or female aged 55 to 90 years, inclusive, at Screening.
2. Can understand the nature of the trial and protocol requirements and provide informed consent or assent before any study assessments are performed.
3. Meets clinical criteria for Possible AD or Probable AD.
4. Living at the same home or residential assisted-living facility for a minimum of 6 weeks before Screening.
5. Have an identified study partner who should have daily contact (approximately 10 hours a week or more).
6. History of psychotic symptoms (meeting International Psychogeriatric Association criteria) (Cummings 2020) for at least 2 months prior to Screening.
7. CGI-S scale with a score ≥ 4 at Screening and Baseline.
8. AD subjects are required to have NPI-C: Hallucinations and Delusions (H+D) score of ≥ 6 AND meet at least 1 of the following criteria at Screening and Baseline:

1. Moderate to severe delusions, defined as NPI-C: Delusions domain score of ≥ 2 on 2 of the 8 items OR
2. Moderate to severe hallucinations, defined as NPI-C: Hallucinations domain score of ≥ 2 on 2 of the 7 items
9. MMSE score of 8 to 22, inclusive, at Screening.

Exclusion Criteria

1. Psychotic symptoms that are primarily attributable to a condition other than the AD causing the dementia.
2. History of major depressive episode with psychotic features during the 12 months prior to Screening.
3. History of bipolar disorder, schizophrenia, or schizoaffective disorder.
4. Significant or severe medical conditions including pulmonary, hepatic, renal, hematologic, gastrointestinal, endocrine, immunologic, dermatologic, neurologic, cardiovascular, or oncologic disease or any other condition that, in the opinion of the Investigator, could jeopardize the safety of the subject, ability to complete or comply with the study procedures or validity of the study results.
5. History or high risk of urinary retention, gastric retention, or narrow-angle glaucoma as evaluated by the Investigator.
6. Prior exposure to KarXT.
7. History of hypersensitivity to KarXT excipients or trospium chloride.
8. Experienced any significant adverse events (AEs) due to trospium.
9. Participation in another clinical study in which the subject received an experimental or investigational drug within 3 months before Screening or has participated in more than 2 clinical studies in the 12 months prior to Screening.
Minimum Eligible Age

55 Years

Maximum Eligible Age

90 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Karuna Therapeutics

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Bristol-Myers Squibb

Role: STUDY_DIRECTOR

Bristol-Myers Squibb

Locations

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Local Institution - 1116

Chandler, Arizona, United States

Site Status

Local Institution - 1044

Phoenix, Arizona, United States

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Local Institution - 1104

Anaheim, California, United States

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Local Institution - 1119

Canoga Park, California, United States

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Local Institution - 1151

Encino, California, United States

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Local Institution - 1142

Lancaster, California, United States

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Local Institution - 1117

Los Alamitos, California, United States

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Local Institution - 1103

Sherman Oaks, California, United States

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Local Institution - 1007

Walnut Creek, California, United States

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Local Institution - 1156

Clermont, Florida, United States

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Local Institution - 1138

Cutler Bay, Florida, United States

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Local Institution - 1162

Delray Beach, Florida, United States

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Local Institution - 1164

Doral, Florida, United States

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Local Institution - 1165

Fort Myers, Florida, United States

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Local Institution - 1155

Hialeah, Florida, United States

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Local Institution - 1107

Hialeah, Florida, United States

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Local Institution - 1120

Hialeah, Florida, United States

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Local Institution - 1140

Hialeah, Florida, United States

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Local Institution - 0150

Homestead, Florida, United States

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Local Institution - 1145

Homestead, Florida, United States

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Local Institution - 1127

Largo, Florida, United States

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Local Institution - 1039

Maitland, Florida, United States

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Local Institution - 1146

Maitland, Florida, United States

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Local Institution - 1159

Miami, Florida, United States

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Local Institution - 1118

Miami, Florida, United States

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Local Institution - 1111

Miami, Florida, United States

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Local Institution - 1108

Miami, Florida, United States

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Local Institution - 1125

Miami, Florida, United States

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Local Institution - 1115

Miami, Florida, United States

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Local Institution - 1143

Miami, Florida, United States

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Local Institution - 1113

Miami, Florida, United States

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Local Institution - 1009

Miami, Florida, United States

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Local Institution - 1129

Miami, Florida, United States

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Local Institution - 1150

Miami, Florida, United States

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Local Institution - 1109

Miami, Florida, United States

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Local Institution - 1158

Miami, Florida, United States

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Local Institution - 1147

Miami, Florida, United States

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Local Institution - 1105

Miami, Florida, United States

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Local Institution - 1157

Miami, Florida, United States

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Local Institution - 1126

Miami Gardens, Florida, United States

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Local Institution - 1102

Miami Lakes, Florida, United States

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Local Institution - 1101

Okeechobee, Florida, United States

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Local Institution - 1136

Orlando, Florida, United States

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Local Institution - 1112

Orlando, Florida, United States

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Local Institution - 1137

Port Orange, Florida, United States

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Local Institution - 1133

Sweetwater, Florida, United States

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Local Institution - 1041

Tampa, Florida, United States

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Local Institution - 1124

Tampa, Florida, United States

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Local Institution - 1123

Tampa, Florida, United States

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Local Institution - 1110

Tampa, Florida, United States

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Local Institution - 1131

Viera, Florida, United States

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Decatur, Georgia, United States

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Local Institution - 1148

Elgin, Illinois, United States

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Local Institution - 1114

Marrero, Louisiana, United States

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Local Institution - 1139

Rochester Hills, Michigan, United States

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Local Institution - 1132

Flowood, Mississippi, United States

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Local Institution - 1122

Dayton, Ohio, United States

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Local Institution - 1106

Cypress, Texas, United States

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Local Institution - 1163

Houston, Texas, United States

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Local Institution - 1154

Katy, Texas, United States

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Local Institution - 1134

Stafford, Texas, United States

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Local Institution - 2801

Hasselt, Limburg, Belgium

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Local Institution - 2802

Leuven, Vlaams Brabant, Belgium

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Local Institution - 2803

Roeselare, West-Vlaanderen, Belgium

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Local Institution - 6002

Providencia, Santiago Metropolitan, Chile

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Local Institution - 6003

Antofagasta, , Chile

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Local Institution - 6001

Las Condes, , Chile

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Local Institution - 7007

Hefei, Anhui, China

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Local Institution - 7004

Beijing, Beijing Municipality, China

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Beijing, Beijing Municipality, China

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Chongqing, Chongqing Municipality, China

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Guangzhou, Guangdong, China

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Guangzhou, Guangdong, China

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Local Institution - 7009

Guangzhou, Guangdong, China

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Shenzhen, Guangdong, China

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Nanjing, Jiangsu, China

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Nanchang, Jiangxi, China

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Shanghai, Shanghai Municipality, China

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Shanghai, Shanghai Municipality, China

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Chengdu, Sichuan, China

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Local Institution - 7019

Tianjin, Tianjin Municipality, China

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Hangzhou, Zhejiang, China

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Hangzhou, Zhejiang, China

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Local Institution - 7006

Hangzhou, Zhejiang, China

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Local Institution - 7020

Hangzhou, Zhejiang, China

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Local Institution - 7018

Wenzhou, Zhejiang, China

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Local Institution - 4805

Athens, Attica, Greece

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Local Institution - 4803

Athens, Attica, Greece

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Local Institution - 4802

Chaidari, Athens, Attica, Greece

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Local Institution - 4806

Marousi, Attica, Greece

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Local Institution - 4801

Heraklion, , Greece

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Local Institution - 4601

Pécs, Baranya, Hungary

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Local Institution - 4602

Budapest, , Hungary

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Local Institution - 4603

Miskolc, , Hungary

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Local Institution - 1502

Saltillo Centro, Coahuila, Mexico

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Local Institution - 1503

Monterrey, Nuevo León, Mexico

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Local Institution - 1505

Monterrey, Nuevo León, Mexico

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Local Institution - 1501

Culiacán, Sinaloa, Mexico

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Local Institution - 1506

México, , Mexico

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Local Institution - 6103

Pueblo Libre, Lima region, Peru

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Local Institution - 4206

Lublin, Lublin Voivodeship, Poland

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Local Institution - 4207

Lodz, Lódzkie, Poland

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Local Institution - 4208

Katowice, Silesian Voivodeship, Poland

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Local Institution - 4204

Bydgoszcz, , Poland

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Katowice, , Poland

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Local Institution - 4202

Lodz, , Poland

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Local Institution - 4201

Ścinawa, , Poland

Site Status

Local Institution - 7208

Buk-gu, Daegu Gwang'yeogsi, South Korea

Site Status

Local Institution - 7207

Seongnam-si, Gyeonggido, South Korea

Site Status

Local Institution - 7205

Incheon, Incheon Gwang'yeogsi, South Korea

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Local Institution - 7202

Seongnam-si, , South Korea

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Local Institution - 7206

Seoul, , South Korea

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Local Institution - 7203

Seoul, , South Korea

Site Status

Local Institution - 7201

Seoul, , South Korea

Site Status

Local Institution - 4702

Atakum, Samsun, Turkey (Türkiye)

Site Status

Local Institution - 4701

Eskişehir, , Turkey (Türkiye)

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Local Institution - 4704

Istanbul, , Turkey (Türkiye)

Site Status

Local Institution - 4705

Izmir, , Turkey (Türkiye)

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Local Institution - 4703

Izmir, , Turkey (Türkiye)

Site Status

Countries

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United States Belgium Chile China Greece Hungary Mexico Peru Poland South Korea Turkey (Türkiye)

Related Links

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Other Identifiers

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KAR-032

Identifier Type: OTHER

Identifier Source: secondary_id

CN012-0027

Identifier Type: OTHER

Identifier Source: secondary_id

CN012-0027

Identifier Type: -

Identifier Source: org_study_id

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